Optimal Dosing of 1st Line Antituberculosis and Antiretroviral Drugs in Children (a Pharmacokinetic Study)

NCT ID: NCT01637558

Last Updated: 2017-10-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

200 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-11-30

Study Completion Date

2017-07-31

Brief Summary

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The aims of this project are to:

1. To evaluate the pharmacokinetics of first line antituberculosis drugs (isoniazid, rifampicin, pyrazinamide and ethambutol) when applying the 2010 WHO/IUATLD dosing guidelines across pediatric populations (0-12 years of age, HIV infected and uninfected, and with varied nutritional status) in Cape Town, South Africa and Blantyre, Malawi.
2. To evaluate an 8-hourly weight band-based dosing strategy for lopinavir/ritonavir using the commercially available lopinavir/ritonavir (4:1 ratio) in children in South Africa receiving rifampicin-based antituberculosis treatment.
3. To evaluate the pharmacokinetics of nevirapine in children in Malawi receiving rifampicin-based antituberculosis treatment.

Detailed Description

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HIV and tuberculosis are a major public health problem in children. Challenges to treat children with tuberculosis include a lack of knowledge about optimal dosing of first line antituberculosis drugs across ages, nutritional status and HIV infection status, the absence of an appropriate regimen to co-administer rifampin and lopinavir/ritonavir, the key first line drugs for tuberculosis and HIV, and uncertainty about NVP exposure in young children during rifampin-based tuberculosis therapy.

In total, 240 children \< 12 years of age with tuberculosis will be enrolled at Red Cross Children's Hospital in Cape Town and Queen Elizabeth Central Hospital, Blantyre. In the second month of antituberculosis treatment, one dose of the drugs in their first-line regimens will be administered according to 2010 WHO/IUATLD guidelines (study drugs) and blood will be sampled for pharmacokinetic analysis over the following 8-10 hours.

Children on antiretroviral treatment (started prior to or during TB treatment) will receive 2 weeks of antiretrovirals (lopinavir/ritonavir or nevirapine) according in the study doses (adjusted 8 hourly doses of lopinavir/ritonavir, or nevirapine doses according to WHO's recommended weight band-based doses) in combination with antituberculosis treatment, prior to pharmacokinetic assessments of both antiretroviral and antituberculosis drugs. Children receiving nevirapine will also undergo pharmacokinetic evaluation 1 month after completion of antituberculosis treatment to evaluate nevirapine concentrations in the absence of antituberculosis drugs. In addition to the 240 children with tuberculosis, 25 HIV infected South African children without tuberculosis will be recruited to evaluate lopinavir concentrations in the absence of antituberculosis drugs.

A population approach will be used to estimate the optimal doses of rifampicin, isoniazid, pyrazinamide and ethambutol in children according to covariates (e.g. age, weight, HIV status, nutritional status) found to have an important influence on the drug concentrations. Similarly population models will be used to describe lopinavir/ritonavir and nevirapine pharmacokinetics in children receiving rifampicin-based antituberculosis treatment, evaluate the dosing approaches and to simulate alternative optimal dosing approaches as indicated.

Conditions

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Tuberculosis HIV

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Main TB cohort

Children with tuberculosis 0-12 years of age

Group Type NO_INTERVENTION

No interventions assigned to this group

Lopinavir/Ritonavir - Cases

children 3-20 kg with tuberculosis and indication for LPV/r-based ART

Group Type EXPERIMENTAL

8 hourly LPV/r during TB treatment

Intervention Type DRUG

8 hourly LPV/r during TB treatment

Lopinavir/Ritonavir - Controls

Children 3-20 kg on LPV/r-based ART; no TB

Group Type EXPERIMENTAL

Lopinavir/Ritonavir

Intervention Type DRUG

Nevirapine arm

children with TB and indication for nevi rapine-based ART

Group Type EXPERIMENTAL

Nevirapine

Intervention Type DRUG

Interventions

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8 hourly LPV/r during TB treatment

8 hourly LPV/r during TB treatment

Intervention Type DRUG

Nevirapine

Intervention Type DRUG

Lopinavir/Ritonavir

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

ALL STUDY PARTICIPANTS

* Aged \< 12 years.
* Weighing \> 1.5 kg and \< 30 kg.
* Written informed permission of parent or legal guardian for their child to participate.
* Absence of clear indication of unwillingness or refusal to participate, and in children \> 7 years of age, assent to participate.
* No contraindications to PK sampling (children with obviously very poor venous access will not be included).
* Able to comply with study visits and procedures including regular adherence to routine medication, and adherence to the study medication.
* Enrollment will be deferred in children with acute severe illness which would likely jeopardize participation (such as illness causing severe respiratory impairment, acute severe diarrhea, acute central nervous system impairment, severe life threatening systemic illness, or other severe conditions requiring hospitalization which would jeopardize participation). Children may be enrolled after recovery from acute illness.

ADDITIONAL CRITERIA FOR THE MAIN TB COHORT AND SUBSTUDIES

1. Main TB cohort

INCLUSION A recent diagnosis of TB and receiving intensive phase antiTB treatment with 1st-line drugs (rifampicin, isoniazid, pyrazinamide with or without ethambutol, in standard doses).
2. LPV SUBSTUDY

CASES \& CONTROLS
* Children in whom ART with a LPV/r-containing regimen is indicated, OR, Children established on a LPV/r-containing regimen.
* ALT \< 5-times the upper limit of the normal range.
* Children weighing 3.0 - 19.9 kg.
* Neonates must have a postmenstrual age of at least 42 weeks and a postnatal age of at least 14 days.

CASES

\- HIV infected children enrolled to the main cohort with at least 2 weeks remaining before the end of intensive phase antiTB treatment such that PK sampling can be scheduled after 2 weeks of combined ART and antiTB treatment, but before the continuation phase of antiTB treatment is started.

CONTROLS

\- HIV infected children without TB.

Weighted enrollment of controls will be performed such that the number of controls in each of the age groups \< 6 months, 6 months to 2 years, and \> 2 years, will be approximately equal to the numbers of cases in those age groups. As most of the children with TB will be started on ART after their TB diagnosis, recruitment of controls will be focused on children who have recently started ART (on treatment \< 3 months).
3. NVP SUBSTUDY

* HIV infected children receiving intensive phase antiTB treatment and enrolled to the main study cohort
* Started on ART including NVP (in WHO's recommended weight band-based doses) and 2 nucleoside reverse transcriptase inhibitors.

Exclusion Criteria

* Indication for increased or reduced doses of 1st-line antiTB drugs (e.g. marked hepatic or renal impairment, TB meningitis).
Minimum Eligible Age

1 Month

Maximum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Liverpool School of Tropical Medicine

OTHER

Sponsor Role collaborator

Uppsala University

OTHER

Sponsor Role collaborator

University of North Carolina

OTHER

Sponsor Role collaborator

University of Cape Town

OTHER

Sponsor Role lead

Responsible Party

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Helen Margaret McIlleron

Assistant Prof

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Helen M McIlleron, PhD

Role: PRINCIPAL_INVESTIGATOR

University of Cape Town

Heather Zar, PhD

Role: PRINCIPAL_INVESTIGATOR

University of Cape Town

Locations

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Queen Elizabeth Central Hospital

Blantyre, , Malawi

Site Status

Red Cross Childrens Hospital

Cape Town, Western Cape, South Africa

Site Status

KIDCRU, Tygerberg Hospital, Department of Paediatrics and Child Health, Stellenbosch University, South Africa.

Cape Town, Western Cape, South Africa

Site Status

Desmond Tutu Centre

Cape Town, Western Cape, South Africa

Site Status

Countries

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Malawi South Africa

References

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Galileya LT, Wasmann RE, Chabala C, Rabie H, Lee J, Njahira Mukui I, Hesseling A, Zar H, Aarnoutse R, Turkova A, Gibb D, Cotton MF, McIlleron H, Denti P. Evaluating pediatric tuberculosis dosing guidelines: A model-based individual data pooled analysis. PLoS Med. 2023 Nov 21;20(11):e1004303. doi: 10.1371/journal.pmed.1004303. eCollection 2023 Nov.

Reference Type DERIVED
PMID: 37988391 (View on PubMed)

Rabie H, Rawizza H, Zuidewind P, Winckler J, Zar H, Van Rie A, Wiesner L, McIlleron H. Pharmacokinetics of adjusted-dose 8-hourly lopinavir/ritonavir in HIV-infected children co-treated with rifampicin. J Antimicrob Chemother. 2019 Aug 1;74(8):2347-2351. doi: 10.1093/jac/dkz171.

Reference Type DERIVED
PMID: 31081020 (View on PubMed)

Bekker A, Schaaf HS, Draper HR, van der Laan L, Murray S, Wiesner L, Donald PR, McIlleron HM, Hesseling AC. Pharmacokinetics of Rifampin, Isoniazid, Pyrazinamide, and Ethambutol in Infants Dosed According to Revised WHO-Recommended Treatment Guidelines. Antimicrob Agents Chemother. 2016 Mar 25;60(4):2171-9. doi: 10.1128/AAC.02600-15. Print 2016 Apr.

Reference Type DERIVED
PMID: 26810651 (View on PubMed)

Other Identifiers

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DATiC

Identifier Type: -

Identifier Source: org_study_id