Cladribine Plus Pegylated Interpheron Alfa-2a in Systemic Mastocytosis

NCT ID: NCT01602939

Last Updated: 2016-08-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2/PHASE3

Total Enrollment

10 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-05-31

Study Completion Date

2017-06-30

Brief Summary

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The aim of this study is to evaluate the efficacy in terms of clinical and biological response rates of Cladribine plus Pegylated Interpheron alpha-2a therapy in patients with advanced systemic mastocytosis carrying D816V or other exon 17 KIT mutations.

Detailed Description

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Conditions

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Systemic Mastocytosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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2CDA+IFN

Group Type EXPERIMENTAL

Cladribine and pegylated interpheron alpha-2a

Intervention Type DRUG

Cladribine (0.07 mg/Kg/day) s.c for 5 consecutive days each month for a total of 6 months.Cladribine daily doses could be increased up to 0.14 mg/Kg in the fourth, fifth and sixth cycles of therapy if no objetive response is achieved after the third cycle.

Pegylated Interpheron alpha-2a (1 mcgr/Kg) s.c weekly for a total of 6 months.

Interventions

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Cladribine and pegylated interpheron alpha-2a

Cladribine (0.07 mg/Kg/day) s.c for 5 consecutive days each month for a total of 6 months.Cladribine daily doses could be increased up to 0.14 mg/Kg in the fourth, fifth and sixth cycles of therapy if no objetive response is achieved after the third cycle.

Pegylated Interpheron alpha-2a (1 mcgr/Kg) s.c weekly for a total of 6 months.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age older than 18 years.
* Diagnosis of advanced systemic mastocytosis (aggressive systemic mastocytosis or proggressing systemic mastocytosis) with D816V or other exon 17 KIT mutations.
* ECOG ≤ 3.
* Signed informed consent.

Exclusion Criteria

* Impaired liver function (total bilirubin ≥ 2.0 mg/dl, AST or ALT \> 3 x upper limit of normal)not related to mastocytosis.
* Impaired renal function (≥ 2.0 mg/dL)not related to mastocytosis.
* Grade III-IV cytopenias not related to mastocytosis. Severe cardiopathy (grade III/IV of NYHA, or left ventricular ejection fraction \< 50%).
* Pregnancy or breastfeeding.
* Female patients who do not use contraceptive methods.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hospital Virgen de la Salud

OTHER

Sponsor Role lead

Responsible Party

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LUIS ESCRIBANO

Director of the Instituto de Estudios de Mastocitosis de Castilla La Mancha

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Luis Escribano, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Instituto de Estudios de Mastocitosis de Castilla La Mancha

Locations

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Instituto de Estudios de Mastocitosis de Castilla La Mancha; Hospital Virgen del Valle

Toledo, Toledo, Spain

Site Status RECRUITING

Countries

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Spain

Central Contacts

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Luis Escribano, MD, PhD

Role: CONTACT

+34925269335

Iván Alvarez-Twose, MD

Role: CONTACT

+34925269336

Facility Contacts

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Luis Escribano, MD, PhD

Role: primary

+34925269335

Iván Alvarez-Twose, MD

Role: backup

+34925269336

Other Identifiers

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EC11-187

Identifier Type: -

Identifier Source: org_study_id

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