Trial Outcomes & Findings for A Phase II Study of Increased-Dose Abiraterone Acetate in Patients With Castration Resistant Prostate Cancer (NCT NCT01637402)

NCT ID: NCT01637402

Last Updated: 2020-08-17

Results Overview

A PSA response for the dose escalation group is defined as a participant with a documented PSA decline after 12 weeks of therapy with standard-dose, then had disease progression, and then achieved a ≥30% PSA decline after 12 weeks from the start of dose escalation therapy.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

41 participants

Primary outcome timeframe

Up to 12 weeks from start of dose escalation

Results posted on

2020-08-17

Participant Flow

Participants were recruited through the Urologic Oncology Program at University of California, San Francisco

All participants were prescribed the standard dose(STD). Participants who did not exhibit prostate-specific antigen (PSA) decline at 12 weeks were deemed 'primary-resistant' and taken off study. Participants continued STD until progression, at which time, they were assigned to the escalated dose was for a minimum of 12 weeks.

Participant milestones

Participant milestones
Measure
Standard Dose
Abiraterone 1000 mg once daily Prednisone 5 mg twice daily
Escalated Dose
Abiraterone 1000 mg twice daily Prednisone 5 mg twice daily
Standard Dose Regimen
STARTED
41
0
Standard Dose Regimen
COMPLETED
38
0
Standard Dose Regimen
NOT COMPLETED
3
0
Week 12 Evaluation
STARTED
38
0
Week 12 Evaluation
COMPLETED
32
0
Week 12 Evaluation
NOT COMPLETED
6
0
Treatment Regiments Post Week 12
STARTED
14
18
Treatment Regiments Post Week 12
COMPLETED
5
14
Treatment Regiments Post Week 12
NOT COMPLETED
9
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Standard Dose
Abiraterone 1000 mg once daily Prednisone 5 mg twice daily
Escalated Dose
Abiraterone 1000 mg twice daily Prednisone 5 mg twice daily
Standard Dose Regimen
Lack of Efficacy
2
0
Standard Dose Regimen
Adverse Event
1
0
Week 12 Evaluation
Lack of Efficacy
6
0
Treatment Regiments Post Week 12
Not evaluable for response after 12wks
0
4
Treatment Regiments Post Week 12
Withdrawal by Subject
4
0
Treatment Regiments Post Week 12
Progression after escalation arm closed
5
0

Baseline Characteristics

Measure Description: This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Patients Who Received Treatment
n=41 Participants
Abiraterone Acetate: Standard dose: 1,000 mg, once daily, oral administration Increased dose offered after week 12 evaluation to participants who progressed after decline on standard dose: 1,000 mg, twice daily, oral administration Prednisone: 5 mg, twice daily, oral administration
Age, Continuous
67.4 years
n=18 Participants • Measure Description: This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Sex: Female, Male
Female
0 Participants
n=41 Participants
Sex: Female, Male
Male
41 Participants
n=41 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Ethnicity (NIH/OMB)
Not Hispanic or Latino
17 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Asian
0 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Black or African American
0 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
White
16 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
More than one race
0 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Unknown or Not Reported
2 Participants
n=18 Participants • This measure presents data for the 18 participants that were subsequently randomized to the second treatment arm
Region of Enrollment
United States
41 participants
n=41 Participants
Prior Therapies
Radical Prostatectomy
12 Participants
n=41 Participants
Prior Therapies
Definitive Radiotherapy
15 Participants
n=41 Participants
Prior Therapies
Metastatic at Diagnosis
14 Participants
n=41 Participants
Prostate Specific Antigen levels
23.18 ng/dl
n=41 Participants

PRIMARY outcome

Timeframe: Up to 12 weeks from start of dose escalation

A PSA response for the dose escalation group is defined as a participant with a documented PSA decline after 12 weeks of therapy with standard-dose, then had disease progression, and then achieved a ≥30% PSA decline after 12 weeks from the start of dose escalation therapy.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=14 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
Plasma Abiraterone concentration at time of disease progression on standard dose
Number of Patients With PSA Response From Dose Escalation
0 Participants

SECONDARY outcome

Timeframe: Up to 24 months

Frequency of any treatment-related toxicity with increased-dose Abiraterone Acetate by maximum observed grade will be tabulated for the study cohort. Toxicities will be graded for management according to NCI Common Terminology Criteria for Adverse Events (CTCAE) version 4.0 as a measure of patient safety.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
n=18 Participants
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
n=18 Participants
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=18 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
n=18 Participants
Plasma Abiraterone concentration at time of disease progression on standard dose
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Hypokalemia
0 Participants
0 Participants
0 Participants
1 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Purpura
0 Participants
0 Participants
1 Participants
0 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Dry Mouth
0 Participants
0 Participants
1 Participants
0 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Hypertension
0 Participants
0 Participants
0 Participants
1 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Alanine aminotransferase increase
1 Participants
0 Participants
0 Participants
0 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Irritability
0 Participants
0 Participants
0 Participants
1 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Aspartate aminotransferase increased
0 Participants
0 Participants
0 Participants
1 Participants
Number of Participants With Worst-grade, Treatment-related Toxicities for Dose Escalation Group
Fatigue
0 Participants
0 Participants
0 Participants
1 Participants

SECONDARY outcome

Timeframe: up to 24 months

Time to PSA progression as defined by RECIST criteria or by the Prostate Cancer Working Group 2 (PCWG) criteria for patients whom were treated with increased dose Abiraterone Acetate.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=14 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
Plasma Abiraterone concentration at time of disease progression on standard dose
Time to PSA Progression for Dose Escalation Cohort
12 months
Interval 6.0 to 14.5

SECONDARY outcome

Timeframe: up to 24 months

Population: Progression-free survival could not be calculated due to the lack of objective response in the dose escalation group (i.e. no patients were progression-free).

Progression free survival for patients treated with increased dose Abiraterone Acetate

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 24 months

Population: Only 26 patients on the standard dose had pharmacokinetic samples available for analysis at time of first blood draw. No patients displayed a response to increased-dose therapy therefore data for concentration at time of response to increased dose was not collected.

Pharmacokinetic assessment at the initiation of standard dose therapy, at the time of initial disease progression, at the time of a response to increased dose of abiraterone acetate and at the time of disease progression on increased-dose therapy.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
n=14 Participants
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=26 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
n=26 Participants
Plasma Abiraterone concentration at time of disease progression on standard dose
Serum Concentration Levels of Abiraterone Acetate Over Time
31.5 nanograms per millilitre (ng/mL)
Interval 5.2 to 148.0
5.5 nanograms per millilitre (ng/mL)
Interval 1.26 to 56.2
14.2 nanograms per millilitre (ng/mL)
Interval 0.8 to 221.0

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: Testosterone levels were maximally suppressed below the laboratory limit of detection (LOD) at week 12 for patients on standard-dose therapy so no correlation could be performed. There were no responders in dose escalation so evaluation of hormonal changes with dose-escalated group was not pursued.

Pearson's correlation coefficients ("r") will be calculated to summarize the relationship between testosterone values at baseline and at 12 weeks. Testosterone labs will be obtained at an earlier time point if the patient comes off study for disease progression before week 12. Coefficients are on a continuous scale ranging from -1 to +1 with a value of -1 indicating a perfect negative linear association of testosterone levels between the 2 time points, a value of 0 indicating no association between testosterone levels between the two time points, and a value of +1 indicating a positive linear association of testosterone levels between the two time points.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: Testosterone levels were maximally suppressed below the laboratory limit of detection (LOD) at week 12 for patients on standard-dose therapy so no correlation could be performed. There were no responders in the dose escalation group so evaluation of hormonal changes with dose-escalated group was not pursued.

The distribution of the baseline testosterone levels and the change in hormone level at 12 weeks will be compared between patients experiencing a PSA decline \>30% (responders) and patients without such a PSA decline (primary-resistant) using a two group t statistic. Measurements will be obtained at an earlier time point if the patient comes off study for disease progression before week 12.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=7 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
n=19 Participants
Plasma Abiraterone concentration at time of disease progression on standard dose
Comparison of Circulating Testosterone Levels Between Primary-Resistant Patients and Responders
NA Nanograms per decilitre (ng/dL)
Standard Deviation NA
below the level of detection
NA Nanograms per decilitre (ng/dL)
Standard Deviation NA
below the level of detection

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: No DHEA values were collected for week 12 in dose escalation group so correlation of for dose escalation could not be performed.

Pearson's correlation coefficients ("r") will be calculated to summarize the relationship between DHEA values at baseline and at 12 weeks. DHEA labs will be obtained at an earlier time point if the patient comes off study for disease progression before week 12. Coefficients are on a continuous scale ranging from -1 to +1 with a value of -1 indicating a perfect negative linear association of DHEA levels between the 2 time points, a value of 0 indicating no association between DHEA levels between the two time points, and a value of +1 indicating a positive linear association of DHEA levels between the two time points.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=26 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
Plasma Abiraterone concentration at time of disease progression on standard dose
Correlation of Circulating Dehydroepiandrosterone (DHEA) Levels From Baseline to Week 12
0 correlation coefficient (r)

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: Twenty-six patients had both baseline and follow-up samples available for analysis. There were no responders in dose escalation group so evaluation of hormonal changes with dose-escalated group was not pursued.

The distribution of the baseline DHEA levels and the change in hormone level at 12 weeks will be compared between patients experiencing a PSA decline \>30% (responders) and patients without such a PSA decline (primary-resistant) using a two group t statistic. Measurements will be obtained at an earlier time point if the patient comes off study for disease progression before week 12.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=7 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
n=19 Participants
Plasma Abiraterone concentration at time of disease progression on standard dose
Comparison of Circulating DHEA Levels Between Primary-Resistant and Responders
Initial draw
56.2 ng/dL
Interval 11.2 to 223.9
79.4 ng/dL
Interval 11.2 to 281.83
Comparison of Circulating DHEA Levels Between Primary-Resistant and Responders
Progression / Week 12
28.5 ng/dL
Interval 14.1 to 141.2
13.5 ng/dL
Interval 3.1 to 44.7

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: DHEA-S levels were maximally suppressed below the laboratory limit of detection (LOD) at week 12 for patients on standard-dose therapy so no correlation could be performed. There were no responders in dose escalation so evaluation of hormonal changes with dose-escalated group was not pursued.

Pearson's correlation coefficients ("r") will be calculated to summarize the relationship between DHEA-S values at baseline and at 12 weeks. DHEA-S labs will be obtained at an earlier time point if the patient comes off study for disease progression before week 12. Coefficients are on a continuous scale ranging from -1 to +1 with a value of -1 indicating a perfect negative linear association of DHEA-S levels between the 2 time points, a value of 0 indicating no association between DHEA-S levels between the two time points, and a value of +1 indicating a positive linear association of DHEA-S levels between the two time points.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: DHEA-S levels were maximally suppressed below the laboratory limit of detection (LOD) at week 12 for patients on standard-dose therapy so no correlation could be performed. There were no responders in dose escalation so evaluation of hormonal changes with dose-escalated group was not pursued.

The distribution of the baseline DHEA-S levels and the change in hormone level at 12 weeks will be compared between patients experiencing a PSA decline \>30% (responders) and patients without such a PSA decline (primary-resistant) using a two group t statistic. Measurements will be obtained at an earlier time point if the patient comes off study for disease progression before week 12.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=7 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
n=19 Participants
Plasma Abiraterone concentration at time of disease progression on standard dose
Comparison of Circulating DHEA-S Levels Between Primary-Resistant Patients and Responders
NA microgram per deciliter (µg/dL)
Standard Deviation NA
below the level of detection
NA microgram per deciliter (µg/dL)
Standard Deviation NA
below the level of detection

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: Androstenedione levels were maximally suppressed below the laboratory limit of detection (LOD) at week 12 for patients on standard-dose therapy so no correlation could be performed. There were no responders in dose escalation so evaluation of hormonal changes with dose-escalated group was not pursued.

Pearson's correlation coefficients ("r") will be calculated to summarize the relationship between androstenedione values at baseline and at 12 weeks. Androstenedione labs will be obtained at an earlier time point if the patient comes off study for disease progression before week 12. Coefficients are on a continuous scale ranging from -1 to +1 with a value of -1 indicating a perfect negative linear association of androstenedione levels between the 2 time points, a value of 0 indicating no association between androstenedione levels between the two time points, and a value of +1 indicating a positive linear association of androstenedione levels between the two time points.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline and Week 12

Population: Androstenedione levels were maximally suppressed below the laboratory limit of detection (LOD) at week 12 for patients on standard-dose therapy so no correlation could be performed. There were no responders in dose escalation so evaluation of hormonal changes with dose-escalated group was not pursued.

The distribution of the baseline androstenedione levels and the change in hormone level at 12 weeks will be compared between patients experiencing a PSA decline \>30% (responders) and patients without such a PSA decline (primary-resistant) using a two group t statistic. Measurements will be obtained at an earlier time point if the patient comes off study for disease progression before week 12.

Outcome measures

Outcome measures
Measure
Dose Escalation (CTCAE Grade 3)
Worst grade adverse event with CTCAE Grade 3 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation (CTCAE Grade 4)
Worst grade adverse event with CTCAE Grade 4 for patients taking Abiraterone 1000 mg twice daily, Prednisone 5 mg twice daily
Dose Escalation
n=7 Participants
Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Concentration at Time of Disease Progression on Standard Dose
n=19 Participants
Plasma Abiraterone concentration at time of disease progression on standard dose
Comparison of Circulating Androstenedione Levels Between Primary-Resistant Patients and Responders
NA ng/dL
Standard Deviation NA
below the level of detection
NA ng/dL
Standard Deviation NA
below the level of detection

Adverse Events

Standard Dose Therapy

Serious events: 7 serious events
Other events: 34 other events
Deaths: 0 deaths

Dose Escalation

Serious events: 1 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Standard Dose Therapy
n=41 participants at risk
Abiraterone 1000 mg daily, Prednisone 5 mg twice daily
Dose Escalation
n=18 participants at risk
Dose Escalation (until PSA decrease of at least 30% after 12 weeks): Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Cardiac disorders
Atrial fibrillation
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Constipation
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Dental caries
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Nausea
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Vomiting
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
General disorders
Fatigue
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Infections and infestations
Lung infection
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Infections and infestations
Upper respiratory infection
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Investigations
Alanine aminotransferase increased
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Investigations
Aspartate aminotransferase increased
2.4%
1/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Metabolism and nutrition disorders
Anorexia
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Metabolism and nutrition disorders
Hypokalemia
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Musculoskeletal and connective tissue disorders
Generalized muscle weakness
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Neoplasms benign, malignant and unspecified (incl cysts and polyps) - Other, specify
2.4%
1/41 • Up to 24 months
5.6%
1/18 • Up to 24 months

Other adverse events

Other adverse events
Measure
Standard Dose Therapy
n=41 participants at risk
Abiraterone 1000 mg daily, Prednisone 5 mg twice daily
Dose Escalation
n=18 participants at risk
Dose Escalation (until PSA decrease of at least 30% after 12 weeks): Abiraterone 1,000 mg, twice daily, Prednisone 5 mg twice daily
Vascular disorders
Hypertension
12.2%
5/41 • Up to 24 months
11.1%
2/18 • Up to 24 months
Vascular disorders
Hot flashes
12.2%
5/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Vascular disorders
Vascular disorders - Other, specify
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Gastrointestinal disorders
Diarrhea
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Nausea
7.3%
3/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Gastrointestinal disorders
Dyspepsia
7.3%
3/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Vomiting
7.3%
3/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Gastrointestinal disorders
Oral pain
2.4%
1/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Gastrointestinal disorders
Dry mouth
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
General disorders
Fatigue
12.2%
5/41 • Up to 24 months
11.1%
2/18 • Up to 24 months
General disorders
Pain
9.8%
4/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
General disorders
Edema limbs
7.3%
3/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
General disorders
Irritability
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Metabolism and nutrition disorders
Hypokalemia
14.6%
6/41 • Up to 24 months
11.1%
2/18 • Up to 24 months
Metabolism and nutrition disorders
Hypomagnesemia
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Metabolism and nutrition disorders
Anorexia
2.4%
1/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Musculoskeletal and connective tissue disorders
Pain in extremity
14.6%
6/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Musculoskeletal and connective tissue disorders
Myalgia
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Musculoskeletal and connective tissue disorders
Muscle weakness lower limb
2.4%
1/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Musculoskeletal and connective tissue disorders
Flank pain
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Infections and infestations
Upper respiratory infection
12.2%
5/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Infections and infestations
Skin infection
2.4%
1/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Nervous system disorders
Dizziness
7.3%
3/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Nervous system disorders
Peripheral sensory neuropathy
4.9%
2/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Injury, poisoning and procedural complications
Bruising
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Injury, poisoning and procedural complications
Fall
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Injury, poisoning and procedural complications
Fracture
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Skin and subcutaneous tissue disorders
Skin and subcutaneous tissue disorders - Other, specify
9.8%
4/41 • Up to 24 months
0.00%
0/18 • Up to 24 months
Skin and subcutaneous tissue disorders
Dry skin
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Skin and subcutaneous tissue disorders
Purpura
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Renal and urinary disorders
Urinary incontinence
7.3%
3/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Renal and urinary disorders
Cystitis noninfective
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Respiratory, thoracic and mediastinal disorders
Pneumonitis
0.00%
0/41 • Up to 24 months
11.1%
2/18 • Up to 24 months
Eye disorders
Cataract
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Investigations
Creatinine increased
12.2%
5/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Investigations
Alanine aminotransferase increased
7.3%
3/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Investigations
Aspartate aminotransferase increased
7.3%
3/41 • Up to 24 months
5.6%
1/18 • Up to 24 months
Psychiatric disorders
Anxiety
0.00%
0/41 • Up to 24 months
5.6%
1/18 • Up to 24 months

Additional Information

Dr. Terry Friedlander, MD

University of California, San Francisco

Phone: 415-514-6380

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place