Trial Outcomes & Findings for An Observational Study of Epoetin Beta (NeoRecormon) in Participants With Cancer Receiving Chemotherapy (NCT NCT01809314)

NCT ID: NCT01809314

Last Updated: 2016-08-19

Results Overview

The change in Hb level from Baseline to the EOT visit at Month 4 was averaged among all participants and expressed in grams per liter (g/L).

Recruitment status

COMPLETED

Target enrollment

1167 participants

Primary outcome timeframe

Baseline, Month 4

Results posted on

2016-08-19

Participant Flow

Participant milestones

Participant milestones
Measure
NeoRecormon in Symptomatic Anemia
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Overall Study
STARTED
1167
Overall Study
COMPLETED
422
Overall Study
NOT COMPLETED
745

Reasons for withdrawal

Reasons for withdrawal
Measure
NeoRecormon in Symptomatic Anemia
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Overall Study
Withdrawal Prior to Treatment
1
Overall Study
Adverse Event
6
Overall Study
Insufficient Therapeutic Response
14
Overall Study
Lost to Follow-up
724

Baseline Characteristics

An Observational Study of Epoetin Beta (NeoRecormon) in Participants With Cancer Receiving Chemotherapy

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
NeoRecormon in Symptomatic Anemia
n=1167 Participants
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Age, Continuous
60.8 years
STANDARD_DEVIATION 13.0 • n=5 Participants
Sex/Gender, Customized
Male
398 participants
n=5 Participants
Sex/Gender, Customized
Female
709 participants
n=5 Participants
Sex/Gender, Customized
Unknown
60 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline, Month 4

Population: All Participants Enrolled; only those who provided data at all study visits were included in the analysis.

The change in Hb level from Baseline to the EOT visit at Month 4 was averaged among all participants and expressed in grams per liter (g/L).

Outcome measures

Outcome measures
Measure
NeoRecormon in Symptomatic Anemia
n=280 Participants
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Change in Hemoglobin (Hb) Level From Baseline to End of Treatment (EOT)
14.58 g/L
Interval 12.684 to 16.478

SECONDARY outcome

Timeframe: Baseline, Month 4

Population: All Participants Enrolled; only those who provided data at all study visits were included in the analysis. The "Number of Participants Analyzed" reflects the total combined number of participants who provided data for the endpoint. The number of participants used in the denominator for each calculation (n) was based on the ECOG status at Baseline.

ECOG performance status was determined at Baseline and at the EOT visit at Month 4. The assessment used a 3-point scale, including scores of 0 (fully active/able to carry on all pre-disease activities without restriction), 1 (restricted in physically strenuous activity but ambulatory/able to carry out light or sedentary work), or 2 (ambulatory for more than 50% of waking hours and capable of all self care but unable to carry out any work activities). The traditional 6-point scale was not valid because only participants with a performance status of 0, 1, or 2 were eligible for the study. The percentage of participants by change in ECOG performance status was reported. For example, the percentage of participants with ECOG performance status of 0 at Baseline and 2 at EOT is shown in the table as "Baseline 0, EOT 2". Transition to a lower performance status indicates improved/increased independence.

Outcome measures

Outcome measures
Measure
NeoRecormon in Symptomatic Anemia
n=272 Participants
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 0, EOT 0 (n=71)
77.5 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 0, EOT 1 (n=71)
19.7 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 0, EOT 2 (n=71)
2.8 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 1, EOT 0 (n=168)
23.8 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 1, EOT 1 (n=168)
67.3 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 1, EOT 2 (n=168)
8.9 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 2, EOT 0 (n=33)
21.2 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 2, EOT 1 (n=33)
48.5 percentage of participants
Percentage of Participants by Change in Eastern Cooperative Oncology Group (ECOG) Performance Status From Baseline to EOT
Baseline 2, EOT 2 (n=33)
30.3 percentage of participants

SECONDARY outcome

Timeframe: Baseline to Month 1, Month 1 to 2, Month 2 to 3, Month 3 to 4

Population: All Participants Enrolled. The "Number of Participants Analyzed" reflects the total combined number of participants who provided data for the endpoint. The number of participants who provided data for the analysis at each timepoint (n) is shown in the table.

The percentage of participants who required blood transfusions was reported at each assessment visit and was based on the 1-month period preceding the respective visit.

Outcome measures

Outcome measures
Measure
NeoRecormon in Symptomatic Anemia
n=1073 Participants
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Percentage of Participants Who Required Blood Transfusions During the Study
Baseline to Month 1 (n=1073)
4.1 percentage of participants
Percentage of Participants Who Required Blood Transfusions During the Study
Month 1 to 2 (n=853)
4.1 percentage of participants
Percentage of Participants Who Required Blood Transfusions During the Study
Month 2 to 3 (n=650)
3.8 percentage of participants
Percentage of Participants Who Required Blood Transfusions During the Study
Month 3 to 4 (n=281)
3.9 percentage of participants

Adverse Events

NeoRecormon in Symptomatic Anemia

Serious events: 7 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
NeoRecormon in Symptomatic Anemia
n=1167 participants at risk
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Blood and lymphatic system disorders
Anaemia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Blood and lymphatic system disorders
Febrile neutropenia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Blood and lymphatic system disorders
Granulocytopenia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Blood and lymphatic system disorders
Pancytopenia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Blood and lymphatic system disorders
Thrombocytopenia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
General disorders
Death
0.26%
3/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Non-Hodgkin's lymphoman
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Respiratory, thoracic and mediastinal disorders
Pulmonary embolism
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.

Other adverse events

Other adverse events
Measure
NeoRecormon in Symptomatic Anemia
n=1167 participants at risk
Participants with symptomatic anemia who received epoetin beta (NeoRecormon) according to standard of care and the Summary of Product Characteristics were observed for 4 months. Treatment was selected at the discretion of the prescriber prior to enrollment and not chosen by the Sponsor in this non-interventional study.
Cardiac disorders
Dyspnoea
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Gastrointestinal disorders
Gastrooesophageal reflux disease
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
General disorders
Asthenia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Immune system disorders
Drug hypersensitivity
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Infections and infestations
Pneumonia
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Surgical and medical procedures
Abdominal cavity drainage
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Surgical and medical procedures
Hospitalisation
0.09%
1/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.
Surgical and medical procedures
Transfusion
0.17%
2/1167 • From Baseline to Month 4
Analysis Population Description: All Participants Enrolled.

Additional Information

Medical Communications

Hoffmann-La Roche

Phone: 800-821-8590

Results disclosure agreements

  • Principal investigator is a sponsor employee The Study being conducted under this Agreement is part of the Overall Study. Investigator is free to publish in reputable journals or to present at professional conferences the results of the Study, but only after the first publication or presentation that involves the Overall Study. The Sponsor may request that Confidential Information be deleted and/or the publication be postponed in order to protect the Sponsor's intellectual property rights.
  • Publication restrictions are in place

Restriction type: OTHER