Trial Outcomes & Findings for High Dose Lurasidone for Patients With Treatment Resistant Schizophrenia (NCT NCT01569659)

NCT ID: NCT01569659

Last Updated: 2025-02-28

Results Overview

Specify Full Scale Name and Construct: Positive and Negative Symptom Scale (PANSS) Scale description: A 45-minute clinical interview is conducted. The patient is rated from 1 to 7 on 30 different symptoms based on the interview as well as reports of family members or primary care hospital workers. These 30 items are split into three categories (Positive, Negative and General Psychopathology symptoms of schizophrenia), and the information is used to evaluate the presence, absence and severity of each. A score of 1 on an item indicates the absence of the symptom, up to a 7 which indicates the presence of the symptom is extreme. The minimum and maximum for the whole scale would be 30-210, and for each of the three categories are as follows: Positive scale (7 Items)--minimum score = 7, maximum score = 49; Negative scale (7 Items)--minimum score = 7, maximum score = 49; General Psychopathology scale (16 Items)--minimum score = 16, maximum score = 112.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

101 participants

Primary outcome timeframe

Baseline to end of randomized phase (24 weeks)

Results posted on

2025-02-28

Participant Flow

101 subject were enrolled in phase 1 for a period of 6 weeks to determine Treatment Resistant Status (TRS). 34 determined NOT TRS so were discontinued. The remaining 67 moved to phase 2. 34 remained in standard dose of Lurasidone and 44 were on High dose Lurasidone.

Participant milestones

Participant milestones
Measure
Standard Dose of Lurasidone
Only those patients who still have persistent moderate to severe positive symptoms, even if they have shown some improvement at 80 mg/day will proceed to phase II (randomization). In phase II, 30 subjects will be randomized to continue 80 mg lurasidone. Lurasidone: 80 mg/day for up to 30 weeks
High Dose of Lurasidone
In phase II, 40 patients will initiate a titration schedule, beginning at 120 mg at week 7. The high-dose group will be increased an additional 40 mg/day every week, thereafter, to a total of 240 mg/day, if adequately tolerated, which would include a worsening of psychopathology as assessed by the PANSS or Clinical Global Impressions-Severity (CGI-S). The dose will remain at 240/day, or the highest dose tolerated, for a duration of 6 months from the time the 120 mg/day dose was initiated. Lurasidone: Up to 240 mg/day for up to 30 weeks
Overall Study
STARTED
34
33
Overall Study
COMPLETED
22
22
Overall Study
NOT COMPLETED
12
11

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

High Dose Lurasidone for Patients With Treatment Resistant Schizophrenia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Standard Dose of Lurasidone
n=34 Participants
Only those patients who still have persistent moderate to severe positive symptoms, even if they have shown some improvement at 80 mg/day will proceed to phase II (randomization). In phase II, 30 subjects will be randomized to continue 80 mg lurasidone. Lurasidone: 80 mg/day for up to 30 weeks
High Dose of Lurasidone
n=33 Participants
In phase II, 40 patients will initiate a titration schedule, beginning at 120 mg at week 7. The high-dose group will be increased an additional 40 mg/day every week, thereafter, to a total of 240 mg/day, if adequately tolerated, which would include a worsening of psychopathology as assessed by the PANSS or CGI-S. The dose will remain at 240/day, or the highest dose tolerated, for a duration of 6 months from the time the 120 mg/day dose was initiated. Lurasidone: Up to 240 mg/day for up to 30 weeks
Total
n=67 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
34 Participants
n=5 Participants
33 Participants
n=7 Participants
67 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Continuous
47 years
STANDARD_DEVIATION 10.7 • n=5 Participants
45.2 years
STANDARD_DEVIATION 11.9 • n=7 Participants
46.1 years
STANDARD_DEVIATION 11.4 • n=5 Participants
Sex: Female, Male
Female
20 Participants
n=5 Participants
18 Participants
n=7 Participants
38 Participants
n=5 Participants
Sex: Female, Male
Male
14 Participants
n=5 Participants
15 Participants
n=7 Participants
29 Participants
n=5 Participants
Region of Enrollment
United States
34 participants
n=5 Participants
33 participants
n=7 Participants
67 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline to end of randomized phase (24 weeks)

Population: Participants with baseline persistent moderate to severe positive symptoms

Specify Full Scale Name and Construct: Positive and Negative Symptom Scale (PANSS) Scale description: A 45-minute clinical interview is conducted. The patient is rated from 1 to 7 on 30 different symptoms based on the interview as well as reports of family members or primary care hospital workers. These 30 items are split into three categories (Positive, Negative and General Psychopathology symptoms of schizophrenia), and the information is used to evaluate the presence, absence and severity of each. A score of 1 on an item indicates the absence of the symptom, up to a 7 which indicates the presence of the symptom is extreme. The minimum and maximum for the whole scale would be 30-210, and for each of the three categories are as follows: Positive scale (7 Items)--minimum score = 7, maximum score = 49; Negative scale (7 Items)--minimum score = 7, maximum score = 49; General Psychopathology scale (16 Items)--minimum score = 16, maximum score = 112.

Outcome measures

Outcome measures
Measure
Standard Dose of Lurasidone
n=34 Participants
Only those patients who still have persistent moderate to severe positive symptoms, even if they have shown some improvement at 80 mg/day will proceed to phase II (randomization). In phase II, 30 subjects will be randomized to continue 80 mg lurasidone. Lurasidone: 80 mg/day for up to 30 weeks
High Dose of Lurasidone
n=33 Participants
In phase II, 40 patients will initiate a titration schedule, beginning at 120 mg at week 7. The high-dose group will be increased an additional 40 mg/day every week, thereafter, to a total of 240 mg/day, if adequately tolerated, which would include a worsening of psychopathology as assessed by the PANSS or CGI-S. The dose will remain at 240/day, or the highest dose tolerated, for a duration of 6 months from the time the 120 mg/day dose was initiated. Lurasidone: Up to 240 mg/day for up to 30 weeks
Change in Positive Symptoms of Schizophrenia
22.6 units on a scale
Standard Deviation 3.3
24.2 units on a scale
Standard Deviation 4.3

Adverse Events

Standard Dose of Lurasidone

Serious events: 0 serious events
Other events: 28 other events
Deaths: 0 deaths

High Dose of Lurasidone

Serious events: 1 serious events
Other events: 30 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Standard Dose of Lurasidone
n=34 participants at risk
Only those patients who still have persistent moderate to severe positive symptoms, even if they have shown some improvement at 80 mg/day will proceed to phase II (randomization). In phase II, 30 subjects will be randomized to continue 80 mg lurasidone. Lurasidone: 80 mg/day for up to 30 weeks
High Dose of Lurasidone
n=33 participants at risk
In phase II, 40 patients will initiate a titration schedule, beginning at 120 mg at week 7. The high-dose group will be increased an additional 40 mg/day every week, thereafter, to a total of 240 mg/day, if adequately tolerated, which would include a worsening of psychopathology as assessed by the PANSS or CGI-S. The dose will remain at 240/day, or the highest dose tolerated, for a duration of 6 months from the time the 120 mg/day dose was initiated. Lurasidone: Up to 240 mg/day for up to 30 weeks
Cardiac disorders
Death
0.00%
0/34
3.0%
1/33 • Number of events 1

Other adverse events

Other adverse events
Measure
Standard Dose of Lurasidone
n=34 participants at risk
Only those patients who still have persistent moderate to severe positive symptoms, even if they have shown some improvement at 80 mg/day will proceed to phase II (randomization). In phase II, 30 subjects will be randomized to continue 80 mg lurasidone. Lurasidone: 80 mg/day for up to 30 weeks
High Dose of Lurasidone
n=33 participants at risk
In phase II, 40 patients will initiate a titration schedule, beginning at 120 mg at week 7. The high-dose group will be increased an additional 40 mg/day every week, thereafter, to a total of 240 mg/day, if adequately tolerated, which would include a worsening of psychopathology as assessed by the PANSS or CGI-S. The dose will remain at 240/day, or the highest dose tolerated, for a duration of 6 months from the time the 120 mg/day dose was initiated. Lurasidone: Up to 240 mg/day for up to 30 weeks
Gastrointestinal disorders
Nausea
23.5%
8/34 • Number of events 8
27.3%
9/33 • Number of events 9
Nervous system disorders
Insomnia
17.6%
6/34 • Number of events 6
12.1%
4/33 • Number of events 4
Gastrointestinal disorders
Vomiting
11.8%
4/34 • Number of events 4
6.1%
2/33 • Number of events 2
Musculoskeletal and connective tissue disorders
Back pain
14.7%
5/34 • Number of events 5
6.1%
2/33 • Number of events 2
Nervous system disorders
Headache
8.8%
3/34 • Number of events 3
15.2%
5/33 • Number of events 5
Nervous system disorders
Suicidality
5.9%
2/34 • Number of events 2
9.1%
3/33 • Number of events 3
Gastrointestinal disorders
Dry mouth
8.8%
3/34 • Number of events 3
3.0%
1/33 • Number of events 1
Nervous system disorders
Akathasia
5.9%
2/34 • Number of events 2
9.1%
3/33 • Number of events 3
Infections and infestations
Coughing
5.9%
2/34 • Number of events 2
6.1%
2/33 • Number of events 2
Gastrointestinal disorders
Emesis
5.9%
2/34 • Number of events 2
3.0%
1/33 • Number of events 1
Metabolism and nutrition disorders
Weight gain
5.9%
2/34 • Number of events 2
0.00%
0/33
Nervous system disorders
Aggression
0.00%
0/34
6.1%
2/33 • Number of events 2
Metabolism and nutrition disorders
Hypnatremia
0.00%
0/34
6.1%
2/33 • Number of events 2

Additional Information

Herbert Meltzer, MD

Northwestern University

Phone: 312-503-9096

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place