Safety and Efficacy of Carboplatin/Paclitaxel and Carboplatin/Paclitaxel/Bevacizumab With and Without Pictilisib in Previously Untreated Advanced or Recurrent Non-small Cell Lung Cancer

NCT ID: NCT01493843

Last Updated: 2017-04-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

501 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-01-20

Study Completion Date

2016-03-30

Brief Summary

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This multicenter, randomized, double-blind, placebo-controlled trial will evaluate the efficacy and safety of carboplatin/paclitaxel and carboplatin/paclitaxel/bevacizumab with and without pictilisib in particpants with previously untreated advanced or recurrent non-small cell lung cancer (NSCLC). Particpants will be randomized to receive 4 cycles of carboplatin (C)/paclitaxel (P) and either pictilisib or placebo, with (participants with non-squamous NSCLC) or without (participants with squamous NSCLC) bevacizumab (B). Anticipated time on study treatment is until disease progression or intolerable toxicity occurs. Participants in placebo arms with disease progression may cross over to open-label active pictilisib.

Detailed Description

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Conditions

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Non-Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Arm A: 340 mg pictilisib + CP

Participants with advanced (Stage IV) or recurrent squamous NSCLC will be administered 340 mg pictilisib plus carboplatin (C) plus paclitaxel (P).

Group Type EXPERIMENTAL

pictilisib

Intervention Type DRUG

Pictilisib, 260 milligrams (mg) or 340 mg, will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, pictilisib will be taken once daily continuously.

carboplatin

Intervention Type DRUG

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

paclitaxel

Intervention Type DRUG

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Arm B: Placebo + CP

Participants with advanced (Stage IV) or recurrent squamous NSCLC will be administered placebo corresponding to 340 mg pictilisib plus carboplatin (C) plus paclitaxel (P). Participants with investigator assessed radiographic progression of NSCLC per RECIST 1.1 will be allowed to cross over to Arm A during the first 4 cycles with carboplatin + paclitaxel or after chemotherapy has been completed (Cycle \>/= 5).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo corresponding to 260 mg or 340 mg pictilisib will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, placebo will be taken once daily continuously.

carboplatin

Intervention Type DRUG

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

paclitaxel

Intervention Type DRUG

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Arm C: 340 mg pictilisib + CPB

Participants with advanced (Stage IV) or recurrent non-squamous NSCLC will be administered 340 mg pictilisib plus carboplatin (C) plus paclitaxel (P) plus bevacizumab (B).

Group Type EXPERIMENTAL

pictilisib

Intervention Type DRUG

Pictilisib, 260 milligrams (mg) or 340 mg, will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, pictilisib will be taken once daily continuously.

bevacizumab

Intervention Type DRUG

Bevacizumab, 15 milligrams per kilogram (mg/kg) will be administered intravenously (IV) at Day 1 of each 21-day cycle for a maximum of 34 cycles.

carboplatin

Intervention Type DRUG

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

paclitaxel

Intervention Type DRUG

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Arm D: Placebo + CPB

Participants with advanced (Stage IV) or recurrent non-squamous NSCLC will be administered placebo corresponding to 340 mg pictilisib plus carboplatin (C) plus paclitaxel (P). Participants with investigator assessed radiographic progression of NSCLC per RECIST 1.1 will be allowed to cross over to Arm C during the first 4 cycles with carboplatin + paclitaxel + bevacizumab or after chemotherapy has been completed (Cycle \>/= 5).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo corresponding to 260 mg or 340 mg pictilisib will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, placebo will be taken once daily continuously.

bevacizumab

Intervention Type DRUG

Bevacizumab, 15 milligrams per kilogram (mg/kg) will be administered intravenously (IV) at Day 1 of each 21-day cycle for a maximum of 34 cycles.

carboplatin

Intervention Type DRUG

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

paclitaxel

Intervention Type DRUG

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Arm E: 260 mg pictilisib + CPB

Participants with advanced (Stage IV) or recurrent non-squamous NSCLC will be administered 260 mg pictilisib plus carboplatin (C) plus paclitaxel (P) plus bevacizumab (B).

Group Type EXPERIMENTAL

pictilisib

Intervention Type DRUG

Pictilisib, 260 milligrams (mg) or 340 mg, will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, pictilisib will be taken once daily continuously.

bevacizumab

Intervention Type DRUG

Bevacizumab, 15 milligrams per kilogram (mg/kg) will be administered intravenously (IV) at Day 1 of each 21-day cycle for a maximum of 34 cycles.

carboplatin

Intervention Type DRUG

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

paclitaxel

Intervention Type DRUG

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Arm F: Placebo + CPB

Participants with advanced (Stage IV) or recurrent non-squamous NSCLC will be administered placebo corresponding to 260 mg pictilisib plus carboplatin (C) plus paclitaxel (P). Participants with investigator assessed radiographic progression of NSCLC per RECIST 1.1 will be allowed to cross over to Arm E during the first 4 cycles with carboplatin + paclitaxel + bevacizumab or after chemotherapy has been completed (Cycle \>/= 5).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo corresponding to 260 mg or 340 mg pictilisib will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, placebo will be taken once daily continuously.

bevacizumab

Intervention Type DRUG

Bevacizumab, 15 milligrams per kilogram (mg/kg) will be administered intravenously (IV) at Day 1 of each 21-day cycle for a maximum of 34 cycles.

carboplatin

Intervention Type DRUG

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

paclitaxel

Intervention Type DRUG

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Interventions

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pictilisib

Pictilisib, 260 milligrams (mg) or 340 mg, will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, pictilisib will be taken once daily continuously.

Intervention Type DRUG

Placebo

Placebo corresponding to 260 mg or 340 mg pictilisib will be taken orally once daily on Days 1-14 of a 21-day cycle for four cycles. Starting with Cycle 5, placebo will be taken once daily continuously.

Intervention Type DRUG

bevacizumab

Bevacizumab, 15 milligrams per kilogram (mg/kg) will be administered intravenously (IV) at Day 1 of each 21-day cycle for a maximum of 34 cycles.

Intervention Type DRUG

carboplatin

Carboplatin will be administered IV to achieve an initial target area under the concentration curve (AUC) of 6 milligrams per milliliter per minute (mg/mL per min) on Day 1 of each 21-day cycle for a maximum of four cycles.

Intervention Type DRUG

paclitaxel

Paclitaxel will be administered at 200 milligrams per square meter (mg/m\^2) IV on Day 1 of each 21-day cycle for a maximum of four cycles.

Intervention Type DRUG

Other Intervention Names

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GDC-0941 Avastin

Eligibility Criteria

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Inclusion Criteria

* Histologically documented advanced (Stage IV) or recurrent squamous (Arms A and B) or non-squamous (Arms C, D, E, and F) non-small cell lung cancer (NSCLC)
* Consent to the collection of an archival formalin-fixed paraffin-embedded (FFPE) block or freshly cut unstained tumor slides from archival tumor tissue or a newly collected tumor sample
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
* Disease that is measurable per Response Evaluation Criteria In Solid Tumors (RECIST) v1.1
* Adequate hematologic and end organ function
* Use of two effective forms of contraception

Exclusion Criteria

* NSCLC with documented epidermal growth factor receptor (EGFR) mutation associated with response to EGFR inhibitors or documented fusion gene involving anaplastic lymphoma kinase (ALK) gene
* Prior therapy (including chemotherapy, antibody therapy, tyrosine kinase inhibitors, radiotherapy, immunotherapy, hormonal therapy, or investigational therapy) before Day 1 of Cycle 1 for the treatment of advanced (Stage IV) or recurrent NSCLC
* Known central nervous system (CNS) disease except for treated brain metastases
* Type I diabetes
* Type II diabetes requiring chronic therapy with insulin
* Any other diseases, metabolic dysfunction, physical examination finding, or clinical laboratory finding giving reasonable suspicion of a disease or condition that contraindicates the use of an investigational drug or that may affect the interpretation of the results or render the participant at high risk for treatment complications
* Medical conditions that would contraindicate bevacizumab therapy in non-squamous NSCLC (Arms C, D, E, and F)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Alabama Oncology

Birmingham, Alabama, United States

Site Status

Highlands Oncology Group

Rogers, Arkansas, United States

Site Status

cCare

Encinitas, California, United States

Site Status

Kaiser Permanente - Oakland

Oakland, California, United States

Site Status

Desert Hematology Oncology Group

Rancho Mirage, California, United States

Site Status

Kaiser Permanente - Roseville

Roseville, California, United States

Site Status

Kaiser Permanente Sacramento Medical Center

Sacramento, California, United States

Site Status

Southern CA Permanente Med Grp

San Diego, California, United States

Site Status

Kaiser Permanente

San Francisco, California, United States

Site Status

K. Permanente - Santa Clara

Santa Clara, California, United States

Site Status

Stockton Hema Onc Med Grp Inc

Stockton, California, United States

Site Status

Kaiser Permanente - Vallejo

Vallejo, California, United States

Site Status

K. Permanente - Walnut Creek

Walnut Creek, California, United States

Site Status

Hematology Oncology PC; Bennett Cancer Center

Stamford, Connecticut, United States

Site Status

Lynn Regional Cancer Center West

Boca Raton, Florida, United States

Site Status

Florida Cancer Specialists - Fort Myers (Colonial Center Dr)

Fort Myers, Florida, United States

Site Status

Cancer Specialists; North Florida ;Jacksonville (AC Skinner Pkwy)

Jacksonville, Florida, United States

Site Status

Advanced Medical Specialties

Miami, Florida, United States

Site Status

Florida Cancer Specialists (St. Petersburg - St. Anthony's Professional Building)

St. Petersburg, Florida, United States

Site Status

University Cancer & Blood Center, LLC

Athens, Georgia, United States

Site Status

Peachtree Hematology & Oncology Consultants, Pc

Atlanta, Georgia, United States

Site Status

Georgia Cancer Specialists

Atlanta, Georgia, United States

Site Status

Hematology-Oncology of Indiana, Pc

Indianapolis, Indiana, United States

Site Status

Franklin Square Hospital

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital.

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Inst.

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Wayne State University; Hemat/Onc, 4HW CRC

Detroit, Michigan, United States

Site Status

Nebraska Methodist Hospital

Omaha, Nebraska, United States

Site Status

Va Sierra Nevada Health Care System

Reno, Nevada, United States

Site Status

San Juan Oncology Associates

Farmington, New Mexico, United States

Site Status

Roswell Park Cancer Inst.

Buffalo, New York, United States

Site Status

Piedmont Hematology Oncology Associates

Winston-Salem, North Carolina, United States

Site Status

Gabrail Cancer Center

Canton, Ohio, United States

Site Status

The Christ Hospital

Cincinnati, Ohio, United States

Site Status

Univ Hosp Case Medical Center

Cleveland, Ohio, United States

Site Status

Center for Biomedical Research LLC

Knoxville, Tennessee, United States

Site Status

The Sarah Cannon Research Inst

Nashville, Tennessee, United States

Site Status

Vanderbilt

Nashville, Tennessee, United States

Site Status

University of Texas M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

Wellmonth Physician Services

Bristol, Virginia, United States

Site Status

Blue Ridge Cancer Care - Roanoke

Roanoke, Virginia, United States

Site Status

VA Puget Sound Health Care Sys

Seattle, Washington, United States

Site Status

Northwest Medical Specialties

Tacoma, Washington, United States

Site Status

Clinica Universitaria Reina Fabiola

Córdoba, , Argentina

Site Status

Instituto FIDES

La Plata, , Argentina

Site Status

Isis Centro Especializado de Luces; Oncology

Santa Fe, , Argentina

Site Status

Royal Prince Alfred Hospital; Sydney Cancer Centre

Camperdown, New South Wales, Australia

Site Status

St Vincent'S Hospital

Darlinghurst, New South Wales, Australia

Site Status

Calvary Mater Newcastle; Medical Oncology

Waratah, New South Wales, Australia

Site Status

Flinders Medical Centre; Medical Oncology

Bedford Park, South Australia, Australia

Site Status

Royal Hobart Hospital; Medical Oncology

Hobart, Tasmania, Australia

Site Status

Footscray Hospital

Footscray, Victoria, Australia

Site Status

Royal Melbourne Hospital; Hematology and Medical Oncology

Parkville, Victoria, Australia

Site Status

Centro de Oncologia da Bahia - CENOB

Salvador, Estado de Bahia, Brazil

Site Status

Clinica de Tratamento e Pesquisa Oncologica - Oncotek

Brasília, Federal District, Brazil

Site Status

Instituto Nacional de Cancer - INCa; Oncologia

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

Liga Norte Riograndense Contra O Câncer

Natal, Rio Grande do Norte, Brazil

Site Status

Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital Mae de Deus

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Centro de Pesquisas Oncologicas - CEPON

Florianópolis, Santa Catarina, Brazil

Site Status

Hospital Amaral Carvalho

Jaú, São Paulo, Brazil

Site Status

Instituto do Cancer do Estado de Sao Paulo - ICESP

São Paulo, São Paulo, Brazil

Site Status

Instituto de Oncologia de Sorocaba - CEPOS

Sorocaba, São Paulo, Brazil

Site Status

Mcgill University - Royal Victoria Hospital; Oncology

Montreal, Quebec, Canada

Site Status

Hopital du Sacre-Coeur

Montreal, Quebec, Canada

Site Status

Clinica Santa Maria

Santiago, , Chile

Site Status

Fundacion Arturo Lopez Perez

Santiago, , Chile

Site Status

Instituto Oncologico del sur

Temuco, , Chile

Site Status

Hospital Clinico Vina del Mar

Viña del Mar, , Chile

Site Status

Hopital Morvan

Brest, , France

Site Status

Clinique Victor Hugo; Radiotherapie

Le Mans, , France

Site Status

Clinique Catherine de Sienne; Service de cancérologie

Nantes, , France

Site Status

Ico Rene Gauducheau; Oncologie

Saint-Herblain, , France

Site Status

Centre Hospitalier de Villefranche sur Saone

Villefranche-sur-Saône, , France

Site Status

Institut Gustave Roussy; Departement Oncologie Medicale

Villejuif, , France

Site Status

Zentralklinik Bad Berka GmbH; Abteilung Onkologie und Hämatologie

Bad Berka, , Germany

Site Status

Asklepios-Fachkliniken Muenchen-Gauting; Onkologie

Gauting, , Germany

Site Status

Krankenhaus Grosshansdorf;Pneumologie & Thoraxchirurgie

Großhansdorf, , Germany

Site Status

St. Vincentius Kliniken Karlsruhe; Abteilung Hämatologie / Onkologie

Karlsruhe, , Germany

Site Status

Universitätsmedizin der Johannes Gutenberg-Universität Mainz, Medizinische Klinik, Pneumologie

Mainz, , Germany

Site Status

Universitätsklinikum Regensburg; Klinik und Poliklinik für Innere Medizin II, Pneumologie

Regensburg, , Germany

Site Status

Universitätsklinikum Ulm; Medizinische Uni-Klinik III Abt. Innere Medizin III Hämatologie u. Onkolo.

Ulm, , Germany

Site Status

Schwarzwald-Baar Klinikum/VS GmbH; Onkologie/Hämatologie/Infektologie

Villingen-Schwenningen, , Germany

Site Status

Orszagos Koranyi TBC es Pulmonologiai Intezet

Budapest, , Hungary

Site Status

Koch Robert Korhaz

Edelény, , Hungary

Site Status

Veszprem Megyei Onkormanyzat Tudogyogyintezet

Farkasgyepű, , Hungary

Site Status

Vas Megyei Markusovszky Korhaz ; Pulmonology

Szombathely, , Hungary

Site Status

Tudogyogyintezet Torokbalint

Törökbálint, , Hungary

Site Status

Zala Megyei Korhaz; Dept of Pulmonary Medicine

Zalaegerszeg, , Hungary

Site Status

Shaare Zedek Medical Center; Oncology Dept

Jerusalem, , Israel

Site Status

Meir Medical Center; Oncology

Kfar Saba, , Israel

Site Status

Chaim Sheba Medical Center; Oncology Dept

Ramat Gan, , Israel

Site Status

Ausl Di Bologna-Ospedale Bellaria;U.O. Oncologia Medica

Bologna, Emilia-Romagna, Italy

Site Status

Irccs Centro Di Riferimento Oncologico (CRO); Dipartimento Di Oncologia Medica

Aviano, Friuli Venezia Giulia, Italy

Site Status

ASST DI MONZA; Oncologia Medica

Monza, Lombardy, Italy

Site Status

Az. Osp. S. Luigi Gonzaga; Malattie Apparato Respiratorio 5 Ad Indirizzo Oncologico

Orbassano, Piedmont, Italy

Site Status

A.O.U.I. VERONA-OSPEDALE POLICLINICO G.B. ROSSI BORGO ROMA;ONCOLOGIA MEDICA-d.U.

Verona, Veneto, Italy

Site Status

Amphia Ziekenhuis

Breda, , Netherlands

Site Status

Catharina-ziekenhuis; Longgeneeskunde en Tuberculose

Eindhoven, , Netherlands

Site Status

Universitair Medisch Centrum Groningen

Groningen, , Netherlands

Site Status

Regional Oncology Center

Chelyabinsk, , Russia

Site Status

Moscow city oncology hospital #62 of Moscow Healthcare Department

Moscow, , Russia

Site Status

City Oncology Hospital; Chemotherapy Dept

Nizhny Novgorod, , Russia

Site Status

Rsrch Onc Inst of Rosmed Tech; n.a. prof. N.N. Petrov; Dept of Surgery

Saint Petersburg, , Russia

Site Status

Leningrad Regional Clinical Hospital

Saint Petersburg, , Russia

Site Status

Hospital Nuestra Señora de Sonsoles; servicio de Oncologia

Ávila, , Spain

Site Status

Hospital Univ Vall d'Hebron; Servicio de Oncologia

Barcelona, , Spain

Site Status

Hospital Universitari Germans Trias i Pujol; Servicio de Oncologia

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Universitario Puerta de Hierro; Servicio de Oncologia

Madrid, , Spain

Site Status

Kiev City Clinical Oncology Center

Kiev, , Ukraine

Site Status

Volyn Regional Oncology Dispensary

Lutsk, , Ukraine

Site Status

State Oncology Regional Treatment-Diagnostic Center; Chemotherapy Department

Lviv, , Ukraine

Site Status

Crimean Republican Institute; Oncology Clin Dispensary; Chemotherapy Dept

Simferopol, , Ukraine

Site Status

Sumy Reg. Clin. Oncological Dispensary; Thoracall Department

Sumy, , Ukraine

Site Status

Zaporizhzhia Regional Clinical Oncology Dispensary; Zaporizhzhya State Medical University

Zaporizhzhya, , Ukraine

Site Status

Royal Surrey County Hospital; St. Lukes Cancer Centre

Guildford, , United Kingdom

Site Status

Leicester Royal Infirmary; Dept. of Medical Oncology

Leicester, , United Kingdom

Site Status

Christie Hospital Nhs Trust; Medical Oncology

Manchester, , United Kingdom

Site Status

Countries

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United States Argentina Australia Brazil Canada Chile France Germany Hungary Israel Italy Netherlands Russia Spain Ukraine United Kingdom

Other Identifiers

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2011-002893-21

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GO27912

Identifier Type: -

Identifier Source: org_study_id

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