Rituximab Trial for Pediatric Nephrotic Syndrome

NCT ID: NCT01716442

Last Updated: 2012-10-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2/PHASE3

Total Enrollment

88 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-08-31

Study Completion Date

2013-11-30

Brief Summary

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Anti-CD20 agent has been proposed as a rescue therapy for refractory nephrotic syndrome(NS) on the basis of favorable clinical observations. Yet the long-term effect on maintaining remission or the likelihood of becoming rituximab-dependent is unclear and the information on the safety profile of rituximab is limited. This trial was designed to investigate the safety and efficacy of Rituximab in children with refractory NS.

Detailed Description

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Conditions

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Steroid Resistant Nephrotic Syndrome Steroid Dependent Nephrotic Syndrome

Keywords

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rituximab nephrotic refractory

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants

Study Groups

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steroid-resistant

Steroid-resistant group: n=27 , enroll all for treatment

Group Type ACTIVE_COMPARATOR

Rituximab

Intervention Type DRUG

Per dose: Rituximab 375 mg/m2 (max.500mg/day). efficacy monitored by CD19 cell count. If CD19 cells are not depleted, second or third doses are given at 2-3 weeks interval.

steroid-dependent-rituximab

steroid-responsive group: n=38

Group Type ACTIVE_COMPARATOR

Rituximab

Intervention Type DRUG

Per dose: Rituximab 375 mg/m2 (max.500mg/day). efficacy monitored by CD19 cell count. If CD19 cells are not depleted, second or third doses are given at 2-3 weeks interval.

steroid-dependent-placebo

steroid-responsive group: n=23

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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Rituximab

Per dose: Rituximab 375 mg/m2 (max.500mg/day). efficacy monitored by CD19 cell count. If CD19 cells are not depleted, second or third doses are given at 2-3 weeks interval.

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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Mabthera 2005110300291 (rituximab)

Eligibility Criteria

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Inclusion Criteria

(A)steroid/calcineurin inhibitor resistant nephrotic syndrome

1. steroid resistance: no remission after 4 weeks of daily oral corticosteroid (60mg/m2/day)
2. calcineurin inhibitor resistance: no remission after 3 months of therapeutic dose administration of cyclosporine and/or tacrolimus
3. no remission defined by persistent proteinuria of nephrotic range for the last 3 months
4. post-transplant patients were included in the study

(B)steroid-dependent nephrotic syndrome

1. Steroid-dependent patients who had been on various known medications (such as corticosteroids, cyclophosphamide, chlorambucil, calcineurin inhibitors, levamisole ..) continuously for more than 2 years
2. definition of dependency: more than two consecutive relapse events in 2 weeks after discontinuation of steroid or calcineurin inhibitor

* no improvement in relapsing frequency with calcineurin inhibitor use
* unable to continue with calcineurin inhibitor due to side effects
* unable to continue with calcineurin inhibitor due to prolonged use (over 2 years)
* other conditions in which the clinician considers difficult to control disease with steroids or calcineurin inhibitors only.

Exclusion Criteria

* previous rituximab use
* secondary nephrotic syndrome
* estimated GFR \<60mL/min/1.73m2 or under 50% of age-matched standard GFR
* chronic or acute active infection (e.g. hepatitis B,C, herpes, varicella zoster)
* prior live vaccine inoculation within 1 month (from the study enrollment)
* cardiovascular diseases, pulmonary or pleural diseases
* uncontrolled hypertension
* leukocytopenia (absolute neutrophil count \<1500/mm3) or thrombocytopenia (\<75000/mm3)
* pregnancy
Minimum Eligible Age

1 Year

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Seoul National University Childrens Hospital

OTHER

Sponsor Role lead

Responsible Party

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Hee Gyung Kang

Associate Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Hee Gyung Kang A. Kang, M.D., Ph.D.

Role: PRINCIPAL_INVESTIGATOR

Seoul National University Children's Hospital

Locations

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Seoul National University Children's Hospital

Seoul, , South Korea

Site Status RECRUITING

Countries

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South Korea

Central Contacts

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Hee Gyung A. Kang, M.D., Ph.D.

Role: CONTACT

Phone: +82-2072-0658

Email: [email protected]

References

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Liu ID, Willis NS, Craig JC, Hodson EM. Interventions for idiopathic steroid-resistant nephrotic syndrome in children. Cochrane Database Syst Rev. 2025 May 8;5(5):CD003594. doi: 10.1002/14651858.CD003594.pub7.

Reference Type DERIVED
PMID: 40337980 (View on PubMed)

Larkins NG, Hahn D, Liu ID, Willis NS, Craig JC, Hodson EM. Non-corticosteroid immunosuppressive medications for steroid-sensitive nephrotic syndrome in children. Cochrane Database Syst Rev. 2024 Nov 8;11(11):CD002290. doi: 10.1002/14651858.CD002290.pub6.

Reference Type DERIVED
PMID: 39513526 (View on PubMed)

Other Identifiers

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RTX-2012

Identifier Type: -

Identifier Source: org_study_id