A Study of Lebrikizumab in Adolescent Participants With Uncontrolled Asthma Who Are on Inhaled Corticosteroids and a Second Controller Medication

NCT ID: NCT01875003

Last Updated: 2017-05-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

348 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-31

Study Completion Date

2016-12-28

Brief Summary

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This randomized, multicenter, double-blind, placebo-controlled, parallel-group study will evaluate the efficacy, safety, and tolerability of lebrikizumab in adolescent participants with asthma whose disease remains uncontrolled despite daily treatment with inhaled corticosteroids (ICS) therapy and at least one second controller medication. Participants will be randomized in a 1:1:1 ratio to receive double-blind treatment with either lebrikizumab ('High' or 'Low') or placebo, administered as subcutaneous (SC) every 4 weeks (Q4W) for 52 weeks, in addition to their standard-of-care therapy. This will be followed by an optional 52-week double-blind active-treatment extension. The anticipated time on study treatment is up to 104 weeks. Participants who complete the study to Week 104, discontinue prematurely or decide not to take part in the optional active-treatment extension will transition to the 20-week safety follow-up period.

Detailed Description

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Conditions

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Asthma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Lebrikizumab High

Participants with uncontrolled asthma on ICS therapy (total daily dose of 500-2000 micrograms \[mcg\] of fluticasone propionate dry powder inhaler \[DPI\] or equivalent) and a second controller medication, will receive SC injection of lebrikizumab (high dose) Q4W for 52 weeks during placebo-controlled period and up to 76 weeks or 104 weeks for participants who will be willing to take part in optional active-treatment extension period.

Group Type EXPERIMENTAL

Lebrikizumab

Intervention Type DRUG

Lebrikizumab will be administered as SC injection at high or low dose Q4W.

Standard of Care

Intervention Type DRUG

Participants will continue to receive ICS therapy (total daily dose of 500-2000 mcg fluticasone propionate DPI or equivalent) along with at least one second controller medications (e.g. long-acting beta agonists \[LABAs\], leukotriene receptor antagonists (LTRAs), long-acting muscarinic antagonists (LAMAs), or theophylline) as standard of care.

Lebrikizumab Low

Participants with uncontrolled asthma on ICS therapy (total daily dose of 500-2000 mcg of fluticasone propionate DPI or equivalent) and a second controller medication, will receive SC injection of lebrikizumab (low dose) Q4W for 52 weeks during placebo-controlled period and up to 76 weeks or 104 weeks for participants who will be willing to take part in optional active-treatment extension period.

Group Type EXPERIMENTAL

Lebrikizumab

Intervention Type DRUG

Lebrikizumab will be administered as SC injection at high or low dose Q4W.

Standard of Care

Intervention Type DRUG

Participants will continue to receive ICS therapy (total daily dose of 500-2000 mcg fluticasone propionate DPI or equivalent) along with at least one second controller medications (e.g. long-acting beta agonists \[LABAs\], leukotriene receptor antagonists (LTRAs), long-acting muscarinic antagonists (LAMAs), or theophylline) as standard of care.

Placebo

Participants with uncontrolled asthma on ICS therapy (total daily dose of 500-2000 mcg of fluticasone propionate DPI or equivalent) and a second controller medication, will receive SC injection of lebrikizumab matching placebo Q4W for 52 weeks during placebo-controlled period and then SC injection of lebrikizumab at high or low dose will be administered from Weeks 52 to 76 or 104 to participants who are willing to take part in optional active-treatment extension period.

Group Type PLACEBO_COMPARATOR

Lebrikizumab

Intervention Type DRUG

Lebrikizumab will be administered as SC injection at high or low dose Q4W.

Placebo

Intervention Type DRUG

Lebrikizumab matching placebo will be administered as SC injection Q4W.

Standard of Care

Intervention Type DRUG

Participants will continue to receive ICS therapy (total daily dose of 500-2000 mcg fluticasone propionate DPI or equivalent) along with at least one second controller medications (e.g. long-acting beta agonists \[LABAs\], leukotriene receptor antagonists (LTRAs), long-acting muscarinic antagonists (LAMAs), or theophylline) as standard of care.

Interventions

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Lebrikizumab

Lebrikizumab will be administered as SC injection at high or low dose Q4W.

Intervention Type DRUG

Placebo

Lebrikizumab matching placebo will be administered as SC injection Q4W.

Intervention Type DRUG

Standard of Care

Participants will continue to receive ICS therapy (total daily dose of 500-2000 mcg fluticasone propionate DPI or equivalent) along with at least one second controller medications (e.g. long-acting beta agonists \[LABAs\], leukotriene receptor antagonists (LTRAs), long-acting muscarinic antagonists (LAMAs), or theophylline) as standard of care.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Asthma diagnosis for greater than or equal to (\>/=) 12 months prior to Visit 1
* Bronchodilator response during screening
* Pre-bronchodilator FEV1 of 40 percent (%) - 90% predicted at both Visits 2 and 3
* On high dose ICS therapy for \>/= 6 months prior to Visit 1
* On an eligible second controller medication for 6 months prior to Visit 1
* Uncontrolled asthma as defined by the protocol both during screening and at the time of randomization
* Demonstrated adherence with controller medication during the screening period

Exclusion Criteria

* History of severe allergic reaction or anaphylactic reaction to a biologic agent or known hypersensitivity to any component of the lebrikizumab injection
* Maintenance oral corticosteroid therapy within 3 months prior to Visit 1
* Treatment with systemic (oral, intravenous \[IV\], or intramuscular \[IM\]) corticosteroids within 4 weeks prior to Visit 1 or during the screening period
* Treatment with intra-articular corticosteroids within 4 weeks prior to Visit 1 or during the screening period or anticipated need for intra-articular corticosteroids during the course of the study
* Infection that meets the following criteria: Any infection requiring hospital admission or requiring treatment with IV or IM antibiotics within 4 weeks prior to Visit 1 or during screening; any active infection that required treatment with oral antibiotics within 2 weeks prior to Visit 1 or during screening; upper or lower respiratory tract infection within 4 weeks prior to Visit 1 or during screening; active parasitic infection or Listeria monocytogenes infection within 6 months prior to Visit 1 or during screening
* History of active tuberculosis requiring treatment
* Known immunodeficiency, including, but not limited to, human immunodeficiency virus (HIV) infection
* Evidence of acute or chronic hepatitis or known liver cirrhosis
* History of cystic fibrosis, bronchiectasis, and/or other clinically significant lung disease other than asthma
* Diagnosis or history of malignancy or current evaluation for potential malignancy
* Current smoker or former smoker with a history of greater than (\>) 10 pack-years
* History of alcohol or drug abuse
* Past and/or current use of any anti- interleukin (IL) -13 or anti-IL-4/IL-13 therapy, including lebrikizumab
* Use of other monoclonal antibody therapy, including omalizumab, within 6 months or 5 drug half-lives (whichever is longer) prior to Visit 1
* Initiation of or change in allergen immunotherapy within 3 months prior to Visit 1 or during screening
* History of bronchial thermoplasty
Minimum Eligible Age

12 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Allergy Associates of Tucson

Tucson, Arizona, United States

Site Status

Kaiser Permanente Los Angeles

Los Angeles, California, United States

Site Status

Southern California Research Center

Mission Viejo, California, United States

Site Status

Allergy & Asthma Consultants

Redwood City, California, United States

Site Status

Dignity Health Medical Foundation

Sacramento, California, United States

Site Status

Bensch Research Associates

Stockton, California, United States

Site Status

Allergy & Asthma Medical Group; Clinical Research Division

Walnut Creek, California, United States

Site Status

Colorado Children's Hospital; The Breathing Institute

Aurora, Colorado, United States

Site Status

IMMUNOe International Research Centers

Centennial, Colorado, United States

Site Status

Asthma & Allergy; Associates, P.C.

Colorado Springs, Colorado, United States

Site Status

National Jewish Medical and Research Center

Denver, Colorado, United States

Site Status

Abel and Buchheim

Miami, Florida, United States

Site Status

Compass Research East, LLC

Orlando, Florida, United States

Site Status

Sarasota Clinical Research

Sarasota, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Brookstone Clinical Res Ctr

Columbus, Georgia, United States

Site Status

Georgia Pain Clinic

Marietta, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

The Clinical Research Center

Shiloh, Illinois, United States

Site Status

Riley Hospital for Children; Pediatric Nephrology

Indianapolis, Indiana, United States

Site Status

Abraham Research PLLC

Florence, Kentucky, United States

Site Status

Breathe America Shreveport Inc

Shreveport, Louisiana, United States

Site Status

Asthma, Allergy & Sinus Center

Baltimore, Maryland, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Univ of Michigan Medical Ctr

Ann Arbor, Michigan, United States

Site Status

Cardinal Glennon Child's Hosp; Endrocrinology

St Louis, Missouri, United States

Site Status

Parikh Institute for Research LLC

New Jersey, New Jersey, United States

Site Status

University of New Mexico; School of Med

Albuquerque, New Mexico, United States

Site Status

Parikh Institute for Research LLC

New York, New York, United States

Site Status

Urban Health Plan, Inc.

The Bronx, New York, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Promedica Toledo Children's Hospital

Toledo, Ohio, United States

Site Status

Bend Memorial Clinic

Bend, Oregon, United States

Site Status

Allergy, Asthma, & Dermatology Research Center, Llc

Lake Oswego, Oregon, United States

Site Status

Clinical Research Inst. of Southern Oregon, Pc

Medford, Oregon, United States

Site Status

TTS Research

Boerne, Texas, United States

Site Status

Allergy & Asthma Research Center of El Paso

El Paso, Texas, United States

Site Status

Allergy & Asthma Res Ctr PA

San Antonio, Texas, United States

Site Status

South Texas Allergy and Asthma Medical Professionals

San Antonio, Texas, United States

Site Status

Bridgerland Clinical Research

North Logan, Utah, United States

Site Status

O & O Alpan, LLC

Fairfax, Virginia, United States

Site Status

Bellingham Asthma, Allergy & Immunology

Bellingham, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Centro Médico Vitae

Buenos Aires, , Argentina

Site Status

Fundación Faicep

Buenos Aires, , Argentina

Site Status

Fundacion Cidea

Buenos Aires, , Argentina

Site Status

INAER

Buenos Aires, , Argentina

Site Status

Instituto Respirar

Mendoza, , Argentina

Site Status

INSARES

Mendoza, Mendoza City, , Argentina

Site Status

Centro Respiratorio Infantil

Rosario, , Argentina

Site Status

Investigaciones en Patologias Respiratorias

San Miguel de Tucumán, , Argentina

Site Status

Centro Integral de Medicina Respiratoria (CIMER)

San Miguel de Tucumán, , Argentina

Site Status

Instituto Del Buen Aire

Santa Fe, , Argentina

Site Status

Sanatorio Británico de Rosario

Santa Fé, , Argentina

Site Status

CEMER Centro Médico de Enfermedades Respiratorias

Vicente López, , Argentina

Site Status

Centro de Referencia em Enfermidades Respiratorias e Alergia - CEAR

Salvador, Estado de Bahia, Brazil

Site Status

Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital Sao Lucas - PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Faculdade de Medicina do ABC - FMABC

Santo André, São Paulo, Brazil

Site Status

Pesquisare Saúde Sociedade Simples

Santo André, São Paulo, Brazil

Site Status

Hospital Alemao Oswaldo Cruz; Pesquisa Clinica

São Paulo, São Paulo, Brazil

Site Status

Instituto de Pesquisa Clínica e Medicina Avançada Ltda

São Paulo, São Paulo, Brazil

Site Status

CMPC/Clinica de Alergia Martti Antila

Sorocaba, São Paulo, Brazil

Site Status

Dr. Tharwat A. Fera Inc.

Vancouver, British Columbia, Canada

Site Status

Brian Lyttle's Private Practice

London, Ontario, Canada

Site Status

Centre de Recherche Applique En Allergie de Quebec

Québec, Quebec, Canada

Site Status

Hospital Santa Clara

Bogotá, , Colombia

Site Status

Hospital Pablo Tobon Uribe

Medellin-Antioquia, , Colombia

Site Status

Hofstetr Alois MUDr. s.r.o.

Jihlava, , Czechia

Site Status

Alergologie Teplice, s.r.o.

Teplice, , Czechia

Site Status

Groupe Hospitalier Pellegrin; Pharmacie

Bordeaux, , France

Site Status

Groupe Hospitalier Necker Enfants Malades

Paris, , France

Site Status

Hopital Armand Trousseau

Paris, , France

Site Status

Hopital Charles Nicolle; cic

Rouen, , France

Site Status

Universitaetsklinikum Frankfurt

Frankfurt, , Germany

Site Status

Evangelisches Krankenhaus Hamm

Hamm, , Germany

Site Status

Praxis Dr. med. Jan Feimer

München, , Germany

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Heim Pál Gyermekkórház

Budapest, , Hungary

Site Status

Kenezy Korhaz Rendelointezet

Debrecen, , Hungary

Site Status

Borsod-Abaúj-Zemplén Megyei Kórház és Egyetemi Oktató Kórház

Miskolc, , Hungary

Site Status

Szegedi Tudományegyetem Szent-Györgyi Albert Klinikai Központ

Szeged, , Hungary

Site Status

Papp és Társa Bt.

Szigetvár, , Hungary

Site Status

Tudogyogyintezet Torokbalint

Törökbálint, , Hungary

Site Status

Barzilai Medical Center

Ashkelon, , Israel

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Rambam Health Care Campus

Haifa, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Schneider Children's Medical Center

Petah Tikva, , Israel

Site Status

Chaim Sheba Medical Center

Tel Litwinsky, , Israel

Site Status

Azienda Policlinico Umberto I; Dipartimento Integrato di Pediatria e Neuropsichiatria Infantile

Rome, Lazio, Italy

Site Status

Ospedale Pediatrico Bambino Gesu

Rome, Lazio, Italy

Site Status

Fondazione IRCCS Policlinico San Matteo

Pavia, Lombardy, Italy

Site Status

Azienda Ospedaliero - Universitaria Policlinico - Vittorio Emanuele

Catania, Sicily, Italy

Site Status

National Hospital Organization Mie Hospital

Tsu, , Japan

Site Status

National Hospital Organization Shimoshizu National Hospital

Yotsukaidō, , Japan

Site Status

Grupo Medico Camino

DF, , Mexico

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Instituto Jalisciense de Investigacion Clinica S.A. de C.V.

Guadalajara, , Mexico

Site Status

Centro de Investigacion Medico Biologico y Terapia Avanzada, S.C.

Guadalajara, , Mexico

Site Status

Unidad Medica de Occidente

Guadalajara, , Mexico

Site Status

Instituto Nacional de Pediatría

Mexico City, , Mexico

Site Status

Hospital Universitario Dr. Jose Eleuterio González; Enfermedades Pulmonares Crónicas

Monterrey, , Mexico

Site Status

Unidad de Investigacion Clinica En Medicina (Udicem) S.C.

Monterrey, , Mexico

Site Status

Consultorio Especialidad Alergologia Pediatrica

Villahermosa, , Mexico

Site Status

Hospital Dos de Mayo; Parque Historia De la Medicina Peruana S/n

Lima, , Peru

Site Status

Hospital Nacional Luis N Saenz PNP

Lima, , Peru

Site Status

Clinica Internacional

Lima, , Peru

Site Status

Centro de Investigación Ricardo Palma

Lima, , Peru

Site Status

Clinica Anglo Americana

Lima, , Peru

Site Status

Clinica San Borja

Lima, , Peru

Site Status

Prywatna Praktyka Lekarska

Bialystok, , Poland

Site Status

Malopolskie Centrum Alergologii

Krakow, , Poland

Site Status

SPZOZ Uniwersytecki Szpital Kliniczny nr 1 im. Norberta Barlickiego Uniwersytetu Medycznego w Lodzi

Lodz, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny im. M. Kopernika w Lodzi

Lodz, , Poland

Site Status

Centrum Alergologii NZOZ

Lublin, , Poland

Site Status

Centrum Alergologii Teresa Hofman

Poznan, , Poland

Site Status

ALERGO-MED Specjalistyczna Przychodnia Lekarska Sp. z o. o

Tarnów, , Poland

Site Status

Klinika Chorób Wewnetrznych i Alergologii MSW

Warsaw, , Poland

Site Status

Hospital Infante D. Pedro; Servico de Imunoalergologia

Aveiro, , Portugal

Site Status

Hospital Particular do Algarve - Unidade de Faro

Faro, , Portugal

Site Status

Hospital Dona Estefania; Servico de Imunoalergologia

Lisbon, , Portugal

Site Status

Hospital CUF Porto; Servico de Imunoalergologia

Senhora Da Hora - Porto, , Portugal

Site Status

Alersa

Košice, , Slovakia

Site Status

ALERGOMEA s.r.o.

Lučenec, , Slovakia

Site Status

Imunoalergologia Dzurilla s.r.o.

Nitra, , Slovakia

Site Status

Uni of Cape Town Lung Inst.

Cape Town, , South Africa

Site Status

Westville Hospital

Durban, , South Africa

Site Status

Sebastian Peter

Durban, , South Africa

Site Status

WWCT Lakeview Hospital

Johannesburg, , South Africa

Site Status

Medicross Sophiatown

Johannesburg, , South Africa

Site Status

GCT Mercantile; Clinical Research Centre

Port Elizabeth, , South Africa

Site Status

Bothe ke Bontle Health Services

Pretoria, , South Africa

Site Status

Soweto Clinical Trial Centre

Soweto, , South Africa

Site Status

Limpopo Clinical Research Initiative; Tamboti Medical Centre

Tabazimbi, , South Africa

Site Status

Inha University Hospital

Incheon, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

KyungHee Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Germans Trias i Pujol; Servicio de Farmacia

Badalona, Barcelona, Spain

Site Status

Hospital Sant Joan De Deu

Esplugues de Llobregas, Barcelona, Spain

Site Status

Corporacio Sanitaria Parc Tauli; Servicio de Oncologia

Sabadell, Barcelona, Spain

Site Status

Hospital de Manises

Manises, Valencia, Spain

Site Status

Hospital Quiron Teknon

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Clínica Dr. Lobatón

Cadiz, , Spain

Site Status

Clinica Ojeda de Asma Y Alergia

Madrid, , Spain

Site Status

Hospital Regional Universitario Carlos Haya

Málaga, , Spain

Site Status

Chung Shan M. U. H.

Taichung, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Cheng Kung Univ Hosp

Tainan City, , Taiwan

Site Status

Chang Gung Memorial Hospital

Taoyuan District, , Taiwan

Site Status

Municipal Medical Institution; Chernivtsi Regional Children's Hospital

Chernivtsi, , Ukraine

Site Status

Public Institution City Clinical Hospital # 6 of Dnipropetrovsk Regional Board

Dnipro, , Ukraine

Site Status

State Institution of Pediatrics Obstetrics and Gynecology of NAMSU

Kiev, , Ukraine

Site Status

Municipal Institution "Kryvyi Rih City Clinical Hospital #8" of Dnipropetrovsk Regional Council

Kryvyi Rih, , Ukraine

Site Status

SI National Institute of Phthisiology and Pulmonology n.a. F.G.Yanovskyi under NAMS of Ukraine

Kyiv, , Ukraine

Site Status

SI Research Centre of Radiation Medicine of AMSU

Kyiv, , Ukraine

Site Status

Municipal Institution Zaporizhzhya Regional Clinical Child Hospital

Zaporizhzhya, , Ukraine

Site Status

Birmingham Children's Hospital NHS Foundation Trust

Birmingham, , United Kingdom

Site Status

Birmingham Heartlands Hospital

Birmingham, , United Kingdom

Site Status

Dumfries and Galloway Royal Infirmary; Department of Paediatrics

Dumfries, , United Kingdom

Site Status

Royal Hospital For Children

Glasgow, , United Kingdom

Site Status

University of Leicester

Leicester, , United Kingdom

Site Status

Royal Brompton Hospital; Respiratory Department

London, , United Kingdom

Site Status

Sheffield Childrens Hospital

Sheffield, , United Kingdom

Site Status

Southampton General Hospital

Southampton, , United Kingdom

Site Status

Countries

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United States Argentina Brazil Canada Colombia Czechia France Germany Hungary Israel Italy Japan Mexico Peru Poland Portugal Slovakia South Africa South Korea Spain Taiwan Ukraine United Kingdom

References

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Szefler SJ, Roberts G, Rubin AS, Zielen S, Kuna P, Alpan O, Anzures-Cabrera J, Chen Q, Holweg CTJ, Kaminski J, Putnam WS, Matthews JG, Kamath N. Efficacy, safety, and tolerability of lebrikizumab in adolescent patients with uncontrolled asthma (ACOUSTICS). Clin Transl Allergy. 2022 Jul 14;12(7):e12176. doi: 10.1002/clt2.12176. eCollection 2022 Jul.

Reference Type DERIVED
PMID: 35846226 (View on PubMed)

Other Identifiers

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2012-000180-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

WB28183

Identifier Type: -

Identifier Source: org_study_id

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