Effect of KB003 in Subjects With Asthma Inadequately Controlled by Corticosteroids

NCT ID: NCT01603277

Last Updated: 2015-02-02

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

160 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-07-31

Study Completion Date

2014-01-31

Brief Summary

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This study will evaluate the safety, tolerability and efficacy of a single dose level of KB003 in subjects with inadequately controlled asthma.

Detailed Description

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Conditions

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Moderate-to-Severe Asthma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Anti-GM-CSF Monoclonal Antibody 400mg

Group Type EXPERIMENTAL

Anti-GM-CSF Monoclonal Antibody 400mg

Intervention Type BIOLOGICAL

Anti-GM-CSF Monoclonal Antibody 400mg

Normal Saline

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Normal Saline

Interventions

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Anti-GM-CSF Monoclonal Antibody 400mg

Anti-GM-CSF Monoclonal Antibody 400mg

Intervention Type BIOLOGICAL

Placebo

Normal Saline

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* A diagnosis of asthma established for at least 2 years
* Symptomatic asthma as defined by the Juniper Asthma Control Questionnaire
* Symptomatic asthma despite stable treatment with inhaled corticosteroids fluticasone or budesonide, or other corticosteroids, for at least 12 weeks
* Currently receiving inhaled long-acting beta agonist (LABA) or previously documented LABA intolerability or lack of responsiveness
* At least 2 exacerbations (no more than 6) in the previous 12 months that required systemic corticosteroids or at least a doubling of daily oral dose

Exclusion Criteria

* Acute asthma worsening (requiring emergency room visit, hospitalization, urgent care, physician visit, or change in asthma medications) or lower respiratory tract infection requiring the use of antibiotics, within 4 weeks prior to Screening Visit.
* History of life-threatening asthma with admission to the intensive care unit requiring the use of mechanical ventilation within the past 12 months
* Use of any immunosuppressive or immunomodulatory agents within 12 weeks or an investigational agent within 4 weeks prior to Screening Visit
* History of any cardiovascular, neurological, hepatic, or renal condition
* History of smoking within the past 12 months
Minimum Eligible Age

16 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Humanigen, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Nestor A. Molfino, MD, MSc

Role: STUDY_CHAIR

KaloBios Pharmaceuticals, Inc.

Locations

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Birmingham, Alabama, United States

Site Status

Fullerton, California, United States

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Granada Hills, California, United States

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Los Angeles, California, United States

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Rancho Mirage, California, United States

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Sacramento, California, United States

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San Jose, California, United States

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Centennial, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Waterbury, Connecticut, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Tampa, Florida, United States

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Winter Park, Florida, United States

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Duluth, Georgia, United States

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Lawrenceville, Georgia, United States

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Savannah, Georgia, United States

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Lexington, Kentucky, United States

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Ann Arbor, Michigan, United States

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St Louis, Missouri, United States

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Reno, Nevada, United States

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Summit, New Jersey, United States

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Winston-Salem, North Carolina, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Warwick, Rhode Island, United States

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Charleston, South Carolina, United States

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Charleston, South Carolina, United States

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Greenville, South Carolina, United States

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Arlington, Texas, United States

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Sugarland, Texas, United States

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Milwaukee, Wisconsin, United States

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Cairns, Queensland, Australia

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Woolonggabba, Queensland, Australia

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Bedford Park, South Australia, Australia

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Woodville, South Australia, Australia

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Box Hill, Victoria, Australia

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Frankston, Victoria, Australia

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Melbourne, Victoria, Australia

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Nedlands, Western Australia, Australia

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Marseille, , France

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Montpellier, , France

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Rennes, , France

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Strasbourg, , France

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Tours, , France

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Bialystok, Podlaskie Voivodeship, Poland

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Mrozy, Silesian Voivodeship, Poland

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Wiłomin, Slaski, Poland

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Biała Rawska, , Poland

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Bydgoszcz, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Piasta, , Poland

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Dnipropetrovsk, , Ukraine

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Donetsk, , Ukraine

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Odesa, , Ukraine

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Simferopol, , Ukraine

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Vinnytsia, , Ukraine

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Yalta, , Ukraine

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Zaporizhzhya, , Ukraine

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Wishaw, Lanarkshire, United Kingdom

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Northwood, Middlesex, United Kingdom

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Bradford, West Yorkshire, United Kingdom

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Leeds, West Yorkshire, United Kingdom

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Southampton, , United Kingdom

Site Status

Countries

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United States Australia France Poland Ukraine United Kingdom

References

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Molfino NA, Kuna P, Leff JA, Oh CK, Singh D, Chernow M, Sutton B, Yarranton G. Phase 2, randomised placebo-controlled trial to evaluate the efficacy and safety of an anti-GM-CSF antibody (KB003) in patients with inadequately controlled asthma. BMJ Open. 2016 Jan 6;6(1):e007709. doi: 10.1136/bmjopen-2015-007709.

Reference Type DERIVED
PMID: 26739717 (View on PubMed)

Other Identifiers

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KB003-04

Identifier Type: -

Identifier Source: org_study_id

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