Systemic Therapies for Pediatric Atopic Dermatitis

NCT ID: NCT01447381

Last Updated: 2012-11-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Total Enrollment

250 participants

Study Classification

OBSERVATIONAL

Study Start Date

2011-10-31

Study Completion Date

2021-07-31

Brief Summary

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While many patients with atopic dermatitis (eczema) can be managed with topical creams and treatments for itch, some children have such severe, long-standing disease that they need treatment with oral medications that decrease the ability of the immune system to react. However, there is not enough information on the proper use of these medications or how well they work compared with each other. The current study looks at the response of children treated with these medications to provide this information and improve their use.

Detailed Description

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Severe and/or refractory cases of atopic dermatitis (AD) can require systemic immunosuppressive therapy for disease control, yet there are few studies regarding the appropriate use of these drugs for pediatric AD and even less data comparing them. The current observational study will observe the effect of these therapies on children with moderate to severe atopic dermatitis as they are treated. These drugs being observed will be cyclosporine, azathioprine, mycophenolate mofetil, and methotrexate.

Conditions

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Dermatitis, Atopic

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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mycophenolate mofetil

Moderate to severe atopic dermatitis being treated with systemic mycophenolate mofetil

No interventions assigned to this group

cyclosporine

Moderate to severe atopic dermatitis being treated with systemic cyclosporine

No interventions assigned to this group

azathioprine

Moderate to severe atopic dermatitis being treated with systemic azathioprine

No interventions assigned to this group

methotrexate

Moderate to severe atopic dermatitis being treated with systemic methotrexate

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of moderate, severe, or very severe atopic dermatitis meeting the Hanifin and Rajka criteria
* Needs systemic therapy (e.g. cyclosporine, azathioprine, mycophenolate mofetil, or methotrexate) for severe atopic dermatitis
* Subject has severe or recalcitrant disease interrupting daily life as evidenced by fulfilling 2 or more of the following 4 criteria:

* Failure of multimodal therapy including emollients/barrier repair, topical anti-inflammatory agents (medium to high potency topical corticosteroids, and/or low-potency or topical calcineurin inhibitors if facial/intertriginous areas), and antihistamines
* Significant impairment in quality of life (physical, psychological, emotional) such as significant sleep disruption, poor school performance, or frequent school absenteeism, per the judgement of the investigator.
* Inability to receive, prior failure, or the need for more than one course of phototherapy
* Prior failure or need for more than one course of another oral immunosuppressive medication
* No serious medical condition that precludes the use of oral immunosuppressives based on the subject's medical history, physical examination, and safety laboratory tests.
* Negative PPD within the last year prior to study initiation.
* Female of childbearing potential has a negative pregnancy test at the time of starting the systemic drug and who consents to be abstinent or using an effective method of contraception during the study. Effective contraception is defined as IUD, condom with spermicide, diaphragm with spermicide, or stable use of a hormonal contraceptive (oral, implant, injection or transdermal patch) beginning at least 1 month prior to starting the systemic drug.
* Subject and parent/guardian are willing and able to comply with study instructions and return to the clinic for all required visits.

Exclusion Criteria

* Female who is pregnant, nursing, or planning a pregnancy during the study period.
* Concurrent participation in another clinical trial with an investigational drug or device that may impact on the individual's atopic dermatitis.
* Subjects with clinically significant hepatic disease, history of lymphoma or myelosuppression, low TMPT activity (if starting azathioprine), renal disease (if starting cyclosporine or azathioprine), hypertension (if starting cyclosporine), blood dyscrasias, or central nervous system disorders, such as uncontrolled seizures or peripheral neuropathy, or taking systemic medications that could interact adversely with the study medicine (e.g. erythromycin use with cyclosporine).
* Subjects with any underlying disease that the Investigator deems uncontrolled, and poses a concern for subject safety while participating on the study.
* Subject has a history of clinically significant drug or alcohol abuse in the last year.
* Subject is considered by the Investigator, for any reason, to be an unsuitable candidate for the study.
* Active systemic infection that could worsen with systemic therapy for AD.
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of California, San Diego

OTHER

Sponsor Role collaborator

Rady Children's Hospital, San Diego

OTHER

Sponsor Role lead

Responsible Party

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Wynnis Tom, MD

Assistant Clinical Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Wynnis Tom, MD

Role: PRINCIPAL_INVESTIGATOR

Rady Children's Hospital and UC San Diego

Locations

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Rady Children's Hospital

San Diego, California, United States

Site Status RECRUITING

University of California, San Francisco

San Francisco, California, United States

Site Status RECRUITING

Children's Memorial Hospital

Chicago, Illinois, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Lori Murphy, BS, CCRP

Role: CONTACT

Phone: 858-576-1700

Email: [email protected]

Facility Contacts

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Wynnis Tom, MD

Role: primary

Lawrence Eichenfield, MD

Role: backup

Kelly M. Cordoro, MD

Role: primary

Duri Yun, MD

Role: primary

Katherine Mercy, MD

Role: backup

References

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Meagher LJ, Wines NY, Cooper AJ. Atopic dermatitis: review of immunopathogenesis and advances in immunosuppressive therapy. Australas J Dermatol. 2002 Nov;43(4):247-54. doi: 10.1046/j.1440-0960.2002.00610.x.

Reference Type BACKGROUND
PMID: 12423430 (View on PubMed)

Akhavan A, Rudikoff D. The treatment of atopic dermatitis with systemic immunosuppressive agents. Clin Dermatol. 2003 May-Jun;21(3):225-40. doi: 10.1016/s0738-081x(02)00362-0. No abstract available.

Reference Type BACKGROUND
PMID: 12781440 (View on PubMed)

Other Identifiers

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CMH 2011-14488

Identifier Type: -

Identifier Source: org_study_id