Trial Outcomes & Findings for Intravenous Ketamine in the Treatment of Obsessive-Compulsive Disorder (NCT NCT01371110)

NCT ID: NCT01371110

Last Updated: 2018-01-18

Results Overview

The primary efficacy outcome is change in the Y-BOCCS rating score on a scale from baseline to 24 hrs post-administration of ketamine. The 10 Y-BOCCS items are each scored on a four-point scale from 0 = "no symptoms" to 4 = "extreme symptoms." The sum of the first five items is a severity index for obsessions. The sum of the last five an index for compulsions. A translation of total score into an approximate index of overall severity is: 0-7 - subclinical; 8-15 - mild; 16-23 - moderate; 24-31 - severe; 32-40 - extreme.

Recruitment status

TERMINATED

Study phase

PHASE1/PHASE2

Target enrollment

3 participants

Primary outcome timeframe

Baseline and 24 Hours

Results posted on

2018-01-18

Participant Flow

Subjects were recruited from the Mood and Anxiety Disorders Program (MAPs). In addition, referrals from clinicians in the Mount Sinai Medical Center, community clinics, and affiliated hospitals were also sought.

Eligible participants met treatment-resistant criteria if they failed to respond to ≥ 2 adequate pharmacotherapy trials with SRIs FDA approved medications for OCD with or without adjunctive antipsychotics, as well as cognitive behavioral therapy.

Participant milestones

Participant milestones
Measure
Ketamine (Randomized Week 1, Cross Over Midazolam Week 3))
Study participants will receive a one-time intravenous infusion of 0.5 mg/kg racemic ketamine hydrochloride Ketamine: Ketamine hydrochloride is a nonbarbiturate anesthetic. It is formulated as a slight acid (pH 3.5 to 5.5) sterile solution for intravenous or intramuscular injection in concentrations containing the equivalent of either 50 or 100mg ketamine base per milliliter.
Midazolam (Randomized Wk 1, Cross Over Ketamine Wk 3)
Study participants will receive a one-time intravenous infusion of 0.045 mg/kg midazolam Midazolam: Midazolam is a short-acting benzodiazepine central nervous (CNS) depressant.
Overall Study
STARTED
1
2
Overall Study
COMPLETED
1
2
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Intravenous Ketamine in the Treatment of Obsessive-Compulsive Disorder

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ketamine (Randomized Week 1, Cross Over Midazolam Week 3))
n=1 Participants
Study participants will receive a one-time intravenous infusion of 0.5 mg/kg racemic ketamine hydrochloride Ketamine: Ketamine hydrochloride is a nonbarbiturate anesthetic. It is formulated as a slight acid (pH 3.5 to 5.5) sterile solution for intravenous or intramuscular injection in concentrations containing the equivalent of either 50 or 100mg ketamine base per milliliter.
Midazolam (Randomized Wk 1, Cross Over Ketamine Wk 3)
n=2 Participants
Study participants will receive a one-time intravenous infusion of 0.045 mg/kg midazolam Midazolam: Midazolam is a short-acting benzodiazepine central nervous (CNS) depressant.
Total
n=3 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Continuous
49 years
n=5 Participants
48.5 years
n=7 Participants
48.6 years
n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Region of Enrollment
United States
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline and 24 Hours

The primary efficacy outcome is change in the Y-BOCCS rating score on a scale from baseline to 24 hrs post-administration of ketamine. The 10 Y-BOCCS items are each scored on a four-point scale from 0 = "no symptoms" to 4 = "extreme symptoms." The sum of the first five items is a severity index for obsessions. The sum of the last five an index for compulsions. A translation of total score into an approximate index of overall severity is: 0-7 - subclinical; 8-15 - mild; 16-23 - moderate; 24-31 - severe; 32-40 - extreme.

Outcome measures

Outcome measures
Measure
Ketamine (Randomized Week 1, Cross Over Midazolam Week 3))
n=1 Participants
Study participants will receive a one-time intravenous infusion of 0.5 mg/kg racemic ketamine hydrochloride Ketamine: Ketamine hydrochloride is a nonbarbiturate anesthetic. It is formulated as a slight acid (pH 3.5 to 5.5) sterile solution for intravenous or intramuscular injection in concentrations containing the equivalent of either 50 or 100mg ketamine base per milliliter.
Midazolam (Randomized Wk 1, Cross Over Ketamine Wk 3)
n=2 Participants
Study participants will receive a one-time intravenous infusion of 0.045 mg/kg midazolam Midazolam: Midazolam is a short-acting benzodiazepine central nervous (CNS) depressant.
Change in Yale-Brown Obsessive Compulsive Scale (Y-BOCCS) Rating OCD Symptom Severity From Baseline to 24-hours After Ketamine Administration
-2.98 Units on a scale
Interval -2.98 to -2.98
-2.185 Units on a scale
Interval -14.98 to 10.61

SECONDARY outcome

Timeframe: up to 14 days

Percentage of patients who meet response (defined as 25% reduction in Y-BOCCS score) and remission (defined as Y-BOCS score ≤10) criteria at 24 hrs post-infusion and durability of efficacy up to two weeks after administration. Assessments will be performed 24, 48 and 72 hrs post-infusion and after 7, 10, and 14 days.

Outcome measures

Outcome measures
Measure
Ketamine (Randomized Week 1, Cross Over Midazolam Week 3))
n=1 Participants
Study participants will receive a one-time intravenous infusion of 0.5 mg/kg racemic ketamine hydrochloride Ketamine: Ketamine hydrochloride is a nonbarbiturate anesthetic. It is formulated as a slight acid (pH 3.5 to 5.5) sterile solution for intravenous or intramuscular injection in concentrations containing the equivalent of either 50 or 100mg ketamine base per milliliter.
Midazolam (Randomized Wk 1, Cross Over Ketamine Wk 3)
n=2 Participants
Study participants will receive a one-time intravenous infusion of 0.045 mg/kg midazolam Midazolam: Midazolam is a short-acting benzodiazepine central nervous (CNS) depressant.
Percentage of Patients Who Meet Response and Remission
0 percentage of participants
50 percentage of participants

Adverse Events

Ketamine

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Midazolam

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Ketamine
n=1 participants at risk
Study participants will receive a one-time intravenous infusion of 0.5 mg/kg racemic ketamine hydrochloride Ketamine: Ketamine hydrochloride is a nonbarbiturate anesthetic. It is formulated as a slight acid (pH 3.5 to 5.5) sterile solution for intravenous or intramuscular injection in concentrations containing the equivalent of either 50 or 100mg ketamine base per milliliter.
Midazolam
n=2 participants at risk
Study participants will receive a one-time intravenous infusion of 0.045 mg/kg midazolam Midazolam: Midazolam is a short-acting benzodiazepine central nervous (CNS) depressant.
Psychiatric disorders
Suicidality
0.00%
0/1 • 4 weeks
50.0%
1/2 • Number of events 1 • 4 weeks
Gastrointestinal disorders
Diarrhea
0.00%
0/1 • 4 weeks
50.0%
1/2 • Number of events 1 • 4 weeks
Nervous system disorders
Dizziness
0.00%
0/1 • 4 weeks
50.0%
1/2 • Number of events 1 • 4 weeks
Nervous system disorders
Headache
100.0%
1/1 • Number of events 1 • 4 weeks
0.00%
0/2 • 4 weeks
Psychiatric disorders
Fatigue
100.0%
1/1 • Number of events 1 • 4 weeks
0.00%
0/2 • 4 weeks

Additional Information

Wayne Goodman

Baylor College of Medicine (previously Icahn School of Medicine at Mount Sinai)

Phone: 713-798-4945

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place