Safety and Efficacy Study of Enzalutamide in Patients With Advanced, Androgen Receptor-Positive, Triple Negative Breast Cancer

NCT ID: NCT01889238

Last Updated: 2024-12-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

118 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-06-12

Study Completion Date

2024-01-10

Brief Summary

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The purpose of this study is to determine if enzalutamide is safe and effective in the treatment of patients with advanced breast cancer that express the androgen receptor but do not express the estrogen or progesterone receptor and are not Her2 amplified.

Detailed Description

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Conditions

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Advanced, Androgen Receptor Positive Triple Negative Breast Cancer

Keywords

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breast cancer triple negative androgen receptor positive

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Enzalutamide

160 mg administered as four 40 mg soft gelatin capsules orally once daily

Group Type EXPERIMENTAL

Enzalutamide

Intervention Type DRUG

160 mg administered as four soft gelatin capsules orally once daily

Interventions

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Enzalutamide

160 mg administered as four soft gelatin capsules orally once daily

Intervention Type DRUG

Other Intervention Names

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Xtandi® MDV3100

Eligibility Criteria

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Inclusion Criteria

* Women at least 18 years of age;
* Advanced AR+ TNBC;
* Availability of a representative tumor specimen:
* Either measurable disease or bone only nonmeasurable disease;
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.

Exclusion Criteria

* Any severe concurrent disease, infection, or comorbid condition;
* Any condition or reason that interferes with the patient's ability to participate in the trial, that may cause undue risk, or complicates the interpretation of safety data;
* Current or previously treated brain metastasis or active leptomeningeal disease;
* Current hormone replacement therapy;
* Local palliative radiation therapy within 7 days before day 1;
* History of another invasive cancer within 5 years of day 1;
* Absolute neutrophil count \< 1500/µL, platelet count \< 75,000/µL, or hemoglobin \< 9 g/dL (5.6 mmol/L) at the screening visit;
* Creatinine \> 1.5 times upper limit of normal (ULN) at the screening visit;
* History of seizure or any condition that may predispose to seizure;
* Clinically significant cardiovascular disease;
* Active gastrointestinal disorder affecting absorption;
* Major surgery within 4 weeks before day 1;
* Treatment with any commercially available anticancer agent within 14 days before day 1;
* Treatment with any investigational agent within 2 weeks before day 1;
* Treatment with any of the following medications within 2 weeks before day 1: Estrogens, including hormone replacement therapy; Androgens (testosterone, dihydroepiandrosterone, etc);Systemic radionuclides (eg, samarium or strontium);Vaccine therapy;
* Hypoglycemic episode requiring medical intervention while on insulin treatment within 12 months before day 1;
* Hypersensitivity reaction to the active pharmaceutical ingredient or any of the capsule components, including Labrasol, butylated hydroxyanisole, and butylated hydroxytoluene.
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Astellas Pharma Inc

INDUSTRY

Sponsor Role collaborator

Medivation LLC, a wholly owned subsidiary of Pfizer Inc.

INDUSTRY

Sponsor Role collaborator

Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Pfizer CT.gov Call Center

Role: STUDY_CHAIR

Pfizer

Locations

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Rocky Mountain Cancer Centers

Colorado Springs, Colorado, United States

Site Status

Rocky Mountain Cancer Centers

Lakewood, Colorado, United States

Site Status

Rocky Mountain Cancer Center Sky Ridge

Lone Tree, Colorado, United States

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Rocky Mountain Cancer Centers

Lone Tree, Colorado, United States

Site Status

Florida Cancer Specialists

Altamonte Springs, Florida, United States

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Florida Cancer Specialists

Bonita Springs, Florida, United States

Site Status

Florida Cancer Specialists

Bradenton, Florida, United States

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Florida Cancer Specialists

Brandon, Florida, United States

Site Status

Florida Cancer Specialists

Cape Coral, Florida, United States

Site Status

Florida Cancer Specialists

Clearwater, Florida, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

Florida Cancer Specialist South Division

Fort Myers, Florida, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

Florida Cancer Specialists

Gainesville, Florida, United States

Site Status

Florida Cancer Specialists

Hudson, Florida, United States

Site Status

Florida Cancer Specialists

Largo, Florida, United States

Site Status

Florida Cancer Specialists

Naples, Florida, United States

Site Status

Florida Cancer Specialists

New Port Richey, Florida, United States

Site Status

Florida Cancer Specialists

Orange City, Florida, United States

Site Status

Florida Cancer Specialists

Orlando, Florida, United States

Site Status

Florida Cancer Specialists

Port Charlotte, Florida, United States

Site Status

Florida Cancer Specialists

Sarasota, Florida, United States

Site Status

Florida Cancer Specialists

Sarasota, Florida, United States

Site Status

Florida Cancer Specialists

Spring Hill, Florida, United States

Site Status

Florida Cancer Specialists

St. Petersburg, Florida, United States

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Florida Cancer Specialists

Tampa, Florida, United States

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Florida Cancer Specialists

Tavares, Florida, United States

Site Status

Florida Cancer Specialists

Venice, Florida, United States

Site Status

Florida Cancer Specialists

Venice, Florida, United States

Site Status

Northwestern Medical Faculty Foundation(NMFF)/ Women's Cancer Center Shared Laboratories

Chicago, Illinois, United States

Site Status

Northwestern Medical Faculty Foundation

Chicago, Illinois, United States

Site Status

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status

The University of Chicago Medical Center, Investigational Drug Service Department of Pharmacy

Chicago, Illinois, United States

Site Status

The University of Chicago

Chicago, Illinois, United States

Site Status

University of Chicago Comprehensive Cancer Center at Silver Cross Hospital

New Lenox, Illinois, United States

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Indiana University Health Hospital

Indianapolis, Indiana, United States

Site Status

Indiana University Health Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, United States

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Investigational Drug Services

Indianapolis, Indiana, United States

Site Status

Sidney and Lois Eskenazi Hospital

Indianapolis, Indiana, United States

Site Status

Springmill Medical Clinic

Indianapolis, Indiana, United States

Site Status

Oncology Hematology Care, Inc.

Crestview Hills, Kentucky, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

The West Clinic, PC

Corinth, Mississippi, United States

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The West Clinic, PC

Southaven, Mississippi, United States

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Siteman Cancer Center

City of Saint Peters, Missouri, United States

Site Status

Barnes-Jewish Hospital

St Louis, Missouri, United States

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Washington University Infusion Center Pharmacy

St Louis, Missouri, United States

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Washington University School of Medicine

St Louis, Missouri, United States

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Siteman Cancer Center-South County

St Louis, Missouri, United States

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Siteman Cancer Center-West County

St Louis, Missouri, United States

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Hematology Oncology Associates of Northern NJ

Morristown, New Jersey, United States

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Memorial Sloan Kettering - I Chemotherapy Practice/Investigational Drug Service

New York, New York, United States

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Memorial Sloan-Kettering Cancer Center

New York, New York, United States

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Cone Health Cancer Center

Greensboro, North Carolina, United States

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Wesley Long Community Hospital

Greensboro, North Carolina, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Oncology Hematology Care, Inc.

Fairfield, Ohio, United States

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Greenville Health System

Greenville, South Carolina, United States

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Greenville Health System

Seneca, South Carolina, United States

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Greenville Health System

Spartanburg, South Carolina, United States

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Tennessee Oncology, PLLC

Dickson, Tennessee, United States

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Tennessee Oncology, PLLC

Franklin, Tennessee, United States

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Tennessee Oncology, PLLC

Gallatin, Tennessee, United States

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Tennessee Oncology, PLLC

Hermitage, Tennessee, United States

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Tennessee Oncology, PLLC

Lebanon, Tennessee, United States

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Tennessee Oncology, PLLC

Lebanon, Tennessee, United States

Site Status

The West Clinic, PC

Memphis, Tennessee, United States

Site Status

The West Clinic, PC

Memphis, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Murfreesboro, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

The Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Vanderbilt Breast Center at One Hundred Oaks

Nashville, Tennessee, United States

Site Status

Vanderbilt Health Pharmacy One Hundred Oaks

Nashville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Henry-Joyce Cancer Clinic

Nashville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Smyrna, Tennessee, United States

Site Status

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States

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Texas Oncology - Memorial City

Houston, Texas, United States

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Texas Oncology - Longview Cancer Center

Longview, Texas, United States

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Texas Oncology-Tyler

Tyler, Texas, United States

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Virginia Cancer Institute

Mechanicsville, Virginia, United States

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Virginia Cancer Institute

Midlothian, Virginia, United States

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Virginia Oncology Associates

Newport News, Virginia, United States

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Virginia Oncology Associates

Norfolk, Virginia, United States

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Virginia Cancer Institute

Richmond, Virginia, United States

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Virginia Cancer Institute

Richmond, Virginia, United States

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Virginia Oncology Associates

Virginia Beach, Virginia, United States

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UZA

Edegem, Antwerpen, Belgium

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Institut Jules Bordet

Brussels, , Belgium

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British Columbia Cancer Agency - Vancouver Centre

Vancouver, British Columbia, Canada

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Sunnybrook Research Institute

Toronto, Ontario, Canada

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McGill University Health Centre-Cedars Cancer Centre

Montreal, Quebec, Canada

Site Status

Department of Radiology

Dooradoyle, Limerick, Ireland

Site Status

3rd Floor,Oncology Link office

Dublin, , Ireland

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Department of Radiology

Dublin, , Ireland

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Institute for Cancer Research

Dublin, , Ireland

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Mater Private Hospital

Dublin, , Ireland

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Pharmacy Department

Dublin, , Ireland

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Radiology Department

Dublin, , Ireland

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Pharmacy Department

Dublin, , Ireland

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Cancer Clinical Trials Unit, Mid-Western Cancer center

Limerick, , Ireland

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Pharmacy Department

Limerick, , Ireland

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Dipartimento di Oncologia Medica, IRCCS Ospedale San Raffaele

Milan, , Italy

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Farmacia (magazzino ricevimento merc), IRCCS Ospedale San Raffaele

Milan, , Italy

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U.O Farmaceutica, Nuovo Ospedale di Prato Palazzina dei servizi

Prato, , Italy

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U.O. Oncologia Medica, Nuovo Ospedale di Prato

Prato, , Italy

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Hospital Universitario HM Monteprincipe

Boadilla del Monte, Madrid, Spain

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Grupo Hospitalario Quiron - Hospital Quiron Barcelona

Barcelona, , Spain

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Hospital Universitari Vall d'Hebron

Barcelona, , Spain

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Hospital Universitario Ramon Y Cajal

Madrid, , Spain

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Hospital Universitario 12 Octubre

Madrid, , Spain

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Centro Intergral Oncologico Clara Campal

Madrid, , Spain

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Hospital de Madrid Norte-Sanchinarro.

Madrid, , Spain

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Clinical Investigation and Research Unit

Brighton, England, United Kingdom

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Pharmacy Department

Brighton, England, United Kingdom

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Radiation Safety Service, Medical Physics Department

Brighton, England, United Kingdom

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Histopathology Department

Nottingham, England, United Kingdom

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Nottingham University Hospital

Nottingham, England, United Kingdom

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Pharmacy Department

Nottingham, England, United Kingdom

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Radiology Department

Nottingham, England, United Kingdom

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Radiology Department

Nottingham, England, United Kingdom

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Department of Radiology

Truro, England, United Kingdom

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Pharmacy Department

Truro, England, United Kingdom

Site Status

Royal Cornwall Hospitals NHS trust

Truro, Cornwall, England, United Kingdom

Site Status

Countries

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United States Belgium Canada Ireland Italy Spain United Kingdom

References

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Kumar V, Yu J, Phan V, Tudor IC, Peterson A, Uppal H. Androgen Receptor Immunohistochemistry as a Companion Diagnostic Approach to Predict Clinical Response to Enzalutamide in Triple-Negative Breast Cancer. JCO Precis Oncol. 2017 Nov;1:1-19. doi: 10.1200/PO.17.00075.

Reference Type DERIVED
PMID: 35172518 (View on PubMed)

Traina TA, Miller K, Yardley DA, Eakle J, Schwartzberg LS, O'Shaughnessy J, Gradishar W, Schmid P, Winer E, Kelly C, Nanda R, Gucalp A, Awada A, Garcia-Estevez L, Trudeau ME, Steinberg J, Uppal H, Tudor IC, Peterson A, Cortes J. Enzalutamide for the Treatment of Androgen Receptor-Expressing Triple-Negative Breast Cancer. J Clin Oncol. 2018 Mar 20;36(9):884-890. doi: 10.1200/JCO.2016.71.3495. Epub 2018 Jan 26.

Reference Type DERIVED
PMID: 29373071 (View on PubMed)

Other Identifiers

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2013-000698-57

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

C3431007

Identifier Type: OTHER

Identifier Source: secondary_id

MDV3100-11

Identifier Type: -

Identifier Source: org_study_id