Single-Dose Pharmacokinetics (PK) Study of Novel Neurogenic Compound NSI-189

NCT ID: NCT01310881

Last Updated: 2011-11-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

35 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-02-28

Study Completion Date

2011-11-30

Brief Summary

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This is a subject single blinded, randomized, placebo-controlled, single dose, first-time-in-human study with three or more ascending cohorts.

Detailed Description

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Each subject will undergo Screening (Day -28 to Day -2). Subjects will return to the clinical site on Day -1, be admitted to the unit, and eligibility will be reconfirmed. Eligible subjects will receive a single dose of investigational medicinal product (IMP, NSI-189 Phosphate or Placebo) on Day 1 and will be followed for safety and PK until discharge on Day 3. Subjects who are experiencing any significant AEs that are considered possibly related to study drug will be kept at the unit for an additional day (or longer) until the event resolves or it is considered medically safe for the subject to be discharged. Subjects will have a telephone Follow-up on Day 4 and return to the unit on Day 7 (± 1) for End-of-study. Participation of an individual subject may last up to 36 days from the time of Screening until the End-of-study.

Conditions

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Depression

Keywords

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Neurogenesis hippocampal stem cells depression stroke

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Dose 1

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Dose 2

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Dose 3

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Dose 4

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Dose 5

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Dose 6

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Dose 7

Group Type EXPERIMENTAL

NSI-189 Phosphate

Intervention Type DRUG

Once daily oral administration

Interventions

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NSI-189 Phosphate

Once daily oral administration

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* A subject must meet all of the following criteria:

1. Subject has the ability to understand the purpose and risks of the study and to provide signed and dated informed consent.
2. Males and females between 18 to 55 years of age, inclusive, at the time of informed consent.
3. The following applies to female subjects:

• Non-childbearing potential (surgically sterile \[hysterectomy or bilateral tubal ligation\] or post-menopausal ≥ 1 year with follicle stimulating hormone \>40 U/L).
4. The following applies to male subjects:

• Male subjects with a female partner of childbearing potential will be required to use an effective method of birth control or practice abstinence during this study and for 3 months following discontinuation of IMP.
5. Non-smokers (or other nicotine use) as determined by history (no nicotine use over the past year) and by negative urine cotinine test at screening and Day -1.
6. BMI ≥ 19.5 and ≤30.0 kg/m2, at screening. Bodyweight must be \>50 kg.
7. Healthy, determined by pre-study medical evaluation and investigator discretion (medical history, physical examination, vital signs, ECG, and clinical laboratory evaluations).

Exclusion Criteria

1. Clinically significant history or evidence of cardiovascular, respiratory, hepatic, renal, gastrointestinal, endocrine, neurological, immunological, dermatological or psychiatric disorder(s), or other major disease as determined by the Investigator or designee.
2. History of seizures including febrile seizures, loss of consciousness, or any clinically significant finding on the neurologic examination.
3. Clinically significant abnormal clinical chemistry values, as determined by the Investigator.
4. Clinically significant (as determined by the Investigator) 12-lead ECG abnormalities, including corrected QT interval using Bazett's correction method of \>450 msec for males and \>470 msec for females.
5. History of severe allergic or anaphylactic reactions.
6. Subjects who have plans to undergo elective procedures/surgeries at any time during the study through the follow-up visits.
7. A positive screening test for human immunodeficiency virus (HIV), hepatitis C virus antibody (HCVAb), hepatitis B core antibody (HBcAb), or hepatitis B surface antigen (HBsAg).
8. Serious infection (e.g. pneumonia, septicemia) as determined by the Investigator within 3 months prior to Day -1.
9. Fever or bacterial, or viral infection (including upper respiratory tract infection) within 2 weeks prior to Day -1.
10. Treatment with any prescribed medication within 28 days prior to Day -1.
11. Treatment with any over-the-counter products (OTC), including herbal and/or alternative health preparations and procedures within the 14 days prior to Day -1. Note: Intermittent treatment with acetaminophen \[≤1000 mg/day\] and/or ibuprofen \[≤400 mg/day\] is permitted.
12. Current enrollment in any other drug, biologic, device, or clinical study, or treatment with an investigational product or approved therapy for investigational use within 30 days (or 5 half-lives, whichever is longer) prior to Day -1.
13. Any live or attenuated immunization/vaccination within 1 month prior to the study drug administration or planned to occur during the study period.
14. Donation of blood (\>500 mL) or blood products within 1 month prior to screening.
15. History of alcohol or substance abuse (cocaine, amphetamines, barbiturates, opiates, benzodiazepines, cannabinoids, etc.) (as determined by the Investigator).
16. Vigorous exercise (as determined by the Investigator) within 48 hours prior to the study drug administration.
17. Inability to comply with study requirements.
18. Any disorder that would interfere with the absorption, distribution, metabolism, or excretion of drugs.
19. Any concurrent disease or condition that, in the opinion of the Investigator, would make the subject unsuitable for participation in the clinical study.
20. Subject unwilling to avoid consumption of coffee and caffeine containing beverages within 48 hours prior to Day -1 until discharge from the clinical site.
21. Use of an investigational product within 30 days prior to Day -1.
22. Subject is unable to understand the protocol requirements, instructions and study-related restrictions, the nature, scope and possible consequences of the clinical study.
23. Subject is unlikely to comply with the protocol requirements, instructions and study-related restrictions.
24. Subject has previously been enrolled in this clinical study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Neuralstem Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Karl Johe, PhD

Role: STUDY_DIRECTOR

Neuralstem Inc.

David Han, MD

Role: PRINCIPAL_INVESTIGATOR

California Clinical Trials

Locations

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California Clinical Trials

Glendale, California, United States

Site Status

Countries

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United States

References

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Kessler RC, Berglund P, Demler O, Jin R, Koretz D, Merikangas KR, Rush AJ, Walters EE, Wang PS; National Comorbidity Survey Replication. The epidemiology of major depressive disorder: results from the National Comorbidity Survey Replication (NCS-R). JAMA. 2003 Jun 18;289(23):3095-105. doi: 10.1001/jama.289.23.3095.

Reference Type BACKGROUND
PMID: 12813115 (View on PubMed)

Deng W, Aimone JB, Gage FH. New neurons and new memories: how does adult hippocampal neurogenesis affect learning and memory? Nat Rev Neurosci. 2010 May;11(5):339-50. doi: 10.1038/nrn2822. Epub 2010 Mar 31.

Reference Type BACKGROUND
PMID: 20354534 (View on PubMed)

DeCarolis NA, Eisch AJ. Hippocampal neurogenesis as a target for the treatment of mental illness: a critical evaluation. Neuropharmacology. 2010 May;58(6):884-93. doi: 10.1016/j.neuropharm.2009.12.013. Epub 2010 Jan 6.

Reference Type BACKGROUND
PMID: 20060007 (View on PubMed)

Marlatt MW, Lucassen PJ. Neurogenesis and Alzheimer's disease: Biology and pathophysiology in mice and men. Curr Alzheimer Res. 2010 Mar;7(2):113-25. doi: 10.2174/156720510790691362.

Reference Type BACKGROUND
PMID: 19860727 (View on PubMed)

Kernie SG, Parent JM. Forebrain neurogenesis after focal Ischemic and traumatic brain injury. Neurobiol Dis. 2010 Feb;37(2):267-74. doi: 10.1016/j.nbd.2009.11.002. Epub 2009 Nov 10.

Reference Type BACKGROUND
PMID: 19909815 (View on PubMed)

Kempermann G, Krebs J, Fabel K. The contribution of failing adult hippocampal neurogenesis to psychiatric disorders. Curr Opin Psychiatry. 2008 May;21(3):290-5. doi: 10.1097/YCO.0b013e3282fad375.

Reference Type BACKGROUND
PMID: 18382230 (View on PubMed)

Other Identifiers

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NS2010-2

Identifier Type: -

Identifier Source: org_study_id