Expanded Access Program of Ponatinib

NCT ID: NCT01592136

Last Updated: 2018-02-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

APPROVED_FOR_MARKETING

Study Classification

EXPANDED_ACCESS

Brief Summary

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This protocol will allow expanded access of ponatinib to patients ≥18 years with chronic myeloid leukemia (CML) any phase or Philadelphia chromosome positive acute lymphoblastic leukemia (Ph+ALL) who have failed all available treatment options.

Detailed Description

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This protocol will allow expanded access of ponatinib to patients ≥18 years with CML or Ph+ALL who have failed all available treatment options. Patients with chronic (CP) or accelerated phase (AP) CML must be previously treated with and resistant or intolerant to imatinib, dasatinib and nilotinib or develop the T315I mutation after any tyrosine kinase inhibitor (TKI) therapy. Patients with blast phase (BP) CML and Ph+ ALL must be previously treated with and resistant or intolerant to imatinib and dasatinib or develop the T315I mutation after any TKI therapy. No formal analysis will be performed on any data obtained. Safety information will be collected and adverse events will be tabulated for reporting purposes only.

Conditions

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Chronic Myeloid Leukemia (CML) Philadelphia Chromosome Positive Acute Lymphoblastic Leukemia (Ph+ ALL)

Interventions

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ponatinib

Patients will receive ponatinib 45 mg orally as a single dose once daily with or without food. Each patient will receive daily ponatinib until disease progression, unacceptable toxicity, or withdrawal of consent

Intervention Type DRUG

Other Intervention Names

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AP24534

Eligibility Criteria

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Inclusion Criteria

1. CP-CML and AP-CML patients previously treated with and resistant or intolerant to imatinib, dasatinib and nilotinib or those who developed the T315I mutation after any TKI therapy. BP-CML and Ph+ ALL patients previously treated with and resistant or intolerant to imatinib and dasatinib or those who developed the T315I mutation after any TKI therapy.
2. Patients must be ≥ 18 years old.
3. Provide written informed consent.
4. Eastern Cooperative Oncology Group (ECOG) performance status ≤ 2.
5. Men and women of childbearing potential must agree to effective contraception from the time of signing informed consent through the Follow-up Visit, approximately 30 days after last dose of ponatinib.

Exclusion Criteria

1. Are eligible for an ongoing and accessible clinical trial of ponatinib
2. Have not adequately recovered from AEs due to agents previously administered
3. Require concurrent treatment with immunosuppressive agents, other than corticosteroids prescribed for a short course of therapy.
4. Have previously been treated with ponatinib.
5. Have significant or active cardiovascular disease, specifically including, but not restricted to:

* Myocardial infarction within 3 months prior to first dose of ponatinib,
* History of clinically significant atrial arrhythmia or any ventricular arrhythmia,
* Unstable angina within 3 months prior to first dose of ponatinib,
* Congestive heart failure within 3 months prior to first dose of ponatinib.
6. Have abnormal QTcF (\> 450 ms for males or \> 470 ms for females)
7. Have a significant bleeding disorder unrelated to CML or Ph+ ALL.
8. Have a history of pancreatitis or alcohol abuse
9. Have elevated amylase or lipase (\> 1.5 x ULN for institution) at entry.
10. Have inadequate hepatic function or any of the following:

* Total bilirubin \> 1.5 x ULN for institution at entry
* Alanine aminotransferase and aspartate aminotransferase \> 2.5 x ULN for institution at entry
* Prothrombin time \>1.5 x ULN for institution at entry
11. Have inadequate renal function or serum creatinine \> 2.5 x ULN for institution at entry
12. Have uncontrolled hypertriglyceridemia or triglycerides \> 450 mg/dL at entry.
13. Have malabsorption syndrome or other gastrointestinal illness that could affect absorption of orally administered ponatinib.
14. Women who are pregnant or lactating.
15. Underwent major surgery within 14 days prior to the first dose of ponatinib.
16. Have ongoing or active infection (including known history of human immunodeficiency virus \[HIV\], hepatitis B virus \[HBV\], or hepatitis C virus \[HCV\]).
17. Suffer from any condition or illness that, in the opinion of the Investigator would compromise patient safety or interfere with the evaluation of the safety of the study drug.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ariad Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Moores UCSD Cancer Center, Site #165

La Jolla, California, United States

Site Status

Southern California Permanente Medical Group, Site #161

San Marcos, California, United States

Site Status

Kaiser Permanente Medical Center, Site #158

Vallejo, California, United States

Site Status

Smilow Cancer Hospital at Yale New Haven, Site #182

New Haven, Connecticut, United States

Site Status

Cancer Institute of Florida, Site #187

Altamonte Springs, Florida, United States

Site Status

H. Lee Moffitt Cancer Center & Research Institute, Site #017

Tampa, Florida, United States

Site Status

Emory University, Site # 058

Atlanta, Georgia, United States

Site Status

University of Chicago Medical Center, Site #001

Chicago, Illinois, United States

Site Status

Indiana Blood and Marrow Transplantation, Site #138

Indianapolis, Indiana, United States

Site Status

Norton Cancer Institute, Site #142

Louisville, Kentucky, United States

Site Status

University of Maryland, Site #040

Baltimore, Maryland, United States

Site Status

Tufts Medical Center, Site #141

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute, Site 008

Boston, Massachusetts, United States

Site Status

University of Massachusetts Worcester, Site #152

Worcester, Massachusetts, United States

Site Status

University of Michigan Health System, Site #011

Ann Arbor, Michigan, United States

Site Status

Karmanos Cancer Institute, Site #034

Detroit, Michigan, United States

Site Status

Mayo Clinic, Site #044

Rochester, Minnesota, United States

Site Status

Freeman Cancer Institute, Site #190

Joplin, Missouri, United States

Site Status

Washington University School of Medicine, Site 007

St Louis, Missouri, United States

Site Status

John Theurer Cancer Center at Hackensack University Medical Center, Site 128

Hackensack, New Jersey, United States

Site Status

Roswell Park Cancer Institute, Site #029

Buffalo, New York, United States

Site Status

Weill Cornell Medical College - New York Presbyterian Hospital, Site #006

New York, New York, United States

Site Status

University of Rochester, Site 137

Rochester, New York, United States

Site Status

Duke University Medical Center, Site 003

Durham, North Carolina, United States

Site Status

Jewish Hospital, Site #175

Cincinnati, Ohio, United States

Site Status

Oregon Health & Science University (OHSU), Site 048

Portland, Oregon, United States

Site Status

Hospital of the University of Pennsylvania, Site #013

Philadelphia, Pennsylvania, United States

Site Status

Jeanes Hospital of TUHS, Site #127

Philadelphia, Pennsylvania, United States

Site Status

Medical University of South Carolina, Site #148

Charleston, South Carolina, United States

Site Status

Tennesse Oncology, PLLC, Site # 076

Nashville, Tennessee, United States

Site Status

The University of Texas M.D. Anderson Cancer Center, Site #005

Houston, Texas, United States

Site Status

Huntsman Cancer Institute at the University of Utah, Site #043

Salt Lake City, Utah, United States

Site Status

Seattle Cancer Care Alliance, Site #100

Seattle, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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AP24534-12-901

Identifier Type: -

Identifier Source: org_study_id

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