Open-label Extension Study in Patients 65 Years or Older With Chronic Lymphocytic Leukemia or Small Lymphocytic Lymphoma

NCT ID: NCT01724346

Last Updated: 2024-09-19

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

269 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-12-03

Study Completion Date

2023-08-18

Brief Summary

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An Open-label Extension Study in Patients 65 Years or Older with Chronic Lymphocytic Leukemia (CLL) or Small Lymphocytic Lymphoma (SLL) Who Participated in Study PCYC-1115-CA (Ibrutinib versus Chlorambucil)

Detailed Description

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Conditions

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Chronic Lymphocytic Leukemia Small Lymphocytic Lymphoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Open label study

Study Groups

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Chlorambucil

Participants who received chlorambucil 0.5 mg/kg (to maximum 0.8 mg/kg) Days 1 and 15 of 28-day cycle up to 12 cycles in Study 1115. In Study 1116, participants had the option to crossover to next-line ibrutinib 420 mg/day after disease progression (PD).

Group Type EXPERIMENTAL

Ibrutinib

Intervention Type DRUG

Ibrutinib 420 mg (3 x 140-mg capsules) is administered orally once daily

Ibrutinib

Participants who received ibrutinib 420 mg daily in Study 1115 received ibrutinib orally once daily. Participants continuing in first-line ibrutinib therapy entered Study 1116 at the ibrutinib dose tolerated in Study 1115.

Group Type EXPERIMENTAL

Next-line ibrutinib

Intervention Type DRUG

Ibrutinib 420 mg (3 x 140-mg capsules) is administered orally once daily

Interventions

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Ibrutinib

Ibrutinib 420 mg (3 x 140-mg capsules) is administered orally once daily

Intervention Type DRUG

Next-line ibrutinib

Ibrutinib 420 mg (3 x 140-mg capsules) is administered orally once daily

Intervention Type DRUG

Other Intervention Names

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PCI-32765 PCI-32765

Eligibility Criteria

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Inclusion Criteria

1. Randomized in the parent study, PCYC-1115-CA
2. Informed consent for Study PCYC-1116-CA
3. Independent review committee (IRC)-confirmed disease progression (PD) in the parent study PCYC-1115-CA or closure of the parent study

Exclusion Criteria

1. Disease progression involving the central nervous system (CNS) or transformation to another histology
2. Intervening chemotherapy, immunotherapy, or investigational agent specifically to treat CLL if administered before date of IRC confirmed progressive disease
3. In the 4 weeks before dosing: radiation therapy, major surgery, or receipt of an investigational drug
4. Requirement for treatment with a strong CYP3A inhibitor
5. Uncontrolled systemic infection or requirement for IV antibiotics
6. Noncompliance on the parent study(PCYC-1115-CA)
Minimum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role collaborator

Pharmacyclics LLC.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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City of Hope /ID# 1116-0047

Duarte, California, United States

Site Status

Moores Cancer Center at UC San Diego /ID# 1116-0408

La Jolla, California, United States

Site Status

Stanford University/Stanford Cancer Center, Campus Drive /ID# 1116-0038

Stanford, California, United States

Site Status

University of Chicago /ID# 1116-0126

Chicago, Illinois, United States

Site Status

Norton Cancer Institute - St Matthews /ID# 1116-0071

Louisville, Kentucky, United States

Site Status

Comprehensive Cancer Centers of Nevada /ID# 1116-0712

Henderson, Louisiana, United States

Site Status

University of Massachusetts - Worcester /ID# 1116-0307

Worcester, Massachusetts, United States

Site Status

Washington University-School of Medicine /ID# 1116-0221

St Louis, Missouri, United States

Site Status

Northwell Health/Long Island Jewish Hospital /ID# 1116-0350

New Hyde Park, New York, United States

Site Status

University of Rochester Medical Center /ID# 1116-0127

Rochester, New York, United States

Site Status

Southeastern Medical Oncology Center /ID# 1116-0656

Goldsboro, North Carolina, United States

Site Status

Kaiser Permanente - Northwest /ID# 1116-0677

Portland, Oregon, United States

Site Status

University of Pittsburgh - UPMC (Hillman Cancer Center) /ID# 1116-0050

Pittsburgh, Pennsylvania, United States

Site Status

University of Texas MD Anderson Cancer Center /ID# 1116-0032

Houston, Texas, United States

Site Status

Oncology of San Antonio /ID# 1116-0653

San Antonio, Texas, United States

Site Status

Providence St. Mary Regional Cancer Center /ID# 1116-0731

Walla Walla, Washington, United States

Site Status

St George Hospital /ID# 1116-0654

Kogarah, New South Wales, Australia

Site Status

Princess Alexandra Hospital /ID# 1116-0503

Woolloongabba, Queensland, Australia

Site Status

Flinders Medical Centre /ID# 1116-0163

Bedford Park, South Australia, Australia

Site Status

Royal Hobart /ID# 1116-0555

Hobart, Tasmania, Australia

Site Status

Box Hill Hospital /ID# 1116-0193

Box Hill, Victoria, Australia

Site Status

Monash Medical Centre /ID# 1116-0556

Clayton, Victoria, Australia

Site Status

St Vincent's Hospital Melbourne /ID# 1116-0501

Fitzroy Melbourne, Victoria, Australia

Site Status

Austin Health /ID# 1116-0170

Heidelberg, Victoria, Australia

Site Status

ZNA Cadix /ID# 1116-0561

Antwerp, Antwerpen, Belgium

Site Status

UCL Saint-Luc /ID# 1116-0164

Woluwe-Saint-Lambert, Brussels Capital, Belgium

Site Status

UZ Gent /ID# 1116-0560

Ghent, Oost-Vlaanderen, Belgium

Site Status

Universitair Ziekenhuis Leuven /ID# 1116-0559

Leuven, Vlaams-Brabant, Belgium

Site Status

Tom Baker Cancer Centre /ID# 1116-0157

Calgary, Alberta, Canada

Site Status

Cross Cancer Institute /ID# 1116-0018

Edmonton, Alberta, Canada

Site Status

Beijing Cancer Hospital /ID# 1116-0670

Beijing, Beijing Municipality, China

Site Status

Peking University Third Hospital /ID# 1116-0673

Beijing, Beijing Municipality, China

Site Status

Jiangsu Province Hospital /ID# 1116-0671

Nanjing, Jiangsu, China

Site Status

The First Affiliated Hospital, Zhejiang University School of Medicine /ID# 1116-0675

Hangzhou, Zhejiang, China

Site Status

Fakultni nemocnice Brno /ID# 1116-0562

Brno, , Czechia

Site Status

Fakultni nemocnice Hradec Kralove /ID# 1116-0564

Hradec Králové, , Czechia

Site Status

Fakultni nemocnice Plzen /ID# 1116-0566

Pilsen, , Czechia

Site Status

St James Hospital /ID# 1116-0570

Dublin, Dublin, Ireland

Site Status

University Hospital Galway /ID# 1116-0571

Galway, , Ireland

Site Status

Rambam Health Care Campus /ID# 1116-0576

Haifa, H_efa, Israel

Site Status

Bnai Zion Medical Center /ID# 1116-0573

Haifa, H_efa, Israel

Site Status

Rabin Medical Center /ID# 1116-0575

Haifa, H_efa, Israel

Site Status

Shaare Zedek Medical Center /ID# 1116-0577

Jerusalem, Jerusalem, Israel

Site Status

Galilee Medical Center /ID# 1116-0578

Nahariya, Northern District, Israel

Site Status

Tel Aviv Sourasky Medical Center /ID# 1116-0856

Tel Aviv, , Israel

Site Status

Institute of Hematology Seràgnoli /ID# 1116-0580

Bologna, Emilia-Romagna, Italy

Site Status

Ospedale San Raffaele IRCCS /ID# 1116-0523

Milan, Milano, Italy

Site Status

ASST Grande Ospedale Metropolitano Niguarda /ID# 1116-0581

Milan, Milano, Italy

Site Status

Università La Sapienza /ID# 1116-0583

Rome, Roma, Italy

Site Status

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico /ID# 1116-0584

Milan, , Italy

Site Status

Azienda Ospedaliero-Universitaria di Modena /ID# 1116-0524

Modena, , Italy

Site Status

Azienda Ospedaliero Universitaria Maggiore della Carita di Novara /ID# 1116-0582

Novara, , Italy

Site Status

Universita degli Studi di Padova /ID# 1116-0527

Padua, , Italy

Site Status

Policlinico Universitario A Gemelli /ID# 1116-0891

Rome, , Italy

Site Status

Auckland City Hospital /ID# 1116-0588

Grafton, Auckland, New Zealand

Site Status

North Shore Hospital /ID# 1116-0663

Takapuna, Auckland, New Zealand

Site Status

Haematology Waikato Hospital /ID# 1116-0586

Hamilton, Waikato Region, New Zealand

Site Status

Wellington Blood and Cancer Centre /ID# 1116-0587

Wellington South, Wellington Region, New Zealand

Site Status

Canterbury Health Labs Canterbury Disrict Health Board /ID# 1116-0589

Christchurch, , New Zealand

Site Status

MTZ Clinical Research Sp. z o.o. /ID# 1116-0363

Warsaw, Masovian Voivodeship, Poland

Site Status

Szpital Specjalistyczny w Brzozowie Podkarpacki Osrodek Onkologiczny im. ks. B. /ID# 1116-0592

Brzozów, Podkarpackie Voivodeship, Poland

Site Status

Samodzielny Publiczny Szpital Klinczny Nr-1- Akademickie Cenrum Klinic /ID# 1116-0529

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Samodzielny Publiczny Zaklad Opieki Zdrowotnej /ID# 1116-0591

Chorzów, Silesian Voivodeship, Poland

Site Status

Medical Univ. of Lodz and Copernicus Memorial Hospital /ID# 1116-0531

Lodz, , Poland

Site Status

State Institution of Health of the Ryazan Regional Clinical Hospital /ID# 1116-0707

Ryazan, Ryazan Oblast, Russia

Site Status

Hospital Duran i Reynals /ID# 1116-0604

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Universitario Puerta de Hierro - Majadahonda /ID# 1116-0536

Majadahonda, Madrid, Spain

Site Status

Hospital Universitario Vall d'Hebron /ID# 1116-0534

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona /ID# 1116-0533

Barcelona, , Spain

Site Status

Hospital Santa Creu i Sant Pau /ID# 1116-0535

Barcelona, , Spain

Site Status

Hospital Universitario HM Sanchinarro /ID# 1116-0537

Madrid, , Spain

Site Status

Gazi Universitesi Tip Fakultes /ID# 1116-0608

Yenimahalle, Ankara, Turkey (Türkiye)

Site Status

Ankara Universitesi Tip Fakultesi Ibn-i Sina /ID# 1116-0606

Ankara, , Turkey (Türkiye)

Site Status

Ic Hastaliklari Anabilim Dali/Ege University Medical Faculty /ID# 1116-0714

Izmir, , Turkey (Türkiye)

Site Status

Dokuz Eylul University Medical Faculty /ID# 1116-0601

Izmir, , Turkey (Türkiye)

Site Status

Erciyes Universiitesi Tip Fakultesi /ID# 1116-0602

Kayseri, , Turkey (Türkiye)

Site Status

CNE Vinnytsya Regional Clinical Hospital named after N.I.Pirogov /ID# 1116-0595

Vinnytsia, Vinnytsia Oblast, Ukraine

Site Status

Communal Nonprofit Enterprise Cherkasy Regional Oncology Dispensary /ID# 1116-0597

Cherkasy, , Ukraine

Site Status

Municipal Non-Profit Enterprise City Clinical Hospital 4 of Dnipro City Council /ID# 1116-0594

Dnipro, , Ukraine

Site Status

SI Institute of Blood Pathology and Transfusion Medicine of NAMS of Ukraine /ID# 1116-0596

Lviv, , Ukraine

Site Status

University Hospitals Dorset NHS Foundation Trust /ID# 1116-0551

Poole, Dorset, United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust /ID# 1116-0367

Southampton, Hampshire, United Kingdom

Site Status

Nottingham University Hospitals NHS Trust /ID# 1116-0548

Nottingham, Nottinghamshire, United Kingdom

Site Status

Oxford University Hospitals NHS Foundation Trust /ID# 1116-0668

Oxford, Oxfordshire, United Kingdom

Site Status

Cardiff & Vale University Health Board /ID# 1116-0607

Cardiff, Wales, United Kingdom

Site Status

East Suffolk and North Essex NHS Foundation Trust /ID# 1116-0549

Colchester, , United Kingdom

Site Status

Leeds Teaching Hospitals NHS Trust /ID# 1116-0550

Leeds, , United Kingdom

Site Status

King's College Hospital NHS Foundation Trust /ID# 1116-0544

London, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada China Czechia Ireland Israel Italy New Zealand Poland Russia Spain Turkey (Türkiye) Ukraine United Kingdom

References

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Burger JA, Barr PM, Robak T, Owen C, Tedeschi A, Sarma A, Patten PEM, Grosicki S, McCarthy H, Offner F, Szafer-Glusman E, Zhou C, Szoke A, Neumayr L, Dean JP, Ghia P, Kipps TJ. Final analysis of the RESONATE-2 study: up to 10 years of follow-up of first-line ibrutinib treatment for CLL/SLL. Blood. 2025 Oct 30;146(18):2168-2176. doi: 10.1182/blood.2024028205.

Reference Type DERIVED
PMID: 40737596 (View on PubMed)

Barr PM, Owen C, Robak T, Tedeschi A, Bairey O, Burger JA, Hillmen P, Dearden C, Grosicki S, McCarthy H, Li JY, Offner F, Moreno C, Jermain M, Zhou C, Hsu E, Szoke A, Kipps TJ, Ghia P. Many People With Chronic Lymphocytic Leukemia or Small Lymphocytic Lymphoma Benefit From Ibrutinib Treatment Up To 8 Years: A Plain Language Summary. Future Oncol. 2023 Jan 9. doi: 10.2217/fon-2022-0898. Online ahead of print.

Reference Type DERIVED
PMID: 36617990 (View on PubMed)

Barr PM, Owen C, Robak T, Tedeschi A, Bairey O, Burger JA, Hillmen P, Coutre SE, Dearden C, Grosicki S, McCarthy H, Li JY, Offner F, Moreno C, Zhou C, Hsu E, Szoke A, Kipps TJ, Ghia P. Up to 8-year follow-up from RESONATE-2: first-line ibrutinib treatment for patients with chronic lymphocytic leukemia. Blood Adv. 2022 Jun 14;6(11):3440-3450. doi: 10.1182/bloodadvances.2021006434.

Reference Type DERIVED
PMID: 35377947 (View on PubMed)

Coutre SE, Byrd JC, Hillmen P, Barrientos JC, Barr PM, Devereux S, Robak T, Kipps TJ, Schuh A, Moreno C, Furman RR, Burger JA, O'Dwyer M, Ghia P, Valentino R, Chang S, Dean JP, James DF, O'Brien SM. Long-term safety of single-agent ibrutinib in patients with chronic lymphocytic leukemia in 3 pivotal studies. Blood Adv. 2019 Jun 25;3(12):1799-1807. doi: 10.1182/bloodadvances.2018028761.

Reference Type DERIVED
PMID: 31196847 (View on PubMed)

Barr PM, Robak T, Owen C, Tedeschi A, Bairey O, Bartlett NL, Burger JA, Hillmen P, Coutre S, Devereux S, Grosicki S, McCarthy H, Li J, Simpson D, Offner F, Moreno C, Zhou C, Styles L, James D, Kipps TJ, Ghia P. Sustained efficacy and detailed clinical follow-up of first-line ibrutinib treatment in older patients with chronic lymphocytic leukemia: extended phase 3 results from RESONATE-2. Haematologica. 2018 Sep;103(9):1502-1510. doi: 10.3324/haematol.2018.192328. Epub 2018 Jun 7.

Reference Type DERIVED
PMID: 29880603 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2012-003968-44

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

PCYC-1116-CA

Identifier Type: -

Identifier Source: org_study_id

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