Liposomal Cytarabine in the Treatment of Central Nervous System Resistant or Relapsed Acute Lymphoblastic Leukemia in Children

NCT ID: NCT01593488

Last Updated: 2023-03-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

31 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-03-31

Study Completion Date

2024-12-31

Brief Summary

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The purpose of this study is to describe the activity and toxicity of a new formulation of cytarabine called liposomal cytarabine given into the central nervous system for the treatment of central nervous system localization of acute lymphoblastic leukemia (ALL) in children and adolescents.

Detailed Description

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Liposomal cytarabine (DepoCyte) is a new formulation of the drug cytarabine, a drug commonly used in the treatment of ALL. This formulation of the drug can be given intrathecally (into the spinal fluid), and is released slowly over a longer period, about two weeks. This allows a longer exposure of the drug to the central nervous system, and requires fewer intrathecal injections for the patient.

Conditions

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Acute Lymphoblastic Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Intrathecal liposomal cytarabine

Group Type EXPERIMENTAL

liposomal cytarabine

Intervention Type DRUG

given intrathecally in induction phase every 15 days until CSF response for up to 7 injections. Then it is given every 4 weeks during consolidation phase while patient awaiting bone marrow transplant. For those patients who are not candidates for a bone marrow transplant, the drug will be given every 3 months for 4 administrations (maintenance therapy)

Interventions

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liposomal cytarabine

given intrathecally in induction phase every 15 days until CSF response for up to 7 injections. Then it is given every 4 weeks during consolidation phase while patient awaiting bone marrow transplant. For those patients who are not candidates for a bone marrow transplant, the drug will be given every 3 months for 4 administrations (maintenance therapy)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age \< 18 years
* Diagnosis of acute lymphoblastic leukemia (ALL)
* Central nervous system involvement with malignant cells present in cerebrospinal fluid
* CNS involvement may be refractive to prior systemic therapy, a first recurrence after prior systemic and intrathecal therapy or a second recurrence
* CNS involvement may be an isolated lesion or present with other sites of disease
* ECOG performance status 0-2
* Life expectancy of at least 8 weeks
* Absence of severe organ dysfunction
* Informed consent

Exclusion Criteria

* Eligibility for AIEOP studies of first recurrence of ALL,and receiving therapy in a center participating in the AIEOP studies
* Concurrent treatment with experimental therapies
* Severe neurologic toxicities from previous chemotherapy
* Severe coagulopathy at time of recurrence
* Sepsis
* Intrathecal therapy within 1 week of planned study therapy
* Total body or head and spine radiation within 8 weeks of enrolment
* Bone marrow transplant within 8 weeks of start of study therapy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Santobono-Pausilpon Hospital

UNKNOWN

Sponsor Role collaborator

IRCCS Azienda Ospedaliero-Universitaria di Bologna

OTHER

Sponsor Role collaborator

University of Bologna

OTHER

Sponsor Role collaborator

National Cancer Institute, Naples

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Rosanna Parasole, M.D.

Role: PRINCIPAL_INVESTIGATOR

Santobono-Pausilipon Hospital

Massimo Di Maio, M.D.

Role: PRINCIPAL_INVESTIGATOR

National Cancer Institute, Naples

Francesco Perrone, M.D., Ph.D.

Role: PRINCIPAL_INVESTIGATOR

National Cancer Institute, Naples

A. Pession

Role: PRINCIPAL_INVESTIGATOR

Policlinico S. Orsola-Malpighi, Bologna

William Morello

Role: PRINCIPAL_INVESTIGATOR

Policlinico S. Orsola-Malpighi, Bologna

E. Strocchi

Role: PRINCIPAL_INVESTIGATOR

University of Bologna

Locations

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P.O. Gaspare Rodolico

Catania, , Italy

Site Status

Istituto G. Gasilini

Genova, , Italy

Site Status

Ospedale S. Gerardo Clinica Pediatrica

Monza, , Italy

Site Status

AORN Santobon - Pauslipon

Napoli, , Italy

Site Status

A.O. Università Padova

Padua, , Italy

Site Status

ARNAS Osp Civico di Cristina

Palermo, , Italy

Site Status

IRCCS Ospedale Bambino Gesu'

Roma, , Italy

Site Status

Casa Sollievo della Sofferenza

San Giovanni Rotondo, , Italy

Site Status

IRCCS Burlo Garofalo Istituto per l'Infanzia Emato Oncologia

Trieste, , Italy

Site Status

Ospedale Policlinico G.B. Rossi

Verona, , Italy

Site Status

Countries

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Italy

Other Identifiers

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2011-002622-48

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CILI

Identifier Type: -

Identifier Source: org_study_id

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