Trial Outcomes & Findings for Metformin as a Chemoprevention Agent in Non-small Cell Lung Cancer (NCT NCT01717482)

NCT ID: NCT01717482

Last Updated: 2020-03-10

Results Overview

To evaluate the feasibility of patient randomization, accrual, and tissue collection in a pilot study of metformin versus observation following resection of stage IA-IIIA lung squamous cell cancer for patients by assessing the reasons patients decline randomization, tracking accrual numbers, and tracking collected tissue and reasons why tissue was not collected.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

6 participants

Primary outcome timeframe

2 years

Results posted on

2020-03-10

Participant Flow

Participant milestones

Participant milestones
Measure
Metformin
Metformin 850mg twice per day Metformin
Observation
Standard of Care Observation Placebo Comparator: Standard of Care Observation
Overall Study
STARTED
4
2
Overall Study
COMPLETED
0
2
Overall Study
NOT COMPLETED
4
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Metformin as a Chemoprevention Agent in Non-small Cell Lung Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Metformin
n=4 Participants
Metformin 850mg twice per day Metformin
Observation
n=2 Participants
Standard of Care Observation Placebo Comparator: Standard of Care Observation
Total
n=6 Participants
Total of all reporting groups
Age, Continuous
63.25 years
STANDARD_DEVIATION 6.87 • n=5 Participants
62.5 years
STANDARD_DEVIATION 7.5 • n=7 Participants
63 years
STANDARD_DEVIATION 7.09 • n=5 Participants
Sex: Female, Male
Female
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Sex: Female, Male
Male
2 Participants
n=5 Participants
2 Participants
n=7 Participants
4 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
4 Participants
n=5 Participants
2 Participants
n=7 Participants
6 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
4 participants
n=5 Participants
2 participants
n=7 Participants
6 participants
n=5 Participants

PRIMARY outcome

Timeframe: 2 years

Population: Study terminated due to poor accrual and funding ended

To evaluate the feasibility of patient randomization, accrual, and tissue collection in a pilot study of metformin versus observation following resection of stage IA-IIIA lung squamous cell cancer for patients by assessing the reasons patients decline randomization, tracking accrual numbers, and tracking collected tissue and reasons why tissue was not collected.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: 4 years

Population: Study terminated due to poor accrual and funding ended

To compare the 2-year recurrence free survival (RFS) rate between metformin and observation.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 4 years

Population: Study terminated due to poor accrual and funding ended

To develop the metformin sensitivity index based on iPS cell line metformin sensitivity measurements from the first 20 patients randomized to the metformin arm. We will then To apply the metformin sensitivity index on the remaining 25 patients randomized to metformin and the 45 observation patients (70 patients total) to compare the 2-year RFS rate between metformin-sensitive and metformin-not-sensitive patients.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 4 years

Population: Study terminated due to poor accrual and funding ended

To compare participant adverse events between metformin and observation arms using CTCAE version 4.

Outcome measures

Outcome data not reported

Adverse Events

Metformin

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Observation

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Metformin
n=4 participants at risk
Metformin 850mg twice per day Metformin
Observation
n=2 participants at risk
Standard of Care Observation Placebo Comparator: Standard of Care Observation
General disorders
Nausea
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
Gastrointestinal disorders
Constipation
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
General disorders
Dizziness
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
General disorders
Back Pain
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
General disorders
Abdominal Pain
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
Respiratory, thoracic and mediastinal disorders
Pleual Effusion
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
General disorders
Stomach pain
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period
Gastrointestinal disorders
Bloating
25.0%
1/4 • Number of events 1 • Adverse Events were collected over a 24 months time period
0.00%
0/2 • Adverse Events were collected over a 24 months time period

Additional Information

Dennis Wigle, M.D., Ph.D.

Mayo Clinic

Phone: 507-284-8462

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place