Trial Outcomes & Findings for Erlotinib Hydrochloride in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia (NCT NCT01664897)

NCT ID: NCT01664897

Last Updated: 2020-01-07

Results Overview

Overall Response is complete remission (CR) + CR with incomplete hematologic recovery (CRi) + Partial remission (PR) + Hematologic improvement (HI) + Morphologic Leukemia-Free State (MLF). (CR) is Bone marrow; \</=5% blasts, no Auer rods or extramedullary disease and peripheral blood counts \>/= 1.0x10\^9/L Neutrophils, \>/= 100x10\^9/L platelets and no circulating blasts. (CRi), same as CR for bone marrow and \<1.0x10\^9/L neutrophils and \< 100x10\^9/L platelets in peripheral blood counts. PR is all CR criteria if abnormal prior to treatment except \>/= 50%reduction in bone marrow blast but still \> 5%. MLF is \</=5% myeloblasts on bone marrow . HI response must be described by the number of positively affected cell lines..

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

29 participants

Primary outcome timeframe

Up to 3 months post-treatment

Results posted on

2020-01-07

Participant Flow

Recruitment Period: May 2013 to May 2014

Participant milestones

Participant milestones
Measure
Treatment (Erlotinib Hydrochloride)
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Overall Study
STARTED
29
Overall Study
COMPLETED
29
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Erlotinib Hydrochloride in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Treatment (Erlotinib Hydrochloride)
n=29 Participants
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
13 Participants
n=5 Participants
Age, Categorical
>=65 years
16 Participants
n=5 Participants
Age, Continuous
67 years
n=5 Participants
Sex: Female, Male
Female
12 Participants
n=5 Participants
Sex: Female, Male
Male
17 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
3 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
5 Participants
n=5 Participants
Race (NIH/OMB)
White
20 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Region of Enrollment
United States
29 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Up to 3 months post-treatment

Overall Response is complete remission (CR) + CR with incomplete hematologic recovery (CRi) + Partial remission (PR) + Hematologic improvement (HI) + Morphologic Leukemia-Free State (MLF). (CR) is Bone marrow; \</=5% blasts, no Auer rods or extramedullary disease and peripheral blood counts \>/= 1.0x10\^9/L Neutrophils, \>/= 100x10\^9/L platelets and no circulating blasts. (CRi), same as CR for bone marrow and \<1.0x10\^9/L neutrophils and \< 100x10\^9/L platelets in peripheral blood counts. PR is all CR criteria if abnormal prior to treatment except \>/= 50%reduction in bone marrow blast but still \> 5%. MLF is \</=5% myeloblasts on bone marrow . HI response must be described by the number of positively affected cell lines..

Outcome measures

Outcome measures
Measure
Treatment (Erlotinib Hydrochloride)
n=29 Participants
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Participants With a Response
3 Participants

PRIMARY outcome

Timeframe: Up to 30 days

Safety summaries will include tabulations in the form of tables and listings. The number of participants affected by treatment-emergent adverse events will be reported.

Outcome measures

Outcome measures
Measure
Treatment (Erlotinib Hydrochloride)
n=29 Participants
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Incidence of Clinically Significant, Non-hematologic Grade 3 or 4 Toxicities at Least Possibly Related to Erlotinib Hydrochloride
Fatigue
10 Participants
Incidence of Clinically Significant, Non-hematologic Grade 3 or 4 Toxicities at Least Possibly Related to Erlotinib Hydrochloride
Diarrhea
10 Participants
Incidence of Clinically Significant, Non-hematologic Grade 3 or 4 Toxicities at Least Possibly Related to Erlotinib Hydrochloride
Nausea
8 Participants
Incidence of Clinically Significant, Non-hematologic Grade 3 or 4 Toxicities at Least Possibly Related to Erlotinib Hydrochloride
Rash
7 Participants

PRIMARY outcome

Timeframe: Up to 97 weeks

Time from date of treatment start until date of death due to any cause or last Follow-up.

Outcome measures

Outcome measures
Measure
Treatment (Erlotinib Hydrochloride)
n=29 Participants
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Overall Survival
14 Weeks
Interval 2.3 to 96.9

PRIMARY outcome

Timeframe: Up to 21 weeks

Time from date of treatment start until the date of first objective documentation of disease-relapse.

Outcome measures

Outcome measures
Measure
Treatment (Erlotinib Hydrochloride)
n=29 Participants
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Event-free Survival
5 Weeks
Interval 1.7 to 21.0

SECONDARY outcome

Timeframe: Up to 30 days

Population: Samples and data required for the above outcome measure were not done, therefore we cannot report any outcomes for the above outcome measure.

Descriptive statistics will be used to summarize the expression of biomarkers and the concentrations of plasma erlotinib hydrochloride. The Wilcoxon rank sum test will be used to compare the expressions of biomarkers and concentrations of plasma erlotinib hydrochloride between patients with and without response.

Outcome measures

Outcome data not reported

Adverse Events

Treatment (Erlotinib Hydrochloride)

Serious events: 23 serious events
Other events: 29 other events
Deaths: 6 deaths

Serious adverse events

Serious adverse events
Measure
Treatment (Erlotinib Hydrochloride)
n=29 participants at risk
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Blood and lymphatic system disorders
Blood and Lymphatic System disorder - other
3.4%
1/29 • Number of events 1 • 1 year
General disorders
Death
10.3%
3/29 • Number of events 3 • 1 year
Gastrointestinal disorders
Diarrhea
10.3%
3/29 • Number of events 3 • 1 year
Gastrointestinal disorders
Espohageal Ulcer
3.4%
1/29 • Number of events 1 • 1 year
General disorders
Fatigue
10.3%
3/29 • Number of events 3 • 1 year
General disorders
Fever
10.3%
3/29 • Number of events 3 • 1 year
Vascular disorders
Hematoma
3.4%
1/29 • Number of events 1 • 1 year
Metabolism and nutrition disorders
Hyperbilirubinemia
3.4%
1/29 • Number of events 1 • 1 year
Vascular disorders
Hypotension
3.4%
1/29 • Number of events 1 • 1 year
Infections and infestations
Lung Infection
31.0%
9/29 • Number of events 10 • 1 year
Gastrointestinal disorders
Nausea
3.4%
1/29 • Number of events 1 • 1 year
Infections and infestations
Neutropenic Fever
17.2%
5/29 • Number of events 8 • 1 year
Gastrointestinal disorders
Oral Mucositis
3.4%
1/29 • Number of events 1 • 1 year
General disorders
Pain
3.4%
1/29 • Number of events 2 • 1 year
Respiratory, thoracic and mediastinal disorders
Pleuritic Pain
3.4%
1/29 • Number of events 1 • 1 year
Nervous system disorders
Seizure
3.4%
1/29 • Number of events 1 • 1 year
Infections and infestations
Sepsis
10.3%
3/29 • Number of events 4 • 1 year
Skin and subcutaneous tissue disorders
Skin Infection
3.4%
1/29 • Number of events 1 • 1 year
Vascular disorders
Thromboembolic Event
3.4%
1/29 • Number of events 1 • 1 year
Metabolism and nutrition disorders
Tumor Lysis Syndrome
3.4%
1/29 • Number of events 1 • 1 year

Other adverse events

Other adverse events
Measure
Treatment (Erlotinib Hydrochloride)
n=29 participants at risk
Patients receive erlotinib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. Erlotinib Hydrochloride: Given PO Laboratory Biomarker Analysis: Correlative studies
Infections and infestations
Pneumonia
48.3%
14/29 • Number of events 14 • 1 year
Infections and infestations
Neutropenic Fever
44.8%
13/29 • Number of events 13 • 1 year
Respiratory, thoracic and mediastinal disorders
Shortness of breath
37.9%
11/29 • Number of events 11 • 1 year
General disorders
Fatigue
34.5%
10/29 • Number of events 10 • 1 year
Gastrointestinal disorders
Diarrhea
34.5%
10/29 • Number of events 10 • 1 year
Gastrointestinal disorders
Nausea
27.6%
8/29 • Number of events 8 • 1 year
Skin and subcutaneous tissue disorders
Rash
24.1%
7/29 • Number of events 7 • 1 year
General disorders
Edema
17.2%
5/29 • Number of events 5 • 1 year
Musculoskeletal and connective tissue disorders
Muscle Aches
17.2%
5/29 • Number of events 5 • 1 year
Eye disorders
Watery eyes
17.2%
5/29 • Number of events 5 • 1 year
Nervous system disorders
Dizziness
13.8%
4/29 • Number of events 4 • 1 year

Additional Information

Jorge Cortes MD./Professor

The University of Texas MD Anderson Cancer Center

Phone: 713-794-5783

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place