Trial Outcomes & Findings for Subcutaneous (SC) Bortezomib-Regimens for Patients With RR MM Failing Prior IV Bortezomib-Containing Regimens (NCT NCT01695330)

NCT ID: NCT01695330

Last Updated: 2017-01-16

Results Overview

Definition of incidence: the number of participants enrolled in the study experiencing treatment-emergent peripheral neuropathy. Emergence of peripheral neuropathy is determined via neurological assessment conducted on Day 1 and Day 11 of each treatment cycle as well as during the End of Study visit. Definition of severity: the severity of any treatment-emergent peripheral neuropathy experienced by a patient on-study. Peripheral neuropathy severity is determined via neurological assessment conducted on Day 1 and Day 11 of each treatment cycle as well as the End of Study visit and is graded on a 0-4 scale based on CTCAE criteria. Incidence of Peripheral Neuropathy Definition: the number of participants enrolled in the study experiencing treatment-emergent peripheral neuropathy. Emergence of peripheral neuropathy is determined via neurological assessment conducted on Day 1 and Day 11 of each treatment cycle as well as during the End of Study visit.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

5 participants

Primary outcome timeframe

Subjects eligible for this study will receive treatment with study drug for a maximum of eight 28 day treatment cycles.

Results posted on

2017-01-16

Participant Flow

Patients with MM who received treatment with a SC bortezomib-containing combination

Participant milestones

Participant milestones
Measure
Subcutaneous Bortezomib
patients with MM who received treatment with a SC bortezomib-containing combination. The patients were required to have received a prior IV bortezomib containing combination regimen that differs from the SC bortezomib-containing treatment.
This is one-arm study.
Overall Study
STARTED
52
0
Overall Study
COMPLETED
5
0
Overall Study
NOT COMPLETED
47
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Subcutaneous (SC) Bortezomib-Regimens for Patients With RR MM Failing Prior IV Bortezomib-Containing Regimens

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Subcutaneous Bortezomib
n=5 Participants
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
4 Participants
n=5 Participants
Age, Categorical
>=65 years
1 Participants
n=5 Participants
Age, Continuous
62 years
STANDARD_DEVIATION 5.1 • n=5 Participants
Gender
Female
3 Participants
n=5 Participants
Gender
Male
2 Participants
n=5 Participants
Region of Enrollment
United States
5 participants
n=5 Participants
The patients were required to have received a prior IV bortezomib containing combination regimen tha
5 participants
n=5 Participants

PRIMARY outcome

Timeframe: Subjects eligible for this study will receive treatment with study drug for a maximum of eight 28 day treatment cycles.

Definition of incidence: the number of participants enrolled in the study experiencing treatment-emergent peripheral neuropathy. Emergence of peripheral neuropathy is determined via neurological assessment conducted on Day 1 and Day 11 of each treatment cycle as well as during the End of Study visit. Definition of severity: the severity of any treatment-emergent peripheral neuropathy experienced by a patient on-study. Peripheral neuropathy severity is determined via neurological assessment conducted on Day 1 and Day 11 of each treatment cycle as well as the End of Study visit and is graded on a 0-4 scale based on CTCAE criteria. Incidence of Peripheral Neuropathy Definition: the number of participants enrolled in the study experiencing treatment-emergent peripheral neuropathy. Emergence of peripheral neuropathy is determined via neurological assessment conducted on Day 1 and Day 11 of each treatment cycle as well as during the End of Study visit.

Outcome measures

Outcome measures
Measure
Subcutaneous Bortezomib
n=5 Participants
Patients with MM who received treatment with a SC bortezomib-containing combination
The Primary Objective of This Study Will be to Investigate the Incidence and Severity of Peripheral Neuropathy Caused by a Prior Intravenous VELCADE-containing Regimen in Comparison to That Caused by a Subcutaneous VELCADE-containing Regimen.
5 Participants

SECONDARY outcome

Timeframe: Subjects eligible for this study will receive treatment with study drug for a maximum of eight 28 day treatment cycles.

Compare overall response rate \[combined CR + very good partial response (VGPR) + PR + MR\] and disease parameters \[time to progression, -progression free survival, -time to first response, -duration of response, -overall survival\] following treatment with a SC bortezomib-containing combination regimen for MM patients who have demonstrated progressive disease form a prior or different IV bortezomib-containing combination regimen. Determine incidence and severity of injection-site reactions with CS administration of bortezomib by number of patients with injection site reaction specific adverse events.

Outcome measures

Outcome data not reported

Adverse Events

Subcutaneous Bortezomib

Serious events: 2 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Subcutaneous Bortezomib
n=5 participants at risk
Bortezomib was administered SC at a dose of 1.0 mg/m2. Doses were administered on days 1, 4, 8, and 11 of a 28-day cycle. When administered subcutaneously, sites for each injection (thigh or abdomen) were rotated and reported. All other drugs used in combination with the SC bortezomib were recorded in the Case Report Forms along with their corresponding doses and schedules.
Immune system disorders
Gr3 Neturopenia
40.0%
2/5 • Number of events 2

Other adverse events

Adverse event data not reported

Additional Information

Dr. James Berenson

Oncotherapeutics

Phone: 310-420-9649

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place