A Phase Ib/II Study of LEE011 in Combination With MEK162 in Patients With NRAS Mutant Melanoma

NCT ID: NCT01781572

Last Updated: 2020-12-07

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

102 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-06-30

Study Completion Date

2018-02-20

Brief Summary

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In the phase Ib, the primary purpose is to establish the maximum tolerated dose (MTD)(s)/recommended phase ll dose (RP2D) and schedule of LEE011 and MEK162 orally administered combination. Once the MTD(s)/RP2D have been determined for each tested schedule, additional patients will be enrolled in the phase II portion of the study at the RP2D on the chosen schedule in order to assess the anti-tumor activity of the combination in addition to continued evaluation of safety.

Detailed Description

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Conditions

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Locally Advanced or Metastatic NRAS Mutant Melanoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Phase Ib

The phase Ib is the dose escalation part where successive cohorts of 3-6 newly enrolled patients receiving various dose pairs considering the recommendation from an adaptive BLRM incorporating the EWOC principle until MTD(s)/RP2D is defined. If multiple alternate dosing schedules are explored in parallel, the allocation of patients will proceed in an alternating fashion. Approximately 40 patients are expected to be treated during the phase Ib part of the study.

Dosing Schedule 1: MEK162 administered orally twice daily on a continuous dosing schedule. LEE011 administered orally once daily for 21 days followed by a 1 week break (28-day cycle).

Dosing Schedule 2: MEK162 administered orally twice daily and LEE011 administered orally once daily for 3 weeks followed by a 1 week break (28-day cycle).

Dosing Schedule 3: MEK162 administered orally twice daily and LEE011 administered once daily for 2 weeks followed by a 1 week break (21-day cycle).

Group Type EXPERIMENTAL

LEE011

Intervention Type DRUG

LEE011 will be administered orally once daily

MEK162

Intervention Type DRUG

MEK162 will be administered orally twice daily

Phase II

The Phase II part will begin once the MTD(s)/RP2D have been determined in the Phase Ib in order to assess antitumor activity of the LEE011and MEK162 combination. Patients enrolled in the Phase II part of the study are required to have measurable disease. Approximately 40 patients will be treated in this part.

Phase II part will begin at the RP2D on the chosen schedule in order to assess antitumor activity of the LEE011 and MEK162 combination.

Group Type EXPERIMENTAL

LEE011

Intervention Type DRUG

LEE011 will be administered orally once daily

MEK162

Intervention Type DRUG

MEK162 will be administered orally twice daily

Interventions

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LEE011

LEE011 will be administered orally once daily

Intervention Type DRUG

MEK162

MEK162 will be administered orally twice daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients must have an Eastern Cooperative Oncology Group (ECOG) performance status of 0 - 1.
* Patients enrolled into phase Ib may be enrolled with evaluable disease only. Patients enrolled into the phase II expansion must have at least one measurable lesion as defined by RECIST 1.1 criteria for solid tumors.
* Patients must have adequate organ function, as defined by the following parameter

1. Absolute Neutrophil Count (ANC) ≥ 1.5 x 109/L.
2. Hemoglobin (Hgb) ≥ 9 g/dL.
3. Platelets ≥ 75 x 109/L without transfusions within 21 days before 1st treatment.
4. PT/INR and aPTT ≤ 1.5 ULN.
5. Serum creatinine ≤1.5 ULN.
6. Serum total bilirubin ≤ 1.5 x upper limit of normal (ULN).
7. AST and ALT ≤ 3 x ULN, except in patients with tumor involvement of the liver who must have AST and ALT ≤ 5 x ULN.

Exclusion Criteria

* Presence of any brain metastases detected by MRI or CT with i.v. contrast of the brain at screening.
* Uncontrolled arterial hypertension despite medical treatment
* Impaired cardiac function or clinically significant cardiac diseases, including any of the following:

1. Left ventricular ejection fraction (LVEF) \< 50% as determined by multiple gated acquisition scan (MUGA) or echocardiogram (ECHO).
2. Congenital long QT syndrome or family history of unexpected sudden cardiac death.
3. QTcF corrected with Frederica's or Bazett's formula QTcB \>450 ms for males and \>470 ms for females on screening ECG.
4. Angina pectoris ≤ 3 months prior to starting study drug
5. Acute myocardial infarction ≤ 3 months prior to starting study drug
6. Clinically significant resting bradycardia
7. History or presence of ventricular tachyarrhythmia
8. Unstable atrial fibrillation (ventricular response \>100 bpm)
9. Complete left bundle branch block
10. Right bundle branch block and left anterior hemi block (bifascicular block)
11. Obligate use of a cardiac pacemaker or implantable cardioverter defibrillator
12. Any other clinically significant heart disease
* Patients who are currently receiving treatment with agents that are known to cause QTc prolongation in humans.
* Patients who have neuromuscular disorders that are associated with elevated CK (e.g., inflammatory myopathies, muscular dystrophy, amyotrophic lateral sclerosis, spinal muscular atrophy) or elevated baseline CK levels (≥ Grade 2)
* Patients who are currently receiving treatment with agents that are metabolized predominantly through CYP3A4 and that have a narrow therapeutic window.
* Patients with concurrent severe and/or uncontrolled concurrent medical conditions that could compromise participation in the study (i.e. uncontrolled diabetes mellitus, clinically significant pulmonary disease, clinically significant neurological disorder, active or uncontrolled infection).
* History or current evidence of retinal vein occlusion (RVO) or current risk factors for RVO (e.g. uncontrolled glaucoma or ocular hypertension, history of hyperviscosity or hypercoagulability syndromes).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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University of California, Dept of Oncology

San Francisco, California, United States

Site Status

California Pacific Medical Center Onc Dept

San Francisco, California, United States

Site Status

Karmanos Cancer Institute Dept of Oncology

Detroit, Michigan, United States

Site Status

Memorial Sloan Kettering Cancer Center Dept Oncology

New York, New York, United States

Site Status

Columbia University Medical Center- New York Presbyterian Onc Dept.

New York, New York, United States

Site Status

Vanderbilt University Medical Center SC - Dept of Oncology .

Nashville, Tennessee, United States

Site Status

University of Texas/MD Anderson Cancer Center Dept of Onc.

Houston, Texas, United States

Site Status

Pfizer Investigative Site 1003

North Sydney, New South Wales, Australia

Site Status

Pfizer Investigative Site 1002

Westmead, New South Wales, Australia

Site Status

Pfizer Investigator Site 1001

East Melbourne, Victoria, Australia

Site Status

Pfizer Investigative Site 1050

Essen, , Germany

Site Status

Pfizer Investigative Site 1053

Gera, , Germany

Site Status

Pfizer Investigative Site 1052

Hanover, , Germany

Site Status

Pfizer Investigative Site 1051

München, , Germany

Site Status

Pfizer Investigative Site 1101

Napoli, , Italy

Site Status

Pfizer Investigative Site 1151

Utrecht, The Netherlands, Netherlands

Site Status

Pfizer Investigative Site 1150

Nijmegen, , Netherlands

Site Status

Countries

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Norway United States Australia Germany Italy Netherlands

References

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Schuler M, Zimmer L, Kim KB, Sosman JA, Ascierto PA, Postow MA, De Vos FYFL, van Herpen CML, Carlino MS, Johnson DB, Berking C, Reddy MB, Harney AS, Berlin JD, Amaria RN. Phase Ib/II Trial of Ribociclib in Combination with Binimetinib in Patients with NRAS-mutant Melanoma. Clin Cancer Res. 2022 Jul 15;28(14):3002-3010. doi: 10.1158/1078-0432.CCR-21-3872.

Reference Type DERIVED
PMID: 35294522 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Other Identifiers

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C4211005

Identifier Type: OTHER

Identifier Source: secondary_id

CMEK162X2114

Identifier Type: -

Identifier Source: org_study_id