Trial Outcomes & Findings for Phase II Pharmacokinetic and Pharmacodynamic Study of DEX in Subjects Aged 12 Months Through <24 Months (NCT NCT01378988)

NCT ID: NCT01378988

Last Updated: 2015-07-24

Results Overview

Area under the plasma concentration-time curve of dexmedetomidine at 0 to Infinity hours

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

5 participants

Primary outcome timeframe

30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Results posted on

2015-07-24

Participant Flow

Participant milestones

Participant milestones
Measure
Dose Level 1
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Overall Study
STARTED
2
3
Overall Study
COMPLETED
2
3
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Phase II Pharmacokinetic and Pharmacodynamic Study of DEX in Subjects Aged 12 Months Through <24 Months

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Total
n=5 Participants
Total of all reporting groups
Age, Continuous
1.43 years
STANDARD_DEVIATION 0.312 • n=5 Participants
1.45 years
STANDARD_DEVIATION 0.274 • n=7 Participants
1.44 years
STANDARD_DEVIATION 0.249 • n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
1 Participants
n=5 Participants
3 Participants
n=7 Participants
4 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Area under the plasma concentration-time curve of dexmedetomidine at 0 to Infinity hours

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Area Under the Plasma Concentration-time Curve (AUC0-∞)
4639.17 picogram*hour per millilitre
Standard Deviation 4058.1893
14203.544 picogram*hour per millilitre
Standard Deviation 13051.6850

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Maximum observed concentration of dexmedetomidine in plasma

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Observed Peak Plasma Concentration (Cmax)
4499.925 picogram per millilitre
Standard Deviation 5826.7367
11737.387 picogram per millilitre
Standard Deviation 3549.7923

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Concentration of dexmedetomidine at steady state in plasma

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Steady State Concentration (Css)
752.298 picogram per millilitre
Standard Deviation 658.0848
2303.277 picogram per millilitre
Standard Deviation 2116.4895

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Terminal elimination half-life of dexmedetomidine. Half-life is the time required for plasma concentration of the drug to decrease by 50%.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Terminal Elimination Half-life (t1/2)
1.958 Hours
Standard Deviation 0.3765
2.260 Hours
Standard Deviation 1.2205

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Observed time to reach maximum plasma concentration of dexmedetomidine, expressed in hours

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Time to Reach Maximum Plasma Concentration (Tmax)
0.083 Hours
Standard Deviation 0.0
0.283 Hours
Standard Deviation 0.3464

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Weight-Adjusted Plasma Clearance of dexmedetomidine after intravenous administration.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Weight-Adjusted Plasma Clearance (CLw)
1.292 Litre per Hours per Kilogram
Standard Deviation 1.1300
0.617 Litre per Hours per Kilogram
Standard Deviation 0.3815

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Clearance of dexmedetomidine after intravenous administration. Clearance is the rate at which the drug is removed from the plasma after the dose.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Plasma Clearance (CL)
12.192 Litre per Hour
Standard Deviation 9.5770
5.836 Litre per Hour
Standard Deviation 2.9357

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Volume of distribution of dexmedetomidine after intravenous administration. Volume of distribution measures how much the drug spreads through the body after the dose.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Volume of Distribution (Vd)
31.845 Litre
Standard Deviation 20.4351
15.780 Litre
Standard Deviation 3.5461

PRIMARY outcome

Timeframe: 30 minutes prior to loading dose (LD); 5 minutes before finishing LD; 0.5, 1, 2 and 4-6 hours during maintenance infusion (MI); 30 minutes prior (within 24 hours of start of MI) and 10 minutes, 0.5, 1, 2, 4 and 10 hours end of MI

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

Weight-Adjusted Volume of distribution of dexmedetomidine after intravenous administration.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Weight-Adjusted Volume of Distribution (Vdw)
3.343 Litre per Kilogram
Standard Deviation 2.4910
1.590 Litre per Kilogram
Standard Deviation 0.6201

PRIMARY outcome

Timeframe: Prior to loading dose and every hour during the maintenance infusion; within 5 minutes after any fentanyl administration during DEX infusion or every 4 hours in case of continuous fentanyl infusion; within 5 minutes prior and after titration of fentanyl

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

FLACC scale is a 5 category observational measure to assess pediatric pain on face, legs, activity, cry and consolability. Responses in each category are scored between 0 to 2 (0 = normal, relaxed to 2 = upset, rigid), for a maximum total score of 10.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Average Total Faces, Legs, Activity, Cry, and Consolability (FLACC) Score
1.575 units on a scale
Standard Deviation 2.2274
3.220 units on a scale
Standard Deviation 2.1707

PRIMARY outcome

Timeframe: During the treatment (6 to 24 hours)

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate PK samples to estimate primary parameters.

The level of sedation will be assessed using the University of Michigan Sedation Scale (UMSS). Score 0 (awake/alert); Score 1 (sleepy/responds appropriately); Score 2 (somnolent/arouses to light stimuli); Score 3 (deep sleep/arouses to deeper physical stimuli); Score 4 (unarousable). The UMSS scores obtained just prior the loading dose (LD) and 5 and 10 minutes during LD; 0, 5, 10, 15, 30, and 60 minutes and thereafter every 4 hours of the maintenance infusion; within 5 minutes of obtaining each pharmacokinetic sample; within 5 minutes prior and after any midazolam rescue during dexmedetomidine infusion period.

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Absolute Time That Subject is in UMSS Range 2-4 During Treatment Period
3.6 Hours
Standard Deviation 3.48
5.8 Hours
Standard Deviation 0.38

PRIMARY outcome

Timeframe: During the treatment (6 to 24 hours)

Population: Full Evaluable Population consisted of all subjects who received study drug for at least 5 hours with adequate pharmacokinetic samples to estimate primary parameters.

Participants who received rescue medication midazolam for sedation and/or fentanyl for analgesic during study drug Infusion

Outcome measures

Outcome measures
Measure
Dose Level 1
n=2 Participants
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance infusion
Dose Level 2
n=3 Participants
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance infusion
Number of Subjects Who Received Rescue Medication for Sedation and Analgesic
Midazolam for sedation
1 participants
1 participants
Number of Subjects Who Received Rescue Medication for Sedation and Analgesic
Fentanyl for Analgesic
1 participants
2 participants

Adverse Events

Dose Level 1

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Dose Level 2

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Dose Level 1
n=2 participants at risk
Dexmedetomidine 0.7 mcg/kg loading dose and 0.5 mcg/kg/hr maintenance dose
Dose Level 2
n=3 participants at risk
Dexmedetomidine 1.0 mcg/kg loading dose and 0.75 mcg/kg/hr maintenance dose
General disorders
Pyrexia
0.00%
0/2
33.3%
1/3
Respiratory, thoracic and mediastinal disorders
Atelectasis
0.00%
0/2
33.3%
1/3

Additional Information

Marcelo Garcia de Rocha MD, Global Medical Director

Hospira

Phone: 224-212-4424

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place