A Study of First-line Maintenance Erlotinib Versus Erlotinib at Disease Progression in Participants With Advanced Non-Small Cell Lung Cancer (NSCLC) Who Have Not Progressed Following Platinum-Based Chemotherapy

NCT ID: NCT01328951

Last Updated: 2016-10-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

643 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-09-30

Study Completion Date

2016-01-31

Brief Summary

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This double-blind, placebo-controlled study will evaluate the benefit of first-line maintenance erlotinib (Tarceva) versus erlotinib at the time of disease progression in participants with advanced NSCLC who have not progressed following 4 cycles of platinum based-chemotherapy and whose tumor does not harbor an epidermal growth factor receptor (EGFR)-activating mutation. Participants will be randomized to receive either erlotinib 150 milligrams (mg) orally (PO) once daily or placebo. Participants who progress on placebo will receive erlotinib 150 mg PO once daily as second-line therapy, and those who progress on erlotinib may switch to a non-investigational, second-line chemotherapy. Treatments will continue until disease progression, death, or unacceptable toxicity. Participants may also be entered into a final Survival Follow-Up (SFU) period upon treatment discontinuation.

Detailed Description

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Conditions

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Non-Squamous Non-Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Early Erlotinib

Participants will receive blinded erlotinib as 150 mg PO once daily in the maintenance setting until disease progression, death, or unacceptable toxicity. Those who demonstrate disease progression may be unblinded to receive an approved second-line therapy (but not EGFR targeted therapies) until disease progression, death, or unacceptable toxicity. Participants may be observed during a final SFU period after discontinuation from study treatment.

Group Type EXPERIMENTAL

Erlotinib

Intervention Type DRUG

Erlotinib will be administered as 150 mg PO once daily until disease progression, death, or unacceptable toxicity, as first-line maintenance or as second-line therapy for those who progress while receiving placebo.

Second-Line Chemotherapy

Intervention Type DRUG

Participants who progress on first-line maintenance erlotinib may receive an approved second-line therapy (but not EGFR targeted therapies) until disease progression, death, or unacceptable toxicity. The selected chemotherapy will be non-investigational and chosen at the discretion of the Investigator.

Late Erlotinib

Participants will receive blinded placebo tablets PO once daily in the maintenance setting until disease progression, death, or unacceptable toxicity. Those who demonstrate disease progression may be unblinded to receive second-line erlotinib as 150 mg PO once daily until disease progression, death, or unacceptable toxicity. Participants may be observed during a final SFU period after discontinuation from study treatment.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered PO once daily as first-line maintenance until disease progression, death, or unacceptable toxicity.

Erlotinib

Intervention Type DRUG

Erlotinib will be administered as 150 mg PO once daily until disease progression, death, or unacceptable toxicity, as first-line maintenance or as second-line therapy for those who progress while receiving placebo.

Interventions

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Placebo

Placebo will be administered PO once daily as first-line maintenance until disease progression, death, or unacceptable toxicity.

Intervention Type DRUG

Erlotinib

Erlotinib will be administered as 150 mg PO once daily until disease progression, death, or unacceptable toxicity, as first-line maintenance or as second-line therapy for those who progress while receiving placebo.

Intervention Type DRUG

Second-Line Chemotherapy

Participants who progress on first-line maintenance erlotinib may receive an approved second-line therapy (but not EGFR targeted therapies) until disease progression, death, or unacceptable toxicity. The selected chemotherapy will be non-investigational and chosen at the discretion of the Investigator.

Intervention Type DRUG

Other Intervention Names

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Tarceva

Eligibility Criteria

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Inclusion Criteria

* Adults greater than or equal to (≥) 18 years of age, or legal age of consent if greater than 18
* Advanced or recurrent (Stage IIIB) or metastatic (Stage IV) NSCLC
* Completion of 4 cycles of platinum-based chemotherapy without progression (end of last chemotherapy cycle less than or equal to \[≤\] 28 days prior to randomization)
* Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1

Exclusion Criteria

* Prior exposure to agents directed at human epidermal growth factor receptor (HER) axis (e.g. erlotinib, gefitinib, cetuximab)
* Participants whose tumors harbor an EGFR-activating mutation
* Prior chemotherapy or therapy with systemic anti-neoplastic therapy for advanced disease before Screening
* Use of pemetrexed in maintenance setting (pemetrexed allowed during the chemotherapy run-in)
* Participants who have undergone complete tumor resection after responding to the platinum-based chemotherapy during the Screening phase
* Any other malignancies within 5 years, except for curatively resected carcinoma in situ of the cervix, basal or squamous cell skin cancer, ductal carcinoma in situ, or organ-confined prostate cancer
* Central nervous system (CNS) metastases or spinal cord compression that has not been definitely treated with surgery and/or radiation, or treated CNS metastases or spinal cord compression without stable disease for ≥2 months
* Human immunodeficiency virus (HIV), hepatitis B, or hepatitis C infection
* Any inflammatory changes of the surface of the eye
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Gilroy, California, United States

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Washington D.C., District of Columbia, United States

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Kansas City, Missouri, United States

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Missoula, Montana, United States

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Lebanon, New Hampshire, United States

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Dayton, Ohio, United States

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Chattanooga, Tennessee, United States

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Spokane, Washington, United States

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Tacoma, Washington, United States

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Belo Horizonte, Minas Gerais, Brazil

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Lajeado, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Ijuí, Rondônia, Brazil

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Florianópolis, Santa Catarina, Brazil

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Santo André, São Paulo, Brazil

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Gabrovo, , Bulgaria

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Haskovo, , Bulgaria

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Plovdiv, , Bulgaria

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Rousse, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Varna, , Bulgaria

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Windsor, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Regina, Saskatchewan, Canada

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Beijing, , China

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Beijing, , China

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Changchun, , China

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Fuzhou, , China

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Guangzhou, , China

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Guangzhou, , China

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Harbin, , China

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Shanghai, , China

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Shanghai, , China

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Shantou, , China

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Shenyang, , China

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Suzhou, , China

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Tianjin, , China

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Wuhan, , China

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Xi'an, , China

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České Budějovice, , Czechia

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Jindřichův Hradec, , Czechia

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Nymburk, , Czechia

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Ostrava - Poruba, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Tábor, , Czechia

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Bayonne, , France

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Compiègne, , France

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Gap, , France

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Libourne, , France

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Lille, , France

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Nantes, , France

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Saint-Brieuc, , France

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Villefranche-sur-Saône, , France

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Deszk, , Hungary

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Farkasgyepű, , Hungary

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Győr, , Hungary

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Gyula, , Hungary

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Mátraháza, , Hungary

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Miskolc, , Hungary

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Székesfehérvár, , Hungary

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Szolnok, , Hungary

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Törökbálint, , Hungary

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Zalaegerszeg, , Hungary

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S. Giovanni Rotondo, Apulia, Italy

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Avellino, Campania, Italy

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Bologna, Emilia-Romagna, Italy

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Parma, Emilia-Romagna, Italy

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Rome, Lazio, Italy

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Rome, Lazio, Italy

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Rome, Lazio, Italy

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Legnago, Lombardy, Italy

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Treviglio, Lombardy, Italy

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Livorno, Tuscany, Italy

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Pisa, Tuscany, Italy

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Verona, Veneto, Italy

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Daugavpils, , Latvia

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Riga, , Latvia

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Riga, , Latvia

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Kaunas, , Lithuania

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Vilnius, , Lithuania

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Arnhem, , Netherlands

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Heerlen, , Netherlands

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Hoorn, , Netherlands

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Sittard-Geleen, , Netherlands

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Zutphen, , Netherlands

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Brzozów, , Poland

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Krakow, , Poland

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Poznan, , Poland

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Wodzisław Śląski, , Poland

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Zamość, , Poland

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Baia Mare, , Romania

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Brasov, , Romania

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Brasov, , Romania

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Brăila, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Cluj-Napoca, , Romania

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Cluj-Napoca, , Romania

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Oradea, , Romania

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Ploieşti, , Romania

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Târgu Mureş, , Romania

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Banská Bystrica, , Slovakia

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Bardejov, , Slovakia

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Košice, , Slovakia

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Nové Zámky, , Slovakia

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Poprad, , Slovakia

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Rimavská Sobota, , Slovakia

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Cape Town, , South Africa

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Cape Town, , South Africa

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George, , South Africa

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Port Elizabeth, , South Africa

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Pretoria, , South Africa

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Gyeonggi-do, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Suwon, , South Korea

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Hat Yai, , Thailand

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Muang, , Thailand

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Muang, , Thailand

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Dnipropetrovsk, , Ukraine

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Donetsk, , Ukraine

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Kharkiv, , Ukraine

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Kirovograd, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Lutsk, , Ukraine

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Sumy, , Ukraine

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Uzhhorod, , Ukraine

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Vinnytsia, , Ukraine

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Zaporizhzhya, , Ukraine

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Countries

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Germany United States Brazil Bulgaria Canada China Czechia France Hungary Italy Latvia Lithuania Netherlands Poland Romania Slovakia South Africa South Korea Taiwan Thailand Ukraine

Other Identifiers

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BO25460

Identifier Type: -

Identifier Source: org_study_id