Clinical Study to Evaluate the Efficacy and Safety of VR506 Using a New Inhaler for the Treatment of Asthma

NCT ID: NCT01720069

Last Updated: 2020-04-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

197 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-10-31

Study Completion Date

2013-10-31

Brief Summary

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To evaluate the clinical efficacy, safety, tolerability and dose-response relationship, using oral corticosteroid (OCS) modulation, of 3 different doses of VR506 using a twice daily regimen from a new dry powder inhaler (nDPI) for 16 weeks in subjects with severe persistent asthma requiring OCS therapy, i.e. Step 5 treatment as defined by modified Global Initiative for Asthma (GINA) guidelines 2011.

Detailed Description

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Conditions

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Asthma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Dose 1 VR506

VR506 inhalation powder delivered via a new dry powder inhaler device

Group Type ACTIVE_COMPARATOR

VR506

Intervention Type DRUG

VR506 inhalation powder delivered via a new dry powder inhaler device

Dose 2 VR506

VR506 inhalation powder delivered via a new dry powder inhaler device

Group Type ACTIVE_COMPARATOR

VR506

Intervention Type DRUG

VR506 inhalation powder delivered via a new dry powder inhaler device

Dose 3 VR506

VR506 inhalation powder delivered via a new dry powder inhaler device

Group Type ACTIVE_COMPARATOR

VR506

Intervention Type DRUG

VR506 inhalation powder delivered via a new dry powder inhaler device

Interventions

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VR506

VR506 inhalation powder delivered via a new dry powder inhaler device

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Written informed consent
* Adolescents aged 12-17 years \& adults aged 18-65 years (both inclusive)
* Documented clinical history of severe asthma requiring prednisone/prednisolone therapy, high-intensity treatment ICS, OCS, LABA
* Stable OCS dose for ≥7 days before Screening Visit \& during Screening Period.
* At least 80% compliant w/regular asthma medication per investigator at end of Screening Period
* Documented asthma reversibility within 5 yrs prior to/during Screening Period, or diagnosis of asthma that is incontrovertible per investigator
* Ability to use nDPI correctly, per investigator's review of completed inhaler operation checklist
* Ability to use eDiary correctly, assessed by investigator at end of Screening Period
* Ability to comply w/study procedures, including blood sampling
* Ability to perform technically satisfactory pulmonary function tests
* Available to complete all study visits before 12 noon
* BMI of 16-26 kg/m2 in adolescents and 18-32 kg/m2 in adults
* Oral PIF ≥40 L/min, using an appropriate device set to match resistance of inhaler
* Good health, except for presence of asthma, per medical history/physical examination
* Negative drug/alcohol/urine cotinine screen. Subjects must test negative for amphetamines, barbiturates, benzodiazepines, cannabinoids, cocaine, cotinine, ethanol \& opiates (unless given as prescription medicine)
* Non-smokers or ex-smokers with a smoking history of less than 10 pack-yrs (e.g. \<20 cigarettes per day for 10 years or \<40 cigarettes per day for 5 years) \& stopped smoking for at least 1 year prior to Screening Visit. Smoking will not be permitted throughout study
* Female subjects of child-bearing potential must be using medically acceptable forms of contraception \[abstinence, hormonal (oral/implant/transdermal/injection), in use for ≥3 consecutive months before first dose of study medication, double barrier (condom w/spermicide, or diaphragm w/spermicide), IUD, or vasectomised partner (≥6 months since vasectomy)\].

Exclusion:

* Regular use (≥3 times/wk) of topical steroids to treat dermatitis/rhinitis/allergic conjunctivitis, within 28 days of Screening Visit
* Subjects who have/who have had, an upper/lower respiratory tract infection within 28 days of Screening Visit
* Subjects w/"brittle asthma
* Subjects w/asthma that required admission to an ICU and/or ventilation within previous 12 months
* Subjects whose comorbidities, per investigator's opinion, are major contributors to their respiratory symptoms (e.g. COPD, bronchiectasis, dysfunctional breathlessness, vocal cord dysfunction, gastro-oesophageal reflux)
* Previously/currently diagnosed as having Churg-Strauss syndrome
* Previously/currently diagnosed as having pulmonary eosinophilia
* History of lung cancer
* Subjects w/current diagnosis of HIV infection
* Active chronic hepatitis B or C infection
* Subjects who have clinically significant abnormality/finding from examination, tests, or history that may compromise subject safety, specifically any history of cardiac, renal or hepatic impairment
* Subjects with an abnormal ECG
* Persistent arterial hypotension, with average SBP readings of ≤95 mmHg
* Persistent elevation of blood pressure, with average SBP readings of ≥160 mmHg or average DBP readings of ≥100 mmHg
* Pregnant or lactating females
* Participation in another clinical study in 28 days prior to Screening Visit
* Evidence of clinically significant renal, hepatic, cardiac, pulmonary (apart from asthma) or metabolic dysfunction, e.g. diabetes mellitus, thyrotoxicosis, uncorrectable hypokalaemia, or predisposition to low levels of serum potassium
* Current/history of drug/alcohol abuse/dependence per WHO criteria
* Inability to communicate well w/investigator
* Donation of ≥450 mL of blood/blood products within previous 3 months prior to screening
* History of allergy/intolerance/contraindications to corticosteroids/lactose, or severe allergy to milk proteins
* Consumption of alcohol- or caffeine-containing foods/beverages from midnight before or during Screening Visit
* History of medically diagnosed chronic respiratory diseases other than asthma (e.g. chronic obstructive pulmonary disease, ABPA in the absence of asthma)
Minimum Eligible Age

12 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Vectura Limited

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Vectura Clinical Trial Site 01001

Los Angeles, California, United States

Site Status

Vectura Clinial Trial Site 01005

Denver, Colorado, United States

Site Status

Vectura Clinical Trial Site 01006

Celebration, Florida, United States

Site Status

Vectura Clinical Trial Site 01015

Hialeah, Florida, United States

Site Status

Vectura Clinical Trial Site 01012

Miami Lakes, Florida, United States

Site Status

Vectura Clinical Trial Site 01014

Orlando, Florida, United States

Site Status

Vectura Clinical Trial Site 01003

Tampa, Florida, United States

Site Status

Vectura Clinical Trial Site 01011

St Louis, Missouri, United States

Site Status

Vectura Clinical Trial Site 01013

Jersey City, New Jersey, United States

Site Status

Vectura Clinical Trial Site 01004

The Bronx, New York, United States

Site Status

Vectura Clinical Trial Site 01007

El Paso, Texas, United States

Site Status

Vectura Clinical Trial Site 08006

Rousse, , Bulgaria

Site Status

Vectura Clinical Trial Site 08005

Sofia, , Bulgaria

Site Status

Vectura Clinical Trial Site 08001

Sofia, , Bulgaria

Site Status

Vectura Clinical Trial Site 08003

Sofia, , Bulgaria

Site Status

Vectura Clinical Trial Site 08007

Sofia, , Bulgaria

Site Status

Vectura Clinical Trial Site 08004

Sofia, , Bulgaria

Site Status

Vectura Clinical Trial Site 08002

Stara Zagora, , Bulgaria

Site Status

Vectura Clinical Trial Site 08008

Varna, , Bulgaria

Site Status

Vectura Clinical Trial Site 03006

Berlin, , Germany

Site Status

Vectura Clinical Trial Site 03009

Berlin, , Germany

Site Status

Vectura Clinical Trial Site 03004

Bonn, , Germany

Site Status

Vectura Clinical Trial Site 03008

Donaustauf, , Germany

Site Status

Vectura Clinical Trial Site 03003

Dortmund, , Germany

Site Status

Vectura Clinical Trial Site 03007

Geesthacht, , Germany

Site Status

Vectura Clinical Trial Site 03001

Hamburg, , Germany

Site Status

Vectura Clinical Trial Site 03005

Heidelberg, , Germany

Site Status

Vectura Clinical Trial Site 03002

Rudersdorf, , Germany

Site Status

Vectura Clinical Trial Site 04001

Budapest, , Hungary

Site Status

Vectura Clinical Trial Site 04004

Budapest, , Hungary

Site Status

Vectura Clinical Trial Site 04003

Debrecen, , Hungary

Site Status

Vectura Clinical Trial Site 04002

Rakoczi, , Hungary

Site Status

Vectura Clinical Trial Site 04005

Rakoczi, , Hungary

Site Status

Vectura Clinical Trial Site 05008

Bialystok, , Poland

Site Status

Vectura Clinical Trial Site 05002

Bialystok, , Poland

Site Status

Vectura Clinical Trial Site 05010

Bialystok, , Poland

Site Status

Vectura Clinical Trial Site 05011

Krakow, , Poland

Site Status

Vectura Clinical Trial Site 05001

Lodz, , Poland

Site Status

Vectura Clinical Trial Site 05006

Lodz, , Poland

Site Status

Vectura Clinical Trial Site 05005

Lublin, , Poland

Site Status

Vectura Clinical Trial Site 05007

Tarnów, , Poland

Site Status

Vectura Clinical Trial Site 05003

Warsaw, , Poland

Site Status

Vectura Clinical Trial Site 05009

Wroclaw, , Poland

Site Status

Vectura Clinical Trial Site 05004

Zawadzkie, , Poland

Site Status

Vectura Clinical Trial Site 07001

Brasov, , Romania

Site Status

Vectura Clinical Trial Site 07008

Bucharest, , Romania

Site Status

Vectura Clinical Trial Site 07005

Bucharest, , Romania

Site Status

Vectura Clinical Trial Site 07013

Bucharest, , Romania

Site Status

Vectura Clinical Trial Site 07003

Bucharest, , Romania

Site Status

Vectura Clinical Trial Site 07006

Cluj-Napoca, , Romania

Site Status

Vectura Clinical Trial Site 07007

Cluj-Napoca, , Romania

Site Status

Vectura Clinical Trial Site 07009

Cluj-Napoca, , Romania

Site Status

Vectura Clinical Trial Site 07014

Craiova, , Romania

Site Status

Vectura Clinical Trial Site 07002

Iași, , Romania

Site Status

Vectura Clinical Trial Site 07004

Marghita, , Romania

Site Status

Vectura Clinical Trial Site 07010

Sadu, , Romania

Site Status

Vectura Clinical Trial Site 07012

Târgu Mureş, , Romania

Site Status

Vectura Clinicl Trial Site 07011

Timuș, , Romania

Site Status

Vectura Clinical Trial Site 06013

AR Crimea, , Ukraine

Site Status

Vectura Clinical Trial Site 06009

Donetsk, , Ukraine

Site Status

Vectura Clinical Trial Site 06012

Ivano-Frankivsk, , Ukraine

Site Status

Vectura Clinical Trial Site 06010

Kharkiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06001

Kharkiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06004

Kharkiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06006

Kyiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06002

Kyiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06015

Kyiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06003

Kyviv, , Ukraine

Site Status

Vectura Clinical Trial Site 06008

Mykolaiv, , Ukraine

Site Status

Vectura Clinical Trial Site 06011

Vinnitsa, , Ukraine

Site Status

Vectura Clinical Trial Site 06007

Zaporizhzhia, , Ukraine

Site Status

Vectura Clinical Trial Site 06014

Zaporizhzhya, , Ukraine

Site Status

Vectura Clinical Trial Site 02003

Cottingham, Hull, United Kingdom

Site Status

Vectura Clinical Trial site 02002

Birmingham, , United Kingdom

Site Status

Vectura Clinical Trial Site 02004

Manchester, , United Kingdom

Site Status

Vectura Clinical Trial Site 02001

Newcastle, , United Kingdom

Site Status

Vectura Clinical Trial Site 02005

Nottingham, , United Kingdom

Site Status

Countries

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United States Bulgaria Germany Hungary Poland Romania Ukraine United Kingdom

Other Identifiers

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VR506/2/004

Identifier Type: -

Identifier Source: org_study_id

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