Trial Outcomes & Findings for Eosinophilic Esophagitis Clinical Therapy Comparison Trial (NCT NCT01821898)

NCT ID: NCT01821898

Last Updated: 2021-01-11

Results Overview

The primary outcome will be the peak eosinophil/high powered field on repeat biopsy after the treatment phase.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

3 participants

Primary outcome timeframe

16 weeks

Results posted on

2021-01-11

Participant Flow

Participant milestones

Participant milestones
Measure
Positive for Food Allergy: Group A
Oral Budesonide Oral Budesonide: This group will receive oral viscous budesonide at a dose of 1 or 2 mg depending on the height divided twice a day. Children \< 10 years will receive 1 mg daily. Children 10 years and older will receive 2 mg daily.
Positive for Food Allergy: Group B
Elimination diet Elimination diet: This group will receive an elimination diet
Overall Study
STARTED
2
1
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
2
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Positive for Food Allergy: Group A
Oral Budesonide Oral Budesonide: This group will receive oral viscous budesonide at a dose of 1 or 2 mg depending on the height divided twice a day. Children \< 10 years will receive 1 mg daily. Children 10 years and older will receive 2 mg daily.
Positive for Food Allergy: Group B
Elimination diet Elimination diet: This group will receive an elimination diet
Overall Study
Withdrawal by Subject
2
1

Baseline Characteristics

Eosinophilic Esophagitis Clinical Therapy Comparison Trial

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Positive for Food Allergy: Group A
n=2 Participants
Oral Budesonide Oral Budesonide: This group will receive oral viscous budesonide at a dose of 1 or 2 mg depending on the height divided twice a day.
Positive for Food Allergy: Group B
n=1 Participants
Elimination diet Elimination diet: This group will receive an elimination diet
Total
n=3 Participants
Total of all reporting groups
Age, Categorical
<=18 years
2 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
2 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
Region of Enrollment
United States
2 participants
n=5 Participants
1 participants
n=7 Participants
3 participants
n=5 Participants
EoE endoscopy score
Patient 1
18 cells/high powered field
n=5 Participants
0 cells/high powered field
n=7 Participants
18 cells/high powered field
n=5 Participants
EoE endoscopy score
Patient 2
0 cells/high powered field
n=5 Participants
21 cells/high powered field
n=7 Participants
21 cells/high powered field
n=5 Participants
EoE endoscopy score
Patient 3
30 cells/high powered field
n=5 Participants
0 cells/high powered field
n=7 Participants
30 cells/high powered field
n=5 Participants

PRIMARY outcome

Timeframe: 16 weeks

Population: None of the enrolled participants had a repeat biopsy because they did not finish the trial due to undue stress and anxiety.

The primary outcome will be the peak eosinophil/high powered field on repeat biopsy after the treatment phase.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 16 weeks

Population: None of the enrolled participants had a PedQL because they did not finish the trial due to undue stress and anxiety.

PedsQL total survey score to assess overall quality of life before and after treatment

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 16 weeks

Population: Pediatric Eosinophilic Esophagitis (EoE) Symptom Severity Module was not completed because the subjects did not finish the trial due to undue stress and anxiety.

Assess the subject's symptoms using the validated tool termed Pediatric Eosinophilic Esophagitis (EoE) Symptom Severity Module by measuring % of normal bolus transit swallow and % of normal peristaltic esophageal body contractions.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Conclusion of study

Population: Analysis was not performed.

Proteomic studies search for certain proteins in the blood that may be linked to active EoE. Immune analysis will help identify better methods for diagnosis, treatment, and prevention of immune system changes leading to diseases.

Outcome measures

Outcome data not reported

Adverse Events

Positive for Food Allergy: Group A

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Positive for Food Allergy: Group B

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Carla M. Davis, MD

Baylor College of Medicine/Texas Children's Hospital

Phone: 832-824-1319

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place