Efficacy and Safety Study of Eprotirome in HeFH Patients Who Are on Optimal Standard of Care

NCT ID: NCT01410383

Last Updated: 2012-09-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

236 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-10-31

Study Completion Date

2014-10-31

Brief Summary

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Eprotirome is a liver selective thyroid hormone that can reduce several independent risk factors for cardiovascular disease, while an euthyroid state is preserved in the extrahepatic tissue.

The purpose of this Phase III study is to assess the long-term efficacy and safety of Eprotirome in Patients with heterozygous Familial Hypercholesterolaemia who are on optimal standard of care.

Detailed Description

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Conditions

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Heterozygous Familial Hypercholesterolaemia

Keywords

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hypercholesterolemia, dyslipidemia, thyroid, safety, Heterozygous Familial Hypercholesterolaemia coronary artery disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Tablets taken daily

Eprotirome I

Group Type EXPERIMENTAL

Eprotirome

Intervention Type DRUG

Tablets taken daily

Eprotirome II

Group Type EXPERIMENTAL

Eprotirome

Intervention Type DRUG

Tablets taken daily

Interventions

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Placebo

Tablets taken daily

Intervention Type DRUG

Eprotirome

Tablets taken daily

Intervention Type DRUG

Eprotirome

Tablets taken daily

Intervention Type DRUG

Other Intervention Names

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KB2115 KB2115

Eligibility Criteria

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Inclusion Criteria

* Patients with confirmed HeFH and 18 years of age at screening
* Presence of clinical atherosclerotic disease that confers high risk for CAD events together with an LDL-C more than 2 mmol/L (more than 80 mg/dL)
* Presence of risk factors for CVD (other than the HeFH diagnosis) together with an LDL-C more than 2.5 mmol/L (more than 100 mg/dL)
* On an optimal standard of care, defined as being on a stable dose of statin (rosuvastatin, atorvastatin, or simvastatin) with or without ezetimibe for 8 weeks prior to randomisation

Exclusion Criteria

* Significant health problems in recent past including heart failure,cardiac electrophysiologic instability, rheumatoid arthritis, thyroid dysfunction, liver disease, cancer, secondary dyslipidaemia
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Karo Bio AB

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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John Kastelein, Professor

Role: PRINCIPAL_INVESTIGATOR

Academic Medical Center (AMC) of the University of Amsterdam

Countries

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Sweden

References

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Sjouke B, Langslet G, Ceska R, Nicholls SJ, Nissen SE, Ohlander M, Ladenson PW, Olsson AG, Hovingh GK, Kastelein JJ. Eprotirome in patients with familial hypercholesterolaemia (the AKKA trial): a randomised, double-blind, placebo-controlled phase 3 study. Lancet Diabetes Endocrinol. 2014 Jun;2(6):455-63. doi: 10.1016/S2213-8587(14)70006-3. Epub 2014 Feb 18.

Reference Type DERIVED
PMID: 24731671 (View on PubMed)

Other Identifiers

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KBT 009

Identifier Type: -

Identifier Source: org_study_id