Trial Outcomes & Findings for Proof-of-Concept Safety Study of CPP-109 (Vigabatrin) for Treatment Refractory Tourette's Disorder (NCT NCT01585207)

NCT ID: NCT01585207

Last Updated: 2018-01-19

Results Overview

The Global Severity score is the sum of the Total Tic score and the TD Impairment score. It is rated by the Investigator on the Yale Global Tic Severity Score ( Y-GTSS, a widely accepted measure of drug efficacy in TD. Scale from 0- 100. Higher score indicates more impairment.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

4 participants

Primary outcome timeframe

weekly from baseline to end of study (10weeks)

Results posted on

2018-01-19

Participant Flow

Participant milestones

Participant milestones
Measure
Vigabatrin
3 tablets, bid for 8 weeks
Overall Study
STARTED
4
Overall Study
COMPLETED
4
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Proof-of-Concept Safety Study of CPP-109 (Vigabatrin) for Treatment Refractory Tourette's Disorder

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Vigabatrin
n=4 Participants
3 tablets, bid for 8 weeks
Age, Continuous
34.75 years
n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
Sex: Female, Male
Male
3 Participants
n=5 Participants
YGTSS (total tic)
39 total tics
STANDARD_DEVIATION 3.67 • n=5 Participants

PRIMARY outcome

Timeframe: weekly from baseline to end of study (10weeks)

The Global Severity score is the sum of the Total Tic score and the TD Impairment score. It is rated by the Investigator on the Yale Global Tic Severity Score ( Y-GTSS, a widely accepted measure of drug efficacy in TD. Scale from 0- 100. Higher score indicates more impairment.

Outcome measures

Outcome measures
Measure
Vigabatrin
n=4 Participants
3 tablets, bid for 8 weeks
Global Severity Score on the Y-GTSS
Week 1
61 units on a scale
Interval 36.0 to 77.0
Global Severity Score on the Y-GTSS
Baseline
80.25 units on a scale
Interval 76.0 to 90.0
Global Severity Score on the Y-GTSS
Week 0
78.75 units on a scale
Interval 75.0 to 83.0
Global Severity Score on the Y-GTSS
Week 2
69.75 units on a scale
Interval 63.0 to 78.0
Global Severity Score on the Y-GTSS
Week 3
61 units on a scale
Interval 57.0 to 68.0
Global Severity Score on the Y-GTSS
Week 4
59 units on a scale
Interval 49.0 to 65.0
Global Severity Score on the Y-GTSS
Week 6
58.75 units on a scale
Interval 44.0 to 68.0
Global Severity Score on the Y-GTSS
Week 8
60.88 units on a scale
Interval 44.0 to 69.5
Global Severity Score on the Y-GTSS
Week 10
70.33 units on a scale
Interval 53.0 to 86.0

Adverse Events

Vigabatrin

Serious events: 0 serious events
Other events: 4 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Vigabatrin
n=4 participants at risk
3 tablets, bid for 8 weeks
General disorders
Fatigue
75.0%
3/4
General disorders
Appetite Increase
25.0%
1/4
General disorders
Sleep Difficulties
25.0%
1/4
Nervous system disorders
Increase in OCD symptoms
25.0%
1/4
General disorders
Dry mouth
25.0%
1/4
Nervous system disorders
Mood swings
25.0%
1/4
Nervous system disorders
Memory impairment
25.0%
1/4
General disorders
Daytime tiredness
25.0%
1/4
General disorders
Vivid dreams
25.0%
1/4
General disorders
Possible weight gain
25.0%
1/4
Eye disorders
Blurry Vision
25.0%
1/4

Additional Information

Dr. Barbara J. Coffey

Icahn School of Medicine at Mount Sinai

Phone: 212-659-1663

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place