Trial Outcomes & Findings for Neoadjuvant Pazopanib in Renal Cell Carcinoma (NCT NCT01361113)

NCT ID: NCT01361113

Last Updated: 2018-04-25

Results Overview

Determine the objective response rate (CR+PR) using Response Evaluation Criteria In Solid Tumors (RECIST) 1.1 at 8 weeks after neoadjuvant treatment with pazopanib in patients with locally advanced renal cell carcinoma. Evaluation of Target Lesions using RECIST 1.1 Criteria: Complete response (CR)-Disappearance of all target lesions. Any pathological lymph node (LN) target or no must have decreased in short axis to \<10mm. Partial response (PR)-At least a 30% decrease in the sum of the longest diameter (LD) of the target lesions taking as reference the baseline sum LD.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

21 participants

Primary outcome timeframe

8 weeks after neoadjuvant treatment

Results posted on

2018-04-25

Participant Flow

28 patients consented to participate in this study; 6 patients were found ineligible and 1 patient refused treatment leaving 21 patients on study.

Participant milestones

Participant milestones
Measure
Single Arm Neoadjuvant Pazopanib
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Overall Study
STARTED
21
Overall Study
COMPLETED
21
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Neoadjuvant Pazopanib in Renal Cell Carcinoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Single Arm Neoadjuvant Pazopanib
n=21 Participants
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Age, Continuous
61.57 years
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
Sex: Female, Male
Male
18 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
4 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
17 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=5 Participants
Race (NIH/OMB)
White
15 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
4 Participants
n=5 Participants
Region of Enrollment
United States
21 participants
n=5 Participants

PRIMARY outcome

Timeframe: 8 weeks after neoadjuvant treatment

Determine the objective response rate (CR+PR) using Response Evaluation Criteria In Solid Tumors (RECIST) 1.1 at 8 weeks after neoadjuvant treatment with pazopanib in patients with locally advanced renal cell carcinoma. Evaluation of Target Lesions using RECIST 1.1 Criteria: Complete response (CR)-Disappearance of all target lesions. Any pathological lymph node (LN) target or no must have decreased in short axis to \<10mm. Partial response (PR)-At least a 30% decrease in the sum of the longest diameter (LD) of the target lesions taking as reference the baseline sum LD.

Outcome measures

Outcome measures
Measure
Single Arm Neoadjuvant Pazopanib
n=21 Participants
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
2 Year Recurrence Free Survival
Single Arm Neoadjuvant Pazopanib Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Response Rate
8 Participants

SECONDARY outcome

Timeframe: 2 years

Estimate recurrence free survival (RFS) following neoadjuvant treatment with pazopanib followed by nephrectomy, specifically reporting the 1 year and 2 year rate estimates with their 95% confidence intervals.

Outcome measures

Outcome measures
Measure
Single Arm Neoadjuvant Pazopanib
n=21 Participants
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
2 Year Recurrence Free Survival
n=21 Participants
Single Arm Neoadjuvant Pazopanib Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Recurrence Free Survival (RFS)
83 percentage of Participants
Interval 57.0 to 94.0
77 percentage of Participants
Interval 49.0 to 91.0

SECONDARY outcome

Timeframe: 14 weeks

Determine if neoadjuvant treatment with pazopanib alters the planned surgical approach of the urologist, per documented radiographic (CT) response.

Outcome measures

Outcome measures
Measure
Single Arm Neoadjuvant Pazopanib
n=21 Participants
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
2 Year Recurrence Free Survival
Single Arm Neoadjuvant Pazopanib Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Number of Participants Who Needed an Altered Surgical Approach After Treatment With Pazopanib
0 Participants

SECONDARY outcome

Timeframe: 9 weeks

Identify any safety issues in subjects treated with pazopanib, neoadjuvantly, followed by nephrectomy. Number of patients that had adverse events reported that had an attribution of; possible, probable, or definite that are graded a 3 or higher according to Common Terminology Criteria for Adverse Events (CTCAE v4.0). Grade 1 Mild; asymptomatic or mild symptoms; clinical or diagnostic observations only; intervention not indicated. Grade 2 Moderate; minimal, local or noninvasive intervention indicated; limiting age appropriate instrumental activities of daily living Grade 3 Severe or medically significant but not immediately life-threatening; hospitalization or prolongation of hospitalization indicated; disabling; limiting self care activities of daily living. Grade 4 Life-threatening consequences; urgent intervention indicated. Grade 5 Death related to adverse event.

Outcome measures

Outcome measures
Measure
Single Arm Neoadjuvant Pazopanib
n=21 Participants
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
2 Year Recurrence Free Survival
Single Arm Neoadjuvant Pazopanib Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Number of Participants With Adverse Events Related to Treatment.
11 Participants

Adverse Events

Single Arm Neoadjuvant Pazopanib

Serious events: 6 serious events
Other events: 21 other events
Deaths: 2 deaths

Serious adverse events

Serious adverse events
Measure
Single Arm Neoadjuvant Pazopanib
n=21 participants at risk
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Metabolism and nutrition disorders
Anorexia
4.8%
1/21 • 9 weeks
Cardiac disorders
Atrial fibrillation
4.8%
1/21 • 9 weeks
Investigations
Cardiac troponin I increased
4.8%
1/21 • 9 weeks
Investigations
CPK increased
4.8%
1/21 • 9 weeks
Nervous system disorders
Dizziness
4.8%
1/21 • 9 weeks
Hepatobiliary disorders
Hepatobiliary disorders - Other, specify
4.8%
1/21 • 9 weeks
Vascular disorders
Hypertension
9.5%
2/21 • 9 weeks
Vascular disorders
Hypotension
4.8%
1/21 • 9 weeks
Skin and subcutaneous tissue disorders
Rash maculo-papular
4.8%
1/21 • 9 weeks
Vascular disorders
Thromboembolic event
4.8%
1/21 • 9 weeks

Other adverse events

Other adverse events
Measure
Single Arm Neoadjuvant Pazopanib
n=21 participants at risk
Pazopanib 800 mg PO once daily for 8 weeks Pazopanib: 800 mg orally once daily for 8 weeks, prior to nephrectomy
Gastrointestinal disorders
Abdominal pain
9.5%
2/21 • 9 weeks
Investigations
Alanine aminotransferase increased
33.3%
7/21 • 9 weeks
Investigations
Alkaline phosphatase increased
4.8%
1/21 • 9 weeks
Blood and lymphatic system disorders
Anemia
9.5%
2/21 • 9 weeks
Metabolism and nutrition disorders
Anorexia
28.6%
6/21 • 9 weeks
Investigations
Aspartate aminotransferase increased
38.1%
8/21 • 9 weeks
Musculoskeletal and connective tissue disorders
Back pain
9.5%
2/21 • 9 weeks
Gastrointestinal disorders
Bloating
4.8%
1/21 • 9 weeks
Blood and lymphatic system disorders
Blood and lymphatic system disorders - Other, specify
4.8%
1/21 • 9 weeks
Investigations
Blood bilirubin increased
19.0%
4/21 • 9 weeks
Reproductive system and breast disorders
Breast pain
4.8%
1/21 • 9 weeks
Cardiac disorders
Cardiac disorders - Other, specify
4.8%
1/21 • 9 weeks
Renal and urinary disorders
Chronic kidney disease
4.8%
1/21 • 9 weeks
Psychiatric disorders
Confusion
4.8%
1/21 • 9 weeks
Gastrointestinal disorders
Constipation
4.8%
1/21 • 9 weeks
Investigations
Creatinine increased
4.8%
1/21 • 9 weeks
Gastrointestinal disorders
Diarrhea
52.4%
11/21 • 9 weeks
Nervous system disorders
Dizziness
19.0%
4/21 • 9 weeks
Gastrointestinal disorders
Dry mouth
4.8%
1/21 • 9 weeks
Nervous system disorders
Dysgeusia
52.4%
11/21 • 9 weeks
Gastrointestinal disorders
Dyspepsia
9.5%
2/21 • 9 weeks
Respiratory, thoracic and mediastinal disorders
Dyspnea
4.8%
1/21 • 9 weeks
General disorders
Fatigue
76.2%
16/21 • 9 weeks
Musculoskeletal and connective tissue disorders
Flank pain
9.5%
2/21 • 9 weeks
General disorders
Flu like symptoms
4.8%
1/21 • 9 weeks
General disorders
General disorders and administration site conditions - Other, specify
4.8%
1/21 • 9 weeks
Musculoskeletal and connective tissue disorders
Generalized muscle weakness
4.8%
1/21 • 9 weeks
Investigations
GGT increased
9.5%
2/21 • 9 weeks
Nervous system disorders
Headache
14.3%
3/21 • 9 weeks
Renal and urinary disorders
Hematuria
4.8%
1/21 • 9 weeks
Respiratory, thoracic and mediastinal disorders
Hiccups
4.8%
1/21 • 9 weeks
Metabolism and nutrition disorders
Hypercalcemia
4.8%
1/21 • 9 weeks
Metabolism and nutrition disorders
Hyperglycemia
4.8%
1/21 • 9 weeks
Metabolism and nutrition disorders
Hyperkalemia
9.5%
2/21 • 9 weeks
Metabolism and nutrition disorders
Hypermagnesemia
4.8%
1/21 • 9 weeks
Vascular disorders
Hypertension
61.9%
13/21 • 9 weeks
Metabolism and nutrition disorders
Hypomagnesemia
9.5%
2/21 • 9 weeks
Metabolism and nutrition disorders
Hyponatremia
4.8%
1/21 • 9 weeks
Endocrine disorders
Hypothyroidism
19.0%
4/21 • 9 weeks
Investigations
Lymphocyte count decreased
4.8%
1/21 • 9 weeks
Metabolism and nutrition disorders
Metabolism and nutrition disorders - Other, specify
4.8%
1/21 • 9 weeks
Gastrointestinal disorders
Mucositis oral
4.8%
1/21 • 9 weeks
Musculoskeletal and connective tissue disorders
Myalgia
4.8%
1/21 • 9 weeks
Gastrointestinal disorders
Nausea
42.9%
9/21 • 9 weeks
General disorders
Non-cardiac chest pain
4.8%
1/21 • 9 weeks
Gastrointestinal disorders
Oral dysesthesia
19.0%
4/21 • 9 weeks
General disorders
Pain
9.5%
2/21 • 9 weeks
Musculoskeletal and connective tissue disorders
Pain in extremity
4.8%
1/21 • 9 weeks
Skin and subcutaneous tissue disorders
Palmar-plantar erythrodysesthesia syndrome
28.6%
6/21 • 9 weeks
Gastrointestinal disorders
Periodontal disease
4.8%
1/21 • 9 weeks
Investigations
Platelet count decreased
4.8%
1/21 • 9 weeks
Nervous system disorders
Presyncope
4.8%
1/21 • 9 weeks
Skin and subcutaneous tissue disorders
Rash acneiform
14.3%
3/21 • 9 weeks
Skin and subcutaneous tissue disorders
Rash maculo-papular
4.8%
1/21 • 9 weeks
Skin and subcutaneous tissue disorders
Skin and subcutaneous tissue disorders - Other, specify
4.8%
1/21 • 9 weeks
Skin and subcutaneous tissue disorders
Skin hypopigmentation
14.3%
3/21 • 9 weeks
Skin and subcutaneous tissue disorders
Skin ulceration
4.8%
1/21 • 9 weeks
Gastrointestinal disorders
Stomach pain
4.8%
1/21 • 9 weeks
Ear and labyrinth disorders
Tinnitus
4.8%
1/21 • 9 weeks
Respiratory, thoracic and mediastinal disorders
Voice alteration
9.5%
2/21 • 9 weeks
Gastrointestinal disorders
Vomiting
23.8%
5/21 • 9 weeks

Additional Information

Robin V. Johnson

UNC Lineberger Comprehensive Cancer Center

Phone: 919-966-1125

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60