A Study to Evaluate the Efficacy and Safety of VX-765 in Subjects With Treatment-Resistant Partial Epilepsy

NCT ID: NCT01501383

Last Updated: 2020-09-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

55 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to evaluate the efficacy, safety and tolerability of VX-765 in subjects with treatment-resistant partial epilepsy.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Epilepsy

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

VX-765 Dose 1 Part A

Group Type ACTIVE_COMPARATOR

VX-765 Part A

Intervention Type DRUG

Tablets of VX-765 given at different doses based on treatment group in Part A

VX-765 Dose 2 Part A

Group Type ACTIVE_COMPARATOR

VX-765 Part A

Intervention Type DRUG

Tablets of VX-765 given at different doses based on treatment group in Part A

VX-765 Dose 3 Part A

Group Type ACTIVE_COMPARATOR

VX-765 Part A

Intervention Type DRUG

Tablets of VX-765 given at different doses based on treatment group in Part A

VX-765 Dose 4 Part A

Group Type ACTIVE_COMPARATOR

VX-765 Part A

Intervention Type DRUG

Tablets of VX-765 given at different doses based on treatment group in Part A

Placebo Dose Part A

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo

VX-765 Dose Part B

Group Type ACTIVE_COMPARATOR

VX-765 Part B

Intervention Type DRUG

Tablets of VX-765 given at different doses based on patients who meet the study eligibility criteria for Part B

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

VX-765 Part A

Tablets of VX-765 given at different doses based on treatment group in Part A

Intervention Type DRUG

Placebo

Matching placebo

Intervention Type DRUG

VX-765 Part B

Tablets of VX-765 given at different doses based on patients who meet the study eligibility criteria for Part B

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Males or females aged 18 to 64 years with a body mass index between 18 and 35 (kg/m2)
* Subjects who have completed the assigned study treatment in Part A may enter Part B if eligible per protocol
* Male or female subjects must agree to use acceptable contraceptive methods, as described in the protocol
* Must have a diagnosis and history of treatment-resistant partial-onset epilepsy for which they are taking 1 to 4 concomitant AEDs at the time of Screening Period
* Have had at least 1 electroencephalogram consistent with partial epilepsy
* Must have had at least 6 partial-onset seizures and a seizure-free period of no more than 3 weeks (21 days) during the Baseline Period.
* Subjects with stable medical conditions (e.g., cannot have a condition that will interfere with the conduct of the study or cause a known increase in risk of the intervention) as determined by the principal investigator
* Must be able and willing to provide written informed consent to participate
* Must be able to understand and comply with protocol requirements and instructions

Exclusion Criteria

* Subjects who are male and their female partner (if of childbearing potential) does not agree to use medically approved methods of contraception as described in the protocol for the duration od the study and for 90 days after last dose of study drug
* Subjects who are male and have a female partner who is pregnant, nursing, or is planning to become pregnant during the study period, or within 90 days of the last dose of study drug.
* Subjects who are pregnant or lactating, or who are of reproductive potential who do not agree to use medically approved birth control methods
* History of nonepileptic, transient alterations in consciousness
* History of status epilepticus in the past 12 months before the screening visit
* Subjects whose seizure frequency cannot be quantified (i.e. seizures with no discrete beginning or end, or period between seizures)
* Subjects who have a significant medical illness including kidney, liver, pulmonary, or gastrointestinal disease; or unstable or poorly controlled conditions such as hypertension, diabetes, or angina pectoris, as judged by the investigator.
* Have a clinically significant psychiatric illness as judged by the investigator
* Subjects who have had an active suicidal plan/intent or active suicidal thoughts, or suicide attempt as defined in the protocol
* Clinically significant laboratory abnormalities during the Screening Visit/Baseline Period, as judged by the investigator
* Subjects who have had serious adverse events (SAEs) thought to be related to study drug that led to discontinuation during Part A may not participate in Part B
* Active hepatitis B, hepatitis C, or human immunodeficiency virus
* Positive drug screen at screening or during the Baseline Period (excluding any allowed prescribed medications) and/or a history of alcoholism or drug addiction within past 2 years
* Subjects on felbamate with fewer than 18 month of continuous felbamate exposure at the time of the Screening Visit or with significant adverse reactions to felbamate
* Subjects treated with vigabatrin fewer than 2 years prior to the Screening Visit or who have a prior history of treatment with vigabatrin without a documented stable examination by an ophthalmologist as defined in the protocol
* Using prohibited medications or treated with any systemic immunosuppressant
* Have experienced a symptomatic viral, fungal, or bacterial infection requiring systemic treatment within 7 days prior to the first dose of study drug
* A current or prior history of illness precluding them from immunomodulatory therapy (e.g., history of recurrent infections)
* Have donated any blood or have had a significant loss of blood (500 mL) as defined in the protocol
* Have participated in any other clinical studies involving an investigational product or device and have received the last dose of the study drug associated with that clinical study within 30 days or 5 half-lives (whichever is longer) of the Screening Visit
* Have participated in earlier VX-765 clinical studies and received at least one dose of study drug
* Subjects who have no completed the full 13-week Treatment Period in part A may not participate in Part B
* Any subject judged by the investigator, sponsor or designee to be inappropriate for the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

64 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Vertex Pharmaceuticals Incorporated

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Alabama

Northport, Alabama, United States

Site Status

Arizona

Phoenix, Arizona, United States

Site Status

Arizon

Phoenix, Arizona, United States

Site Status

Arkansas

Little Rock, Arkansas, United States

Site Status

California

Loma Linda, California, United States

Site Status

Florida

Bradenton, Florida, United States

Site Status

Florida

Wellington, Florida, United States

Site Status

Idaho

Boise, Idaho, United States

Site Status

Maryland

Baltimore, Maryland, United States

Site Status

Michigan

Farmington Hills, Michigan, United States

Site Status

Minnesota

Saint Paul, Minnesota, United States

Site Status

New York

New York, New York, United States

Site Status

New York

The Bronx, New York, United States

Site Status

North Carolina

Asheville, North Carolina, United States

Site Status

North Carolina

Charlotte, North Carolina, United States

Site Status

Ohio

Columbus, Ohio, United States

Site Status

Oklahoma

Oklahoma City, Oklahoma, United States

Site Status

Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Texas

Dallas, Texas, United States

Site Status

Utah

Orem, Utah, United States

Site Status

Virginia

Charlottesville, Virginia, United States

Site Status

Washington

Renton, Washington, United States

Site Status

Germany

Bonn, , Germany

Site Status

Germany

Kork, , Germany

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Germany

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

VX11-765-402

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Long-term Safety and Tolerability of BHV-7000
NCT06443463 ENROLLING_BY_INVITATION PHASE2
Clinical Trial of Vormatrigine in Adult Patients With Epilepsy
NCT07287163 ENROLLING_BY_INVITATION PHASE3