Trial Outcomes & Findings for Trial Comparing the Effects of Intermittent Vismodegib vs. PDT in Patients With Multiple Basal Cell Carcinomas (NCT NCT01556009)

NCT ID: NCT01556009

Last Updated: 2020-11-02

Results Overview

Primary: i. To compare the efficacy of (i) intermittent vismodegib vs. (ii) the efficacy of photodynamic therapy (PDT) in preventing the return of the burden of surgically eligible BCCs (SEBs) to baseline level following 7 months of continuous vismodegib therapy. ii. To compare the cumulative diameter (burden) of SEBs in patients treated intermittently with vismodegib vs. with photodynamic therapy (PDT).

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

24 participants

Primary outcome timeframe

A Data Safety Monitoring Board (DSMB) will review results for an interim analysis when 12 subjects have completed 28 months.

Results posted on

2020-11-02

Participant Flow

The PI has left the institution and sincere efforts were made to contact the PI, but were unsuccessful. No data are available to report.

Participant milestones

Participant milestones
Measure
Drug (Vismodegib)
Vismodegib taken orally 150 mg per day for 7 continuous months then randomized for 3 month intervals to 28 months. Vismodegib: 150 mg per day for 7 continuous months then randomized for 3 month intervals to 28 months.
Aminolevulinic Acid %20 Topical Solution
Aminolevulinic acid HCL 20% topical solution applied every three months from month 10, 13, 16, 19, 22. Applied and incubated for three hours. Aminolevulinic acid %20 topical solution: 20% topical solution applied every three months from month 10, 13, 16, 19, 22. Applied and incubated for three hours.
Overall Study
STARTED
0
0
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Trial Comparing the Effects of Intermittent Vismodegib vs. PDT in Patients With Multiple Basal Cell Carcinomas

Baseline characteristics by cohort

Baseline data not reported

PRIMARY outcome

Timeframe: A Data Safety Monitoring Board (DSMB) will review results for an interim analysis when 12 subjects have completed 28 months.

Population: The PI has left the institution and sincere efforts were made to contact the PI, but were unsuccessful. No data are available to report.

Primary: i. To compare the efficacy of (i) intermittent vismodegib vs. (ii) the efficacy of photodynamic therapy (PDT) in preventing the return of the burden of surgically eligible BCCs (SEBs) to baseline level following 7 months of continuous vismodegib therapy. ii. To compare the cumulative diameter (burden) of SEBs in patients treated intermittently with vismodegib vs. with photodynamic therapy (PDT).

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: A Data Safety Monitoring Board (DSMB) will review results for an interim analysis when 12 subjects have completed 28 months.

Population: The PI has left the institution and sincere efforts were made to contact the PI, but were unsuccessful. No data are available to report.

i. To assess the safety of intermittent vismodegib in patients with multiple BCCs (BCNS and non-BCNS) during months 8-28. ii. To assess resistance of SEBs to treatments in patients with multiple BCCs (BCNS and non-BCNS) treated intermittently during months 8-28. iii. To assess the degree of reduction of SEBs after 7 months of continuous daily vismodegib therapy. iv. To conduct an exploratory evaluation in non-BCNS patients with multiple BCCs (high burden of disease) of the efficacy and tolerability of intermittent vismodegib vs PDT

Outcome measures

Outcome data not reported

Adverse Events

Drug (Vismodegib)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Aminolevulinic Acid %20 Topical Solution

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Ervin H Epstein Jr., MD

Children's Hospital of Oakland Research Institute, Oakland

Phone: 510-450-5688

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place