Trial Outcomes & Findings for Stereotactic Radiosurgery or Other Local Ablation Then Erlotinib in Epidermal Growth Factor Receptor (EGFR) (NCT NCT01573702)

NCT ID: NCT01573702

Last Updated: 2021-01-12

Results Overview

Progression free survival (PFS) after locally ablative therapy and erlotinib in EGFR-mutant NSCLC patients who progressed on prior EGFR-tyrosine kinase inhibitor (TKI) therapy reported as percentage of participants who are alive and without progressive disease at 3 months. Progression is defined using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.1), as a 20% increase in the sum of the longest diameter of target lesions, or the appearance of new lesions.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

32 participants

Primary outcome timeframe

3 months after Initiation of Stereostatic Radiotherapy

Results posted on

2021-01-12

Participant Flow

32 participants were accrued from six institutions between 12/2012 and 6/2016

Of the 32 participants who consented to the study, 5 were determined to be not eligible and 2 withdrew consent prior to starting study treatment

Participant milestones

Participant milestones
Measure
Stereotactic Radiosurgery Followed by Erlotinib
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Overall Study
STARTED
25
Overall Study
COMPLETED
25
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Stereotactic Radiosurgery or Other Local Ablation Then Erlotinib in Epidermal Growth Factor Receptor (EGFR)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 Participants
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Age, Continuous
64 years
n=5 Participants
Sex: Female, Male
Female
16 Participants
n=5 Participants
Sex: Female, Male
Male
9 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
25 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
25 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
25 participants
n=5 Participants
Smoking status
Never smoker
16 Participants
n=5 Participants
Smoking status
Former smoker
7 Participants
n=5 Participants
Smoking status
Unknown
2 Participants
n=5 Participants
Performance status
0, Fully active
16 Participants
n=5 Participants
Performance status
1, Restricted in strenuous activity but ambulatory
9 Participants
n=5 Participants
Mutation type
Exon 19
14 Participants
n=5 Participants
Mutation type
Exon 21
7 Participants
n=5 Participants
Mutation type
Exon 19+ ALK rearrangement
1 Participants
n=5 Participants
Mutation type
Exon 18 and Exon 20
1 Participants
n=5 Participants
Mutation type
None proven; met clinical criteria
2 Participants
n=5 Participants
Charlson Co-morbidity Index
6 units on a scale
n=5 Participants

PRIMARY outcome

Timeframe: 3 months after Initiation of Stereostatic Radiotherapy

Progression free survival (PFS) after locally ablative therapy and erlotinib in EGFR-mutant NSCLC patients who progressed on prior EGFR-tyrosine kinase inhibitor (TKI) therapy reported as percentage of participants who are alive and without progressive disease at 3 months. Progression is defined using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.1), as a 20% increase in the sum of the longest diameter of target lesions, or the appearance of new lesions.

Outcome measures

Outcome measures
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 Participants
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Percentage of Participants With Progression Free Survival
64 percentage of participants
Interval 42.5 to 82.0

SECONDARY outcome

Timeframe: Initiation of Stereotactic Radiotherapy every 6 to 12 weeks until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 60 months

Population: 4 subjects were not evaluable for this outcome due to lack of follow-up measurements on ablated lesions

Count of subjects who had local control of sites previously progressive on erlotinib following SRS followed by erlotinib. Using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.1), local control is defined as Complete Response (CR), Disappearance of all target lesions; or Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; in sites ablated by SRS.

Outcome measures

Outcome measures
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=21 Participants
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Percentage of Participants With Local Control of Sites on Erlotinib Following Stereotactic Radiosurgery (SRS)
7 Participants

SECONDARY outcome

Timeframe: up to 5 years after end of treatment

To estimate overall survival (OS) after locally ablative therapy and erlotinib in EGFR-mutant, NSCLC patients who progressed on prior EGFR-TKI therapy measured as length of time from start of treatment until date of death from any cause

Outcome measures

Outcome measures
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 Participants
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Median Overall Survival
29 Months
Interval 21.7 to 36.3

SECONDARY outcome

Timeframe: From initiation to the end of SRS, up to 15 days

Population: Toxicities occurring in at least two participants from SRS are reported below

Toxicity of SRS will be measured by NCI CTCAE version 4 following completion of SRS, but prior to erlotinib re-initiation. The NCI Common Terminology Criteria for Adverse Events is a descriptive terminology which can be utilized for Adverse Event (AE) reporting. A grading (severity) scale is provided for each AE term. Grade 1 Mild; asymptomatic or mild symptoms; clinical or diagnostic observations only; intervention not indicated. Grade 2 Moderate; minimal, local or noninvasive intervention indicated; limiting age-appropriate instrumental Activities of Daily Living (ADL). Grade 3 Severe or medically significant but not immediately life-threatening; hospitalization or prolongation of hospitalization indicated; disabling; limiting self care ADL. Grade 4 Life-threatening consequences; urgent intervention indicated. Grade 5 Death related to AE.

Outcome measures

Outcome measures
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 Participants
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Fatigue · Grade 1
4 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Fatigue · Grade 2
0 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Fatigue · None
21 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Pain · Grade 1
2 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Pain · Grade 2
1 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Pain · None
22 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Anorexia · Grade 1
2 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Anorexia · Grade 2
0 Participants
Toxicity Rate From Stereotactic Radiosurgery (SRS)
Anorexia · None
23 Participants

SECONDARY outcome

Timeframe: from end of SRS to end of erlotinib treatment (median duration of 5.7 months)

Population: Toxicities grade 3 or higher and attributed to erlotinib re-treatment, or toxicities occurring in at least two participants are reported below

Toxicity of erlotinib will be graded using the NCI Common Terminology Criteria for Adverse Events (NCI CTCAE version 4) which is a descriptive terminology which can be utilized for Adverse Event (AE) reporting. A grading (severity) scale is provided for each AE term. Grade 1 Mild; asymptomatic or mild symptoms; clinical or diagnostic observations only; intervention not indicated. Grade 2 Moderate; minimal, local or noninvasive intervention indicated; limiting age-appropriate instrumental Activities of Daily Living (ADL). Grade 3 Severe or medically significant but not immediately life-threatening; hospitalization or prolongation of hospitalization indicated; disabling; limiting self care ADL. Grade 4 Life-threatening consequences; urgent intervention indicated. Grade 5 Death related to AE.

Outcome measures

Outcome measures
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 Participants
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Toxicity Rate Attributed to Erlotinib
Acneiform rash · Grade 1
5 Participants
Toxicity Rate Attributed to Erlotinib
Acneiform rash · Grade 2
2 Participants
Toxicity Rate Attributed to Erlotinib
Acneiform rash · Grade 3
2 Participants
Toxicity Rate Attributed to Erlotinib
Acneiform rash · None
16 Participants
Toxicity Rate Attributed to Erlotinib
Diarrhea · Grade 1
2 Participants
Toxicity Rate Attributed to Erlotinib
Diarrhea · Grade 3
0 Participants
Toxicity Rate Attributed to Erlotinib
Diarrhea · None
22 Participants
Toxicity Rate Attributed to Erlotinib
Fatigue · Grade 1
2 Participants
Toxicity Rate Attributed to Erlotinib
Fatigue · Grade 2
1 Participants
Toxicity Rate Attributed to Erlotinib
Fatigue · Grade 3
0 Participants
Toxicity Rate Attributed to Erlotinib
Fatigue · None
22 Participants
Toxicity Rate Attributed to Erlotinib
aspartate aminotransferase (AST) increased · Grade 1
2 Participants
Toxicity Rate Attributed to Erlotinib
aspartate aminotransferase (AST) increased · Grade 2
0 Participants
Toxicity Rate Attributed to Erlotinib
aspartate aminotransferase (AST) increased · Grade 3
0 Participants
Toxicity Rate Attributed to Erlotinib
aspartate aminotransferase (AST) increased · None
23 Participants
Toxicity Rate Attributed to Erlotinib
Nausea · Grade 1
2 Participants
Toxicity Rate Attributed to Erlotinib
Nausea · Grade 2
0 Participants
Toxicity Rate Attributed to Erlotinib
Nausea · Grade 3
0 Participants
Toxicity Rate Attributed to Erlotinib
Nausea · None
23 Participants
Toxicity Rate Attributed to Erlotinib
Paronychia · Grade 1
2 Participants
Toxicity Rate Attributed to Erlotinib
Paronychia · Grade 2
0 Participants
Toxicity Rate Attributed to Erlotinib
Paronychia · Grade 3
0 Participants
Toxicity Rate Attributed to Erlotinib
Paronychia · None
23 Participants
Toxicity Rate Attributed to Erlotinib
Weight loss · Grade 1
2 Participants
Toxicity Rate Attributed to Erlotinib
Weight loss · Grade 2
0 Participants
Toxicity Rate Attributed to Erlotinib
Weight loss · Grade 3
0 Participants
Toxicity Rate Attributed to Erlotinib
Weight loss · None
23 Participants
Toxicity Rate Attributed to Erlotinib
Diarrhea · Grade 2
1 Participants

Adverse Events

Stereotactic Radiosurgery Followed by Erlotinib

Serious events: 1 serious events
Other events: 24 other events
Deaths: 16 deaths

Serious adverse events

Serious adverse events
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 participants at risk
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Injury, poisoning and procedural complications
Fracture
4.0%
1/25 • Number of events 2 • From start of treatment to date of death up to 60 months
Injury, poisoning and procedural complications
Fall
4.0%
1/25 • Number of events 1 • From start of treatment to date of death up to 60 months

Other adverse events

Other adverse events
Measure
Stereotactic Radiosurgery Followed by Erlotinib
n=25 participants at risk
Stereotactic Radiosurgery or Other Local Ablation Followed by Erlotinib Stereotactic Radiosurgery: 21 Gy daily for 5 days Erlotinib: 150mg once daily
Gastrointestinal disorders
Abdominal pain
8.0%
2/25 • From start of treatment to date of death up to 60 months
Investigations
Alkaline phosphatase increased
4.0%
1/25 • From start of treatment to date of death up to 60 months
Metabolism and nutrition disorders
Anorexia
16.0%
4/25 • From start of treatment to date of death up to 60 months
Musculoskeletal and connective tissue disorders
Arthralgia
8.0%
2/25 • From start of treatment to date of death up to 60 months
Investigations
Aspartate aminotransferase increased
12.0%
3/25 • From start of treatment to date of death up to 60 months
Musculoskeletal and connective tissue disorders
Back pain
20.0%
5/25 • From start of treatment to date of death up to 60 months
Investigations
Blood bilirubin increased
4.0%
1/25 • From start of treatment to date of death up to 60 months
Eye disorders
Blurred vision
8.0%
2/25 • From start of treatment to date of death up to 60 months
Musculoskeletal and connective tissue disorders
Bone pain
4.0%
1/25 • From start of treatment to date of death up to 60 months
Injury, poisoning and procedural complications
Bruising
4.0%
1/25 • From start of treatment to date of death up to 60 months
Eye disorders
Conjunctivitis
4.0%
1/25 • From start of treatment to date of death up to 60 months
Respiratory, thoracic and mediastinal disorders
Cough
24.0%
6/25 • From start of treatment to date of death up to 60 months
Psychiatric disorders
Depression
4.0%
1/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Diarrhea
12.0%
3/25 • From start of treatment to date of death up to 60 months
Eye disorders
Dry eye
4.0%
1/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Dry skin
16.0%
4/25 • From start of treatment to date of death up to 60 months
Nervous system disorders
Dysgeusia
4.0%
1/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Dyspepsia
12.0%
3/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Dysphagia
4.0%
1/25 • From start of treatment to date of death up to 60 months
Ear and labyrinth disorders
Ear pain
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Edema face
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Edema limbs
8.0%
2/25 • From start of treatment to date of death up to 60 months
Respiratory, thoracic and mediastinal disorders
Epistaxis
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Fatigue
32.0%
8/25 • From start of treatment to date of death up to 60 months
Eye disorders
Flashing lights
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Flu like symptoms
4.0%
1/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Gastroesophageal reflux disease
4.0%
1/25 • From start of treatment to date of death up to 60 months
Nervous system disorders
Headache
12.0%
3/25 • From start of treatment to date of death up to 60 months
Vascular disorders
Hot flashes
4.0%
1/25 • From start of treatment to date of death up to 60 months
Metabolism and nutrition disorders
Hyperglycemia
16.0%
4/25 • From start of treatment to date of death up to 60 months
Metabolism and nutrition disorders
Hyperkalemia
4.0%
1/25 • From start of treatment to date of death up to 60 months
Metabolism and nutrition disorders
Hypernatremia
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Infusion site extravasation
4.0%
1/25 • From start of treatment to date of death up to 60 months
Psychiatric disorders
Insomnia
4.0%
1/25 • From start of treatment to date of death up to 60 months
Nervous system disorders
Lethargy
4.0%
1/25 • From start of treatment to date of death up to 60 months
Investigations
Lymphocyte count decreased
28.0%
7/25 • From start of treatment to date of death up to 60 months
Musculoskeletal and connective tissue disorders
Myalgia
8.0%
2/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Nail loss
4.0%
1/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Nail ridging
4.0%
1/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Nausea
12.0%
3/25 • From start of treatment to date of death up to 60 months
Musculoskeletal and connective tissue disorders
Neck pain
4.0%
1/25 • From start of treatment to date of death up to 60 months
Investigations
Neutrophil count decreased
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Non-cardiac chest pain
12.0%
3/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Oral hemorrhage
4.0%
1/25 • From start of treatment to date of death up to 60 months
General disorders
Pain
12.0%
3/25 • From start of treatment to date of death up to 60 months
Musculoskeletal and connective tissue disorders
Pain in extremity
12.0%
3/25 • From start of treatment to date of death up to 60 months
Infections and infestations
Papulopustular rash
4.0%
1/25 • From start of treatment to date of death up to 60 months
Infections and infestations
Paronychia
8.0%
2/25 • From start of treatment to date of death up to 60 months
Investigations
Platelet count decreased
4.0%
1/25 • From start of treatment to date of death up to 60 months
Respiratory, thoracic and mediastinal disorders
Pneumonitis
4.0%
1/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Pruritus
8.0%
2/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Rash acneiform
20.0%
5/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Rash maculo-papular
16.0%
4/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Skin and subcutaneous tissue disorders - Other, specify
8.0%
2/25 • From start of treatment to date of death up to 60 months
Skin and subcutaneous tissue disorders
Skin hyperpigmentation
4.0%
1/25 • From start of treatment to date of death up to 60 months
Infections and infestations
Skin infection
4.0%
1/25 • From start of treatment to date of death up to 60 months
Respiratory, thoracic and mediastinal disorders
Sore throat
4.0%
1/25 • From start of treatment to date of death up to 60 months
Infections and infestations
Upper respiratory infection
4.0%
1/25 • From start of treatment to date of death up to 60 months
Infections and infestations
Urinary tract infection
4.0%
1/25 • From start of treatment to date of death up to 60 months
Renal and urinary disorders
Urinary tract pain
8.0%
2/25 • From start of treatment to date of death up to 60 months
Renal and urinary disorders
Urinary urgency
4.0%
1/25 • From start of treatment to date of death up to 60 months
Gastrointestinal disorders
Vomiting
4.0%
1/25 • From start of treatment to date of death up to 60 months
Eye disorders
Watering eyes
8.0%
2/25 • From start of treatment to date of death up to 60 months
Investigations
Weight loss
8.0%
2/25 • From start of treatment to date of death up to 60 months
Respiratory, thoracic and mediastinal disorders
Wheezing
8.0%
2/25 • From start of treatment to date of death up to 60 months
Investigations
White blood cell decreased
4.0%
1/25 • From start of treatment to date of death up to 60 months

Additional Information

Robin V. Johnson

UNC Lineberger Comprehensive Cancer Center

Phone: 919-966-1125

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place