Efficacy and Safety of rHuTPO on Platelet Engraftment After Allo-HSCT

NCT ID: NCT01379391

Last Updated: 2015-10-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE4

Total Enrollment

80 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-06-30

Brief Summary

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Factors influencing platelet engraftment after allogeneic hematopoietic stem cell transplantation (Allo-HSCT) includes previous chemotherapy courses, conditioning regimen, HLA compatibility, source of stem cell, CD34+ cell count, infection of virus/bacteria/fungal, graft-versus-host disease (GVHD), etc. Large-scaled clinical trials have demonstrated that platelet count below 20G/L on 14 days after transplantation is an predictive factor for delayed platelet engraftment, which lead to increased platelet infusion requirement and high risk of bleeding. Multivariable survival analysis indicated that delayed platelet engraftment in Allo-HSCT is independent predictive factor for transplantation related mortality (TRM). But effective treatment approaches for delayed platelet recovery after Allo-HSCT are still lacking now.

Recombinant human thrombopoietin (rHuTPO) is a fully modified recombinant human thrombopoietin accurately expressed in mammalian cells. The rHuTPO agent manufactured by the 3Bio Pharmaceutical Limited Liability Company (LLC) in Shenyang is approved by the State Food and Drug Administration (SFDA) of China in 2005 and is the first rHuTPO agent available globally. RHuTPO was approved for for immune thrombocytopenia and chemotherapy-related thrombocytopenia in China. Animal experiments showed that TPO-mobilizing stem cell could promote platelet engraftment in Allo-HSCT in mice. As for efficacy and safety of TPO on platelet engraftment after Allo-HSCT, it's marginally addressed in clinical trials.

Based on preliminary research results, investigator designed a phase IV, open-label, prospective, multicenter Study of the efficacy and safety of recombinant human thrombopoietin injection (rHuTPO, TPIAO)on platelet engraftment in Allo-HSCT in China.

Detailed Description

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Conditions

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Allogeneic Hematopoietic Stem Cell Transplantation Myeloablative Delayed Platelet Engraftment

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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TPO

Patients received myeloablative Allo-HSCT with platelet lower than 20G/L on +14d post-transplantation. Patient enrolled in TPO arm will recieved Recombinant Human Thrombopoietin (rHTPO) treatment fro 14 days.

Group Type ACTIVE_COMPARATOR

Recombinant Human Thrombopoietin (rHTPO)

Intervention Type DRUG

Patients received allogeneic myeloablative hematopoietic stem cell transplantation with platelet count lower than 20G/L on +14 days after Allo-HSCT, met the above enrollment criteria and signed the informed consent forms are eligible subjects.

Administration method of rHuTPO: 300U/kg/d by percutaneous injection; Timing: d14 to d28 after Allo-HSCT.

TPO-Free Arm

No TPO intervention

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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Recombinant Human Thrombopoietin (rHTPO)

Patients received allogeneic myeloablative hematopoietic stem cell transplantation with platelet count lower than 20G/L on +14 days after Allo-HSCT, met the above enrollment criteria and signed the informed consent forms are eligible subjects.

Administration method of rHuTPO: 300U/kg/d by percutaneous injection; Timing: d14 to d28 after Allo-HSCT.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Ages: 18 years to 65 years.
2. Patients received myeloablative allogeneic hematopoietic stem cell transplantation from related or non-related, HLA compatible or incompatible donors. History controls or concurrent controls are used.
3. The platelet count is lower than 20G/L on +14d post-transplant .
4. The informed consent form has been signed.

Exclusion Criteria

1. Patients received non-myeloablative hematopoietic stem cell transplantation.
2. Patients with severe cardio-cerebral diseases with over grade III A YHA cardiac function or with past history of coronary heart disease, cerebral thrombosis, cerebral arteriosclerosis, etc.
3. Patients with severe hepatic or renal dysfunction with more than 5 times the upper limit of normal range (ULN) of serum ALT or AST levels, or with more than 5 times the upper limit of normal range (ULN) of serum TBIL level or less than 40% of normal prothrombin time activity (PTA); or with more than 3 times the ULN of serum Cr.
4. Patients with history of deep vein thrombosis within 8 weeks of enrollment.
5. Patients with hepatic obstructive venous disease without recovery within 2 weeks of enrollment.
6. Patients with thrombotic microangiopathy without recovery within 2 weeks of enrollment.
7. Patients with capillary leaking syndrome without recovery within 2 weeks of enrollment.
8. Patients with other conditions considered unsuitable for the study.
9. Patients with hypercoagulopathy condition with two or more of these criteria: INR lower than 0.82, APTT lower than the lower limit of normal values (23 seconds) or PT lower than the lower limit of normal values (10 seconds).
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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First Affiliated Hospital, Sun Yat-Sen University

OTHER

Sponsor Role collaborator

Third Affiliated Hospital, Sun Yat-Sen University

OTHER

Sponsor Role collaborator

Guangdong Provincial People's Hospital

OTHER

Sponsor Role collaborator

Guangdong No.2 Provincial People's Hospital

OTHER

Sponsor Role collaborator

Guangzhou General Hospital of Guangzhou Military Command

OTHER

Sponsor Role collaborator

Guangzhou Overseas Chinese Hospital,Guangdong

UNKNOWN

Sponsor Role collaborator

Zhongshan People's Hospital, Guangdong, China

OTHER

Sponsor Role collaborator

Southern Medical University, China

OTHER

Sponsor Role collaborator

Nanfang Hospital, Southern Medical University

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jing Sun, MD

Role: PRINCIPAL_INVESTIGATOR

Department of Hematology, Nanfang Hospital

Locations

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Guangzhou General Hospital of Guangzhou Military Command

Guangzhou, Guangdong, China

Site Status RECRUITING

Guangdong General Hospital

Guangzhou, Guangdong, China

Site Status RECRUITING

First Affiliated Hospital, Sun Yat-Sen University

Guangzhou, Guangdong, China

Site Status RECRUITING

Zhujiang Hospital of Southern Medical University

Guangzhou, Guangdong, China

Site Status RECRUITING

Guangdong No.2 Provincial People's Hospital

Guangzhou, Guangdong, China

Site Status RECRUITING

Nanfang Hospital

Guangzhou, Guangdong, China

Site Status RECRUITING

Guangzhou Overseas Chinese Hospital,Guangdong

Guangzhou, Guangdong, China

Site Status RECRUITING

Third Affiliated Hospital, Sun Yat-Sen University

Guangzhou, Guangdong, China

Site Status RECRUITING

Zhongshan People Hospital,Guangdong

Zhongshan, Guangdong, China

Site Status RECRUITING

Countries

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China

Central Contacts

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Hongsheng Zhou, PhD MD

Role: CONTACT

86-20-62787883

Facility Contacts

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Dongjun Lin, MD

Role: primary

Xiaojun Xu, MD

Role: primary

Hongsheng Zhou, MD PhD

Role: primary

86-20-62787883

Kanger Zhu, MD

Role: primary

Yang Xiao, MD

Role: primary

Suijin Wu, MD

Role: primary

Duorong Xu, MD

Role: primary

Yuhua Li, MD PhD

Role: primary

Qing Zhang, MD

Role: primary

Related Links

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http://www.nfyy.com

Website of Nanfang Hospital, Southern Medical University, Guangzhou, 510515, China.

Other Identifiers

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TPO-HSCT-2011

Identifier Type: -

Identifier Source: org_study_id

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