Comparison of Pixantrone + Rituximab With Gemcitabine + Rituximab in Patients With Aggressive B-cell Non-Hodgkin Lymphoma or Follicular Grade 3 Lymphoma Who Have Relapsed After Therapy and Are Not Eligible for Stem Cell Transplant

NCT ID: NCT01321541

Last Updated: 2021-11-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

312 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-04-20

Study Completion Date

2018-09-14

Brief Summary

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The purpose of this study is to evaluate the efficacy of Pixantrone + Rituximab compared to Gemcitabine + Rituximab in patients with relapsed or refractory diffuse large B-cell lymphoma (DLBCL), or follicular grade 3 lymphoma.

Detailed Description

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Eligible patients will be randomized to treatment with pixantrone plus rituximab or gemcitabine plus rituximab in up to six 28-day cycles. At the time patients experience progressive disease during study treatment, early follow- up, or intermediate follow-up, they enter the survival follow up period. Patients who complete study treatment or discontinue study treatment for any other reason will participate in the follow-up periods.

Early Follow-Up: After treatment completion or discontinuation, patient will enter a 24-week follow-up period.

Intermediate Follow-Up: After completing the 24-week early follow-up period, patient will enter an additional 72-week follow-up period.

Survival Follow-Up: All patients will be monitored for survival.

Conditions

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Diffuse Large B-cell Lymphoma de Novo DLBCL DLBCL Transformed From Indolent Lymphoma Follicular Grade 3 Lymphoma

Keywords

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non-hodgkin lymphoma DLBCL relapsed aggressive NHL Diffuse large B-cell lymphoma Rituximab Rituxan Pixantrone NHL non hodgkin's lymphoma de novo DLBCL DLBCL transformed from Indolent Lymphoma Follicular Grade 3 Lymphoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Outcome Assessors

Study Groups

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Pixantrone + Rituximab

Pixantrone and Rituximab

Group Type EXPERIMENTAL

Pixantrone + Rituximab

Intervention Type DRUG

Pixantrone + Rituximab: Rituximab 375 mg/m2 IV on day 1 and pixantrone 50 mg/m2 (equivalent to 85mg/m2 pixantrone dimaleate)IV on days 1, 8, and 15. Regimen is given in 28-day cycles. Up to 6 cycles may be administered.

Gemcitabine + Rituximab

Gemcitabine and Rituximab

Group Type ACTIVE_COMPARATOR

Gemcitabine + Rituximab

Intervention Type DRUG

Gemcitabine + Rituximab: Rituximab 375 mg/m2 IV on day 1 and gemcitabine 1000 mg/m2 IV on days 1, 8, and 15. Regimen is given in 28-day cycles. Up to 6 cycles may be administered.

Interventions

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Pixantrone + Rituximab

Pixantrone + Rituximab: Rituximab 375 mg/m2 IV on day 1 and pixantrone 50 mg/m2 (equivalent to 85mg/m2 pixantrone dimaleate)IV on days 1, 8, and 15. Regimen is given in 28-day cycles. Up to 6 cycles may be administered.

Intervention Type DRUG

Gemcitabine + Rituximab

Gemcitabine + Rituximab: Rituximab 375 mg/m2 IV on day 1 and gemcitabine 1000 mg/m2 IV on days 1, 8, and 15. Regimen is given in 28-day cycles. Up to 6 cycles may be administered.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of DLBCL (de novo DLBCL, or transformed from indolent lymphoma) or follicular grade 3 lymphoma on the basis of tissue biopsy.
2. Patients with de novo DLBCL must have received 1-3 treatment regimens for DLBCL. Patients with follicular grade 3 lymphoma must have received 1-3 treatment regimens for follicular lymphoma (any grade). Patients with DLBCL transformed from indolent lymphoma must have received at least 1-4 treatment regimens for NHL.
3. Received rituximab containing a multi-agent therapy for the treatment of NHL.
4. Not eligible for high-dose chemotherapy and stem cell transplant.
5. Patients with DLBCL transformed from indolent lymphoma must have had a complete or partial response to a therapy for NHL lasting at least 12 weeks.

Exclusion Criteria

1. Primary refractory de novo DLBCL or primary refractory follicular grade 3 lymphoma, defined as documented progression within 12 weeks of the last cycle of the first-line multi-agent regimen.
2. Prior treatment with cumulative dose of doxorubicin or equivalent exceeding 450 mg/m2
3. Any experimental therapy ≤ 28 days prior to randomization
4. Other malignancy within last 5 years except for the following: curatively treated basal cell/squamous cell skin cancer, carcinoma in situ of the cervix, superficial transitional cell bladder carcinoma, or in situ ductal carcinoma of the breast after complete resection
5. Any contraindication or known allergy or hypersensitivity to any study drugs
6. Concomitant therapy with any anticancer agents, immunosuppressive agents, other investigational anticancer therapies. Low-dose corticosteroids for the treatment of non cancer-related illnesses are permitted.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CTI BioPharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Simran B Singh, MS, GWCP

Role: STUDY_DIRECTOR

Sr. Director, Clinical Operations

Locations

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Arizona Clinical Research Center

Tucson, Arizona, United States

Site Status

Arizona Oncology Associates

Tucson, Arizona, United States

Site Status

Highlands Oncology Group

Bentonville, Arkansas, United States

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Highlands Oncology Group

Fayetteville, Arkansas, United States

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Rocky Mountain Cancer Centers

Aurora, Colorado, United States

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Rocky Mountain Cancer Centers

Boulder, Colorado, United States

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Rocky Mountain Cancer Centers

Denver, Colorado, United States

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George Washington University Department of Medicine

Washington D.C., District of Columbia, United States

Site Status

Integrated Community Oncology Network-St. Vincent's

Jacksonville, Florida, United States

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Integrated Community Oncology Network-Southside

Jacksonville, Florida, United States

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Integrated Community Oncology Network

Orange Park, Florida, United States

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Carle Physician Group

Danville, Illinois, United States

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Cancer Care Specialists of Central Illinois

Decatur, Illinois, United States

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Crossroads Cancer Center

Effingham, Illinois, United States

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Carle Foundation Physician Services

Mattoon, Illinois, United States

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Carle Cancer Center

Urbana, Illinois, United States

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Cancer Center of Kansas

Wichita, Kansas, United States

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Cancer Center of Kansas

Wichita, Kansas, United States

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Baptist Hospital East

Louisville, Kentucky, United States

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Harry and Jeanette Weinberg Cancer Institute at Franklin Square

Baltimore, Maryland, United States

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Center for Cancer and Blood Disorders, PC

Bethesda, Maryland, United States

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Cancer & Hematology Center of Western Michigan

Grand Rapids, Michigan, United States

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Metro Minnesota CCOP-Unity Hospital

Fridley, Minnesota, United States

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Metro Minnesota CCOP-St. Johns

Maplewood, Minnesota, United States

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Metro Minnesota Community Clinical Oncology Program

Saint Louis Park, Minnesota, United States

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Metro Minnesota Community Clinical Oncology Program

Saint Louis Park, Minnesota, United States

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Metro Minnesota CCOP-Regions Hospital

Saint Paul, Minnesota, United States

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Missouri Cancer Associates

Columbia, Missouri, United States

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Nebraska Hematology-Oncology, PC

Lincoln, Nebraska, United States

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Hematology-Oncology Associates of Northern New Jersey

Morristown, New Jersey, United States

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North Shore Hematology/Oncology Associates

East Setauket, New York, United States

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Gabrail Cancer Center

Canton, Ohio, United States

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Gabrail Cancer Center

Dover, Ohio, United States

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Toledo Clinical Cancer Center

Toledo, Ohio, United States

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Mercy Cancer Center at St. Anne's

Toledo, Ohio, United States

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Toledo Clinic Cancer Center-Toledo

Toledo, Ohio, United States

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Northwest Cancer Specialists, PC

Portland, Oregon, United States

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Northwest Cancer Specialists, PC

Portland, Oregon, United States

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Northwest Cancer Specialists, PC

Tualatin, Oregon, United States

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Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

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Upstate Oncology Associates

Greenville, South Carolina, United States

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South Carolina Cancer Specialists

Hardeeville, South Carolina, United States

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South Carolina Cancer Specialists

Hilton Head Island, South Carolina, United States

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Joe Arrington Cancer Research and Treatment Center

Lubbock, Texas, United States

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Cancer Care Centers of South Texas-HOAST

New Braunfels, Texas, United States

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Cancer Care Centers of South Texas-HOAST

San Antonio, Texas, United States

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Blue Ridge Cancer Care

Roanoke, Virginia, United States

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Northwest Cancer Specialists, PC

Vancouver, Washington, United States

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Northwest Cancer Specialists, PC

Vancouver, Washington, United States

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Saint Vincent Hospital Green Bay Oncology

Green Bay, Wisconsin, United States

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Green Bay Oncology-St. Mary's Hospital MC

Green Bay, Wisconsin, United States

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Medical University Innsbruck, Department of Internal Medicine V (Hematology and Oncology)

Innsbruck, , Austria

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Hospital Elisabethinen Linz, Internal Department 1 - Hemato-Oncology

Linz, , Austria

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Hanusch Hospital, Department of Internal Medicine III

Vienna, , Austria

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Saint Luc University Hospital, Department of Hematology

Brussels, , Belgium

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General Hospital Delta, Hematology Department

Roeselare, , Belgium

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General Hospital Turnhout, Hematology Department

Turnhout, , Belgium

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UMHAT "Sveti Georgi", Plovdiv, Clinical Hematology Clinic

Plovdiv, , Bulgaria

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UMHAT "Sveti Georgi", Plovdiv, Department of Medical Oncology

Plovdiv, , Bulgaria

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MHAT "Tokuda Hospital Sofia", Hematology Clinic

Sofia, , Bulgaria

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University Multiprofile Hospital for Active Treatment "Sveti Ivan Rilski", Department of Clinical Hematology

Sofia, , Bulgaria

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Specialized Hospital For Active Treatment Of Hematological Diseases, Sofia, Clinical Hematology Clinic

Sofia, , Bulgaria

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MHAT Hristo Botev, Vratsa, First Department of Internal Medicine

Vratsa, , Bulgaria

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University Hospital Brno, Clinic of Internal Medicine - Hematology and Oncology

Brno, , Czechia

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University Hospital Hradec Kralove, 4th Department of Internal Medicne, Clinical Hematology

Hradec Králové, , Czechia

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University Hospital Ostrava, Institute of Clinical Hematology

Ostrava, , Czechia

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University Hospital Kralovske Vinohrady, Department of Clinical Hematology

Prague, , Czechia

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General University Hospital in Prague, 1st Department of Internal Medicine - Department of Hematology

Prague, , Czechia

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Aalborg University Hospital, Department of Hematology

Aalborg, , Denmark

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Service d'hématologie clinique, Avenue Laennec Salouel

Amiens, , France

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Centre hopitalier de la cote basque

Bayonne, , France

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Centre hospitalier de Beziers

Béziers, , France

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Polyclinique de Bordeaux nord Acquitaine

Bordeaux, , France

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Centre hospitalier du Mans

Le Mans, , France

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Centre hospitalier Lyon Sud

Pierre-Bénite, , France

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Saint Quentin Hospital Center, Department of Oncology-Hematology

Saint-Quentin, , France

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Hautepierre Hospital, Department of Hematology and Oncology

Strasbourg, , France

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Gemeinschaftspraxis Drs. Klausmann

Aschaffenburg, , Germany

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Klinikum Chemnitz gGmbH

Chemnitz, , Germany

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Universitätsklinik Köln

Cologne, , Germany

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Klinik für Innere Medizin III

Frankfurt (a.M.), , Germany

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Universitaetsklinikum Halle

Halle, , Germany

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St. Marien Hospital Hamm

Hamm, , Germany

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Klinikum Nürnberg Nord

Nuremberg, , Germany

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Klinikum Mutterhaus der Borromäerinnen

Trier, , Germany

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St. Istvan and St. Laszlo Hospital of Budapest

Budapest, , Hungary

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University of Debrecen

Debrecen, , Hungary

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Moritz Kaposi General Hospital

Kaposvár, , Hungary

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University Hospital "Ospedali Riuniti Umberto I - G.M. Lancisi - G. Salesi"

Ancona, , Italy

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Bologna University Hospital Authority St. Orsola-Malpighi Polyclinic

Bologna, , Italy

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Scientific Institute of Romagna for the Study and Treatment of Cancer (I.R.S.T.) S.R.L.

Meldola, , Italy

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"Ospedali Riuniti Villa Sofia-Cervello" Hospital

Palermo, , Italy

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Romagna Local Health Authority (AUSL Romagna) - "Santa Maria delle Croci"

Ravenna, , Italy

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Romagna Local Health Authority (AUSL Romagna) - "Infermi" Hospital

Rimini, , Italy

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Siena University Hospital Authority Santa Maria alle Scotte Polyclinic

Siena, , Italy

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Santa Maria Hospital

Terni, , Italy

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A.O.U. Città della Salute e della Scienza di Torino

Torino, , Italy

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Independent Public Healthcare Facility Municipal Hospital Group

Chorzów, , Poland

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Marine Hospital of Polish Red Cross, Department of Chemotheraphy

Gdynia, , Poland

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Silesia Medical University, Department of Hematology and Bone Marrow Transplantation

Katowice, , Poland

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Malopolskie Medical Center S.C. , Department of Hematology

Krakow, , Poland

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Nicolaus Copernicus Memorial Provincial Specialist Hospital in Lodz

Lodz, , Poland

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Oncology Center of Lublin Land, Department of Clinical Oncology

Lublin, , Poland

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Institute of Hematology and Transfusion Medicine, Clinic of Hematology

Warsaw, , Poland

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Wroclaw Medical University, Department and Clinic of Hematology, Blood Neoplasms and Bone Marrow Transplantation

Wroclaw, , Poland

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Rapid Diagnosis Polyclinic SA

Brasov, , Romania

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Fundeni Clinical Institute Center for Hematology and Bone Marrow Transplantation

Bucharest, , Romania

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Bucharest University Emergency Hospital, Hematology Clinic

Bucharest, , Romania

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Federal State Public Institution: Main Military Clinical Hospital n.a. N.N. Burdenko of the Russian Ministry of Defense

Moscow, , Russia

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Moscow State Budget Medical Institution: City Clinical Hospital n.a. S.P.Botkin

Moscow, , Russia

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State Medical Institution: Republican Hospital named after V.A. Baranov

Petrozavodsk, , Russia

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St. Petersburg Clinical Research and Practical Center for Specialized Types of Medical Care

Saint Petersburg, , Russia

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State Healthcare Institution: Republican Clinical Oncology Center

Ufa, , Russia

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State Budget Healthcare Institution of Sverdlovsk region: Sverdlovsk Regional Clinical Hospital #1

Yekaterinburg, , Russia

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University Hospital with Outpatient Clinic F.D. Roosevelt Banska Bystrica, Department of Hematology

Banská Bystrica, , Slovakia

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National Cancer Institute, Department of Hematology and Transfusiology

Bratislava, , Slovakia

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University Hospital Martin, Department of Hematology and Transfusiology

Martin, , Slovakia

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J. A. Reiman University Hospital with Polyclinic in Presov

Prešov, , Slovakia

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A Coruña University Hospital

A Coruña, , Spain

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Hospital Universitario Vall Hebrón

Barcelona, , Spain

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Hospital Iniversitario Puerta del Mar

Cadiz, , Spain

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Institut Català de Oncologia (ICO), Hospital Dr Trueta

Girona, , Spain

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Hospital Iniversitario La Paz

Madrid, , Spain

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Hospital Universitario Araba

Vitoria-Gasteiz, , Spain

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Cherkasy Regional Oncology Center, Regional Treatment and Diagnostic Hematology Center

Cherkasy, , Ukraine

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Kharkiv Regional Clinical Oncology Center

Kharkiv, , Ukraine

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National Institute of Cancer

Kyiv, , Ukraine

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State Institution: Institute of Blood Pathology and Transfusion Medicine

Lviv, , Ukraine

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Beatson West of Scotland Cancer Center

Glasgow, , United Kingdom

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St. George's Healthcare NHS Trust

London, , United Kingdom

Site Status

Christie Hospital, Department of Medical Oncology

Manchester, , United Kingdom

Site Status

Countries

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Canada United States Austria Belgium Bulgaria Czechia Denmark France Germany Hungary Italy Poland Romania Russia Slovakia Spain Ukraine United Kingdom

References

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Pettengell R, Dlugosz-Danecka M, Andorsky D, Belada D, Georgiev P, Quick D, Singer JW, Singh SB, Pallis A, Egorov A, Salles G. Pixantrone plus rituximab versus gemcitabine plus rituximab in patients with relapsed aggressive B-cell non-Hodgkin lymphoma not eligible for stem cell transplantation: a phase 3, randomized, multicentre trial (PIX306). Br J Haematol. 2020 Jan;188(2):240-248. doi: 10.1111/bjh.16255. Epub 2019 Dec 27.

Reference Type RESULT
PMID: 31879945 (View on PubMed)

Belada D, Georgiev P, Dakhil S, Inhorn LF, Andorsky D, Beck JT, Quick D, Pettengell R, Daly R, Dean JP, Pavlyuk M, Failloux N, Hubel K. Pixantrone-rituximab versus gemcitabine-rituximab in relapsed/refractory aggressive non-Hodgkin lymphoma. Future Oncol. 2016 Aug;12(15):1759-68. doi: 10.2217/fon-2016-0137. Epub 2016 Apr 20.

Reference Type DERIVED
PMID: 27093976 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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PIX306 (PIX-R Trial)

Identifier Type: -

Identifier Source: org_study_id