Phase 2b Multicenter, Randomized, Double-Blind, Placebo- and Active-Controlled, Parallel-Group Study to Assess the PD Response and Safety of Three Dose Levels of (PB1023) Injection Following 20 Weeks of Weekly SC Dosing in Adults With T2DM

NCT ID: NCT01658501

Last Updated: 2015-12-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

593 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-07-31

Study Completion Date

2013-07-31

Brief Summary

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Primary objective:

The primary objective of this study is to define the dose response of Glymera as measured as the change from baseline in hemoglobin A1c (HbA1c) following 20 weeks of once-weekly dosing.

Secondary objectives:

The secondary objectives are to:

* Describe incidence, severity, and duration of reported gastrointestinal side effects of Glymera compared to active comparator;
* Compare change from baseline in HbA1c following 20 weeks of dosing compared to placebo and active comparator;
* Compare change from baseline in fasting plasma glucose (FPG) following 20 weeks of dosing compared to placebo and active comparator;
* Describe the frequencies of adverse events in the treatment groups; and
* Describe the above endpoints for the following subgroups of subjects according to baseline type 2 diabetes mellitus (T2DM) therapy: diet and exercise only, metformin only, sulfonylurea only, or metformin and sulfonylurea combination therapy.

Detailed Description

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Conditions

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Type 2 Diabetes Mellitus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Diet and Exercise

Diet and exercise only.

Group Type EXPERIMENTAL

50 mg PB1023

Intervention Type DRUG

70 mg PB1023

Intervention Type DRUG

100 mg PB1023

Intervention Type DRUG

Placebo (0.9% Sodium Chloride)

Intervention Type DRUG

Victoza®

Intervention Type DRUG

Metformin

Metformin only

Group Type EXPERIMENTAL

50 mg PB1023

Intervention Type DRUG

70 mg PB1023

Intervention Type DRUG

100 mg PB1023

Intervention Type DRUG

Placebo (0.9% Sodium Chloride)

Intervention Type DRUG

Victoza®

Intervention Type DRUG

Sulfonylurea

Sulfonylurea only

Group Type EXPERIMENTAL

50 mg PB1023

Intervention Type DRUG

70 mg PB1023

Intervention Type DRUG

100 mg PB1023

Intervention Type DRUG

Placebo (0.9% Sodium Chloride)

Intervention Type DRUG

Victoza®

Intervention Type DRUG

Metformin and Sulfonylurea

Metformin and Sulfonylurea combination therapy

Group Type EXPERIMENTAL

50 mg PB1023

Intervention Type DRUG

70 mg PB1023

Intervention Type DRUG

100 mg PB1023

Intervention Type DRUG

Placebo (0.9% Sodium Chloride)

Intervention Type DRUG

Victoza®

Intervention Type DRUG

PB1023

PB1023 weekly SC injection

Group Type EXPERIMENTAL

50 mg PB1023

Intervention Type DRUG

70 mg PB1023

Intervention Type DRUG

100 mg PB1023

Intervention Type DRUG

Diet and Exercise

Intervention Type OTHER

Metformin

Intervention Type DRUG

Sulfonylurea

Intervention Type DRUG

Metformin and Sulfonylurea

Intervention Type DRUG

Placebo Comparator

Placebo (0.9% Sodium Chloride) weekly SC injection

Group Type PLACEBO_COMPARATOR

Placebo (0.9% Sodium Chloride)

Intervention Type DRUG

Diet and Exercise

Intervention Type OTHER

Metformin

Intervention Type DRUG

Sulfonylurea

Intervention Type DRUG

Metformin and Sulfonylurea

Intervention Type DRUG

Active Comparator

Active Comparator (Victoza) daily SC injection

Group Type ACTIVE_COMPARATOR

Victoza®

Intervention Type DRUG

Diet and Exercise

Intervention Type OTHER

Metformin

Intervention Type DRUG

Sulfonylurea

Intervention Type DRUG

Metformin and Sulfonylurea

Intervention Type DRUG

Interventions

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50 mg PB1023

Intervention Type DRUG

70 mg PB1023

Intervention Type DRUG

100 mg PB1023

Intervention Type DRUG

Placebo (0.9% Sodium Chloride)

Intervention Type DRUG

Victoza®

Intervention Type DRUG

Diet and Exercise

Intervention Type OTHER

Metformin

Intervention Type DRUG

Sulfonylurea

Intervention Type DRUG

Metformin and Sulfonylurea

Intervention Type DRUG

Other Intervention Names

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SC Weekly Injection daily SC injection

Eligibility Criteria

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Inclusion Criteria

* Male and female subjects 18 to 75 years of age, inclusive;
* Body mass index ≤45 kg/m2;
* Diagnosed with T2DM with HbA1c of ≥7.0% and ≤11.0% and treated with diet and exercise alone, or with stable doses of metformin alone, sulfonylurea alone or metformin and sulfonylurea.

Exclusion Criteria

* Currently taking or have taken within the last 6 months non-oral antihyperglycemic agents (eg, insulin, Byetta®, Bydureon®, or Victoza). Short-term use of insulin within this period will not be cause for exclusion if insulin was used during the treatment of an acute intercurrent illness;
* Known allergy to or serious adverse effect caused by an approved or investigational glucagon-like peptide-1 (GLP-1) receptor analog/agonist;
* Unstable cardiovascular disease;
* History of weight loss surgery or other gastrointestinal surgical procedures that could possibly interfere with the mechanism of action of GLP-1 receptor agonists;
* Based on contraindications/warnings identified with other GLP-1 receptor agonists, subjects will be excluded if they have: History, symptoms, or signs of pancreatitis or severe gastrointestinal disease (ie, gastroparesis) or Personal or family history of medullary thyroid tumors or history of Multiple Endocrine Neoplasia Syndrome Type 2;
* Clinically significant renal and/or hepatic dysfunction;
* Pregnant or lactating female subjects.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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PhaseBio Pharmaceuticals Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Anniston, Alabama, United States

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Birmingham, Alabama, United States

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Gulf Shores, Alabama, United States

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Huntsville, Alabama, United States

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Mobile, Alabama, United States

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Muscle Shoals, Alabama, United States

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Chandler, Arizona, United States

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Glendale, Arizona, United States

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Goodyear, Arizona, United States

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Tucson, Arizona, United States

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Harrisburg, Arkansas, United States

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Little Rock, Arkansas, United States

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Searcy, Arkansas, United States

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Chula Vista, California, United States

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Concord, California, United States

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Escondido, California, United States

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Hawaiian Gardens, California, United States

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La Mesa, California, United States

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Los Angeles, California, United States

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Oceanside, California, United States

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San Jose, California, United States

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Santa Rosa, California, United States

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Walnut Creek, California, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Stamford, Connecticut, United States

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Brandenton, Florida, United States

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Brooksville, Florida, United States

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Fort Lauderdale, Florida, United States

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Hialeah, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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New Port Richey, Florida, United States

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Oviedo, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Decatur, Georgia, United States

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Marietta, Georgia, United States

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Roswell, Georgia, United States

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Savannah, Georgia, United States

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Boise, Idaho, United States

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Arlington Heights, Illinois, United States

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Chicago, Illinois, United States

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Evansville, Indiana, United States

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Indianapolis, Indiana, United States

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Council Bluffs, Iowa, United States

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Augusta, Kansas, United States

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Newton, Kansas, United States

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Overland Park, Kansas, United States

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Wichita, Kansas, United States

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New Orleans, Louisiana, United States

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Oxon Hill, Maryland, United States

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Ypsilanti, Michigan, United States

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Saint Paul, Minnesota, United States

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St Louis, Missouri, United States

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Fremont, Nebraska, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Berlin, New Jersey, United States

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New Windsor, New York, United States

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Rochester, New York, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Hickory, North Carolina, United States

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Morehead City, North Carolina, United States

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Raleigh, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Delaware, Ohio, United States

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Kettering, Ohio, United States

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Lyndhurst, Ohio, United States

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Wadsworth, Ohio, United States

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Willoughby Hills, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Eugene, Oregon, United States

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Greer, South Carolina, United States

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Spartanburg, South Carolina, United States

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Austin, Texas, United States

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Corpus Christi, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Hurst, Texas, United States

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Katy, Texas, United States

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Magna, Utah, United States

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West Jordan, Utah, United States

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Burke, Virginia, United States

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Richmond, Virginia, United States

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Virginia Beach, Virginia, United States

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Renton, Washington, United States

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Kenosha, Wisconsin, United States

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Countries

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United States

Other Identifiers

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PB1023-PT-CL-0004

Identifier Type: -

Identifier Source: org_study_id