A Study To Evaluate Safety And Efficacy Of IV Sildenafil In The Treatment Of Neonates With Persistent Pulmonary Hypertension Of The Newborn

NCT ID: NCT01720524

Last Updated: 2021-08-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

59 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-05

Study Completion Date

2020-09-28

Brief Summary

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This study will evaluate whether IV sildenafil can reduce the time on inhaled nitric oxide treatment and reduce the failure rate of available treatments for persistent pulmonary hypertension of the newborn.

Detailed Description

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Conditions

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Pulmonary Hypertension, Familial Persistent, of the Newborn

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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placebo

iv placebo of normal saline or 10% dextrose

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type DRUG

IV placebo or 0.9% sodium chloride or 10% dextrose. Infusion rate based on weight.

sildenafil

Active study drug

Group Type EXPERIMENTAL

iv sildenafil

Intervention Type DRUG

loading dose of 0.1 mg/kg over 30 minutes followed by maintenance dose of 0.03 mg/kg/h. To infuse minimum 48 hours and maximum of 14 days.

Interventions

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placebo

IV placebo or 0.9% sodium chloride or 10% dextrose. Infusion rate based on weight.

Intervention Type DRUG

iv sildenafil

loading dose of 0.1 mg/kg over 30 minutes followed by maintenance dose of 0.03 mg/kg/h. To infuse minimum 48 hours and maximum of 14 days.

Intervention Type DRUG

Other Intervention Names

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revatio

Eligibility Criteria

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Inclusion Criteria

* Neonates with persistent pulmonary hypertension of the newborn
* Age \<=96 hours and \>=34 weeks gestational age
* Oxygenation Index \>15 and \<60
* Concurrent treatment with inhaled nitric oxide and \>=50% oxygen

Exclusion Criteria

* Prior or immediate need for extracorporeal membrane oxygenation or cardiopulmonary resuscitation
* Expected duration of mechanical ventilation \<48 hours
* Profound hypoxemia
* Life-threatening or lethal congenital anomaly
Minimum Eligible Age

0 Days

Maximum Eligible Age

4 Days

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer's Upjohn has merged with Mylan to form Viatris Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Arkansas Children's Hospital

Little Rock, Arkansas, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

Site Status

University of California Davis

Sacramento, California, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

Site Status

Children´s National Medical Center

Washington D.C., District of Columbia, United States

Site Status

Indiana University Health Methodist Hospital

Indianapolis, Indiana, United States

Site Status

Riley Hospital for Children at IU Health

Indianapolis, Indiana, United States

Site Status

Sydney and Lois Eskenazi Hospital

Indianapolis, Indiana, United States

Site Status

Children's Mercy Hospitals & Clinics

Kansas City, Missouri, United States

Site Status

Duke University Medical Center (DUMC)

Durham, North Carolina, United States

Site Status

Fairview Hospital

Cleveland, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

OU Follow-Up Program, PREMIEr Clinic, Children's Hospital

Oklahoma City, Oklahoma, United States

Site Status

OU Neonatal Intensive Care Unit at Children's Hospital

Oklahoma City, Oklahoma, United States

Site Status

The University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status

Henry Zarrow Neonatal Intensive Care Unit, Children's Hospital at Saint Francis

Tulsa, Oklahoma, United States

Site Status

Warren Cancer Research Foundation

Tulsa, Oklahoma, United States

Site Status

Vanderbilt Children's Hospital

Nashville, Tennessee, United States

Site Status

Seattle Children's Research Institute

Seattle, Washington, United States

Site Status

Seattle Childrens Hospital

Seattle, Washington, United States

Site Status

Universitair Ziekenhuis Antwerpen

Edegem, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

Site Status

CHUL du CHU de Quebec

Québec, Quebec, Canada

Site Status

Aarhus Universitetshospital, Skejby

Aarhus N, , Denmark

Site Status

Neonatalklinikken Rigshospitalet, 5024

Copenhagen Ø, , Denmark

Site Status

Centre Hospitalier et Regional de Lille - Hopital Jeanne de Flandre

Lille, , France

Site Status

Centre Hospitalier et Régional de Lille,

Lille, , France

Site Status

Hôpital de la Conception Assistance Publique-Hôpitaux de Marseille

Marseille, , France

Site Status

CHU Robert Debré

Paris, , France

Site Status

Hopital NECKER - Enfants Malades

Paris, , France

Site Status

University Hospital of Leipzig

Leipzig, , Germany

Site Status

Neonatologia Fondazione IRCCS Policlinico San Matteo

Pavia, , Italy

Site Status

Radboud University Nijmegen Medical Centre

Nijmegen, , Netherlands

Site Status

Erasmus MC, Sophia Children's hospital

Rotterdam, , Netherlands

Site Status

Haukeland University Hospital

Bergen, Haukeland, Norway

Site Status

Hospital Sant Joan de Deu

Esplugues de Llobregat, Barcelona / Spain, Spain

Site Status

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status

Karolinska University Hospital

Stockholm, , Sweden

Site Status

St. Michael's Hospital

Bristol, , United Kingdom

Site Status

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status

Glenfield Hospital, University Hospitals of Leicester NHS Trust

Leicester, , United Kingdom

Site Status

Great Ormond Street Hospital NHS Foundation Trust

London, , United Kingdom

Site Status

Countries

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United States Belgium Canada Denmark France Germany Italy Netherlands Norway Spain Sweden United Kingdom

References

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Pierce CM, Zhang MH, Jonsson B, Iorga D, Cheruvu N, Balagtas CC, Steinhorn RH. Efficacy and Safety of IV Sildenafil in the Treatment of Newborn Infants with, or at Risk of, Persistent Pulmonary Hypertension of the Newborn (PPHN): A Multicenter, Randomized, Placebo-Controlled Trial. J Pediatr. 2021 Oct;237:154-161.e3. doi: 10.1016/j.jpeds.2021.05.051. Epub 2021 May 27.

Reference Type DERIVED
PMID: 34052232 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan: Redacted SAP Part A of study

View Document

Document Type: Statistical Analysis Plan: Redacted SAP Part B of Study

View Document

Related Links

Other Identifiers

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2012-002619-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

A1481316

Identifier Type: -

Identifier Source: org_study_id

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