Stem Cell Ophthalmology Treatment Study

NCT ID: NCT01920867

Last Updated: 2019-10-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

NA

Total Enrollment

300 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-08-31

Study Completion Date

2020-07-31

Brief Summary

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This study will evaluate the use of autologous bone marrow derived stem cells (BMSC) for the treatment of retinal and optic nerve damage or disease. http://mdstemcells.com/scots-ii/

Detailed Description

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Eyes with loss of vision from retinal or optic nerve conditions generally considered irreversible will be treated with a combination of injections of autologous bone marrow derived stem cells isolated from the bone marrow using standard medical and surgical practices. Retinal conditions may include degenerative, ischemic or physical damage ( examples may include macular degeneration, hereditary retinal dystrophies such as retinitis pigmentosa, stargardt, non-perfusion retinopathies, post retinal detachment. Optic Nerve conditions may include degenerative, ischemic or physical damage ( examples may include optic nerve damage from glaucoma, compression, ischemic optic neuropathy, optic atrophy ). Injections may include retrobulbar, subtenon, intravitreal, intraocular, subretinal and intravenous. Patients will be followed for 12 months with serial comprehensive eye examinations including relevant imaging and diagnostic ophthalmic testing.

Conditions

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Retinal Disease Macular Degeneration Hereditary Retinal Dystrophy Optic Nerve Disease Glaucoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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RB, ST, IV

Injections of BMSC retrobulbar (RB), subtenon (ST) and intravenous (IV)

Group Type ACTIVE_COMPARATOR

RB (Retrobulbar)

Intervention Type PROCEDURE

Retrobulbar injection of Bone Marrow Derived Stem Cells (BMSC)

ST (Subtenon)

Intervention Type PROCEDURE

Subtenon injection of Bone Marrow Derived Stem Cells (BMSC)

IV (Intravenous)

Intervention Type PROCEDURE

Intravenous injection of Bone Marrow Derived Stem Cells (BMSC)

RB, ST, IV, IVIT

Injections of BMSC retrobulbar, subtenon, intravenous and intravitreal ( IVIT )

Group Type ACTIVE_COMPARATOR

RB (Retrobulbar)

Intervention Type PROCEDURE

Retrobulbar injection of Bone Marrow Derived Stem Cells (BMSC)

ST (Subtenon)

Intervention Type PROCEDURE

Subtenon injection of Bone Marrow Derived Stem Cells (BMSC)

IV (Intravenous)

Intervention Type PROCEDURE

Intravenous injection of Bone Marrow Derived Stem Cells (BMSC)

IVIT (Intravitreal)

Intervention Type PROCEDURE

Intravitreal injection of Bone Marrow Derived Stem Cells (BMSC)

RB, ST, IV, IO

Injection of BMSC retrobulbar, subtenon, intravenous and intraocular (IO) with vitrectomy

Group Type ACTIVE_COMPARATOR

RB (Retrobulbar)

Intervention Type PROCEDURE

Retrobulbar injection of Bone Marrow Derived Stem Cells (BMSC)

ST (Subtenon)

Intervention Type PROCEDURE

Subtenon injection of Bone Marrow Derived Stem Cells (BMSC)

IV (Intravenous)

Intervention Type PROCEDURE

Intravenous injection of Bone Marrow Derived Stem Cells (BMSC)

IO (Intraocular)

Intervention Type PROCEDURE

Intraocular injection of Bone Marrow Derived Stem Cells (BMSC) with vitrectomy prior to intraocular injection. For example, may include larger amount of stem cells in the intravitreal cavity, intraneuronal injections or subretinal injections of stem cells.

Interventions

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RB (Retrobulbar)

Retrobulbar injection of Bone Marrow Derived Stem Cells (BMSC)

Intervention Type PROCEDURE

ST (Subtenon)

Subtenon injection of Bone Marrow Derived Stem Cells (BMSC)

Intervention Type PROCEDURE

IV (Intravenous)

Intravenous injection of Bone Marrow Derived Stem Cells (BMSC)

Intervention Type PROCEDURE

IVIT (Intravitreal)

Intravitreal injection of Bone Marrow Derived Stem Cells (BMSC)

Intervention Type PROCEDURE

IO (Intraocular)

Intraocular injection of Bone Marrow Derived Stem Cells (BMSC) with vitrectomy prior to intraocular injection. For example, may include larger amount of stem cells in the intravitreal cavity, intraneuronal injections or subretinal injections of stem cells.

Intervention Type PROCEDURE

Other Intervention Names

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Retrobulbar injection of stem cells Subtenon injection of stem cells Intravenous injection of stem cells Intravitreal injection of stem cells Intraocular injection of stem cells with vitrectomy

Eligibility Criteria

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Inclusion Criteria

* Have objective, documented damage to the retina or optic nerve unlikely to improve OR
* Have objective, documented damage to the retina or optic nerve that is progressive
* AND have less than or equal to 20/40 best corrected central visual acuity in one or both eyes AND/OR an abnormal visual field in one or both eyes.
* Be at least 3 months post-surgical treatment intended to treat any ophthalmologic disease and stable.
* If under current medical therapy ( pharmacologic treatment) for a retinal or optic nerve disease be considered stable on that treatment and unlikely to have visual function improvement ( for example, glaucoma with intraocular pressure stable on topical medications but visual field damage ).
* Have the potential for improvement with BMSC treatment and be at minimal risk of any potential harm from the procedure.
* Be over the age of 18
* Be medically stable and able to be medically cleared by their primary care physician or a licensed primary care practitioner for the procedure. Medical clearance means that in the estimation of the primary care practitioner, the patient can reasonably be expected to undergo the procedure without significant medical risk to health.

Exclusion Criteria

* Patients who are not capable of an adequate ophthalmologic examination or evaluation to document the pathology.
* Patients who are not capable or not willing to undergo follow up eye exams with the principle investigator or their ophthalmologist or optometrist as outlined in the protocol.
* Patients who are not capable of providing informed consent.
* Patients who may be at significant risk to general health or to the eyes and visual function should they undergo the procedure.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MD Stem Cells

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Steven Levy, MD

Role: STUDY_DIRECTOR

MD Stem Cells

Jeffrey Weiss, MD

Role: PRINCIPAL_INVESTIGATOR

MD Stem Cells

Locations

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MD Stem Cells

Westport, Connecticut, United States

Site Status

Countries

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United States

References

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Weiss JN, Levy S, Malkin A. Stem Cell Ophthalmology Treatment Study (SCOTS) for retinal and optic nerve diseases: a preliminary report. Neural Regen Res. 2015 Jun;10(6):982-8. doi: 10.4103/1673-5374.158365.

Reference Type RESULT
PMID: 26199618 (View on PubMed)

Weiss JN, Levy S, Benes SC. Stem Cell Ophthalmology Treatment Study (SCOTS) for retinal and optic nerve diseases: a case report of improvement in relapsing auto-immune optic neuropathy. Neural Regen Res. 2015 Sep;10(9):1507-15. doi: 10.4103/1673-5374.165525.

Reference Type RESULT
PMID: 26604914 (View on PubMed)

Weiss JN, Benes SC, Levy S. Stem Cell Ophthalmology Treatment Study (SCOTS): improvement in serpiginous choroidopathy following autologous bone marrow derived stem cell treatment. Neural Regen Res. 2016 Sep;11(9):1512-1516. doi: 10.4103/1673-5374.191229.

Reference Type RESULT
PMID: 27857759 (View on PubMed)

Kasetty MA, Hedges TR 3rd, Witkin AJ. BILATERAL EPIRETINAL MEMBRANE FORMATION AFTER INTRAVITREAL INJECTIONS OF AUTOLOGOUS MESENCHYMAL STEM CELLS. Retin Cases Brief Rep. 2022 Sep 1;16(5):561-564. doi: 10.1097/ICB.0000000000001032.

Reference Type DERIVED
PMID: 32568958 (View on PubMed)

Weiss JN, Levy S, Benes SC. Stem Cell Ophthalmology Treatment Study (SCOTS): bone marrow-derived stem cells in the treatment of Leber's hereditary optic neuropathy. Neural Regen Res. 2016 Oct;11(10):1685-1694. doi: 10.4103/1673-5374.193251.

Reference Type DERIVED
PMID: 27904503 (View on PubMed)

Other Identifiers

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ICMS-2013-0019.

Identifier Type: -

Identifier Source: org_study_id

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