An Open Label Trial of Afatinib (Giotrif) in Treatment-naive (1st Line) or Chemotherapy Pre-treated Patients With Locally Advanced or Metastatic Non-small Cell Lung Cancer (NSCLC) Harboring EGFR Mutation(s)

NCT ID: NCT01853826

Last Updated: 2025-04-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

481 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-07-17

Study Completion Date

2024-03-06

Brief Summary

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To evaluate the safety and tolerability of afatinib (Giotrif) in patients with locally advanced or metastatic non-small cell lung cancer (NSCLC) harboring EGFR mutation(s) and have never been treated with an EGFR-TKI

Detailed Description

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Conditions

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Carcinoma, Non-Small-Cell Lung

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Afatinib treated-patients

Patients diagnosed with EGFR mutation positive non-small cell lung cancer (NSCLC) locally advanced or metastatic who have never been treated with EGFR tyrosine kinase inhibitors (TKI) received a daily dose of 40 milligrams (mg) of afatinib (Giotrif®), in the form of film-coated tablet over a 28 day cycle. Afatinib was taken orally with 250 milliliters (mL) of water at the same time of the day and without eating anything for at least 3 hours. Patients continued on treatment for as long as there was no disease progression or no other trial withdrawal criteria. The dose was reduced to 30 mg or 20 mg once daily when the initial dose was not tolerated by the patient.

Group Type EXPERIMENTAL

Afatinib

Intervention Type DRUG

Patients received a daily dose of 40 milligrams (mg) of afatinib (Giotrif®), in the form of film-coated tablet over a 28 day cycle. Afatinib was taken orally with 250 milliliters (mL) of water at the same time of the day and without eating anything for at least 3 hours. Patients continued on treatment for as long as there was no disease progression or no other trial withdrawal criteria. The dose was reduced to 30 mg or 20 mg once daily when the initial dose was not tolerated by the patient.

Interventions

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Afatinib

Patients received a daily dose of 40 milligrams (mg) of afatinib (Giotrif®), in the form of film-coated tablet over a 28 day cycle. Afatinib was taken orally with 250 milliliters (mL) of water at the same time of the day and without eating anything for at least 3 hours. Patients continued on treatment for as long as there was no disease progression or no other trial withdrawal criteria. The dose was reduced to 30 mg or 20 mg once daily when the initial dose was not tolerated by the patient.

Intervention Type DRUG

Other Intervention Names

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Giotrif®

Eligibility Criteria

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Inclusion Criteria

Patients with:

* locally advanced or metastatic Non-Small Cell Lung Cancer (NSCLC)
* Epidermal Growth Factor Receptor (EGFR) mutation-positive result per the institution's testing methodology.
* Adequate organ function, defined as all of the following:

1. Absolute Neutrophil Count (ANC) \> 1500/mm3. (ANC \>1000/mm3 may be considered in special circumstances such as benign cyclical neutropenia as judged by the investigator and in discussion with the sponsor).
2. Platelet count \>75,000/mm3
3. Serum creatinine \< 1.5 times of the upper limit of normal
4. Total Bilirubin \< 1.5 times upper limit of (institutional) normal (Patients with Gilbert's syndrome total bilirubin must be \<4 times institutional upper limit of normal).
5. Aspartate Amino Transferase (AST) or Alanine Amino Transferase (ALT) \< three times the upper limit of (institutional) normal (ULN) (if related to liver metastases \< five times ULN).
* Eastern Cooperative Oncology Group (ECOG) score between 0 - 2
* written informed consent by patient or guardian prior to admission into the trial that is consistent with International Conference on Harmonisation (ICH)- Good Clinical Practice (GCP) guidelines and local law.

Exclusion Criteria

Patients who or with:

* prior treatment with an EGFR tyrosine kinase inhibitor (TKI)
* anti-cancer treatment within 2 weeks prior to start of trial treatment (continued use of anti-androgens and/or gonadorelin analogues for treatment of prostate cancer permitted)
* radiotherapy within 14 days prior to drug administration, except as follows:

1. Palliative radiation to organs other than chest may be allowed up to 2 weeks prior to drug administration, and
2. Single dose palliative treatment for symptomatic metastasis outside above allowance to be discussed with sponsor prior to enrolling.
* previous or concomitant malignancies at other sites, except effectively treated non-melanoma skin cancers, carcinoma in situ of the cervix, ductal carcinoma in situ or effectively treated malignancy that has been in remission for more than 3 years and is considered to be cured.
* known pre-existing interstitial lung disease
* meningeal carcinomatosis and symptomatic brain metastases (patients with asymptomatic brain metastases, who were previously treated, are eligible provided they have had Stable Disease (SD) for at least 4 weeks on stable doses of medication)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Boehringer Ingelheim

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Boehringer Ingelheim

Role: STUDY_CHAIR

Boehringer Ingelheim

Locations

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The Prince of Wales Hospital

Randwick, New South Wales, Australia

Site Status

Sunshine Hospital

AT Albans, Victoria, Australia

Site Status

St John of God Murdoch

Murdoch, Western Australia, Australia

Site Status

Medical University of Graz State Hospital - University Hospital Graz

Graz, , Austria

Site Status

Ordensklinikum Linz GmbH - Barmherzige Schwestern

Linz, , Austria

Site Status

Klinik Penzing SMZ Baumgartner Hoehe

Vienna, , Austria

Site Status

Klinikum Wels - Grieskirchen GmbH

Wels, , Austria

Site Status

University Hospital Brno

Brno, , Czechia

Site Status

Hospital Hradec Kralove

Hradec Králové, , Czechia

Site Status

University Hospital Ostrava

Ostrava, , Czechia

Site Status

University Hospital Plzen, Plzen-Bory

Pilsen, , Czechia

Site Status

Chest Hospital of Athens "Sotiria"

Athens, , Greece

Site Status

Metropolitan Hospital, Oncology Clinic

N. Faliro, , Greece

Site Status

General Oncology Hospital "Agioi Anargyri"

Nea Kifissia, , Greece

Site Status

General Hospital of Thessaloniki "G. Papanikolaou"

Thessaloniki, , Greece

Site Status

Koranyi National Institute For Pulmonolgy

Budapest, , Hungary

Site Status

Institute of Chest Diseases Csongrad County,Dpt. Pulmonology

Deszk, , Hungary

Site Status

Pulmonology Institute of Veszprem County, Farkasgyepu

Farkasgyepü, , Hungary

Site Status

Fejer County Saint George University Teaching Hospital

Székesfehérvár, , Hungary

Site Status

Soroka Univ. Medical Center

Beersheba, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Rabin Medical Center Beilinson

Petah Tikva, , Israel

Site Status

Sourasky Medical Center

Tel Aviv, , Israel

Site Status

The Chaim Sheba Medical Center Tel HaShomer

Tel Litwinsky, , Israel

Site Status

Azienda Ospedaliera Santi Antonio e Biagio e Cesare Arrigo

Alessandria, , Italy

Site Status

Az. Ospedaliere Umberto I di Ancona

Ancona, , Italy

Site Status

A. O. Giuseppe Moscati

Avellino, , Italy

Site Status

Centro di riferimento Oncologico

Aviano (PN), , Italy

Site Status

Istituto Tumori Giovanni Paolo II

Bari, , Italy

Site Status

A. O. Ospedali Riuniti di Bergamo

Bergamo, , Italy

Site Status

Policlinico S. Orsola Malpighi

Bologna, , Italy

Site Status

Ospedale Centrale di Bolzano

Bolzano, , Italy

Site Status

A.O. Spedali Civili di Brescia

Brescia, , Italy

Site Status

Azienda Ospedaliera Careggi

Florence, , Italy

Site Status

Azienda Ospedaliera San Martino

Genova, , Italy

Site Status

Osp. S. Maria della Scaletta

Imola, , Italy

Site Status

Azienda Ospedaliera Vito Fazzi

Lecce, , Italy

Site Status

Osp. Campo di Marte

Lucca, , Italy

Site Status

Istituto Scientifico Romagnolo

Meldola (FC), , Italy

Site Status

IRCCS Fondazione Ospedale Maggiore

Milan, , Italy

Site Status

IRCCS San Raffaele

Milan, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Istituto Europeo di Oncologia

Milan, , Italy

Site Status

ASST Grande Ospedale Metropolitano Niguarda

Milan, , Italy

Site Status

Università di Modena e Reggio Emilia

Modena, , Italy

Site Status

A.O. San Gerardo di Monza

Monza (MI), , Italy

Site Status

Istituto Nazionale IRCCS Tumori Fondazione Pascale

Napoli, , Italy

Site Status

Osp. dei Colli Monaldi-Cotugno

Napoli, , Italy

Site Status

A.O.U. Maggiore della Carita'

Novara, , Italy

Site Status

Azienda Sanitaria Ospedale S. Luigi Gonzaga

Orbassano (TO), , Italy

Site Status

Istituto Oncologico Veneto IRCCS

Padua, , Italy

Site Status

A.O. Univ. Policlinico "Paolo Giaccone"

Palermo, , Italy

Site Status

Casa di Cura La Maddalena

Palermo, , Italy

Site Status

Azienda Ospedaliera di Parma

Parma, , Italy

Site Status

Ospedale S.Maria della Misericordia, AO di Perugia

Perugia, , Italy

Site Status

Azienda Ospedaliera Universitaria Pisana

Pisa, , Italy

Site Status

Ospedale S. Maria delle Croci

Ravenna, , Italy

Site Status

Irccs Crob

Rionero in Vulture (PZ), , Italy

Site Status

Università Campus Bio-Medico - ROMA

Roma, , Italy

Site Status

Istittuo Nazionale Tumori Regina Elena - IRCCS

Roma, , Italy

Site Status

A.O. San Camillo Forlanini

Roma, , Italy

Site Status

Poli Univ A. Gemelli

Roma, , Italy

Site Status

Azienda Ospedaliera Sant'Andrea-Università di Roma La Sapienza

Roma, , Italy

Site Status

Azienda Ospedaliera "Santo Maria"

Terni, , Italy

Site Status

AO Città della Salute e Scienza

Torino, , Italy

Site Status

Ospedale S. Maria di Ca' Foncello Azienda ULSS9 TREVISO

Treviso, , Italy

Site Status

A. O. S. Maria della Misericordia

Udine, , Italy

Site Status

Ospedale Policlinico G.B. Rossi (Borgo Roma) di Verona

Verona, , Italy

Site Status

Oncology Center na F. Lukaszczyka

Bydgoszcz, , Poland

Site Status

University Clinical Center, Gdansk

Gdansk, , Poland

Site Status

Provincial Specialist M. Kopernik Hospital

Lodz, , Poland

Site Status

MS Clinsearch, Private Practice

Lublin, , Poland

Site Status

MED POLONIA SP Z O O, Clinical Trials Department,Poznan

Poznan, , Poland

Site Status

Oncology Center-Maria Sklodowska-Curie Institute

Warsaw, , Poland

Site Status

ULS de Coimbra, E.P.E.

Coimbra, , Portugal

Site Status

IPO Lisboa Francisco Gentil, EPE

Lisbon, , Portugal

Site Status

Centro Hospitalar Lisboa Norte Hospital Pulido Valente

Lisbon, , Portugal

Site Status

IPO Porto Francisco Gentil, EPE

Porto, , Portugal

Site Status

ULS de Gaia/Espinho, EPE

Vila Nova de Gaia, , Portugal

Site Status

St.Auton.Heal.Inst."Rep.Clin.Onc.Disp.of MoH of Rep. Tatarstan"

Kazan', , Russia

Site Status

Moscow City Oncology Dispensary, Moscow

Moscow, , Russia

Site Status

FSBI "N.N Blokhin Med.Res.Cent.Onc."MoH of RF

Moscow, , Russia

Site Status

Clinical Oncology Center

Omsk, , Russia

Site Status

St. Petersburg GUZ City Clinical Oncology Dispensary

Saint Petersburg, , Russia

Site Status

FSBI "N.N. Petrov National Medical Research Center of Oncology" of MoH of RF

Saint Petersburg, , Russia

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Hospital A Coruña

A Coruña, , Spain

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Hospital General Universitario de Alicante

Alicante, , Spain

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Hospital Germans Trias i Pujol

Badalona, , Spain

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Hospital Universitario de Cruces

Barakaldo (Bilbao), , Spain

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Hospital del Mar

Barcelona, , Spain

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Hospital Vall d'Hebron

Barcelona, , Spain

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Hospital Clínic de Barcelona

Barcelona, , Spain

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Hospital Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofía

Córdoba, , Spain

Site Status

Hospital Universitario Virgen de las Nieves

Granada, , Spain

Site Status

Hospital Duran i Reynals

L'Hospitalet de Llobregat, , Spain

Site Status

Hospital de Canarias

La Laguna - Tenerife, , Spain

Site Status

Hospital La Princesa

Madrid, , Spain

Site Status

Hospital General Universitario Gregorio Marañón

Madrid, , Spain

Site Status

Hospital Ramón y Cajal

Madrid, , Spain

Site Status

Fundación Jiménez Díaz

Madrid, , Spain

Site Status

Hospital Clínico San Carlos

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital La Paz

Madrid, , Spain

Site Status

Hospital Puerta de Hierro

Majadahonda (Madrid), , Spain

Site Status

Hospital Regional Universitario de Málaga

Málaga, , Spain

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Hospital Virgen de la Victoria

Málaga, , Spain

Site Status

Hospital Central de Asturias

Oviedo, , Spain

Site Status

Hospital Son Espases

Palma de Mallorca, , Spain

Site Status

Hospital de Son Llàtzer

Palma de Mallorca, , Spain

Site Status

Complejo Hospitalario de Navarra

Pamplona, , Spain

Site Status

Hospital Clínico de Santiago

Santiago de Compostela, , Spain

Site Status

Hospital Virgen del Rocío

Seville, , Spain

Site Status

Hospital Politècnic La Fe

Valencia, , Spain

Site Status

Hospital Clínico de Valencia

Valencia, , Spain

Site Status

Hospital General Universitario de Valencia

Valencia, , Spain

Site Status

Hospital Clínico Universitario Lozano Blesa

Zaragoza, , Spain

Site Status

Hospital Miguel Servet

Zaragoza, , Spain

Site Status

Countries

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Australia Austria Czechia Greece Hungary Israel Italy Poland Portugal Russia Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2009-017661-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

1200.55

Identifier Type: -

Identifier Source: org_study_id

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