Trial Outcomes & Findings for Pharmacokinetics of a Single Treatment Cycle of AA4500 0.58 mg in Men With Peyronie's Disease (NCT NCT01430169)

NCT ID: NCT01430169

Last Updated: 2017-10-05

Results Overview

Maximum AUX-I (clostridial type I collagenase) enzyme concentration from pre-injection to 24 hours after Injection 1. AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

20 participants

Primary outcome timeframe

15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Results posted on

2017-10-05

Participant Flow

Participant milestones

Participant milestones
Measure
AA4500
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg (First Injection is administered on Day 1 and the second Injection is administered on Day 2)
Overall Study
STARTED
20
Overall Study
COMPLETED
20
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Pharmacokinetics of a Single Treatment Cycle of AA4500 0.58 mg in Men With Peyronie's Disease

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
AA4500
n=20 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
14 Participants
n=5 Participants
Age, Categorical
>=65 years
6 Participants
n=5 Participants
Age, Continuous
61.0 years
STANDARD_DEVIATION 8.53 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
20 Participants
n=5 Participants
Region of Enrollment
United States
20 participants
n=5 Participants

PRIMARY outcome

Timeframe: 15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Population: Pharmacokinetic (PK) population (N=19). Two subjects were excluded from the analysis due to bioanalytical reasons (ELISA interference)

Maximum AUX-I (clostridial type I collagenase) enzyme concentration from pre-injection to 24 hours after Injection 1. AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=17 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-I Cmax After Injection 1
12.6 ng/mL
Standard Deviation 8.3

PRIMARY outcome

Timeframe: 15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Population: Pharmacokinetic (PK) population (N=19).

Maximum AUX-II (clostridium Type II collagenase) enzyme concentration from pre-injection to 24 hours after Injection 1. AUX-II plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=19 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-II Cmax After Injection 1
15.1 ng/mL
Standard Deviation 19.2

PRIMARY outcome

Timeframe: 15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Population: Pharmacokinetic population (N=19). Two subjects were excluded from the analysis due to bioanalytical reasons (ELISA interference)

Area under the curve from pre-injection to tlast within 24 hours after the Injection 1, where tlast is time to last time with a quantifiable concentration of the enzyme AUX-I. AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=17 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-I AUC0-tlast After Injection 1
3.1 ng*h/mL
Standard Deviation 2.1

PRIMARY outcome

Timeframe: 15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Population: Pharmacokinetic (PK) population (N=19)

Area under the curve from pre-injection to tlast within 24 hours after the Injection 1, where tlast is time to last time with a quantifiable concentration of the enzyme AUX-II. AUX-II plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=19 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-II AUC0-tlast After Injection 1
2.2 ng*h/mL
Standard Deviation 3.9

PRIMARY outcome

Timeframe: 15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Population: Pharmacokinetic (PK) population (N=19). For 3 subjects Tmax was considered missing if concentration was BLQ for all time points at that injection and 2 subjects were excluded from the analysis due to bioanalytical reasons (ELISA interference)

Time to maximum AUX-I enzyme concentration. AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=14 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-I Tmax After Injection 1
0.15 hours
Standard Deviation 0.09

PRIMARY outcome

Timeframe: 15 minutes before Injection 1 (0 hour for Injection 1); 5, 10, 20, and 30 minutes after Injection 1; 1, 2, 4, 8, and 12 hours after Injection 1; 15 minutes before Injection 2 (24 hours after Injection 1)

Population: Pharmacokinetic (PK) population (N=19) One subject was excluded from AUX-II PK analyses due to insufficient quantities of plasma for bioanalysis. Of the 38 AUX-II profiles, 23 had no quantifiable plasma concentrations at any time point through 24 hours post injection.

Time to maximum AUX-II enzyme concentration. AUX-II plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=8 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-II Tmax After Injection 1
0.16 hours
Standard Deviation 0.08

PRIMARY outcome

Timeframe: 15 minutes before Injection 2 (24 hours after Injection 1 or 0 hour for Injection 2); 5, 10, 20, and 30 minutes after Injection 2; 1, 2, 4, 8, and 12 hours after Injection 2; Day 3 (24 hours after Injection 2)

Population: Pharmacokinetic (PK) population (N=19). Two subjects were excluded from the analysis due to bioanalytical reasons (ELISA interference)

Maximum AUX-I enzyme concentration from zero to 24 hours after Injection 2.AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=17 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-I Cmax After Injection 2
12.2 ng/mL
Standard Deviation 9.1

PRIMARY outcome

Timeframe: 15 minutes before Injection 2 (24 hours after Injection 1 or 0 hour for Injection 2); 5, 10, 20, and 30 minutes after Injection 2; 1, 2, 4, 8, and 12 hours after Injection 2; Day 3 (24 hours after Injection 2)

Population: Pharmacokinetic (PK) population (N=19)

Maximum AUX-II enzyme concentration from zero to 24 hours after Injection 2. AUX-II plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=19 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-II Cmax After Injection 2
16.1 ng/mL
Standard Deviation 23.2

PRIMARY outcome

Timeframe: 15 minutes before Injection 2 (24 hours after Injection 1 or 0 hour for Injection 2); 5, 10, 20, and 30 minutes after Injection 2; 1, 2, 4, 8, and 12 hours after Injection 2; Day 3 (24 hours after Injection 2)

Population: Pharmacokinetic (PK) population (N=19). Two subjects were excluded from the analysis due to bioanalytical reasons (ELISA interference)

Area under the curve from zero to tlast within 24 hours after the Injection 2, where tlast is time to last time with a quantifiable concentration of the enzyme AUX-I. AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=17 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-I AUC0-tlast After Injection 2
2.4 ng*h/mL
Standard Deviation 2.3

PRIMARY outcome

Timeframe: 15 minutes before Injection 2 (24 hours after Injection 1 or 0 hour for Injection 2); 5, 10, 20, and 30 minutes after Injection 2; 1, 2, 4, 8, and 12 hours after Injection 2; Day 3 (24 hours after Injection 2)

Population: Pharmacokinetic (PK) population (N=19)

Area under the curve from zero to tlast within 24 hours after the Injection 2, where tlast is time to last time with a quantifiable concentration of the enzyme AUX-II. AUX-II plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=19 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-II AUC0-tlast After Injection 2
2.3 ng*h/mL
Standard Deviation 4.1

PRIMARY outcome

Timeframe: 15 minutes before Injection 2 (24 hours after Injection 1 or 0 hour for Injection 2); 5, 10, 20, and 30 minutes after Injection 2; 1, 2, 4, 8, and 12 hours after Injection 2; Day 3 (24 hours after Injection 2)

Population: Pharmacokinetic (PK) population (N=19). In addition, 2 subjects have been excluded from the analysis due to ELISA interference. Of the 38 AUX-I profiles, 7 had no quantifiable plasma concentrations through 24 hours post injection.

Time to maximum AUX-I enzyme concentration. AUX-I plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=13 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-I Tmax After Injection 2
0.11 hour
Standard Deviation 0.07

PRIMARY outcome

Timeframe: 15 minutes before Injection 2 (24 hours after Injection 1 or 0 hour for Injection 2); 5, 10, 20, and 30 minutes after Injection 2; 1, 2, 4, 8, and 12 hours after Injection 2; Day 3 (24 hours after Injection 2)

Population: Pharmacokinetic (PK) population (N=19) In addition, 2 subjects have been excluded from the analysis due to ELISA interference. Of the 38 AUX-II profiles,23 had no quantifiable plasma concentrations at any time point through 24 hours post injection.

Time to maximum AUX-II enzyme concentration. AUX-II plasma concentrations were determined with a validated enzyme-linked immunosorbent assay (ELISA).

Outcome measures

Outcome measures
Measure
AA4500
n=7 Participants
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
AUX-II Tmax After Injection 2
0.12 hours
Standard Deviation 0.09

Adverse Events

AA4500

Serious events: 0 serious events
Other events: 20 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
AA4500
n=20 participants at risk
collagenase clostridium histolyticum AA4500: Two injections of AA4500 0.58 mg
Reproductive system and breast disorders
Penile haemorrhage
95.0%
19/20 • Number of events 23 • 28 days after the first injection
General disorders
Injection site pain
75.0%
15/20 • Number of events 15 • 28 days after the first injection
Injury, poisoning and procedural complications
Procedural pain
45.0%
9/20 • Number of events 10 • 28 days after the first injection
Reproductive system and breast disorders
Penile swelling
30.0%
6/20 • Number of events 6 • 28 days after the first injection
Reproductive system and breast disorders
Painful erection
20.0%
4/20 • Number of events 4 • 28 days after the first injection
Reproductive system and breast disorders
Penile pain
20.0%
4/20 • Number of events 5 • 28 days after the first injection
Injury, poisoning and procedural complications
Post procedural discomfort
10.0%
2/20 • Number of events 2 • 28 days after the first injection
Musculoskeletal and connective tissue disorders
Arthralgia
5.0%
1/20 • Number of events 1 • 28 days after the first injection
Nervous system disorders
Dizziness
5.0%
1/20 • Number of events 1 • 28 days after the first injection
Injury, poisoning and procedural complications
Fall
5.0%
1/20 • Number of events 1 • 28 days after the first injection
Nervous system disorders
Headache
5.0%
1/20 • Number of events 1 • 28 days after the first injection
General disorders
Injection site haemorrhage
5.0%
1/20 • Number of events 1 • 28 days after the first injection
Reproductive system and breast disorders
Penile blister
5.0%
1/20 • Number of events 1 • 28 days after the first injection
Injury, poisoning and procedural complications
Vascular access complication
5.0%
1/20 • Number of events 1 • 28 days after the first injection

Additional Information

Clinical Trial Coordinator

Endo Pharmaceuticals, Inc.

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: OTHER