To Characterize the Safety and Tolerability of Eculizumab in Two Japanese aHUS Patients

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

2 participants

Study Classification

OBSERVATIONAL

Study Start Date

2012-05-31

Study Completion Date

2012-07-31

Brief Summary

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This protocol is intended to formally collect data on the treatment of aHUS with eculizumab in Japanese patients.

Detailed Description

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Conditions

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ATYPICAL HEMOLYTIC UREMIC SYNDROME (AHUS)

Study Design

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Study Time Perspective

RETROSPECTIVE

Eligibility Criteria

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Inclusion Criteria

1. Patient and/or legal guardian must be willing and able to give written informed consent and id the patient is not an adult and able to read and write, the patient is willing to give written informed assent
2. Eculizumab treatment initiated as personal importation for aHUS in 201

Exclusion Criteria

Not Applicable

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Responsible Party

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Responsibility Role SPONSOR

Locations

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Shinshu University School of Medicine

Matsumoto, , Japan

Site Status

Tokyo Medical and Dental University

Tokyo, , Japan

Site Status

Countries

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Japan

Other Identifiers

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C11-004J

Identifier Type: -

Identifier Source: org_study_id