Trial Outcomes & Findings for Botulinum Toxin for Pelvic Pain in Women With Endometriosis (NCT NCT01553201)

NCT ID: NCT01553201

Last Updated: 2020-07-28

Results Overview

Self reported improvement in pain symptoms - a binary measurement of improvement/no improvement

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

30 participants

Primary outcome timeframe

1 month

Results posted on

2020-07-28

Participant Flow

Participant milestones

Participant milestones
Measure
Botulinum Toxin (BoNT)
OnabotulinumtoxinA 100 Units diluted in 4cc saline, one time intramuscular administration
Placebo
Saline, 4cc, one time intramuscular administration
Overall Study
STARTED
15
15
Overall Study
COMPLETED
15
15
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Botulinum Toxin for Pelvic Pain in Women With Endometriosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Botulinum Toxin (BoNT)
n=15 Participants
OnabotulinumtoxinA 100 Units diluted in 4cc saline, one time intramuscular administration
Placebo
n=14 Participants
Saline, 4cc, one time intramuscular administration
Total
n=29 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
15 Participants
n=5 Participants
14 Participants
n=7 Participants
29 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Female
15 Participants
n=5 Participants
14 Participants
n=7 Participants
29 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=5 Participants
3 Participants
n=7 Participants
4 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
14 Participants
n=5 Participants
11 Participants
n=7 Participants
25 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
White
10 Participants
n=5 Participants
13 Participants
n=7 Participants
23 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 month

Self reported improvement in pain symptoms - a binary measurement of improvement/no improvement

Outcome measures

Outcome measures
Measure
Botulinum Toxin (BoNT)
n=15 Participants
OnabotulinumtoxinA 100 Units diluted in 4cc saline, one time intramuscular administration
Placebo
n=14 Participants
Saline, 4cc, one time intramuscular administration
Number of Participants With Improvement in Pain
11 Participants
4 Participants

Adverse Events

Botulinum Toxin (BoNT)

Serious events: 0 serious events
Other events: 7 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Botulinum Toxin (BoNT)
n=15 participants at risk
OnabotulinumtoxinA 100 Units diluted in 4cc saline, one time intramuscular administration
Placebo
n=15 participants at risk
Saline, 4cc, one time intramuscular administration
Nervous system disorders
Muscular weakness
0.00%
0/15 • 1 month
6.7%
1/15 • Number of events 1 • 1 month
Nervous system disorders
Migraine
6.7%
1/15 • Number of events 1 • 1 month
6.7%
1/15 • Number of events 1 • 1 month
Renal and urinary disorders
Urinary hesitation
13.3%
2/15 • Number of events 2 • 1 month
0.00%
0/15 • 1 month
Renal and urinary disorders
Micturition urgency
6.7%
1/15 • Number of events 1 • 1 month
0.00%
0/15 • 1 month
Nervous system disorders
Pelvic pain
20.0%
3/15 • Number of events 3 • 1 month
0.00%
0/15 • 1 month

Additional Information

Barbara Karp, MD

National Institute of Neurological Disorders & Stroke

Phone: 301-496-0150

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place