Trial Outcomes & Findings for Pilot Study of Using Copeptin to Predict Response to Tolvaptan (NCT NCT01346072)

NCT ID: NCT01346072

Last Updated: 2017-05-17

Results Overview

Total urine output for 24 hours following tolvaptan administration

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

21 participants

Primary outcome timeframe

24 hours

Results posted on

2017-05-17

Participant Flow

100 patients were screened in two periods approximately six months each in duration at a dedicated Heart Failure Clinic at the University of North Carolina Chapel Hill. 43 patients met inclusion/exclusion criteria and had a blood sample sent for copeptin testing. Twenty-one patients were enrolled in the hospital phase of the study.

Blinded copeptin results were reviewed in 43 patients for participation in the hospital phase. 11 patients were selected by targeting the upper quartile of baseline copetin and 10 patients by targeting the lower quartile of screening copeptin levels. A total of 21 patients were enrolled in hospital phase.

Participant milestones

Participant milestones
Measure
Tolvaptan High Copeptin
Tolvaptan: oral, 30 mg, single dose, one time administration High Copeptin ≥ 10 pmol/L at baseline
Tolvaptan Low Copeptin
Tolvaptan: oral, 30 mg, single dose, one time administration Low Copeptin \< 10 pmol/L at baseline
Overall Study
STARTED
11
10
Overall Study
COMPLETED
11
10
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Pilot Study of Using Copeptin to Predict Response to Tolvaptan

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Tolvaptan High Copeptin
n=10 Participants
Tolvaptan: oral, 30 mg, single dose, one time administration High Copeptin ≥ 10 pmol/L at baseline
Tolvaptan Low Copeptin
n=10 Participants
Tolvaptan: oral, 30 mg, single dose, one time administration Low Copeptin \< 10 pmol/L at baseline
Total
n=20 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
7 Participants
n=5 Participants
7 Participants
n=7 Participants
14 Participants
n=5 Participants
Age, Categorical
>=65 years
3 Participants
n=5 Participants
3 Participants
n=7 Participants
6 Participants
n=5 Participants
Age, Continuous
60 years
STANDARD_DEVIATION 11 • n=5 Participants
59 years
STANDARD_DEVIATION 13 • n=7 Participants
60 years
STANDARD_DEVIATION 12 • n=5 Participants
Sex: Female, Male
Female
5 Participants
n=5 Participants
6 Participants
n=7 Participants
11 Participants
n=5 Participants
Sex: Female, Male
Male
5 Participants
n=5 Participants
4 Participants
n=7 Participants
9 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
7 Participants
n=5 Participants
4 Participants
n=7 Participants
11 Participants
n=5 Participants
Race (NIH/OMB)
White
3 Participants
n=5 Participants
5 Participants
n=7 Participants
8 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
10 participants
n=5 Participants
10 participants
n=7 Participants
20 participants
n=5 Participants
LVEF
23 %
STANDARD_DEVIATION 6.0 • n=5 Participants
31 %
STANDARD_DEVIATION 11 • n=7 Participants
27 %
STANDARD_DEVIATION 9.6 • n=5 Participants
Baseline Copeptin
20.5 pmol/L
STANDARD_DEVIATION 8.7 • n=5 Participants
5.7 pmol/L
STANDARD_DEVIATION 1.9 • n=7 Participants
13.1 pmol/L
STANDARD_DEVIATION 9.7 • n=5 Participants
Serum Creatinine
1.18 mg/dL
STANDARD_DEVIATION 0.23 • n=5 Participants
1.03 mg/dL
STANDARD_DEVIATION 0.35 • n=7 Participants
1.10 mg/dL
STANDARD_DEVIATION 0.30 • n=5 Participants
Serum Sodium
141.1 mEq/L
STANDARD_DEVIATION 2.28 • n=5 Participants
140.8 mEq/L
STANDARD_DEVIATION 3.46 • n=7 Participants
141.0 mEq/L
STANDARD_DEVIATION 2.86 • n=5 Participants
Total Daily Dose of Loop Diuretic
124 mg
STANDARD_DEVIATION 104 • n=5 Participants
47 mg
STANDARD_DEVIATION 46 • n=7 Participants
84 mg
STANDARD_DEVIATION 86 • n=5 Participants

PRIMARY outcome

Timeframe: 24 hours

Population: All patients in the Low Copeptin group were included in the analysis. One patient in the High Copeptin group had reduced renal function at baseline versus screening and transient hypovolemia during hospitalization indicative of volume depletion. This patient was excluded prior to review of blinded copeptin results and study data analysis.

Total urine output for 24 hours following tolvaptan administration

Outcome measures

Outcome measures
Measure
Tolvaptan High Copeptin
n=10 Participants
Tolvaptan: oral, 30 mg, single dose, one time administration High Copeptin ≥ 10 pmol/L at baseline
Tolvaptan Low Copeptin
n=10 Participants
Tolvaptan: oral, 30 mg, single dose, one time administration Low Copeptin \< 10 pmol/L at baseline
Urine Output
6498 mL
Standard Deviation 2328
5784 mL
Standard Deviation 1835

PRIMARY outcome

Timeframe: Change over 24 hours

Population: All patients in the Low Copeptin group were included in the analysis. One patient in the High Copeptin group had reduced renal function at baseline versus screening and transient hypovolemia during hospitalization indicative of volume depletion. This patient was excluded prior to review of blinded copeptin results and study data analysis.

Change in body weight from baseline to 24 hours after tolvaptan administration

Outcome measures

Outcome measures
Measure
Tolvaptan High Copeptin
n=10 Participants
Tolvaptan: oral, 30 mg, single dose, one time administration High Copeptin ≥ 10 pmol/L at baseline
Tolvaptan Low Copeptin
n=10 Participants
Tolvaptan: oral, 30 mg, single dose, one time administration Low Copeptin \< 10 pmol/L at baseline
Body Weight
-1.3 Kg
Standard Deviation 1.0
-0.4 Kg
Standard Deviation 1.0

Adverse Events

Tolvaptan High Copeptin

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Tolvaptan Low Copeptin

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Kirkwood F. Adams, Jr., MD

University of North Carolina Chapel Hill

Phone: 919-966-2877

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60