Trial Outcomes & Findings for Early add-on Vildagliptin in Patients With Type 2 Diabetes Inadequately Controlled by Metformin (NCT NCT01766778)

NCT ID: NCT01766778

Last Updated: 2017-05-15

Results Overview

HbA1c is an integrated measure of average glucose concentration in plasma in the last 2-3 months. Blood samples were collected to analyze HbA1c

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

117 participants

Primary outcome timeframe

Baseline, Month 12 (weeK 52)

Results posted on

2017-05-15

Participant Flow

There was 117 patients randomized and received either Vildagliptin 50mg QD or 50 mg BID.

Participant milestones

Participant milestones
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Overall Study
STARTED
56
61
Overall Study
COMPLETED
51
57
Overall Study
NOT COMPLETED
5
4

Reasons for withdrawal

Reasons for withdrawal
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Overall Study
Adverse Event
4
4
Overall Study
Withdrawal by Subject
1
0

Baseline Characteristics

Early add-on Vildagliptin in Patients With Type 2 Diabetes Inadequately Controlled by Metformin

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Total
n=117 Participants
Total of all reporting groups
Age, Continuous
58 Years
STANDARD_DEVIATION 10.3 • n=5 Participants
59 Years
STANDARD_DEVIATION 10.0 • n=7 Participants
58 Years
STANDARD_DEVIATION 10.1 • n=5 Participants
Sex: Female, Male
Female
26 Participants
n=5 Participants
31 Participants
n=7 Participants
57 Participants
n=5 Participants
Sex: Female, Male
Male
30 Participants
n=5 Participants
30 Participants
n=7 Participants
60 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline, Month 12 (weeK 52)

Population: Intent to treat (ITT) analysis set included all randomized patients who received at least one dose of study medication. Patients with both baseline and 12 month data were included in this analysis

HbA1c is an integrated measure of average glucose concentration in plasma in the last 2-3 months. Blood samples were collected to analyze HbA1c

Outcome measures

Outcome measures
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=49 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=50 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Change of Glycosylated Hemoglobin A1c (HbA1c) From Baseline to Month 12
-0.8 percentage of Glycosylated Hemoglobin
Standard Deviation 1.01
-1.0 percentage of Glycosylated Hemoglobin
Standard Deviation 1.24

SECONDARY outcome

Timeframe: Baseline, Month 3, 6, 9 and 12

Population: Intent to treat (ITT) analysis set included all randomized patients who received at least one dose of study medication. .

HbA1c is an integrated measure of average glucose concentration in plasma in the last 2-3 months. Blood samples were collected to analyze HbA1c. Mixed Model of Repeated Measures (MMRM) was used to analyze this outcome. For the MMRM analysis, the model includes terms for treatment, period, treatment-by-period interaction and baseline value, and further adjusted by age, pre-existing hypertension and microvascular and macrovascular complications for diabetes mellitus. The variables selected for baseline adjustment were based on the lowest AIC.

Outcome measures

Outcome measures
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Change of Glycosylated Hemoglobin A1c (HbA1c) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
3 month from baseline
-0.6 percentage of Glycosylated Hemoglobin
Standard Error 0.11
-0.9 percentage of Glycosylated Hemoglobin
Standard Error 0.10
Change of Glycosylated Hemoglobin A1c (HbA1c) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
6 month from baseline
-0.7 percentage of Glycosylated Hemoglobin
Standard Error 0.13
-0.9 percentage of Glycosylated Hemoglobin
Standard Error 0.12
Change of Glycosylated Hemoglobin A1c (HbA1c) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
9 month from baseline
-0.7 percentage of Glycosylated Hemoglobin
Standard Error 0.13
-0.7 percentage of Glycosylated Hemoglobin
Standard Error 0.13
Change of Glycosylated Hemoglobin A1c (HbA1c) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
12 month from baseline
-0.6 percentage of Glycosylated Hemoglobin
Standard Error 0.15
-0.6 percentage of Glycosylated Hemoglobin
Standard Error 0.15

SECONDARY outcome

Timeframe: Baseline, Month 3, 6, 9 and 12

Population: Intent to treat (ITT) analysis set included all randomized patients who received at least one dose of study medication.

Blood samples were collected to analyze fasting plasma glucose. Mixed Model of Repeated Measures (MMRM) was used to analyze this outcome. For the MMRM analysis, the model included terms for treatment, period, treatment-by-period interaction and baseline value, and further adjusted by pre-existing hypertension. The variable selected for baseline adjustment was based on the lowest AIC.

Outcome measures

Outcome measures
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Change in Fasting Plasma Glucose (FPG) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
3 month from baseline
-0.9 mmol/L
Standard Error 0.18
-1.3 mmol/L
Standard Error 0.16
Change in Fasting Plasma Glucose (FPG) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
6 month from baseline
-1.2 mmol/L
Standard Error 0.18
-0.9 mmol/L
Standard Error 0.17
Change in Fasting Plasma Glucose (FPG) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
9 month from baseline
-1.1 mmol/L
Standard Error 0.17
-1.0 mmol/L
Standard Error 0.16
Change in Fasting Plasma Glucose (FPG) From Baseline to Month 3, 6, 9 and 12 (Based on MMRM Analysis)
12 month from baseline
-0.9 mmol/L
Standard Error 0.20
-0.8 mmol/L
Standard Error 0.20

SECONDARY outcome

Timeframe: Month 3, 6, 9, 12

Population: Intent to treat (ITT) analysis set included all randomized patients who received at least one dose of study medication. 'n' indicates patients with HbA1c data in that time point.

Blood samples were collected to analyze HbA1c. Good glycemic control is defined as patient achieving Hb1Ac \< 7.0%. Percentage of patients who achieved HbA1c less than 7.0% at month 3, 6, 9 and 12 were reported for this endpoint.

Outcome measures

Outcome measures
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Percentage of Patients Achieving Good Glycemic Control
At Month 12
49.0 Percentage of patients
40.0 Percentage of patients
Percentage of Patients Achieving Good Glycemic Control
At Month 3
33.3 Percentage of patients
47.5 Percentage of patients
Percentage of Patients Achieving Good Glycemic Control
At Month 6
39.2 Percentage of patients
45.6 Percentage of patients
Percentage of Patients Achieving Good Glycemic Control
At Month 9
45.1 Percentage of patients
47.4 Percentage of patients

SECONDARY outcome

Timeframe: Month 12

Population: Intent to treat (ITT) analysis set included all randomized patients who received at least one dose of study medication. Patients who had reported dosing compliance were included in this analysis.

The overall drug compliance (%) = (Observed Consumption / Expected Consumption) x 100% Where (Observed Consumption / Expected Consumption) = \[1- (Number of missing tablets from all visits/(sum of Allocated Daily Dosage (in tablets) from all visits × No. of Days between the Date Dispensed and the Date Returned))\]

Outcome measures

Outcome measures
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=21 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=21 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Percentage of Overall Drug Compliance in 12 Months
96.90 Percentage of overall drug compliance
Standard Deviation 5.682
97.48 Percentage of overall drug compliance
Standard Deviation 6.277

SECONDARY outcome

Timeframe: Month 12

Population: Intent to treat (ITT) analysis set included all randomized patients who received at least one dose of study medication.

This analysis reported percentage patients with adverse events and patient discontinued from the study due to adverse events. Aslo, percentage of patients with serious adverse events and death was reported.

Outcome measures

Outcome measures
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 Participants
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 Participants
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Number of Patients With Adverse Events, Serious Adverse Events and Death as an Assessment of Overall Safety and Tolerability
Any adverse events
15 Patients
14 Patients
Number of Patients With Adverse Events, Serious Adverse Events and Death as an Assessment of Overall Safety and Tolerability
Serious adverse events
2 Patients
2 Patients
Number of Patients With Adverse Events, Serious Adverse Events and Death as an Assessment of Overall Safety and Tolerability
Death
0 Patients
0 Patients
Number of Patients With Adverse Events, Serious Adverse Events and Death as an Assessment of Overall Safety and Tolerability
Patients discontinued due to any AE/SAE
4 Patients
4 Patients

Adverse Events

LAF237 (Vildagliptin) 50mg Once Daily (QD)

Serious events: 2 serious events
Other events: 14 other events
Deaths: 0 deaths

LAF237 (Vildagliptin) 50mg Twice Daily (BID)

Serious events: 2 serious events
Other events: 7 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 participants at risk
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 participants at risk
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Gastrointestinal disorders
Duodenitis
1.8%
1/56
0.00%
0/61
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Leukemia
0.00%
0/56
1.6%
1/61
Renal and urinary disorders
Renal failure
0.00%
0/56
1.6%
1/61
Renal and urinary disorders
stone impairation over proximal urethra
1.8%
1/56
0.00%
0/61

Other adverse events

Other adverse events
Measure
LAF237 (Vildagliptin) 50mg Once Daily (QD)
n=56 participants at risk
Vildagliptin 50mg QD plus stabilized or maximum tolerated dose of Metformin
LAF237 (Vildagliptin) 50mg Twice Daily (BID)
n=61 participants at risk
Vildagliptin 50mg BID plus stabilized or maximum tolerated dose of Metformin
Infections and infestations
Tinea
0.00%
0/56
3.3%
2/61
Infections and infestations
Upper Respiratory Tract Infection
14.3%
8/56
3.3%
2/61
Investigations
Elevated liver function test
3.6%
2/56
3.3%
2/61
Metabolism and nutrition disorders
Hyperkalemia
1.8%
1/56
3.3%
2/61
Metabolism and nutrition disorders
Hypokalemia
3.6%
2/56
0.00%
0/61
Nervous system disorders
Dizziness
3.6%
2/56
1.6%
1/61
Respiratory, thoracic and mediastinal disorders
Cough
3.6%
2/56
3.3%
2/61
Skin and subcutaneous tissue disorders
Eczema
3.6%
2/56
1.6%
1/61

Additional Information

Study Director

Novartis Pharmaceuticals

Phone: 862-778-8300

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Any publications from a single-site are postponed until the publication of the pooled data (i.e., data from all sites) in the clinical trial or disclosure of trial results in their entirety.
  • Publication restrictions are in place

Restriction type: OTHER