Ganaxolone in Posttraumatic Stress Disorder (PTSD)

NCT ID: NCT01339689

Last Updated: 2022-12-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

112 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-04-30

Study Completion Date

2014-03-31

Brief Summary

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This Phase 2 proof-of-concept study is a double-blind, randomized, placebo-controlled, 15-week investigation of ganaxolone versus placebo for the treatment of Posttraumatic Stress Disorder (PTSD). Up to 120 participants will be enrolled and randomized to receive either ganaxolone or placebo for 6 weeks. After 6 weeks of randomized treatment all participants will continue for 6 weeks on ganaxolone. The aim of the study is to assess the efficacy of ganaxolone compared to placebo for the treatment of PTSD symptoms after 6 weeks of treatment using the Clinician-Administered PTSD Rating Scale (CAPS). The second aim of the study is to evaluate the safety and tolerability of ganaxolone in the PTSD population.

Detailed Description

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Conditions

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PTSD

Keywords

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PTSD Posttraumatic Stress Disorder pharmacotherapy ganaxolone

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ganaxolone

active

Group Type EXPERIMENTAL

Ganaxolone

Intervention Type DRUG

200-600 mg bid, capsules, up to 12 weeks

Placebo

non-active

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

capsules, bid, up to 12 weeks

Interventions

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Ganaxolone

200-600 mg bid, capsules, up to 12 weeks

Intervention Type DRUG

Placebo

capsules, bid, up to 12 weeks

Intervention Type DRUG

Other Intervention Names

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GNX PBO

Eligibility Criteria

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Inclusion Criteria

* Veteran or civilian adult outpatients 18-55 years of age, with primary PTSD as defined by Diagnostic and Statistical manual of Mental Disorders-IV (DSM-IV) for at least 6 months
* Must be in general good health-confirmed by medical history, physical examination, and screening laboratory results
* Negative urine drug screen for drugs of abuse
* Negative urine pregnancy test for females of childbearing potential
* Sexually active participants are required to use a medically acceptable form of birth control

Exclusion Criteria

* Clinically unstable medical disease; progressive CNS disorder/disease; history of seizures (except childhood febrile seizure); moderate or severe traumatic brain injury (TBI)
* Females who are pregnant or currently breast feeding
* Current or past psychotic disorder, bipolar Type I disorder, or dementia
* Participants with recent drug abuse or dependency (excluding nicotine and caffeine)
* Participants unwilling to comply with the required alcohol prohibition during the trial
* Current suicidal or homicidal ideation necessitating intervention, and those with a history of suicide attempt in the past 10 years
* Participants with pending litigation related to the traumatic event
* Participants who are unwilling to withhold grapefruit or grapefruit juice for the duration of the study
* Participants receiving psychotherapy without a stable paradigm for at least 3 months
* Non-English speaking participants.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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INTRuST, Post-Traumatic Stress Disorder - Traumatic Brain Injury Clinical Consortium

OTHER

Sponsor Role collaborator

U.S. Army Medical Research and Development Command

FED

Sponsor Role collaborator

Marinus Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Christine E Marx, MD, MA

Role: PRINCIPAL_INVESTIGATOR

Duke University Medical Center and Durham VA Medical Center

Ann Rasmusson, MD

Role: PRINCIPAL_INVESTIGATOR

Boston University School of Medicine Research Affiliate, National Center for PTSD

Locations

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VA San Diego Healthcare System/ University of California, San Diego

San Diego, California, United States

Site Status

Washington DC VA Medical Center/ Uniformed Services University of the Health Services

Washington D.C., District of Columbia, United States

Site Status

VA Boston Healthcare Services/ Spaulding Rehabilitation Hospital

Boston, Massachusetts, United States

Site Status

Manchester VA Medical Center/ Dartmouth College

Manchester, New Hampshire, United States

Site Status

Durham VA Medical Center /Duke University Medical Center

Durham, North Carolina, United States

Site Status

Cincinnati VA Medical Center/ University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Charleston VA Medica Center/ Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

White River Junction VA Medical Center/ Dartmouth College

White River Junction, Vermont, United States

Site Status

Countries

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United States

References

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Rasmusson AM, Marx CE, Jain S, Farfel GM, Tsai J, Sun X, Geracioti TD, Hamner MB, Lohr J, Rosse R, Summerall L, Naylor JC, Cusin C, Lang AJ, Raman R, Stein MB. A randomized controlled trial of ganaxolone in posttraumatic stress disorder. Psychopharmacology (Berl). 2017 Aug;234(15):2245-2257. doi: 10.1007/s00213-017-4649-y. Epub 2017 Jul 1.

Reference Type DERIVED
PMID: 28667510 (View on PubMed)

Other Identifiers

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1042-0700

Identifier Type: -

Identifier Source: org_study_id