Trial Outcomes & Findings for Patient-Reported Outcome Of Facial Erythema (PROOF) (NCT NCT01885000)

NCT ID: NCT01885000

Last Updated: 2021-08-25

Results Overview

Percentage of participants who are very satisfied/satisfied/somewhat satisfied with the study treatment were reported.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

92 participants

Primary outcome timeframe

Day 8

Results posted on

2021-08-25

Participant Flow

This study was conducted at fourteen centers in Germany, Sweden, United Kingdom from 01 July 2013 (first participant visit) to 14 November 2013 (last participant completed).

A total of 92 participants were randomized, of which 88 participants completed the study.

Participant milestones

Participant milestones
Measure
Brimonidine Tartrate 0.5% Gel
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Overall Study
STARTED
48
44
Overall Study
COMPLETED
46
42
Overall Study
NOT COMPLETED
2
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Brimonidine Tartrate 0.5% Gel
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Overall Study
Adverse Event
1
0
Overall Study
Withdrawal by Subject
1
1
Overall Study
Protocol Violation
0
1

Baseline Characteristics

Patient-Reported Outcome Of Facial Erythema (PROOF)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Brimonidine Tartrate 0.5% Gel
n=48 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=44 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Total
n=92 Participants
Total of all reporting groups
Age, Continuous
53.4 years
STANDARD_DEVIATION 12.9 • n=93 Participants
54.9 years
STANDARD_DEVIATION 12.8 • n=4 Participants
54.1 years
STANDARD_DEVIATION 12.8 • n=27 Participants
Sex: Female, Male
Female
30 Participants
n=93 Participants
26 Participants
n=4 Participants
56 Participants
n=27 Participants
Sex: Female, Male
Male
18 Participants
n=93 Participants
18 Participants
n=4 Participants
36 Participants
n=27 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
White
48 Participants
n=93 Participants
44 Participants
n=4 Participants
92 Participants
n=27 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Skin phototype
Type I
3 Participants
n=93 Participants
6 Participants
n=4 Participants
9 Participants
n=27 Participants
Skin phototype
Type II
34 Participants
n=93 Participants
27 Participants
n=4 Participants
61 Participants
n=27 Participants
Skin phototype
Type III
11 Participants
n=93 Participants
11 Participants
n=4 Participants
22 Participants
n=27 Participants

PRIMARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here over all number of participants 'N' analyzed signifies number of participants evaluable for this outcome measure.

Percentage of participants who are very satisfied/satisfied/somewhat satisfied with the study treatment were reported.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=46 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Percentage of Participants Who Are Very Satisfied/Satisfied/Somewhat Satisfied With the Overall Study Treatment
69.6 Percentage of participants
40.4 Percentage of participants

PRIMARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here over all number of participants 'N' analyzed signifies number of participants evaluable for this outcome measure.

Percentage of participants for each category of facial redness questionnaire on Day 8 was reported. Facial redness questionnaire included 12 questions/categories 1. Satisfied with appearance, 2. Appearance acceptable, 3. Appearance concerned, 4. Embarrassed with facial redness, 5. Self-conscious, 6. Frequency control last 24 hours, 7. Frustrated, 8. Cover up or camouflage, 9. Pay attention to the known triggers, 10. Avoid the known triggers, 11. Interfering with social life, 12. Interfering with work life.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=46 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Percentage of Participants With Facial Redness Questionnaire at Day 8
4. Slightly/ Somewhat/Moderately/Extremely
71.7 percentage of participants
90.4 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
6. Not at all
23.9 percentage of participants
31.7 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
6.Slightly/Somewhat/Moderately/Extremel y
76.1 percentage of participants
68.2 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
8. Slightly/Somewhat
23.9 percentage of participants
11.9 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
9. Not at all/Rarely
47.8 percentage of participants
48.8 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
10.Not at all/Rarely
47.8 percentage of participants
47.6 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
12.Not at all
26.7 percentage of participants
23.8 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
12.Slight/Somewhat/Moderate/Extreme/ Not Applicable/I'm not working
73.4 percentage of participants
76.2 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
3. Somewhat /Moderately /Extremely
71.7 percentage of participants
78.6 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
1. Very dissatisfied/ Dissatisfied
45.7 percentage of participants
69.0 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
1. Dissatisfied or Satisfied/Satisfied
54.3 percentage of participants
31.0 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
2. Very unacceptable/Unacceptable
47.9 percentage of participants
59.5 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
2.Acceptable or Unacceptable/Acceptable
52.1 percentage of participants
40.5 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
3.Not at all/Slightly
28.2 percentage of participants
21.4 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
4. Not at all
28.3 percentage of participants
9.5 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
5.Not at all/Slightly/ Somewhat
73.4 percentage of participants
47.6 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
5. Moderately/Extremely
26.7 percentage of participants
52.3 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
7. Not at all
8.7 percentage of participants
14.3 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
7. Slightly/Somewhat/Moderately/Extremely
91.2 percentage of participants
85.8 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
8.Not at all
60.9 percentage of participants
61.9 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
9.Some of the time/Often/Constantly
52.2 percentage of participants
51.2 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
10. Some of the time/Often/Constantly
52.2 percentage of participants
52.4 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
11. Not at all
34.8 percentage of participants
21.4 percentage of participants
Percentage of Participants With Facial Redness Questionnaire at Day 8
11.Slightly/Somewhat/Moderately/Extremely
65.2 percentage of participants
78.5 percentage of participants

PRIMARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here the over all number of participants analyzed signifies participants who were evaluable for this outcome measure and at specific categories.

EQ-5D-3L is a 3-level, 5-dimensional format standardized instrument for use as a measure of health outcome used to assess the impact of study treatments on participants quality of life as follows: 1) mobility; 2) self-care; 3) usual activities; 4) pain/discomfort; 5) anxiety/depression. Each dimension comprises 3 levels with corresponding numeric scores, where 1 indicates no problems, and 3 indicates extreme problems. Participant selects answer for each of 5 dimensions considering response that best matches his/her health today with anchors ranging from 0 (worst imaginable health state) to 100 (best imaginable health state). An increase in the EQ-5D-3L total score indicates improvement.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=46 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
1. I have no problems in walking about
95.7 Percentage of participants
92.9 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
1.I have some problems in walking about
4.3 Percentage of participants
7.1 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
2. I have no problems with self-care
97.8 Percentage of participants
97.6 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
2. I have some problems washing or dressing myself
2.2 Percentage of participants
2.4 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
3.I have no problems with performing usual activity
91.3 Percentage of participants
90.5 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
3.I have some problems with performing usual activity
8.7 Percentage of participants
9.5 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
4.I have no pain or discomfort
58.7 Percentage of participants
76.2 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
4.I have moderate pain or discomfort
41.3 Percentage of participants
21.4 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
4.I have extreme pain or discomfort
0 Percentage of participants
2.4 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
5.I am not anxious or depressed
87.0 Percentage of participants
73.8 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
5.I am moderately anxious or depressed
10.9 Percentage of participants
26.2 Percentage of participants
EuroQuality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire at Day 8
5.I am extremely anxious or depressed
2.2 Percentage of participants
0 Percentage of participants

PRIMARY outcome

Timeframe: Baseline, Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here the over all number of participants analyzed signifies participants who were evaluable for this outcome measure.

DLQI was a compact health-related quality of life index that has 10 questions and depends on the participants self-declaration about experiences during the previous week. DLQI results range between grades 0 and 30. \[Grade 0-1\]: No effect at all on participant's life, \[Grade 2-5\]: Small effect at all on participant's life, \[Grade 6-10\]: Moderate effect at all on participant's life, \[Grade 11-20\]: Very large effect at all on participant's life, \[Grade 21-30\]: Extremely large effect at all on participant's life. As the DLQI scores increase, the impact of the studied disease on life becomes greater.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=45 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=41 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Percent Change From Baseline in Total Score of Dermatology Life Quality Index (DLQI) Questionnaire at Day 8
-15.4 percent change
Standard Deviation 61.7
-32.6 percent change
Standard Deviation 43.7

PRIMARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here the over all number of participants analyzed signifies participants who were evaluable for this outcome measure.

EQ-5D-3L is a 3-level, 5-dimensional format standardized instrument for use as a measure of health outcome used to assess the impact of study treatments on participants quality of life as follows: 1) mobility; 2) self-care; 3) usual activities; 4) pain/discomfort; 5) anxiety/depression. Each dimension comprises 3 levels with corresponding numeric scores, where 1 indicates no problems, and 3 indicates extreme problems. Participant selects answer for each of 5 dimensions considering response that best matches his/her health today with anchors ranging from 0 (worst imaginable health state) to 100 (best imaginable health state). An increase in the EQ-5D-3L total score indicates improvement.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=45 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Euro Quality of Life-5 Dimensional-3 Level (EQ-5D-3L) Questionnaire (Along With a Visual Analogue Score for the Overall Health State) at Day 8
76.0 Score on scale
Standard Deviation 19.3
80.2 Score on scale
Standard Deviation 13.1

SECONDARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here the over all number of participants analyzed signifies participants who were evaluable for this outcome measure.

Evaluation of erythema by using CEA was assessed by 0 to 4 grades, where 0-Clear skin with no signs of erythema, 1- Almost clear; slight redness, 2-Mild erythema; definite redness, 3-Moderate erythema; marked redness, 4-Severe erythema; fiery redness. Percentage of participants with at least two grade improvement in the CEA was reported.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=46 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Percentage of Participants With at Least Two Grade Improvement in the Clinician's Erythema Assessment (CEA)
47.8 Percentage of participants
7.1 Percentage of participants

SECONDARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here the over all number of participants analyzed signifies participants who were evaluable for this outcome measure.

Percentage of participants with at least two grade improvement in the PSA was reported. Evaluation of erythema severity by using the PSA grades (0-4): 0- No redness, 1- very mild redness, 2-mild redness, 3-moderate redness, 4-severe redness.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=46 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Percentage of Participants With at Least Two Grade Improvement in the Participant Self-assessment
41.3 Percentage of participants
23.8 Percentage of participants

SECONDARY outcome

Timeframe: Day 8

Population: ITT population consisted of the entire population enrolled and randomized. Here the over all number of participants analyzed signifies participants who were evaluable for this outcome measure.

Facial inflammatory lesions of rosacea (including papules and pustules) were counted by evaluator.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=46 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=42 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Change From Baseline in Facial Inflammatory Lesion Counts at Day 8
0.3 number of lesions
Standard Deviation 2.5
0.4 number of lesions
Standard Deviation 1.4

SECONDARY outcome

Timeframe: From start of study drug administration up to Day 8

Population: All Patient Treated (APT) population included all participants enrolled in the study who had received the study treatment at least once.

All clinical medical events, whether observed by the investigator or reported by the participant and whether or not thought to be product- or study procedure-related were considered as adverse events.

Outcome measures

Outcome measures
Measure
Brimonidine Tartrate 0.5% Gel
n=48 Participants
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=44 Participants
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Number of Participants Reported Adverse Events
15 Participants
9 Participants

Adverse Events

Brimonidine Tartrate 0.5% Gel

Serious events: 0 serious events
Other events: 15 other events
Deaths: 0 deaths

Vehicle

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Brimonidine Tartrate 0.5% Gel
n=48 participants at risk
Participants applied brimonidine tartrate 0.5% gel topically once daily for 8 days.
Vehicle
n=44 participants at risk
Participants applied brimonidine tartrate vehicle gel topically once daily for 8 days.
Skin and subcutaneous tissue disorders
Skin burning sensation
0.00%
0/48 • From start of study drug administration up to Day 8
4.5%
2/44 • Number of events 2 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Skin irritation
0.00%
0/48 • From start of study drug administration up to Day 8
2.3%
1/44 • Number of events 1 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Skin tightness
8.3%
4/48 • Number of events 5 • From start of study drug administration up to Day 8
4.5%
2/44 • Number of events 3 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Skin warm
4.2%
2/48 • Number of events 9 • From start of study drug administration up to Day 8
2.3%
1/44 • Number of events 2 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Swelling face
2.1%
1/48 • Number of events 1 • From start of study drug administration up to Day 8
0.00%
0/44 • From start of study drug administration up to Day 8
Vascular disorders
Flushing
4.2%
2/48 • Number of events 2 • From start of study drug administration up to Day 8
0.00%
0/44 • From start of study drug administration up to Day 8
Nervous system disorders
Hypoesthesia
0.00%
0/48 • From start of study drug administration up to Day 8
2.3%
1/44 • Number of events 1 • From start of study drug administration up to Day 8
Respiratory, thoracic and mediastinal disorders
Cough
2.1%
1/48 • Number of events 1 • From start of study drug administration up to Day 8
2.3%
1/44 • Number of events 1 • From start of study drug administration up to Day 8
Infections and infestations
Nasopharyngitis
2.1%
1/48 • Number of events 1 • From start of study drug administration up to Day 8
0.00%
0/44 • From start of study drug administration up to Day 8
Infections and infestations
Rash pustular
4.2%
2/48 • Number of events 2 • From start of study drug administration up to Day 8
0.00%
0/44 • From start of study drug administration up to Day 8
Nervous system disorders
Headache
2.1%
1/48 • Number of events 1 • From start of study drug administration up to Day 8
4.5%
2/44 • Number of events 2 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Erythema
12.5%
6/48 • Number of events 6 • From start of study drug administration up to Day 8
4.5%
2/44 • Number of events 2 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Pain of skin
2.1%
1/48 • Number of events 1 • From start of study drug administration up to Day 8
0.00%
0/44 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Pruritus
2.1%
1/48 • Number of events 1 • From start of study drug administration up to Day 8
2.3%
1/44 • Number of events 1 • From start of study drug administration up to Day 8
Skin and subcutaneous tissue disorders
Rosacea
4.2%
2/48 • Number of events 2 • From start of study drug administration up to Day 8
2.3%
1/44 • Number of events 1 • From start of study drug administration up to Day 8

Additional Information

Clinical Operations

Galderma

Phone: 817 961 5000

Results disclosure agreements

  • Principal investigator is a sponsor employee Disclosure agreement covered by contract.
  • Publication restrictions are in place

Restriction type: OTHER