Trial Outcomes & Findings for A Physical Dependence Study in Schizophrenia (NCT NCT01452919)

NCT ID: NCT01452919

Last Updated: 2022-09-14

Results Overview

The checklist is a 30-item, participant-rated scale that asks whether participants experience symptoms such as nausea, vomiting, loss of appetite, anxiety, irritability, or craving for study drug during the previous day to assess potential symptoms of drug withdrawal. Each item is rated on a 0 (not at all) to 3 (severe). Total scores range from 0-90. Higher scores indicate greater severity of symptoms. The 3-day MA was calculated starting the third day until the last day of double-blind, randomized period. The 3-day MA was the average of scores from that day and previous 2 days. If scores from any of the days during the 3-day was missing, the average was based on the non-missing days. If there was no total scores for any day of the 3-day, the average was considered to be missing. An analysis of covariance (ANCOVA) was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline total score, treatment, pooled investigative site and gender.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

123 participants

Primary outcome timeframe

Randomization up to Week 2 of randomization treatment

Results posted on

2022-09-14

Participant Flow

This study consisted of a 4-week open-label treatment period and a 2-week double-blind randomized withdrawal treatment period.

Participant milestones

Participant milestones
Measure
LY2140023 (Open-Label )
40 milligram (mg) or 80 mg LY2140023 administered orally, twice daily for 4 weeks during open-label treatment period.
Placebo (Randomization)
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Open-Label Treatment
STARTED
123
0
0
Open-Label Treatment
Received at Least 1 Dose of Study Drug
123
0
0
Open-Label Treatment
COMPLETED
103
0
0
Open-Label Treatment
NOT COMPLETED
20
0
0
Randomization Treatment
STARTED
0
50
53
Randomization Treatment
Received at Least 1 Dose of Study Drug
0
50
53
Randomization Treatment
COMPLETED
0
47
51
Randomization Treatment
NOT COMPLETED
0
3
2

Reasons for withdrawal

Reasons for withdrawal
Measure
LY2140023 (Open-Label )
40 milligram (mg) or 80 mg LY2140023 administered orally, twice daily for 4 weeks during open-label treatment period.
Placebo (Randomization)
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Open-Label Treatment
Adverse Event
5
0
0
Open-Label Treatment
Lost to Follow-up
4
0
0
Open-Label Treatment
Perceived lack of efficacy
3
0
0
Open-Label Treatment
Protocol Violation
4
0
0
Open-Label Treatment
Sponsor Decision
1
0
0
Open-Label Treatment
Withdrawal by Subject
2
0
0
Open-Label Treatment
Subject is moving or has moved
1
0
0
Randomization Treatment
Adverse Event
0
0
2
Randomization Treatment
Sponsor Decision
0
1
0
Randomization Treatment
Withdrawal by Subject
0
1
0
Randomization Treatment
Subject is moving or has moved
0
1
0

Baseline Characteristics

A Physical Dependence Study in Schizophrenia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Participants
n=123 Participants
40 milligram (mg) or 80 mg LY2140023 administered orally, twice daily for 4 weeks during open-label treatment period. Placebo, or 40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Age, Continuous
42.86 years
STANDARD_DEVIATION 11.45 • n=5 Participants
Sex: Female, Male
Female
30 Participants
n=5 Participants
Sex: Female, Male
Male
93 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
5 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
118 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
3 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
1 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
82 Participants
n=5 Participants
Race (NIH/OMB)
White
35 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
107 participants
n=5 Participants
Region of Enrollment
Greece
16 participants
n=5 Participants

PRIMARY outcome

Timeframe: Randomization up to Week 2 of randomization treatment

Population: All randomized participants who received at least one dose of study drug and had Discontinuation Symptom Checklist-Modified Rickels total score measurement.

The checklist is a 30-item, participant-rated scale that asks whether participants experience symptoms such as nausea, vomiting, loss of appetite, anxiety, irritability, or craving for study drug during the previous day to assess potential symptoms of drug withdrawal. Each item is rated on a 0 (not at all) to 3 (severe). Total scores range from 0-90. Higher scores indicate greater severity of symptoms. The 3-day MA was calculated starting the third day until the last day of double-blind, randomized period. The 3-day MA was the average of scores from that day and previous 2 days. If scores from any of the days during the 3-day was missing, the average was based on the non-missing days. If there was no total scores for any day of the 3-day, the average was considered to be missing. An analysis of covariance (ANCOVA) was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline total score, treatment, pooled investigative site and gender.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=52 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Maximum 3-Day Moving Average (MA) of the Discontinuation Symptom Checklist-Modified Rickels Total Score
13.23 units on a scale
Standard Error 0.96
11.50 units on a scale
Standard Error 0.99

SECONDARY outcome

Timeframe: Randomization, randomization treatment Weeks 0.5 and 1 and 1.5 and 2

Population: All randomized participants who received at least one dose of study drug and had CIWA-Ar measurements at randomization and specified post-randomization visits.

The CIWA-Ar is a 10-item scale that was used to monitor for symptoms of drug withdrawal. The scale includes the following domains/criteria: nausea, vomiting; anxiety; paroxysmal sweats; tactile disturbances; visual disturbances; tremors; agitation; orientation and clouding of sensorium; auditory disturbances; and headache. Items 1-9 have possible scores of 0 (no symptom)-7 (severe symptom), and item 10 has possible scores of 0 (no symptom)-4 (severe symptom). Total scores range from 0-67. Higher scores indicate greater severity of symptom. The Mixed Model Repeated Measure (MMRM) analysis was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline CIWA-Ar total score, treatment, gender, pooled investigative site, visit, baseline CIWA-Ar total score\*visit and treatment\*visit.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Change From Randomization up to Week 2 in the Clinical Institute Withdrawal Assessment of Alcohol Scale (CIWA-Ar) Total Score
Week 0.5
-0.7 units on a scale
Standard Error 0.3
0.0 units on a scale
Standard Error 0.3
Change From Randomization up to Week 2 in the Clinical Institute Withdrawal Assessment of Alcohol Scale (CIWA-Ar) Total Score
Week 1
-0.9 units on a scale
Standard Error 0.3
-0.5 units on a scale
Standard Error 0.3
Change From Randomization up to Week 2 in the Clinical Institute Withdrawal Assessment of Alcohol Scale (CIWA-Ar) Total Score
Week 1.5
-0.8 units on a scale
Standard Error 0.3
-0.6 units on a scale
Standard Error 0.3
Change From Randomization up to Week 2 in the Clinical Institute Withdrawal Assessment of Alcohol Scale (CIWA-Ar) Total Score
Week 2
-0.4 units on a scale
Standard Error 0.3
-0.5 units on a scale
Standard Error 0.3

SECONDARY outcome

Timeframe: Randomization, randomization treatment Week 2

Population: All randomized participants who received at least one dose of study drug and had BAS global score measurement at randomization and at least one post-randomization BAS global score.

The BAS is a 4-item instrument that evaluates akathisia associated with use of antipsychotic medications. Item 4 is the Global Clinical Assessment (Global Score) and is rated 0 to 5 (0 = absent, 5 = severe). The Mixed Model Repeated Measure (MMRM) analysis was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline BAS global score, treatment, gender, pooled investigative site, visit, baseline BAS global score\*visit and treatment\*visit.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Change From Randomization to Week 2 in Barnes Akathisia Scale (BAS) Global Score
-0.0 units on a scale
Standard Error 0.0
-0.0 units on a scale
Standard Error 0.0

SECONDARY outcome

Timeframe: Randomization, randomization treatment Week 2

Population: All randomized participants who received at least one dose of study drug and had SAS total score measurement at randomization and at least one post-randomization SAS total score.

The SAS is used to measure parkinsonian-type symptoms in participants exposed to antipsychotics. SAS consists of 10 items; each rated on a 5-point scale, with 0 meaning complete absence of the condition and 4 meaning the presence of the condition in extreme form. The total score is obtained by adding the ten items, and ranges from 0 to 40. Higher scores indicate greater severity of illness. The Mixed Model Repeated Measure (MMRM) analysis was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline SAS total score, treatment, gender, pooled investigative site, visit, baseline SAS total score\*visit and treatment\*visit.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Change From Randomization to Week 2 in Simpson-Angus Scale (SAS) Total Score
-0.0 units on a scale
Standard Error 0.0
0.0 units on a scale
Standard Error 0.0

SECONDARY outcome

Timeframe: Randomization, randomization treatment Week 2

Population: All randomized participants who received at least one dose of study drug and had AIMS total score measurement at randomization and at least one post-randomization AIMS total score.

The AIMS is a 12-item scale designed to record the occurrence of dyskinetic movements. Items 1 to 10 are rated on a 5- point scale, with 0 being no dyskinetic movements and 4 being severe dyskinetic movements. Items 11 and 12 are yes/no questions regarding the dental condition of a subject. The AIMS 1-7 total score is the total of items 1 through 7 of the AIMS, and ranges from 0 to 28. Higher scores indicate greater severity of illness. The Mixed Model Repeated Measure (MMRM) analysis was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline AIMS 1-7 total score, treatment, gender, pooled investigative site, visit, baseline AIMS 1-7 total score\*visit and treatment\*visit.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Change From Randomization to Week 2 in Abnormal Involuntary Movement Scale (AIMS) Total Score
0.0 units a scale
Standard Error 0.1
-0.0 units a scale
Standard Error 0.1

SECONDARY outcome

Timeframe: Baseline up to Week 4 of open-label treatment

Population: All enrolled participants who received at least one dose of study drug and had a baseline (before open-label treatment) and at least one post-baseline (during open-label treatment) C-SSRS measurement.

Columbia Suicide Rating Scale (C-SSRS) captures occurrence, severity, and frequency of suicide-related thoughts and behaviors. Suicidal ideation: a "yes" answer to any one of 5 suicidal ideation questions: wish to be dead, and 4 different categories of active suicidal ideation. Suicidal behavior: a "yes" answer to any of 5 suicidal behavior questions: preparatory acts or behavior, aborted attempt, interrupted attempt, actual attempt, and completed suicide. The percentage of participants with treatment-emergent suicidal ideation or behavior during open-label treatment period (with a change from baseline in C-SSRS) was calculated as the number of participants with an increase in suicidal behavior or ideation over baseline (before open-label treatment), divided by the total number of participants multiplied by 100.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=122 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Percentage of Participants With Suicidal Behaviors and Ideations Measured Using the Columbia Suicide Severity Rating Scale (C-SSRS) During Open-Label Treatment Period
Treatment-Emergent Suicidal Ideation
1.6 percentage of participants
Percentage of Participants With Suicidal Behaviors and Ideations Measured Using the Columbia Suicide Severity Rating Scale (C-SSRS) During Open-Label Treatment Period
Treatment-Emergent Suicidal Behavior
0.0 percentage of participants

SECONDARY outcome

Timeframe: Randomization up to Week 2 of randomization treatment

Population: All participants who received at least one dose of study drug and had C-SSRS measurement at randomization and at least one post-randomization C-SSRS measurement.

Columbia Suicide Rating Scale (C-SSRS) captures occurrence, severity, and frequency of suicide-related thoughts and behaviors. Suicidal ideation: a "yes" answer to any one of 5 suicidal ideation questions: wish to be dead, and 4 different categories of active suicidal ideation. Suicidal behavior: a "yes" answer to any of 5 suicidal behavior questions: preparatory acts or behavior, aborted attempt, interrupted attempt, actual attempt, and completed suicide. The percentage of participants with treatment-emergent suicidal ideation or behavior during double-blind randomized treatment period (with a change from baseline in C-SSRS) was calculated as the number of participants with an increase in suicidal behavior or ideation over baseline (randomization), divided by the total number of participants multiplied by 100.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Percentage of Participants With Suicidal Behaviors and Ideations Measured Using the Columbia Suicide Severity Rating Scale (C-SSRS) During Double-Blind Randomized Treatment Period
Treatment-Emergent Suicidal Ideation
0.0 percentage of participants
0.0 percentage of participants
Percentage of Participants With Suicidal Behaviors and Ideations Measured Using the Columbia Suicide Severity Rating Scale (C-SSRS) During Double-Blind Randomized Treatment Period
Treatment-Emergent Suicidal Behavior
0.0 percentage of participants
0.0 percentage of participants

SECONDARY outcome

Timeframe: Randomization, randomization treatment Week 2

Population: All randomized participants who received at least one dose of study drug and had CGI-S measurement at randomization and at least one post-randomization CGI-S measurement.

The CGI-S instrument is used to record the severity of mental illness at the time of assessment. The score ranges from 1 (normal, not at all ill) to 7 (among the most extremely ill). Higher scores indicate greater severity of illness. The Mixed Model Repeated Measure (MMRM) analysis was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline CGI-S score, treatment, gender, pooled investigative site, visit, baseline CGI-S score\*visit and treatment\*visit.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=50 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Change From Randomization to Week 2 in Clinical Global Impression-Severity Scale (CGI-S)
-0.2 units on a scale
Standard Error 0.1
-0.0 units on a scale
Standard Error 0.1

SECONDARY outcome

Timeframe: Randomization, randomization treatment Week 2

Population: All randomized participants who received at least one dose of study drug and had BPRS total score measurement at randomization and at least one post-randomization BPRS total score.

BPRS is an 18-item clinician-administered scale used to assess the degree of severity of a participant's general psychopathological symptoms. Item scores range from 1 (not present) to 7 (extremely severe). Total Scores range from 18 to 126. Higher scores indicate greater severity of illness. The Mixed Model Repeated Measure (MMRM) analysis was used to calculate Least Squares (LS) mean and standard error. LS mean values are controlled for baseline BPRS total score, treatment, gender, pooled investigative site, visit, baseline BPRS total score\*visit and treatment\*visit.

Outcome measures

Outcome measures
Measure
Placebo (Randomization)
n=49 Participants
Placebo administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
LY2140023 (Randomization)
n=52 Participants
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind, randomized withdrawal treatment period.
Change From Randomization to Week 2 in Brief Psychiatric Rating Scale (BPRS) Total Scores
-2.20 units on a scale
Standard Error 0.55
-1.28 units on a scale
Standard Error 0.54

Adverse Events

LY2140023 (Open-Label )

Serious events: 0 serious events
Other events: 83 other events
Deaths: 0 deaths

Placebo (Randomization)

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

LY2140023 (Randomization)

Serious events: 0 serious events
Other events: 20 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
LY2140023 (Open-Label )
n=123 participants at risk
40 milligram (mg) or 80 mg LY2140023 administered orally, twice daily for 4 weeks during open-label treatment period.
Placebo (Randomization)
n=50 participants at risk
Placebo administered orally, twice daily for 2 weeks during double-blind randomized withdrawal treatment period.
LY2140023 (Randomization)
n=53 participants at risk
40 mg or 80 mg LY2140023 administered orally, twice daily for 2 weeks during double-blind randomized withdrawal treatment period.
Ear and labyrinth disorders
Hearing impaired
2.4%
3/123 • Number of events 3
4.0%
2/50 • Number of events 2
0.00%
0/53
Eye disorders
Visual impairment
1.6%
2/123 • Number of events 2
4.0%
2/50 • Number of events 2
1.9%
1/53 • Number of events 1
Gastrointestinal disorders
Constipation
4.9%
6/123 • Number of events 6
2.0%
1/50 • Number of events 1
1.9%
1/53 • Number of events 1
Gastrointestinal disorders
Diarrhoea
4.1%
5/123 • Number of events 7
2.0%
1/50 • Number of events 1
0.00%
0/53
Gastrointestinal disorders
Nausea
28.5%
35/123 • Number of events 39
2.0%
1/50 • Number of events 1
5.7%
3/53 • Number of events 3
Gastrointestinal disorders
Vomiting
8.1%
10/123 • Number of events 17
0.00%
0/50
3.8%
2/53 • Number of events 2
Investigations
Blood creatine phosphokinase increased
7.3%
9/123 • Number of events 9
0.00%
0/50
5.7%
3/53 • Number of events 3
Nervous system disorders
Dizziness
4.9%
6/123 • Number of events 6
0.00%
0/50
0.00%
0/53
Nervous system disorders
Headache
15.4%
19/123 • Number of events 20
8.0%
4/50 • Number of events 4
1.9%
1/53 • Number of events 2
Nervous system disorders
Somnolence
5.7%
7/123 • Number of events 7
0.00%
0/50
0.00%
0/53
Nervous system disorders
Tremor
8.1%
10/123 • Number of events 12
2.0%
1/50 • Number of events 1
3.8%
2/53 • Number of events 2
Psychiatric disorders
Agitation
6.5%
8/123 • Number of events 9
2.0%
1/50 • Number of events 1
7.5%
4/53 • Number of events 4
Psychiatric disorders
Anxiety
8.1%
10/123 • Number of events 11
8.0%
4/50 • Number of events 4
7.5%
4/53 • Number of events 4
Psychiatric disorders
Insomnia
4.9%
6/123 • Number of events 6
0.00%
0/50
0.00%
0/53
Skin and subcutaneous tissue disorders
Hyperhidrosis
5.7%
7/123 • Number of events 7
0.00%
0/50
3.8%
2/53 • Number of events 2

Additional Information

Chief Medical Officer

Eli Lilly and Company

Phone: 800-545-5979

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60