A Clinical Study of the Efficacy of Natalizumab on Reducing Disability Progression in Participants With Secondary Progressive Multiple Sclerosis

NCT ID: NCT01416181

Last Updated: 2017-09-11

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

889 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-09-13

Study Completion Date

2016-04-13

Brief Summary

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This is a Phase 3b, multicenter, international study conducted in 2 parts. Upon completion of the placebo-controlled period (Part 1), participants will have the option of enrolling in a 2-year open-label extension (Part 2).

Part 1: The primary objective of the study is to investigate whether treatment with natalizumab slows the accumulation of disability not related to relapses in participants with secondary progressive multiple sclerosis (SPMS).

The secondary objectives of Part 1 of this study are to determine the proportion of participants with consistent improvement in Timed 25-Foot Walk (T25FW), the change in participant-reported ambulatory status as measured by the 12-item MS Walking Scale (MSWS-12), the change in manual ability based on the ABILHAND Questionnaire, the impact of natalizumab on participant-reported quality of life using the Multiple Sclerosis Impact Scale-29 Physical (MSIS-29 Physical), the change in whole brain volume between the end of study and Week 24 using magnetic resonance imaging (MRI) and the proportion of participants experiencing progression of disability as measured by individual physical Expanded Disability Status Scale (EDSS) system scores.

Part 2: The primary objective of Part 2 of the study is to evaluate the safety profile of natalizumab in participants with SPMS.

The secondary objectives of Part 2 of the study are to investigate long-term disability (based on clinical or participant-reported assessments) in participants with SPMS receiving natalizumab treatment for approximately 4 years and to assess change in brain volume and T2 lesion volume.

Detailed Description

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Conditions

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Secondary Progressive Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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natalizumab

In Part 1 participants were randomized to receive 300 mg of natalizumab intravenously (IV) every 4 weeks for 96 weeks. In Part 2 participants transitioned to receive open-label natalizumab 300 mg IV every 4 weeks for at least 96 weeks.

Group Type EXPERIMENTAL

natalizumab

Intervention Type DRUG

Administered as specified in the treatment arm

Placebo

In Part 1 participants were randomized to receive placebo IV every 4 weeks for 96 weeks. In Part 2 participants transitioned to receive open-label natalizumab 300 mg IV every 4 weeks for at least 96 weeks.

Group Type EXPERIMENTAL

natalizumab

Intervention Type DRUG

Administered as specified in the treatment arm

Placebo

Intervention Type DRUG

Matched placebo in part 1

Interventions

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natalizumab

Administered as specified in the treatment arm

Intervention Type DRUG

Placebo

Matched placebo in part 1

Intervention Type DRUG

Other Intervention Names

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Tysabri BG00002

Eligibility Criteria

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Inclusion Criteria

* Ability to understand the purpose and risks of the study and provide signed and dated informed consent and authorization to use protected health information in accordance with national and local subject privacy regulations.
* SPMS defined as relapsing-remitting disease followed by progression of disability independent of or not explained by multiple sclerosis (MS) relapses for at least 2 years.
* EDSS score of 3.0 to 6.5, inclusive.
* Multiple Sclerosis Severity Score of 4 or higher.
* Documented confirmed evidence of disease progression independent of clinical relapses over the 1 year prior to enrollment as defined in the Study Reference Guide.


* Subjects must have participated in and completed Part 1 per protocol, and have documented assessment attempts for EDSS, T25FW, and 9HPT prior to first open-label dosing.

Exclusion Criteria

* Relapsing remitting multiple sclerosis (RRMS) or primary progressive MS as defined by the revised McDonald Committee criteria.
* Clinical relapse (within 3 months) prior to randomization.
* T25FW test of \>30 seconds during the screening period.
* Any value below the lower limit of normal for blood levels of leukocytes, lymphocytes, or neutrophils.
* Considered by the Investigator to be immunocompromised based on medical history, physical examination, laboratory testing, or any other testing required by local guidelines, or due to prior immunosuppressive or immunomodulating treatment.
* Subjects for whom MRI is contraindicated (i.e., have pacemakers or other contraindicated implanted metal devices, are allergic to gadolinium, or have claustrophobia that cannot be medically managed).
* History of any clinically significant (as determined by the Investigator) cardiac, endocrinologic, hematologic, hepatic, immunologic, metabolic, urologic, pulmonary, neurologic (other than MS), dermatologic, psychiatric, and renal, or other major disease that would preclude participation in a clinical study.
* History of malignant disease, including solid tumors and hematologic malignancies (with the exception of basal cell and squamous cell carcinomas of the skin that have been completely excised and are considered cured).
* Known history of or positive test result for human immunodeficiency virus.
* Positive test result for hepatitis C virus (test for hepatitis C virus antibody or hepatitis B virus (test for hepatitis B surface antigen and/or hepatitis B core antibody).
* History of transplantation or any anti-rejection therapy.
* Presence of any infectious disease (e.g., cellulitis, abscess, pneumonia, septicemia) within 30 days prior to screening.
* History of progressive multifocal leukoencephalopathy or other opportunistic infections.

Treatment History (Part 1)

* Any prior treatment with cell-depleting therapies, including total lymphoid irradiation, cladribine, rituximab, alemtuzumab, or bone marrow ablation.
* Any prior treatment with natalizumab.
* Treatment with mitoxantrone, cyclophosphamide, cyclosporine, azathioprine, methotrexate, mycophenolate mofetil, T cell or T cell receptor vaccination, fingolimod, daclizumab, or cytapheresis within 6 months prior to randomization.
* Treatment with intravenous or oral corticosteroids, intravenous immunoglobulin, or plasmapheresis for treatment of MS within the 3 months prior to randomization.
* Treatment with glatiramer acetate or any interferon beta preparations within 4 weeks prior to randomization.
* Treatment with 4-aminopyridine within 30 days prior to randomization, unless a stable dose has been maintained for at least 30 days prior to randomization and will be continued for the course of this study.


* Subjects with any significant change in clinical status, including laboratory tests that, in the opinion of the Investigator, would make them unsuitable to participate in this extension study. The Investigator must re-review the subject's medical fitness for participation and consider any diseases that would preclude treatment.
* Subjects who discontinued study treatment in Part 1 OR had fewer than 20 infusions in Part 1 OR missed 2 or more consecutive infusions in Part 1.
Minimum Eligible Age

18 Years

Maximum Eligible Age

58 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Fullerton, California, United States

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Los Angeles, California, United States

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Aurora, Colorado, United States

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Tampa, Florida, United States

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Chicago, Illinois, United States

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Lake Barrington, Illinois, United States

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Peoria, Illinois, United States

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Indianapolis, Indiana, United States

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Indianapolis, Indiana, United States

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Kansas City, Kansas, United States

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Lexington, Kentucky, United States

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Lexington, Kentucky, United States

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Baltimore, Maryland, United States

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Burlington, Massachusetts, United States

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Omaha, Nebraska, United States

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Lebanon, New Hampshire, United States

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Teaneck, New Jersey, United States

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Latham, New York, United States

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New York, New York, United States

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Advance, North Carolina, United States

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Charlotte, North Carolina, United States

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Raleigh, North Carolina, United States

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Akron, Ohio, United States

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Uniontown, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Clackamas, Oregon, United States

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Portland, Oregon, United States

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Portland, Oregon, United States

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Nashville, Tennessee, United States

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Charlottesville, Virginia, United States

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Seattle, Washington, United States

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Green Bay, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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La Louvière, , Belgium

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Melsbroek, , Belgium

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Overpelt, , Belgium

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Vancouver, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Kingston, Ontario, Canada

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Gatineau, Quebec, Canada

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Greenfield Park, Quebec, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Hradec Králové, Bohemia, Czechia

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Brno, , Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Arthus C, , Denmark

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Esbjerg, , Denmark

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Glostrup Municipality, , Denmark

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København Ø, , Denmark

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Odense, , Denmark

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Jyväskylä, , Finland

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Tampere, , Finland

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Turku, , Finland

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Nice, Alpes Maritimes, France

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Marseille, Bouches-du-Rhône, France

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Nantes, Loire Atlantique, France

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Nancy, Meurthe et Moselle, France

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Lille, Nord, France

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Bron, Rhone, France

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Salouël, Somme, France

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Bordeaux, , France

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Bad Mergentheim, Baden-Wurttemberg, Germany

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Bad Wilbad, Baden-Wurttemberg, Germany

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Tübingen, Baden-Wurttemberg, Germany

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Munich, Bavaria, Germany

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Munich, Bavaria, Germany

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Hennigsdorf, Brandenburg, Germany

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Teupitz, Brandenburg, Germany

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Kassel, Hesse, Germany

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Düsseldorf, North Rhine-Westphalia, Germany

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Münster, North Rhine-Westphalia, Germany

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Dresden, Saxony, Germany

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Dublin, , Ireland

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Dublin, , Ireland

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Jerusalem, , Israel

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Ramat Gan, , Israel

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Baggiovara, Modena, Italy

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Cefalù, Palermo, Italy

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Gallarate, Varese, Italy

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Bari, , Italy

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Florence, , Italy

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Genova, , Italy

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Milan, , Italy

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Milan, , Italy

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Naples, , Italy

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Napoli, , Italy

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Palermo, , Italy

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Pavia, , Italy

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Rome, , Italy

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Rome, , Italy

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's-Hertogenbosch, , Netherlands

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Amsterdam, , Netherlands

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Breda, , Netherlands

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Hoorn, , Netherlands

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Nieuwegein, , Netherlands

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Sittard-Geleen, , Netherlands

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Bialystok, , Poland

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Gdansk, , Poland

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Katowice, , Poland

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Katowice, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Olsztyn, , Poland

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Plewiska, , Poland

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Poznan, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Warszawa-Miedzylesie, , Poland

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Wroclaw, , Poland

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Belgorod, , Russia

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Kazan', , Russia

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Kazan', , Russia

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Moscow, , Russia

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Saint Petersburg, , Russia

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Tyumen, , Russia

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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El Palmar, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Majadahonda, , Spain

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Málaga, , Spain

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Santa Cruz de Tenerife, , Spain

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Seville, , Spain

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Gothenburg, , Sweden

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Örebro, , Sweden

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Stockholm, , Sweden

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Stockholm, , Sweden

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Stockholm, , Sweden

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Umeå, , Sweden

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Irvine, Ayrshire, United Kingdom

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Edgbaston, Birmingham, United Kingdom

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Exeter, Devon, United Kingdom

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Plymouth, Devon, United Kingdom

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London, Greater London, United Kingdom

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London, Greater London, United Kingdom

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Hammersmith, London, United Kingdom

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Edinburgh, Lothian Region, United Kingdom

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Salford, Manchester, United Kingdom

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Liverpool, Merseyside, United Kingdom

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Norwich, Norfolk, United Kingdom

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Nottingham, Nottinghamshire, United Kingdom

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Morriston, Swansea, United Kingdom

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Newcastle, Tyne, United Kingdom

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Brighton, , United Kingdom

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London, , United Kingdom

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Sheffield, , United Kingdom

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Countries

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United States Belgium Canada Czechia Denmark Finland France Germany Ireland Israel Italy Netherlands Poland Russia Spain Sweden United Kingdom

References

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Loomis SJ, Sadhu N, Fisher E, Gafson AR, Huang Y, Yang C, Hughes EE, Marshall E, Herman A, John S, Runz H, Jia X, Bhangale T, Bronson PG. Genome-wide study of longitudinal brain imaging measures of multiple sclerosis progression across six clinical trials. Sci Rep. 2023 Aug 31;13(1):14313. doi: 10.1038/s41598-023-41099-0.

Reference Type DERIVED
PMID: 37652990 (View on PubMed)

Beynon V, George IC, Elliott C, Arnold DL, Ke J, Chen H, Zhu L, Ke C, Giovannoni G, Scaramozza M, Campbell N, Bradley DP, Franchimont N, Gafson A, Belachew S. Chronic lesion activity and disability progression in secondary progressive multiple sclerosis. BMJ Neurol Open. 2022 Jun 7;4(1):e000240. doi: 10.1136/bmjno-2021-000240. eCollection 2022.

Reference Type DERIVED
PMID: 35720980 (View on PubMed)

Koch MW, Mostert J, Zhang Y, Wolinsky JS, Lublin FD, Strijbis E, Cutter G. Association of Age With Contrast-Enhancing Lesions Across the Multiple Sclerosis Disease Spectrum. Neurology. 2021 Sep 28;97(13):e1334-e1342. doi: 10.1212/WNL.0000000000012603. Epub 2021 Aug 10.

Reference Type DERIVED
PMID: 34376508 (View on PubMed)

Kapoor R, Ho PR, Campbell N, Chang I, Deykin A, Forrestal F, Lucas N, Yu B, Arnold DL, Freedman MS, Goldman MD, Hartung HP, Havrdova EK, Jeffery D, Miller A, Sellebjerg F, Cadavid D, Mikol D, Steiner D; ASCEND investigators. Effect of natalizumab on disease progression in secondary progressive multiple sclerosis (ASCEND): a phase 3, randomised, double-blind, placebo-controlled trial with an open-label extension. Lancet Neurol. 2018 May;17(5):405-415. doi: 10.1016/S1474-4422(18)30069-3. Epub 2018 Mar 12.

Reference Type DERIVED
PMID: 29545067 (View on PubMed)

Related Links

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http://www.tysabri.com

Find out what to expect with TYSABRI MS treatment

Other Identifiers

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2010-021978-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

101MS326

Identifier Type: -

Identifier Source: org_study_id

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