Trial Outcomes & Findings for Dalfampridine for Imbalance in Multiple Sclerosis (NCT NCT01444300)

NCT ID: NCT01444300

Last Updated: 2014-06-16

Results Overview

Automatic Postural Response (APR) latencies will be measured by Computerized Dynamic Posturography (CDP). The restoration of balance after an unexpected movement by Computerized Dynamic Posturography relies on automated postural responses in the upper and lower legs, trunk, shoulders, and neck muscles. APR latency is the reaction- time response to movements of the support surface on which the subject stands. These responses typically occur at onset latencies of \~100 milliseconds. In response to a change, both feet-in-place and stepping strategies can be used to recover balance, with the incidence of stepping responses becoming larger as the change magnitude increases voluntary movements in human subjects.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

24 participants

Primary outcome timeframe

Baseline to 12 weeks

Results posted on

2014-06-16

Participant Flow

People with MS were recruited from several MS clinics in the Portland, OR metro area from September 2011 to August 2013. 24 subjects signed the consent and were enrolled in the study.

Participant milestones

Participant milestones
Measure
Dalfampridine
Dalfampridine: 10mg, twice daily, pill taken by mouth for 12 weeks
Placebo
Placebo: placebo pill, twice daily, for 12 weeks
Overall Study
STARTED
12
12
Overall Study
COMPLETED
8
12
Overall Study
NOT COMPLETED
4
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Dalfampridine
Dalfampridine: 10mg, twice daily, pill taken by mouth for 12 weeks
Placebo
Placebo: placebo pill, twice daily, for 12 weeks
Overall Study
Adverse Event
4
0

Baseline Characteristics

Dalfampridine for Imbalance in Multiple Sclerosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Dalfampridine
n=12 Participants
Dalfampridine: 10mg, twice daily (bid), pill taken by mouth for 12 weeks
Placebo
n=12 Participants
Placebo: placebo pill, twice daily (bid), for 12 weeks
Total
n=24 Participants
Total of all reporting groups
Age, Continuous
47.2 years
STANDARD_DEVIATION 8.9 • n=93 Participants
47.8 years
STANDARD_DEVIATION 10.9 • n=4 Participants
47.5 years
STANDARD_DEVIATION 9.7 • n=27 Participants
Sex: Female, Male
Female
5 Participants
n=93 Participants
6 Participants
n=4 Participants
11 Participants
n=27 Participants
Sex: Female, Male
Male
7 Participants
n=93 Participants
6 Participants
n=4 Participants
13 Participants
n=27 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants
1 Participants
n=4 Participants
1 Participants
n=27 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=93 Participants
1 Participants
n=4 Participants
1 Participants
n=27 Participants
Race (NIH/OMB)
White
11 Participants
n=93 Participants
10 Participants
n=4 Participants
21 Participants
n=27 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=93 Participants
0 Participants
n=4 Participants
1 Participants
n=27 Participants
MS Subtype
Relapsing Remitting MS (RRMS)
12 participants
n=93 Participants
8 participants
n=4 Participants
20 participants
n=27 Participants
MS Subtype
Secondary Progressive MS (SPMS)
0 participants
n=93 Participants
2 participants
n=4 Participants
2 participants
n=27 Participants
MS Subtype
Primary Progressive MS (PPMS)
0 participants
n=93 Participants
2 participants
n=4 Participants
2 participants
n=27 Participants

PRIMARY outcome

Timeframe: Baseline to 12 weeks

Automatic Postural Response (APR) latencies will be measured by Computerized Dynamic Posturography (CDP). The restoration of balance after an unexpected movement by Computerized Dynamic Posturography relies on automated postural responses in the upper and lower legs, trunk, shoulders, and neck muscles. APR latency is the reaction- time response to movements of the support surface on which the subject stands. These responses typically occur at onset latencies of \~100 milliseconds. In response to a change, both feet-in-place and stepping strategies can be used to recover balance, with the incidence of stepping responses becoming larger as the change magnitude increases voluntary movements in human subjects.

Outcome measures

Outcome measures
Measure
Dalfampridine
n=8 Participants
Dalfampridine: 10mg, twice daily (bid), pill taken by mouth for 12 weeks
Placebo
n=12 Participants
Placebo: placebo pill, twice daily (bid), pill taken by mouth for 12 weeks
Change in Automatic Postural Response (APR )Latency
5.71 milliseconds
Standard Deviation 16.2
4.58 milliseconds
Standard Deviation 23.0

SECONDARY outcome

Timeframe: Baseline to 12 weeks

The ABC is an 11-point scale and subjects are asked to indicate personal level of confidence in doing specific activities without losing balance or becoming unsteady on a scale from 0% to 100%. The ratings are added (possible range =0 -1600) and divide by 16 to get each subject's ABC score. A high ABC score indicates a high degree of confidence and a low ABC score indicates a low degree of confidence.

Outcome measures

Outcome measures
Measure
Dalfampridine
n=8 Participants
Dalfampridine: 10mg, twice daily (bid), pill taken by mouth for 12 weeks
Placebo
n=12 Participants
Placebo: placebo pill, twice daily (bid), pill taken by mouth for 12 weeks
Change in Activities-specific Balance Confidence (ABC) Questionnaire Scores
1.30 Scores on a scale
Standard Deviation 9.02
0.41 Scores on a scale
Standard Deviation 10.7

SECONDARY outcome

Timeframe: Baseline to 12 weeks

Outcome measures

Outcome measures
Measure
Dalfampridine
n=8 Participants
Dalfampridine: 10mg, twice daily (bid), pill taken by mouth for 12 weeks
Placebo
n=12 Participants
Placebo: placebo pill, twice daily (bid), pill taken by mouth for 12 weeks
Change in Timed 25 Foot Walking Speed
0.26 seconds
Standard Deviation 0.78
0.39 seconds
Standard Deviation 1.45

Adverse Events

Dalfampridine

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Dalfampridine
n=12 participants at risk
Dalfampridine: 10mg, twice daily, pill taken by mouth for 12 weeks
Placebo
n=12 participants at risk
Placebo: placebo pill, twice daily, for 12 weeks
Nervous system disorders
Insomnia
33.3%
4/12 • Number of events 4
0.00%
0/12
Gastrointestinal disorders
Nausea
41.7%
5/12 • Number of events 5
0.00%
0/12
Musculoskeletal and connective tissue disorders
Muscle weakness
16.7%
2/12 • Number of events 2
50.0%
6/12 • Number of events 6
Musculoskeletal and connective tissue disorders
Balance problems
16.7%
2/12 • Number of events 2
33.3%
4/12 • Number of events 4
Nervous system disorders
Dizziness
25.0%
3/12 • Number of events 3
0.00%
0/12
Skin and subcutaneous tissue disorders
Itching/skin reactions
8.3%
1/12 • Number of events 1
8.3%
1/12 • Number of events 1

Additional Information

Dr. Michelle Cameron

Oregon Health & Science University

Phone: 503-218-1971

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60