Trial Outcomes & Findings for ESBA105 in Patients With Severe Dry Eye (NCT NCT01338610)

NCT ID: NCT01338610

Last Updated: 2013-04-19

Results Overview

An electronic Visual Analog Scale (eVAS) was used by the subject to assess ocular discomfort, both frequency and severity, at Day 0 (pre-treatment) and daily thereafter for 28 days. Assessments were entered into a LogPad® (handheld electronic device). The VAS frequency score ranged from 0 (rarely) to 100 (all the time), and the VAS severity score ranged from 0 (very mildly uncomfortable) to 100 (very severely uncomfortable). The Global Ocular Discomfort Score is a composite of the frequency and severity VAS scores (0-100).

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

334 participants

Primary outcome timeframe

Up to 28 days

Results posted on

2013-04-19

Participant Flow

Subjects were recruited from 16 investigative sites located within the United States. Participant flow data is presented for all subjects exposed to product.

Of the 334 enrolled, 210 subjects did not qualify for Run-In and were exited from the study without exposure to product. Of the 124 entering Run-In, 39 did not qualify for treatment. The 85 subjects qualifying for treatment were randomized 2:1 to receive either ESBA105 or Vehicle.

Participant milestones

Participant milestones
Measure
Run-In Only
ESBA105 vehicle
ESBA105
ESBA105 vehicle (Run-In), ESBA105 ophthalmic solution (treatment)
Vehicle
ESBA105 vehicle (Run-In), ESBA105 vehicle (treatment)
Overall Study
STARTED
39
56
29
Overall Study
COMPLETED
34
55
28
Overall Study
NOT COMPLETED
5
1
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Run-In Only
ESBA105 vehicle
ESBA105
ESBA105 vehicle (Run-In), ESBA105 ophthalmic solution (treatment)
Vehicle
ESBA105 vehicle (Run-In), ESBA105 vehicle (treatment)
Overall Study
Patient Decision Unrelated to Advs Event
1
1
0
Overall Study
Protocol Violation
1
0
1
Overall Study
Adverse Event
3
0
0

Baseline Characteristics

ESBA105 in Patients With Severe Dry Eye

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Run-In Only
n=39 Participants
ESBA105 vehicle
ESBA105
n=56 Participants
ESBA 105 vehicle (Run-In), ESBA105 ophthalmic solution (treatment)
Vehicle
n=29 Participants
ESBA105 vehicle (Run-In), ESBA105 vehicle (treatment)
Total
n=124 Participants
Total of all reporting groups
Age, Customized
<65
24 participants
n=5 Participants
32 participants
n=7 Participants
21 participants
n=5 Participants
77 participants
n=4 Participants
Age, Customized
≥65
15 participants
n=5 Participants
24 participants
n=7 Participants
8 participants
n=5 Participants
47 participants
n=4 Participants
Sex: Female, Male
Female
35 Participants
n=5 Participants
45 Participants
n=7 Participants
26 Participants
n=5 Participants
106 Participants
n=4 Participants
Sex: Female, Male
Male
4 Participants
n=5 Participants
11 Participants
n=7 Participants
3 Participants
n=5 Participants
18 Participants
n=4 Participants
Region of Enrollment
United States
39 participants
n=5 Participants
56 participants
n=7 Participants
29 participants
n=5 Participants
124 participants
n=4 Participants

PRIMARY outcome

Timeframe: Up to 28 days

Population: All subjects randomized to treatment and receiving at least 1 administration of study medication (intent-to-treat). Mixed model repeated measure (MMRM) approach was used to handle missing data during randomized treatment period.

An electronic Visual Analog Scale (eVAS) was used by the subject to assess ocular discomfort, both frequency and severity, at Day 0 (pre-treatment) and daily thereafter for 28 days. Assessments were entered into a LogPad® (handheld electronic device). The VAS frequency score ranged from 0 (rarely) to 100 (all the time), and the VAS severity score ranged from 0 (very mildly uncomfortable) to 100 (very severely uncomfortable). The Global Ocular Discomfort Score is a composite of the frequency and severity VAS scores (0-100).

Outcome measures

Outcome measures
Measure
ESBA105
n=56 Participants
ESBA105 ophthalmic solution
Vehicle
n=29 Participants
ESBA105 vehicle
Visual Analog Scale (VAS) Global Ocular Discomfort Score, Area Under the Curve, Day 0 to Day 28
63.8773 Units on a scale x days
Standard Error 2.4832
70.2194 Units on a scale x days
Standard Error 2.39802

Adverse Events

Run-In

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

ESBA105

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Vehicle

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Christian Leisner

Alcon Research, Ltd.

Phone: 1-888-451-3937

Results disclosure agreements

  • Principal investigator is a sponsor employee Sponsor reserves the right of prior review of any publication or presentation of information related to the study.
  • Publication restrictions are in place

Restriction type: OTHER