Development and Prevention of Severe Heart Disease in Systemic Sclerosis

NCT ID: NCT01829126

Last Updated: 2013-11-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Total Enrollment

765 participants

Study Classification

OBSERVATIONAL

Study Start Date

2013-04-30

Study Completion Date

2016-08-31

Brief Summary

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Systemic sclerosis is an orphan, multiorgan disease affecting the connective tissue of the skin and all internal organs. Cardiac involvement, mainly characterised by small intramyocardial coronary artery involvement and myocardial fibrosis, can cause the development of impaired diastolic ventricular filling, cardiac blocks and ventricular arrhythmias, and can ensue in congestive heart failure and sudden death. Until now, no drug has been proven to have a therapeutic effect on SSc myocardial disease on an evidence-based level. Short-term trials and retrospective studies have suggested a favourable and protective effect of calcium channel blockers and angiotensin converting enzyme inhibitors in patients with myocardial involvement. However, no data are presently available on the prevention and treatment of severe heart disease.

This observational trial is part of the collaborative project "DeSScipher", one out of five observational trials to decipher the optimal management of systemic sclerosis. Aim of this observational trial is to assess the efficacy and safety of calcium channel blockers and angiotensin converting enzyme inhibitors in asymptomatic SSc patients with cardiac involvement.

Detailed Description

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Conditions

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Systemic Sclerosis Cardiac Diseases Heart Block Cardiac Arrhythmia Congestive Heart Failure

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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CCB

Patients receiving calcium channel blockers (CCB)

No interventions assigned to this group

ACEi

Patients receiving angiotensin converting enzyme inhibitors (ACEi)

No interventions assigned to this group

CCB and ACEi

Patients receiving calcium channel blockers (CCB) and angiotensin converting enzyme inhibitors (ACEi)

No interventions assigned to this group

No treatment

Patients not receiving calcium channel blockers (CCB) and/or angiotensin converting enzyme inhibitors (ACEi)

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Juvenile and adult systemic sclerosis patients, with diagnosis according to the SSc ACR/EULAR criteria or the PRES/ACR/EULAR juvenile SSc criteria respectively
* Asymptomatic (for cardiac disease) systemic sclerosis patients at risk for severe heart disease with at least one of the following risk factors: male sex and/or DLCO lower than 80% and/or sPAP \> 30 mmHg and/or synovitis and/or joint contractures and/or digital ulcers and/or proteinuria.

Asymptomatic for cardiac disease is defined by patients without dyspnea NYHA \>/= II, without palpitations and without bilateral leg edema.

Exclusion Criteria

* Any significant pulmonary parenchymal (FVC \< 70% and/or DLCO \< 70%), pulmonary vascular (estimated systolic PAP \> 40 mmHg), gastrointestinal (malabsorption syndrome or paralytic ileus) or renal (serum creatinine level \>1.2 mg/dl, dialysis or previous scleroderma renal crisis) involvement
* Patients with dyspnea class NYHA \>/= II
* Patients with palpitations
* Patients with bilateral leg edema.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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European Union

OTHER

Sponsor Role collaborator

University of Giessen

OTHER

Sponsor Role collaborator

University of Zurich

OTHER

Sponsor Role collaborator

University of Paris 5 - Rene Descartes

OTHER

Sponsor Role collaborator

University of Florence

OTHER

Sponsor Role collaborator

University of Basel

OTHER

Sponsor Role collaborator

University College, London

OTHER

Sponsor Role collaborator

Charite University, Berlin, Germany

OTHER

Sponsor Role collaborator

University of Pecs

OTHER

Sponsor Role collaborator

University of Leeds

OTHER

Sponsor Role collaborator

Schoen Klinik Hamburg Eilbek

OTHER

Sponsor Role collaborator

Gabriele Valentini

OTHER

Sponsor Role lead

Responsible Party

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Gabriele Valentini

Prof. Gabriele Valentini

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Ulf Müller-Ladner, Prof.

Role: STUDY_CHAIR

Justus-Liebig-University Gießen, Kerckhoff Clinic, Departement of Rheumatology and Clinical Immunology

Gabriele Valentini, Prof.

Role: PRINCIPAL_INVESTIGATOR

Policlinico, Via Pansini, Napoli-Italia

Locations

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Université Paris Descartes, Hôpital Cochin, Service de Rhumatologie A & INSERM 1016

Paris, , France

Site Status RECRUITING

Justus-Liebig-University Gießen, Kerckhoff Clinic, Departement of Rheumatology and Clinical Immunology

Bad Nauheim, , Germany

Site Status RECRUITING

Charité Universitätsmedizin Berlin, Charité Centrum 12 für Innere Medizin und Dermatologie, Medizinische Klinik mit Schwerpunkt Rheumatologie und Klinische Immunologie

Berlin, , Germany

Site Status RECRUITING

Centre for Pediatric Rheumatology, Klinikum Eilbek

Hamburg, , Germany

Site Status RECRUITING

Pecsi Tudomanyegyetem - University of Pecs

Pécs, , Hungary

Site Status RECRUITING

University of Florence, Denothe Centre, Division of Rheumatology AOUC, Department of Biomedicine

Florence, , Italy

Site Status RECRUITING

Policlinico, Via Pansini

Napoli-Italia, , Italy

Site Status RECRUITING

Felix-Platter Spital, University of Basel

Basel, , Switzerland

Site Status RECRUITING

University of Zurich, Department of Rheumatology

Zurich, , Switzerland

Site Status RECRUITING

The Universitiy of Leeds, Division of Rheumatic and Musculoskeletal Disease, St James's University Hospital

Leeds, , United Kingdom

Site Status RECRUITING

Royal Free Hospital, University College London

London, , United Kingdom

Site Status RECRUITING

Countries

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France Germany Hungary Italy Switzerland United Kingdom

Central Contacts

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Gabriele Valentini, Prof.

Role: CONTACT

Phone: 39815464487

Email: [email protected]

Other Identifiers

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HEALTH-F5-2012-305495-OT5

Identifier Type: -

Identifier Source: org_study_id