Trial Outcomes & Findings for Gulf War Illness Nasal Irrigation Study (NCT NCT01700725)

NCT ID: NCT01700725

Last Updated: 2019-05-21

Results Overview

Sino-Nasal Outcome Test (SNOT-20) is a recommended tool for clinical trial research involving CRS. Sinus disease specific quality of life will be measured using the total score of this validated 20 item questionnaire. It is a reliable and valid outcome measure for patients with CRS (Cronbach's α 0.9, test-retest r = 0.9) that describes the health burden and is sensitive to clinical change. Patients who are more affected by CRS tend to have greater SNOT-20 scores (P \< 0.01). The SNOT-20 score is expected to improve in NI-treated subjects compared to controls. Findings of the PI's prior RCT of adults with CRS are consistent with the above evidence. The total range of possible scores is 0-100. The higher the score, the worse the symptoms.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

40 participants

Primary outcome timeframe

Change from baseline week 8, change from baseline week 26

Results posted on

2019-05-21

Participant Flow

Participant milestones

Participant milestones
Measure
Nasal Irrigation - Xylitol
Nasal Irrigation with Xylitol plus routine care for symptoms of CRS and fatigue
Nasal Irrigation - Saline
Nasal irrigation using saline plus routine care for symptoms of CRS and fatigue
Control Group
Control group subjects continue to use routine care only
Overall Study
STARTED
14
14
12
Overall Study
COMPLETED
14
14
12
Overall Study
NOT COMPLETED
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Gulf War Illness Nasal Irrigation Study

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Nasal Irrigation - Xylitol
n=14 Participants
Nasal Irrigation with Xylitol plus routine care for symptoms of CRS and fatigue
Nasal Irrigation - Saline
n=14 Participants
Nasal irrigation using saline plus routine care for symptoms of CRS and fatigue
Control Group
n=12 Participants
Control group subjects continue to use routine care only
Total
n=40 Participants
Total of all reporting groups
Age, Continuous
53.7 years
STANDARD_DEVIATION 9.2 • n=5 Participants
52.7 years
STANDARD_DEVIATION 6.7 • n=7 Participants
55.0 years
STANDARD_DEVIATION 7.7 • n=5 Participants
53.8 years
STANDARD_DEVIATION 7.8 • n=4 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
1 Participants
n=7 Participants
3 Participants
n=5 Participants
8 Participants
n=4 Participants
Sex: Female, Male
Male
10 Participants
n=5 Participants
13 Participants
n=7 Participants
9 Participants
n=5 Participants
32 Participants
n=4 Participants
Race/Ethnicity, Customized
Non-Hispanic White
12 Participants
n=5 Participants
8 Participants
n=7 Participants
11 Participants
n=5 Participants
31 Participants
n=4 Participants
Race/Ethnicity, Customized
White Hispanic
1 Participants
n=5 Participants
2 Participants
n=7 Participants
1 Participants
n=5 Participants
4 Participants
n=4 Participants
Race/Ethnicity, Customized
African American
1 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
2 Participants
n=4 Participants
Race/Ethnicity, Customized
Asian
0 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
Race/Ethnicity, Customized
Pacific Islander / Hawaiian
0 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
Race/Ethnicity, Customized
Multiple Races
0 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
Region of Enrollment
United States
14 participants
n=5 Participants
14 participants
n=7 Participants
12 participants
n=5 Participants
40 participants
n=4 Participants
Education
Highschool or Less
1 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
3 Participants
n=4 Participants
Education
Some College
8 Participants
n=5 Participants
8 Participants
n=7 Participants
4 Participants
n=5 Participants
20 Participants
n=4 Participants
Education
College Graduate
5 Participants
n=5 Participants
5 Participants
n=7 Participants
7 Participants
n=5 Participants
17 Participants
n=4 Participants
Sinusitis Symptoms
20.5 years
STANDARD_DEVIATION 7.8 • n=5 Participants
16.4 years
STANDARD_DEVIATION 9.9 • n=7 Participants
22.4 years
STANDARD_DEVIATION 2.3 • n=5 Participants
19.8 years
STANDARD_DEVIATION 7.7 • n=4 Participants
Fatigue
19.3 years
STANDARD_DEVIATION 8.4 • n=5 Participants
19.9 years
STANDARD_DEVIATION 6.0 • n=7 Participants
23.8 years
STANDARD_DEVIATION 3.1 • n=5 Participants
20.7 years
STANDARD_DEVIATION 6.6 • n=4 Participants
SNOT-20
50.8 units on a scale
STANDARD_DEVIATION 14.7 • n=5 Participants
47.6 units on a scale
STANDARD_DEVIATION 13.7 • n=7 Participants
47.2 units on a scale
STANDARD_DEVIATION 8.7 • n=5 Participants
48.5 units on a scale
STANDARD_DEVIATION 12.7 • n=4 Participants
SF-36
51.1 units on a scale
STANDARD_DEVIATION 15.8 • n=5 Participants
59.0 units on a scale
STANDARD_DEVIATION 17.6 • n=7 Participants
62.7 units on a scale
STANDARD_DEVIATION 14.1 • n=5 Participants
57.3 units on a scale
STANDARD_DEVIATION 16.3 • n=4 Participants
MFI
59.4 units on a scale
STANDARD_DEVIATION 5.4 • n=5 Participants
60.5 units on a scale
STANDARD_DEVIATION 6.0 • n=7 Participants
61.7 units on a scale
STANDARD_DEVIATION 4.7 • n=5 Participants
60.4 units on a scale
STANDARD_DEVIATION 5.3 • n=4 Participants

PRIMARY outcome

Timeframe: Change from baseline week 8, change from baseline week 26

Population: Data from one participant in the control group and two participants in the Saline group at 26 weeks was unable to be collected.

Sino-Nasal Outcome Test (SNOT-20) is a recommended tool for clinical trial research involving CRS. Sinus disease specific quality of life will be measured using the total score of this validated 20 item questionnaire. It is a reliable and valid outcome measure for patients with CRS (Cronbach's α 0.9, test-retest r = 0.9) that describes the health burden and is sensitive to clinical change. Patients who are more affected by CRS tend to have greater SNOT-20 scores (P \< 0.01). The SNOT-20 score is expected to improve in NI-treated subjects compared to controls. Findings of the PI's prior RCT of adults with CRS are consistent with the above evidence. The total range of possible scores is 0-100. The higher the score, the worse the symptoms.

Outcome measures

Outcome measures
Measure
Nasal Irrigation - Xylitol
n=14 Participants
Nasal Irrigation with Xylitol plus routine care for symptoms of CRS and fatigue
Nasal Irrigation - Saline
n=14 Participants
Nasal irrigation using saline plus routine care for symptoms of CRS and fatigue
Control Group
n=12 Participants
Control group subjects continue to use routine care only
Change in Sino-Nasal Outcome Test (SNOT-20) Score From Baseline
Baseline to Week 8
-16.9 score on a scale
Standard Deviation 4.9
-8.8 score on a scale
Standard Deviation 5.0
-3.4 score on a scale
Standard Deviation 5.3
Change in Sino-Nasal Outcome Test (SNOT-20) Score From Baseline
Baseline to Week 26
-18.9 score on a scale
Standard Deviation 4.9
-16.9 score on a scale
Standard Deviation 5.3
-3.5 score on a scale
Standard Deviation 5.6

SECONDARY outcome

Timeframe: Baseline to weeks 8 & 26

Population: Data from several participants was unable to be collected at various timepoints.

The Multidimensional Fatigue Inventory is a validated disease specific outcome measure for fatigue. The instrument has good internal consistency (average Cronbach's alpha 0.84). Construct validity was established after comparisons between and within groups, assuming differences in fatigue based on differences in circumstances and/or activity level. Convergent validity was investigated by correlating the MFI-scales with a Visual Analogue Scale measuring fatigue. Fatigue is expected to improve in the NI-treated patients compared to controls. The total range of possible scores is 0-100. The higher the score, the more fatigue.

Outcome measures

Outcome measures
Measure
Nasal Irrigation - Xylitol
n=12 Participants
Nasal Irrigation with Xylitol plus routine care for symptoms of CRS and fatigue
Nasal Irrigation - Saline
n=14 Participants
Nasal irrigation using saline plus routine care for symptoms of CRS and fatigue
Control Group
n=12 Participants
Control group subjects continue to use routine care only
Change in Multidimensional Fatigue Inventory (MFI) Over Baseline
Baseline to Week 8
0.6 score on a scale
Standard Deviation 2.4
0.9 score on a scale
Standard Deviation 2.3
0.5 score on a scale
Standard Deviation 2.5
Change in Multidimensional Fatigue Inventory (MFI) Over Baseline
Baseline to Week 26
1.9 score on a scale
Standard Deviation 2.8
-1.4 score on a scale
Standard Deviation 2.4
10.4 score on a scale
Standard Deviation 3.0

SECONDARY outcome

Timeframe: Baseline and weeks 8 & 26

Population: Data from one participant at 26 weeks in the control group was unable to be collected.

SF-36 is a validated questionnaire designed to assess health status, function and overall health related quality of life. The SF-36 includes one multi-item scale that assesses eight health concepts: 1) limitations in physical activities because of health problems; 2) limitations in social activities because of physical or emotional problems; 3) limitations in usual role activities because of physical health problems; 4) bodily pain; 5) general mental health (psychological distress and well-being); 6) limitations in usual role activities because of emotional problems; 7) vitality (energy and fatigue); and 8) general health perceptions. Gulf War Illness and chronic rhinosinusitis both affect sleep and breathing parameters. Prior studies suggest that both may be improved with SNI in some subjects. Eighteen relevant sleep and breathing related questions to the SF-36. The total range is 0-100. The lower the score, the more disability.

Outcome measures

Outcome measures
Measure
Nasal Irrigation - Xylitol
n=14 Participants
Nasal Irrigation with Xylitol plus routine care for symptoms of CRS and fatigue
Nasal Irrigation - Saline
n=14 Participants
Nasal irrigation using saline plus routine care for symptoms of CRS and fatigue
Control Group
n=12 Participants
Control group subjects continue to use routine care only
Change in Medical Outcomes Survey Short Form-36 (SF-36) Over Baseline
Baseline to Week 8
1.1 score on a scale
Standard Deviation 3.5
3.9 score on a scale
Standard Deviation 3.6
-0.1 score on a scale
Standard Deviation 3.8
Change in Medical Outcomes Survey Short Form-36 (SF-36) Over Baseline
Baseline to Week 26
6.4 score on a scale
Standard Deviation 3.5
7.3 score on a scale
Standard Deviation 3.6
2.0 score on a scale
Standard Deviation 4.0

Adverse Events

Nasal Irrigation - Xylitol

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Nasal Irrigation - Saline

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Control Group

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

David Rabago, MD

University of Wisconsin - Madison

Phone: 608-843-0850

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place