Safety Study of Unlicensed IND Cord Blood Units Manufactured by the National Cord Blood Program for Unrelated Transplantation

NCT ID: NCT01656603

Last Updated: 2024-04-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

9999 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-02-29

Study Completion Date

2025-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study will evaluate the safety of infusion of the investigational cord blood units by carefully documenting all infusion-related problems.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The primary aim of this study is to examine the safety of administration of the unlicensed investigational NCBP hematopoietic progenitor cell-cord blood (HPC-CORD BLOOD) products in a multi-institution setting. Therefore, the study will evaluate prospectively the incidence of serious adverse reactions as well as the incidence of all infusion related reactions after administration of the unlicensed, investigational NCBP CBU.

Definitions of Infusion-related adverse reactions:

Mild - Moderate: reactions during or after the infusion of the cord blood (CB) product that require some medical intervention but do not affect the overall patient status or outcome.

Severe: serious, life-threatening or fatal infusion reactions, requiring major medical intervention. These include: anaphylactic shock, acute cardiac, pulmonary or renal failure, seizures, patient transfer to the Intensive Care Unit, or death within 48 hours of the CB infusion. Adverse Reactions will also be classified by grade, according to the Common Terminology Criteria for Adverse Events v4.0 (CTCAE).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Infusion Reactions

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

unlicensed CBU

The Principal Investigators will be the transplant physicians at participating US transplant centers

Group Type EXPERIMENTAL

unlicensed CBU

Intervention Type BIOLOGICAL

infusion of unlicensed cord blood units

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

unlicensed CBU

infusion of unlicensed cord blood units

Intervention Type BIOLOGICAL

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Diagnosis: Patients with disorders affecting the hematopoietic system that are inherited, acquired, or result from myeloablative treatment.
2. Patients: Patients of any age and either gender
3. Cord blood product manufactured by the NCBP (at least one, if the graft contains more than one units)

Exclusion Criteria

1. Patients who are receiving licensed cord blood products (only)
2. Patients who are receiving unlicensed cord blood products from other banks (only)
3. Patients who are transplanted at non-US transplant centers
4. Patients who are receiving cord blood products that will be "manipulated" post-thaw (e.g., ex vivo expansion, incubation in vitro, etc.)
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

New York Blood Center

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Patricia Shi, MD

Role: PRINCIPAL_INVESTIGATOR

NY Blood Center

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Children's of Alabama

Birmingham, Alabama, United States

Site Status RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

Mayo Clinic Arizona

Phoenix, Arizona, United States

Site Status COMPLETED

University of Arizona Medical Center

Tucson, Arizona, United States

Site Status COMPLETED

City of Hope

Duarte, California, United States

Site Status RECRUITING

UCSD Moores Cancer Center

La Jolla, California, United States

Site Status RECRUITING

Cedars Sinai Medical Center

Los Angeles, California, United States

Site Status COMPLETED

UCLA Healthcare

Los Angeles, California, United States

Site Status RECRUITING

Rady Children's Hospital

San Diego, California, United States

Site Status RECRUITING

Stanford Health Care

Stanford, California, United States

Site Status RECRUITING

The Children's Hospital of Colorado

Aurora, Colorado, United States

Site Status RECRUITING

University of Colorado Hospital

Aurora, Colorado, United States

Site Status RECRUITING

Presbyterian / St. Luke's Medical Center

Denver, Colorado, United States

Site Status RECRUITING

Alfred I. DuPont Hospital for Children

Wilmington, Delaware, United States

Site Status RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Nemour's Children's Clinic and Hospital

Jacksonville, Florida, United States

Site Status RECRUITING

University of Miami Health System Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status RECRUITING

University of Miami/Jackson Memorial Hospital

Miami, Florida, United States

Site Status RECRUITING

Florida Hospital, Florida Center for Cellular Therapy

Orlando, Florida, United States

Site Status RECRUITING

All Children's Hospital, John Hopkins Medicine

St. Petersburg, Florida, United States

Site Status RECRUITING

Northside Hosptal

Atlanta, Georgia, United States

Site Status RECRUITING

Children's Healthcare of Atlanta

Atlanta, Georgia, United States

Site Status RECRUITING

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status RECRUITING

Loyola University Medical Center

Maywood, Illinois, United States

Site Status RECRUITING

Midwestern Regional Medical Center

Zion, Illinois, United States

Site Status COMPLETED

Indiana University

Indianapolis, Indiana, United States

Site Status RECRUITING

James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status RECRUITING

National Institutes of Health

Bethesda, Maryland, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

Dana Farber Cancer Instistute

Boston, Massachusetts, United States

Site Status RECRUITING

Children's Hospital of Michigan

Detroit, Michigan, United States

Site Status RECRUITING

Henry Ford Health System

Detroit, Michigan, United States

Site Status RECRUITING

Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Site Status RECRUITING

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status RECRUITING

Barnes-Jewish Hospital at University of Washington / Sireman Cancer Center

St Louis, Missouri, United States

Site Status RECRUITING

St. Louis University Hospital

St Louis, Missouri, United States

Site Status RECRUITING

The Nebraska Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

Northwell Health - North Shore University Hospital

Lake Success, New York, United States

Site Status RECRUITING

Cohen Children's Medical Center of NY

New Hyde Park, New York, United States

Site Status RECRUITING

New York Presbyterian Hospital WCMC

New York, New York, United States

Site Status RECRUITING

Mount Sinai Hospital

New York, New York, United States

Site Status RECRUITING

Memorial Sloan-Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

University of Rochester Medical Center

Rochester, New York, United States

Site Status RECRUITING

Akron Children's Hospital

Akron, Ohio, United States

Site Status RECRUITING

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Seidman Cancer Center

Cleveland, Ohio, United States

Site Status RECRUITING

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status RECRUITING

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status RECRUITING

Arthur G. James Cancer Hospital

Columbus, Ohio, United States

Site Status RECRUITING

Stephenson Oklahoma Cancer Center

Oklahoma City, Oklahoma, United States

Site Status RECRUITING

Southwestern Regional Medical Center

Tulsa, Oklahoma, United States

Site Status COMPLETED

Doernbecher Children's Hospital / Oregon Health & Science University

Portland, Oregon, United States

Site Status COMPLETED

Penn State Health / Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status RECRUITING

Abramson Cancer Center of the University of Pennsylvania Medical Center

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Children's Hopsital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

St Jude Children's Research Center

Memphis, Tennessee, United States

Site Status RECRUITING

Children's Medical Center of Dallas

Dallas, Texas, United States

Site Status RECRUITING

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status RECRUITING

Texas Children's Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Methodist Hospital / Texas Transplant Institute

San Antonio, Texas, United States

Site Status COMPLETED

University of Virginia

Charlottesville, Virginia, United States

Site Status RECRUITING

Virginia Commonwealth University Massey Cancer Center

Richmond, Virginia, United States

Site Status RECRUITING

Fred Hutchinson Cancer Research Center / Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status RECRUITING

West Virginia University Hospitals Inc

Morgantown, West Virginia, United States

Site Status RECRUITING

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Site Status RECRUITING

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Dorothy Sung

Role: CONTACT

718-706-5202

Emeline Masson Frenet

Role: CONTACT

718-752-4710

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

MD

Role: primary

Sachit Patel, MD

Role: primary

Robert Greiner, MD

Role: primary

Kelly Ross, MD

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

6637-01

Identifier Type: -

Identifier Source: org_study_id

NCT01861093

Identifier Type: -

Identifier Source: nct_alias

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Cord Blood Cells in Patients With Acute SCI
NCT05693181 UNKNOWN PHASE1/PHASE2